ADAPT Forward 1 - ISA1 - a Study to Evaluate Empasiprubart IV as add-on Therapy to Efgartigimod IV in Participants With AChR-Ab Seropositive Generalized Myasthenia Gravis With a Partial Clinical Response to Efgartigimod

NCT ID: NCT07284420

Last Updated: 2026-02-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

70 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-12-19

Study Completion Date

2028-03-07

Brief Summary

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This study is part of the ADAPT Forward platform study (NCT07294170). ADAPT Forward is a platform study with the aim to look at how safe different drugs are and how well they work for people with myasthenia gravis. The goal is to find the best therapeutic approach to reduce patients' side effects and improve their quality of life.

The aim of this ISA1 is to evaluate the safety and therapeutic relevance of empasiprubart as add-on therapy to efgartigimod in participants with AChR-Ab seropositive generalized myasthenia gravis.

The ADAPT Forward master protocol is registered on https://clinicaltrials.gov/study/NCT07294170

Detailed Description

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Once the master protocol and ISA1 screening periods are completed, eligible participants can enroll in the run-in period (part A) where they will receive efgartigimod IV. Eligible participants can then continue to the add-on period (part B) where they will receive both efgartigimod IV and empasiprubart IV.

Participants who are not eligible for part B will continue directly to the safety follow-up period (part C) where they will receive efgartigimod IV only.

The study duration for each participant is approximately up to 54 weeks.

Conditions

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AChR-Ab Seropositive Generalized Myasthenia Gravis Myasthenia Gravis MG gMG Generalized Myasthenia Gravis Generalized Myasthenia Gravis (gMG)

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Efgartigimod IV + Empasiprubart IV

Participants receive efgartigimod IV in part A, B and C and empasiprubart IV in part B

Group Type EXPERIMENTAL

Efgartigimod IV

Intervention Type BIOLOGICAL

Intravenous infusion of efgartigimod

Empasiprubart IV

Intervention Type BIOLOGICAL

Intravenous infusion of empasiprubart

Efgartigimod IV (part A + C)

Participants not eligible for part B, receiving efgartigimod IV in part A and C

Group Type EXPERIMENTAL

Efgartigimod IV

Intervention Type BIOLOGICAL

Intravenous infusion of efgartigimod

Interventions

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Efgartigimod IV

Intravenous infusion of efgartigimod

Intervention Type BIOLOGICAL

Empasiprubart IV

Intravenous infusion of empasiprubart

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

* Is seropositive for anti-acetylcholine receptor antibodies (AChR-Ab)
* Has confirmed diagnosis of gMG and is Myasthenia Gravis Foundation of America (MGFA) Class II, III, IVa, or IVb
* Has documented immunization against encapsulated bacterial pathogens (Neisseria meningitidis and Streptococcus pneumoniae) within 5 years of ISA screening or is willing to receive immunization at least 14 days before the first study drug administration

Exclusion Criteria

* Clinical diagnosis of systemic lupus erythematosus (SLE)
* Any known complement deficiency
* Current administration of a complement inhibitor or received zilucoplan or eculizumab \<2 months or ravulizumab \<6 months before the first study drug administration
* Patients proven to be refractory to efgartigimod (ie, not achieving a clinically meaningful improvement in total Myasthenia Gravis Activities of Daily Living (MG-ADL) score defined as an improvement of ≥2 points)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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argenx

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Profound Research LLC - Carlsbad

Carlsbad, California, United States

Site Status RECRUITING

Visionary Investigators Network

Miami, Florida, United States

Site Status RECRUITING

Dent Neurologic Institute - Amherst

Amherst, New York, United States

Site Status RECRUITING

Erlanger Health System

Chattanooga, Tennessee, United States

Site Status RECRUITING

National Neuromuscular Research Institute

Austin, Texas, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Sabine Coppieters, MD

Role: CONTACT

857-350-4834

Facility Contacts

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Gregory Sahagian, MD

Role: primary

857-350-4834

Andrew Lerman, MD

Role: primary

857-350-4834

Luisa Rojas Estupinan, MD

Role: primary

857-350-4834

Joshua Alpers, MD

Role: primary

857-350-4834

Yessar Hussain, MD

Role: primary

857-350-4834

Other Identifiers

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2025-522492-28-00

Identifier Type: CTIS

Identifier Source: secondary_id

ARGX-999-2-MG-20001

Identifier Type: -

Identifier Source: org_study_id

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