Study of Posoleucel (ALVR105,Viralym-M) for Multi-Virus Prevention in Patients Post-Allogeneic Hematopoietic Cell Transplant

NCT ID: NCT05305040

Last Updated: 2024-05-16

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2/PHASE3

Total Enrollment

451 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-03-24

Study Completion Date

2024-01-30

Brief Summary

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This is a Phase 3 study to evaluate posoleucel (ALVR105, Viralym-M); an allogeneic, off-the-shelf multi-virus specific T cell therapy that targets six viral pathogens: BK virus, cytomegalovirus, adenovirus, Epstein-Barr virus, human herpesvirus 6 and JC virus.

Detailed Description

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This is a Phase 2/3, multicenter, randomized, double-blind, placebo controlled trial comparing posoleucel to placebo for the prevention of infection or disease due to AdV, BKV, CMV, EBV, HHV-6, or JCV in high-risk adult and pediatric patients after allogeneic HCT.

There are 2 parts to the study, a Phase 3 randomized study cohort described in this posting, and an open label Phase 2 cohort described in NCT04693637, which has completed enrollment. In this Phase 3 part, approximately 302 eligible allogeneic HCT recipients will be enrolled and will receive 7 doses of posoleucel or placebo over 12 weeks, followed by a 12 week follow-up period.

Conditions

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Adenovirus Infection BK Virus Infection Cytomegalovirus Infections Epstein-Barr Virus Infections Human Herpes Virus-6 Infection JC Virus Infection

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

PREVENTION

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Posoleucel (ALVR105)

Administered as 2-4 milliliter infusion, visually identical to placebo

Group Type EXPERIMENTAL

Posoleucel (ALVR105)

Intervention Type BIOLOGICAL

Administered as 2-4 milliliter infusion, visually identical to placebo

Placebo

Administered as 2-4 milliliter infusion, visually identical to Posoleucel (ALVR105)

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type BIOLOGICAL

Administered as 2-4 milliliter infusion, visually identical to Posoleucel (ALVR105)

Interventions

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Posoleucel (ALVR105)

Administered as 2-4 milliliter infusion, visually identical to placebo

Intervention Type BIOLOGICAL

Placebo

Administered as 2-4 milliliter infusion, visually identical to Posoleucel (ALVR105)

Intervention Type BIOLOGICAL

Other Intervention Names

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Viralym-M

Eligibility Criteria

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Inclusion Criteria

* Any age at the day of screening visit.
* No known or suspected clinically significant disease from AdV, BKV, CMV, EBV, HHV-6, and/or JCV
* Within 25 days of receiving a first allogeneic HCT and have demonstrated clinical engraftment at time of dosing
* Meet one or more of the following criteria at the time of randomization:

* Related (sibling) donor with at least one mismatch at one of these HLA-gene loci: HLA-A, -B or -DR
* Haploidentical donor
* Matched or Mismatched unrelated donor
* Use of umbilical cord blood as stem cell source
* Ex vivo graft manipulation resulting in T cell depletion
* Received anti-thymocyte globulin or alemtuzumab (Campath-1H)

Exclusion Criteria

* History of AdV, BKV, CMV, EBV, HHV-6, and/or JCV end-organ disease within 6 months prior to randomization
* Evidence of active Grade \>2 acute GVHD
* Presence of non-minor uncontrolled or progressive bacterial, viral or fungal infections
* Known history or current (suspected) diagnosis of Grade ≥3 CRS requiring treatment associated with the administration of peptides, proteins, and/or antibodies
* Ongoing therapy with high-dose systemic corticosteroids (ie, prednisone equivalent dose \>1.0 mg/kg/day) within 24 hours prior to dosing
* Relapse of primary malignancy other than minimal residual disease
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AlloVir

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Alabama at Birmingham Children's of Alabama

Birmingham, Alabama, United States

Site Status

Honor Health Research Institute

Scottsdale, Arizona, United States

Site Status

City of Hope

Duarte, California, United States

Site Status

University of California, Los Angeles (UCLA)

