Study to Evaluate Viralym-M (ALVR105) for the Treatment of Virus-Associated Hemorrhagic Cystitis (HC)

NCT ID: NCT04390113

Last Updated: 2024-05-14

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

97 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-03-18

Study Completion Date

2024-01-30

Brief Summary

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Study to Evaluate Viralym-M (ALVR105) for the Treatment of Virus-Associated Hemorrhagic Cystitis (HC).

Detailed Description

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The study hypothesis is that the administration of posoleucel (ALVR105) to patients with virus-associated HC will demonstrate superiority for the time to resolution of HC (as measured by resolution of macroscopic hematuria) compared to patients treated with placebo. The primary hypothesis will be tested in patients with BK virus (BKV) viruria to demonstrate superiority over placebo in this population (BK Intent-to-Treat \[ITT\] Population). A supplementary analysis will be conducted in all patients with any virus-associated HC (cytomegalovirus \[CMV\], human herpesvirus 6 \[HHV-6\], Epstein-Barr virus \[EBV\], JC virus \[JCV\], and/or adenovirus \[AdV\]) in order to evaluate efficacy in this broader population (ITT Population).

Conditions

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BK Virus Infection Hemorrhagic Cystitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Placebo

Administered as 2-4 milliliter infusion, visually identical to Posoleucel (ALVR105)

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type BIOLOGICAL

Administered as 2-4 milliliter infusion, visually identical to Posoleucel (ALVR105)

Posoleucel (ALVR105)

Administered as 2-4 milliliter infusion, visually identical to placebo

Group Type EXPERIMENTAL

Posoleucel (ALVR105)

Intervention Type BIOLOGICAL

Administered as 2-4 milliliter infusion, visually identical to placebo

Interventions

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Posoleucel (ALVR105)

Administered as 2-4 milliliter infusion, visually identical to placebo

Intervention Type BIOLOGICAL

Placebo

Administered as 2-4 milliliter infusion, visually identical to Posoleucel (ALVR105)

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

Participants must meet all of the following criteria in order to be eligible to participate in the study:

* Male or female ≥1 year of age.
* Had an allogeneic hematopoietic cell transplant (HCT) performed ≥21 days and ≤1 year prior to randomization.
* Myeloid engraftment confirmed, defined as an absolute neutrophil count ≥500/mm³ for 3 consecutive laboratory values obtained on different days, and platelet count \>10,000/mm³ at the time of randomization.
* Diagnosed with HC based on the following criteria (all 3 criteria must be met):

1. Clinical signs and/or symptoms of cystitis.
2. Grade ≥3 hematuria, defined as macroscopic hematuria with visible clots.
3. Viruria with ≥1 target virus (ie, BKV, JCV, AdV, CMV, EBV, and/or HHV-6).
* At least 1 identified, suitably matched posoleucel (ALVR105) cell line for infusion is available.

Exclusion Criteria

Participants who meet any of the following criteria will be excluded from participation in the study:

* Ongoing therapy with high-dose systemic corticosteroids (ie, prednisone dose \>0.5 mg/kg/day or equivalent).
* Therapy with antithymocyte globulin, alemtuzumab (Campath-1H), or other immunosuppressive T cell-targeted monoclonal antibodies ≤28 days before randomization.
* Evidence of active Grade \>2 acute graft versus host disease (GVHD).
* Uncontrolled or progressive bacterial or fungal infections.
* Uncontrolled or progressive viral infections not targeted by posoleucel (ALVR105).
* Uncontrolled or progressive EBV-associated post-transplant lymphoproliferative disorder.
* Known or presumed pneumonia secondary to any organism that is not considered to be well-controlled by antimicrobial therapy.
* Pregnant or lactating or planning to become pregnant.
Minimum Eligible Age

1 Year

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AlloVir

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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City of Hope National Medical Center

Duarte, California, United States

Site Status

Children's Hospital of Los Angeles

Los Angeles, California, United States

Site Status

Yale University School of Medicine - Yale Cancer Center

New Haven, Connecticut, United States

Site Status

Children's National Medical Center

Washington D.C., District of Columbia, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

