Dose-escalating Safety and Preliminary Efficacy of DaxibotulinumtoxinA for Injection in Cervical Dystonia

NCT ID: NCT02706795

Last Updated: 2019-11-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

37 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-09-30

Study Completion Date

2017-07-17

Brief Summary

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This is an open-label, dose-escalation study to assess the safety and preliminary efficacy of daxibotulinumtoxinA in subjects with isolated cervical dystonia (CD).

Detailed Description

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Conditions

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Torticollis (Spasmodic)

Study Design

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Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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daxibotulinumtoxinA (DAXI) for injection

DAXI for injection

Group Type EXPERIMENTAL

DaxibotulinumtoxinA

Intervention Type BIOLOGICAL

Low, mid, and high dose sequential treatments of daxibotulinumtoxinA in dose-escalation safety and efficacy study

Interventions

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DaxibotulinumtoxinA

Low, mid, and high dose sequential treatments of daxibotulinumtoxinA in dose-escalation safety and efficacy study

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

* Meets diagnostic criteria for isolated cervical dystonia
* Has moderate severity with a baseline Toronto Western Spasmodic Torticollis Rating Scale (TWSTRS) - Total score of at least 20 and a TWSTRS-Severity subscale score or at least 15
* Has been using stable doses of focal dystonia medications for at least 3 months and willing to continue through end of study

Exclusion Criteria

* Cervical dystonia attributable to an underlying etiology, such as traumatic torticollis or tardive torticollis; predominant retrocollis or anterocollis cervical dystonia
* Significant dystonia in other body areas, or is currently being treated with botulinum toxin for dystonia in other areas than isolated cervical dystonia
* Neurological abnormalities other than cervical dystonia
* History of severe dysphagia or aspiration, or current clinically significant swallowing disorder
* Previous neck surgery, phenol injection to the neck muscles, myotomy or denervation surgery in the neck/shoulder region, or intrathecal baclofen
* Marked limitation on passive range of motion that suggests contractures or other structural abnormality, e.g. cervical contractures or cervical spinal deformity
* Profound atrophy of cervical musculature
* Any neurological condition that may place the subject at increased risk with exposure to botulinum toxin type A, including peripheral motor neuropathic diseases such as amyotrophic lateral sclerosis and motor neuropathy, and neuromuscular junctional disorders such as Lambert-Eaton syndrome and myasthenia gravis
* Suboptimal efficacy response to any prior botulinum toxin type A product, when a previous treatment produced more optimal therapeutic response, as judged subjectively by the Investigator
* Previous treatment with any botulinum toxin product for any condition within the 6 months prior to Screening and during the study; presence of any blood coagulation disorder; or on anticoagulation treatment with international normalized ratio (INR) \> 3.5
Minimum Eligible Age

30 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Revance Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Nubia Kaba

Role: STUDY_DIRECTOR

Sponsor GmbH

Locations

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The Parkinson's & Movement Disorder Institute

Fountain Valley, California, United States

Site Status

Colorado Springs Neurological Associates

Colorado Springs, Colorado, United States

Site Status

University of Florida Center for Movement Disorders & Neurorestoration

Gainesville, Florida, United States

Site Status

Precision Research Organization

Miami Lakes, Florida, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

Emory University

Atlanta, Georgia, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

Kansas City Bone & Joint Clinic

Overland Park, Kansas, United States

Site Status

The NeuroMedical Center Clinic

Baton Rouge, Louisiana, United States

Site Status

Wake forest Baptist Health

Winston-Salem, North Carolina, United States

Site Status

Riverhills Healthcare, Inc.

Cincinnati, Ohio, United States

Site Status

Coastal Neurology

Port Royal, South Carolina, United States

Site Status

Parkinson's Disease Center and Movement Disorder Clinic

Houston, Texas, United States

Site Status

Countries

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United States

References

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Jankovic J, Truong D, Patel AT, Brashear A, Evatt M, Rubio RG, Oh CK, Snyder D, Shears G, Comella C. Injectable DaxibotulinumtoxinA in Cervical Dystonia: A Phase 2 Dose-Escalation Multicenter Study. Mov Disord Clin Pract. 2018 Apr 26;5(3):273-282. doi: 10.1002/mdc3.12613. eCollection 2018 May-Jun.

Reference Type DERIVED
PMID: 30009213 (View on PubMed)

Other Identifiers

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RT002-CL005

Identifier Type: -

Identifier Source: org_study_id

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