Single Treatment of DaxibotulinumtoxinA for Injection in Adults With Isolated Cervical Dystonia (ASPEN-1)

NCT ID: NCT03608397

Last Updated: 2022-12-05

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

301 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-06-20

Study Completion Date

2020-06-16

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This is a randomized, double-blind, placebo-controlled, parallel group, multi-center trial of two doses of daxibotulinumtoxinA (DAXI) for injection (high-dose; low-dose in adult subjects with isolated (primary) cervical dystonia (CD).

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Approximately 300 subjects, recruited from approximately 80 study centers in the United States (US), Canada, and Europe will be randomized to DAXI for injection high dose, DAXI for injection low dose, or placebo group, respectively. Subjects will be stratified by treatment center and history of prior treatment with botulinum neurotoxin (BoNT).

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Cervical Dystonia

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Approximately 300 subjects, recruited from study centers in the United States (US), Canada, and Europe will be randomized to DAXI high dose, DAXI low dose or placebo group.
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Double Blinded

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

DAXI for injection low dose

Low Dose Group

Group Type EXPERIMENTAL

DaxibotulinumtoxinA for injection

Intervention Type BIOLOGICAL

DaxibotulinumtoxinA for injection is a sterile, white to off-white lyophilized product containing the active ingredient, daxibotulinumtoxinA, and inactive ingredients to be reconstituted with sterile, non-preserved, 0.9% sodium chloride solution saline.

DAXI for injection high dose

High Dose Group

Group Type EXPERIMENTAL

DaxibotulinumtoxinA for injection

Intervention Type BIOLOGICAL

DaxibotulinumtoxinA for injection is a sterile, white to off-white lyophilized product containing the active ingredient, daxibotulinumtoxinA, and inactive ingredients to be reconstituted with sterile, non-preserved, 0.9% sodium chloride solution saline.

Placebo

Placebo Group

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type BIOLOGICAL

Placebo is a sterile lyophilized product consisting of inactive ingredients without the neurotoxin to be reconstituted with sterile, non-preserved 0.9% sodium chloride solution.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

DaxibotulinumtoxinA for injection

DaxibotulinumtoxinA for injection is a sterile, white to off-white lyophilized product containing the active ingredient, daxibotulinumtoxinA, and inactive ingredients to be reconstituted with sterile, non-preserved, 0.9% sodium chloride solution saline.

Intervention Type BIOLOGICAL

Placebo

Placebo is a sterile lyophilized product consisting of inactive ingredients without the neurotoxin to be reconstituted with sterile, non-preserved 0.9% sodium chloride solution.

Intervention Type BIOLOGICAL

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Adults, 18 to 80 years of age
* Meets diagnostic criteria for isolated CD (idiopathic; dystonic symptoms localized to the head, neck, shoulder areas) with at least moderate severity at Baseline (Day 1), defined as a TWSTRS-total score of at least 20, with at least 15 on the TWSTRS-Severity subscale, at least 3 on the TWSTRS-Disability subscale, and at least 1 on the TWSTRS-Pain subscale

Exclusion Criteria

* Cervical dystonia attributable to an underlying etiology, (e.g., traumatic torticollis or tardive torticollis)
* Predominant retrocollis or anterocollis CD
* Significant dystonia in other body areas, or is currently being treated with BoNT for dystonia in areas other than those associated with isolated CD
* Severe dysphagia (Grade 3 or 4 on the Dysphagia Severity Scale) at Screening or Baseline (prior to study treatment)
* Any neuromuscular neurological conditions that may place the subject at increased risk of morbidity with exposure to BoNT, including peripheral motor neuropathic diseases (e.g., amyotrophic lateral sclerosis and motor neuropathy, and neuromuscular junctional disorders such as Lambert-Eaton syndrome and myasthenia gravis)
* Previous treatment with any BoNT product for any condition within the 14 weeks prior to Screening
* Botulinum Neurotoxin Type A (BoNTA), except the investigational daxibotulinumtoxinA, treatment-experienced subjects who had suboptimal or no treatment response to the most recent BoNTA injection for CD, as determined by the investigator, or history of primary or secondary non-response to BoNTA injections, known to have neutralizing antibodies to BoNTA; or have a history of botulinum toxin type B (rimabotulinumtoxinB \[Myobloc/Neurobloc\]) injection for CD due to non-response or suboptimal response to BoNTA
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Syneos Health

OTHER

Sponsor Role collaborator

Revance Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

HOPE Research Institute

Phoenix, Arizona, United States

Site Status

Movement Disorders Center of Arizona

Scottsdale, Arizona, United States

Site Status

The Parkinsons and Movement Disorder Institute

Fountain Valley, California, United States

Site Status

University of California, Irvine

Irvine, California, United States

Site Status

Loma Linda University

Loma Linda, California, United States

Site Status

USC Keck School of Medicine

Los Angeles, California, United States

Site Status

Care Access Research

Pasadena, California, United States

Site Status

Sutter Institute for Medical Research

Sacramento, California, United States

Site Status

Rocky Mountain Movement Disorders Center

Englewood, Colorado, United States

Site Status

Associated Neurologist, P.C.