Moffitt

Tampa, Florida, United States

Site Status

Northside Hospital

Atlanta, Georgia, United States

Site Status

Northwestern Memorial Hospital

Chicago, Illinois, United States

Site Status

University of Kansas Cancer Center

Kansas City, Kansas, United States

Site Status

Johns Hopkins Medicine

Baltimore, Maryland, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

University of Minnesota

Minneapolis, Minnesota, United States

Site Status

Children's Mercy Hospital - Kansas City

Kansas City, Missouri, United States

Site Status

University of Nebraska Medical Center

Omaha, Nebraska, United States

Site Status

Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status

Roswell Park Comprehensive Cancer Center

Buffalo, New York, United States

Site Status

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status

Ohio State University Medical Center (OSUMC)

Columbus, Ohio, United States

Site Status

Oregon Health & Science University

Portland, Oregon, United States

Site Status

Children's Hospital of Philadelphia (CHOP)

Philadelphia, Pennsylvania, United States

Site Status

The University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status

Virginia Commonwealth University

Richmond, Virginia, United States

Site Status

Fred Hutchinson Cancer Research Center

Seattle, Washington, United States

Site Status

Froedtert Hospital and the Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

CHU de Lille - Hopital Claude Huriez

Lille, , France

Site Status

CHU de Nantes - Hôtel-Dieu

Nantes, , France

Site Status

AP-HP Hopital Saint-Louis

Paris, , France

Site Status

HCL Centre Hospitalier Lyon Sud

Pierre-Bénite, , France

Site Status

IUCT-Oncopole

Toulouse, , France

Site Status

Azienda Ospedaliero-Universitaria Careggi

Florence, , Italy

Site Status

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano

Milan, , Italy

Site Status

IRCCS Ospedale San Raffaele

Milan, , Italy

Site Status

Ospedale Pediatrico Bambino Gesù

Roma, , Italy

Site Status

Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro Cuore

Rome, , Italy

Site Status

Istituto Clinico Humanitas

Rozzano, , Italy

Site Status

Azienda Ospedaliera Universitaria Integrata Verona-Ospedale Borgo Trento

Verona, , Italy

Site Status

Chonnam National University Hwasun Hospital

Jeongnam, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Pusan National University Hospital

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Seoul St. Mary's Hospital, The Catholic University of Korea

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Hospital Clinic Barcelona

Barcelona, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital Regional Universitario de Malaga

Málaga, , Spain

Site Status

Hospital Universitari i Politecnic La Fe

Valencia, , Spain

Site Status

Karolinska University Hospital

Stockholm, , Sweden

Site Status

University Hospitals Bristol NHS Foundation Trust

Bristol, , United Kingdom

Site Status

Queen Elizabeth University Hospital - Glasgow

Glasgow, , United Kingdom

Site Status

Great Ormond Street Hospital for Children

London, , United Kingdom

Site Status

Hammersmith Hospital

London, , United Kingdom

Site Status

The Royal Marsden NHS Foundation Trust

London, , United Kingdom

Site Status

University College London Hospital

London, , United Kingdom

Site Status

Nottingham University Hospitals

Nottingham, , United Kingdom

Site Status

Countries

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United States France Italy South Korea Spain Sweden United Kingdom

References

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Tzannou I, Papadopoulou A, Naik S, Leung K, Martinez CA, Ramos CA, Carrum G, Sasa G, Lulla P, Watanabe A, Kuvalekar M, Gee AP, Wu MF, Liu H, Grilley BJ, Krance RA, Gottschalk S, Brenner MK, Rooney CM, Heslop HE, Leen AM, Omer B. Off-the-Shelf Virus-Specific T Cells to Treat BK Virus, Human Herpesvirus 6, Cytomegalovirus, Epstein-Barr Virus, and Adenovirus Infections After Allogeneic Hematopoietic Stem-Cell Transplantation. J Clin Oncol. 2017 Nov 1;35(31):3547-3557. doi: 10.1200/JCO.2017.73.0655. Epub 2017 Aug 7.

Reference Type BACKGROUND
PMID: 28783452 (View on PubMed)

Vasileiou S, Kuvalekar M, Velazquez Y, Watanabe A, Leen AM, Gilmore SA. Phenotypic and functional characterization of posoleucel, a multivirus-specific T cell therapy for the treatment and prevention of viral infections in immunocompromised patients. Cytotherapy. 2024 Aug;26(8):869-877. doi: 10.1016/j.jcyt.2024.03.012. Epub 2024 Mar 19.

Reference Type DERIVED
PMID: 38597860 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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AVM-003-HC

Identifier Type: -

Identifier Source: org_study_id

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