Los Angeles, California, United States

Site Status

Stanford University

Palo Alto, California, United States

Site Status

University of California San Francisco - Benioff Children's Hospital

San Francisco, California, United States

Site Status

University of Colorado Hospital

Aurora, Colorado, United States

Site Status

Yale University School of Medicine - Yale Cancer Center

New Haven, Connecticut, United States

Site Status

Childrens National Health System

Washington D.C., District of Columbia, United States

Site Status

University of Florida (UF) - Gainesville

Gainesville, Florida, United States

Site Status

Moffitt Cancer Center

Tampa, Florida, United States

Site Status

Northside Hospital

Atlanta, Georgia, United States

Site Status

Loyola University Medical Center

Maywood, Illinois, United States

Site Status

Indiana University Hospital Simon Comprehensive Cancer Center

Indianapolis, Indiana, United States

Site Status

University of Kansas Hospital

Kansas City, Kansas, United States

Site Status

University of Maryland

Baltimore, Maryland, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

University of Minnesota

Minneapolis, Minnesota, United States

Site Status

Children's Mercy Hospital

Kansas City, Missouri, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status

Roswell Park Cancer Institute

Buffalo, New York, United States

Site Status

Columbia University

New York, New York, United States

Site Status

Weill Cornell Medical College

New York, New York, United States

Site Status

Stony Brook University Hospital Cancer Center

Stony Brook, New York, United States

Site Status

Carolinas Medical Center/Levine

Charlotte, North Carolina, United States

Site Status

Nationwide Children's Hospital

Columbus, Ohio, United States

Site Status

Oregon Health & Science University

Portland, Oregon, United States

Site Status

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

Children's Medical Center Dallas

Dallas, Texas, United States

Site Status

University of Utah/Primary Childrens Hospital

Salt Lake City, Utah, United States

Site Status

University of Virginia

Charlottesville, Virginia, United States

Site Status

Virginia Commonwealth University

Richmond, Virginia, United States

Site Status

Fred Hutchinson Cancer Research Center

Seattle, Washington, United States

Site Status

Froedtert Hospital and the Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Royal Adelaide Hospital

Adelaide, , Australia

Site Status

Austin Health

Heidelberg, , Australia

Site Status

Royal Brisbane and Women's Hospital

Herston, , Australia

Site Status

Royal Melbourne Hospital

Parkville, , Australia

Site Status

Queensland Children's Hospital

South Brisbane, , Australia

Site Status

Westmead Hospital

Westmead, , Australia

Site Status

A.Z. Sint-Jan Brugge Oostende AV

Bruges, , Belgium

Site Status

Institut Jules Bordet and the Childrens Hospital

Brussels, , Belgium

Site Status

University Hospital Gasthuisberg and Leuven

Leuven, , Belgium

Site Status

Alberta Children's Hospital

Calgary, , Canada

Site Status

Cellular Therapy Program - CHU Sainte-Justine (McGill)

Montreal, , Canada

Site Status

Hopital Maisonneve Rosemont

Montreal, , Canada

Site Status

The Hospital for Sick Children Blood & Marrow Transplant / Cellular Therapy Program

Toronto, , Canada

Site Status

UHN Blood and Marrow Transplant (BMT) Program (Princess Margaret) Cancer Center

Toronto, , Canada

Site Status

Leukemia/ BMT Program of British Columbia - Vancouver General Hospital

Vancouver, , Canada

Site Status

Centre Hospitalier Regional Universitaire de Lille

Lille, , France

Site Status

CHU de Nantes

Nantes, , France

Site Status

AP-HP Hopital Saint-Louis

Paris, , France

Site Status

Hopital Saint Antoine

Paris, , France

Site Status

Hopital Universitaire Robert Debre

Paris, , France

Site Status

Centre Hospitalier Lyon Sud

Pierre-Bénite, , France

Site Status

IUCT-Oncopole

Toulouse, , France

Site Status

Azienda Ospedaliero-Universitaria Careggi

Florence, , Italy

Site Status

Ospedale San Raffaele

Milan, , Italy

Site Status

Fondazione I.R.C.C.S. Policlinico San Matteo

Pavia, , Italy

Site Status

IRCSS Ospedale Pediatrico Bambino Gesu

Roma, , Italy

Site Status

University of Sacred Heart Policlinico A. Gemelli

Rome, , Italy

Site Status

Humanitas Cancer Center

Rozzano, , Italy

Site Status

Azienda Ospedaliera Universitaria Integrata Verona (AOUI)