Danbury, Connecticut, United States

Site Status

New England Institute for Clinical Research

Stamford, Connecticut, United States

Site Status

MedStar Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status

Parkinson's Disease and Movement Disorders Center of Boca Raton

Boca Raton, Florida, United States

Site Status

Design Neuroscience Center

Doral, Florida, United States

Site Status

University of Florida Center for Movement Disorders and Neurorestoration

Gainesville, Florida, United States

Site Status

Infinity Clinical Research

Hollywood, Florida, United States

Site Status

University of Florida Health Science Center Jacksonville

Jacksonville, Florida, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

Suncoast Neuroscience Associates

St. Petersburg, Florida, United States

Site Status

USF Parkinson's Disease and Movement Disorders Center

Tampa, Florida, United States

Site Status

Emory University

Atlanta, Georgia, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

Kansas Institute of Reseach

Overland Park, Kansas, United States

Site Status

Michigan State University

East Lansing, Michigan, United States

Site Status

QUEST Research Institute

Farmington, Michigan, United States

Site Status

Henry Ford West Bloomfield Hospital

West Bloomfield, Michigan, United States

Site Status

St Louis University

St Louis, Missouri, United States

Site Status

Washington University

St Louis, Missouri, United States

Site Status

University of Nebraska Medical Center

Omaha, Nebraska, United States

Site Status

Mount Sinai Movement Disorders Center

New York, New York, United States

Site Status

University of Rochester

Rochester, New York, United States

Site Status

Duke University

Durham, North Carolina, United States

Site Status

Wake Forest Health Sciences

Winston-Salem, North Carolina, United States

Site Status

Thomas Jefferson University

Philadelphia, Pennsylvania, United States

Site Status

University of Pennsylvania, Department of Neurology

Philadelphia, Pennsylvania, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Coastal Neurology

Port Royal, South Carolina, United States

Site Status

Wesley Neurology Clinic

Cordova, Tennessee, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Texas Neurology. P.A.

Dallas, Texas, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

Houston Methodist Neurological Institute

Houston, Texas, United States

Site Status

Central Texas Neurology Consultants

Round Rock, Texas, United States

Site Status

University of Vermont Medical Center

Burlington, Vermont, United States

Site Status

Medical University Innsbruck

Innsbruck, , Austria

Site Status

Universitaetsklinik fuer Neurologie

Vienna, , Austria

Site Status

University Health Network, Toronto Western Hospital

Toronto, Ontario, Canada

Site Status

Fakultni nemocnice Olomouc, Neurologicka klinika

Olomouc, , Czechia

Site Status

Fakultní nemocnice Ostrava, Neurologicka klinika

Ostrava-Poruba, , Czechia

Site Status

Lekarna Pardubicke nemocnice

Pardubice, , Czechia

Site Status

Neurologicka klinika 1. LF UK a VFN v Praze

Prague, , Czechia

Site Status

Vestra Clinics s.r.o.

Rychnov nad Kněžnou, , Czechia

Site Status

Hôpital Neurologique Pierre Wertheimer

Bron, , France

Site Status

CHU Grenoble Alpes

Grenoble, , France

Site Status

Hôpital Roger Salengro - CHRU de Lille

Lille, , France

Site Status

CHU Caremeau, Service de Neurologie

Nîmes, , France

Site Status

Praxis fuer Neurologie im Bismark Karrée

Berlin, , Germany

Site Status

Universitaetsklinikum Duesseldorf

Düsseldorf, , Germany

Site Status

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status

Klinikum rechts der Isar der TUM

München, , Germany

Site Status

GFO Kliniken Troisdorf, Betriebsstätte St. Johannes Sieglar

Troisdorf, , Germany

Site Status

Universitätsklinikum Tübingen

Tübingen, , Germany

Site Status

Szpital sw. Wojciecha Podmiot Leczniczy Copernicus Sp. Z o.o.

Gdansk, , Poland

Site Status

Marta Dagmara BANACH Marta Banach Specjalistyczny Gabinet Neurologiczny

Krakow, , Poland

Site Status

Krakowska Akademia Neurologii

Krakow, , Poland

Site Status

Wojewodzki Szpital Specjalistyczny w Olsztynie

Olsztyn, , Poland

Site Status

Centrum Medyczne Pratia Warszawa

Warsaw, , Poland

Site Status

Mazowiecki Szpital Brodnowski Sp. z o.o.

Warsaw, , Poland

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Hospital Universitario Burgos

Burgos, , Spain

Site Status

Hospital Universitario de La Princesa

Madrid, , Spain

Site Status

Royal Devon and Exeter Foundation Trust Hospital

Exeter, , United Kingdom

Site Status

The Walton Centre NHS Foundation Trust

Liverpool, , United Kingdom

Site Status

Salford Royal NHS Foundation Trust

Salford, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Austria Canada Czechia France Germany Poland Spain United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Comella CL, Jankovic J, Hauser RA, Patel AT, Banach MD, Ehler E, Vitarella D, Rubio RG, Gross TM; ASPEN-1 Study Group. Efficacy and Safety of DaxibotulinumtoxinA for Injection in Cervical Dystonia: ASPEN-1 Phase 3 Randomized Controlled Trial. Neurology. 2024 Feb 27;102(4):e208091. doi: 10.1212/WNL.0000000000208091. Epub 2024 Jan 31.

Reference Type DERIVED
PMID: 38295339 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

1720302

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Dysport® Adult Upper Limb Spasticity
NCT01313299 COMPLETED PHASE3