Verona, , Italy

Site Status

Pusan National University Hospital

Busan, , South Korea

Site Status

Chonnam National University Hwasun Hospital

Hwasun, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Seoul St. Mary's Hospital

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Institut Catala d'Oncologia

Barcelona, , Spain

Site Status

Hospital General Universitario Gregorio Maranon

Madrid, , Spain

Site Status

Hospital Regional Universitario de Malaga

Málaga, , Spain

Site Status

Hospital Universitari i Politecnic La Fe de Valencia

Valencia, , Spain

Site Status

Acibadem Adana Hospital

Adana, , Turkey (Türkiye)

Site Status

Baskent Adana Hospital

Adana, , Turkey (Türkiye)

Site Status

Ankara Onkoloji Egitim Ve Arastirma Hastanesi

Ankara, , Turkey (Türkiye)

Site Status

Ankara University Hospital

Ankara, , Turkey (Türkiye)

Site Status

Gazi University Medical Faculty Hospital

Ankara, , Turkey (Türkiye)

Site Status

Medical Park Hospital

Antalya, , Turkey (Türkiye)

Site Status

Ege University Medical Faculty

Izmir, , Turkey (Türkiye)

Site Status

Anadolu Medical Center Hospital

Kocaeli, , Turkey (Türkiye)

Site Status

Inonu University Turgut Özal Medical Centre

Malatya, , Turkey (Türkiye)

Site Status

Bristol Haematology and Oncology Centre

Bristol, , United Kingdom

Site Status

University Hospitals Bristol - Bristol Hospital for Children

Bristol, , United Kingdom

Site Status

Addenbrooke's Hospital

Cambridge, , United Kingdom

Site Status

Queen Elizabeth University Hospital - Glasgow

Glasgow, , United Kingdom

Site Status

Great Ormond Street Hospital for Children

London, , United Kingdom

Site Status

Countries

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United States Australia Belgium Canada France Italy South Korea Spain Turkey (Türkiye) United Kingdom

References

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Posoleucel (ALVR105), an Off-the-Shelf, Multivirus-Specific T-Cell Therapy, for the Prevention of Viral Infections Post-HCT: Results from an Open-Label Cohort of a Phase 2 Trial Sanjeet S Dadwal, Michael Shuster, Gary Douglas Myers, Keith Boundy, Marshelle Warren, Elizabeth Stoner, Thuy Truong, Joshua A. Hill Blood (2021) 138 (Supplement 1): 1760.

Reference Type BACKGROUND

Tzannou I, Papadopoulou A, Naik S, Leung K, Martinez CA, Ramos CA, Carrum G, Sasa G, Lulla P, Watanabe A, Kuvalekar M, Gee AP, Wu MF, Liu H, Grilley BJ, Krance RA, Gottschalk S, Brenner MK, Rooney CM, Heslop HE, Leen AM, Omer B. Off-the-Shelf Virus-Specific T Cells to Treat BK Virus, Human Herpesvirus 6, Cytomegalovirus, Epstein-Barr Virus, and Adenovirus Infections After Allogeneic Hematopoietic Stem-Cell Transplantation. J Clin Oncol. 2017 Nov 1;35(31):3547-3557. doi: 10.1200/JCO.2017.73.0655. Epub 2017 Aug 7.

Reference Type BACKGROUND
PMID: 28783452 (View on PubMed)

Vasileiou S, Kuvalekar M, Velazquez Y, Watanabe A, Leen AM, Gilmore SA. Phenotypic and functional characterization of posoleucel, a multivirus-specific T cell therapy for the treatment and prevention of viral infections in immunocompromised patients. Cytotherapy. 2024 Aug;26(8):869-877. doi: 10.1016/j.jcyt.2024.03.012. Epub 2024 Mar 19.

Reference Type DERIVED
PMID: 38597860 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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P-105-202 Phase 3

Identifier Type: -

Identifier Source: org_study_id

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