Efficacy and Safety of DaxibotulinumtoxinA for Injection for the Treatment of Adult Upper Limb Spasticity

NCT ID: NCT03821402

Last Updated: 2023-09-21

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

83 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-12-12

Study Completion Date

2020-11-23

Brief Summary

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This is a randomized, Double-Blind, Placebo-Controlled, Parallel Group, Dose-Ranging, trial to Evaluate the Efficacy and Safety of DaxibotulinumtoxinA for Injection for the Treatment of Upper Limb Spasticity in Adults After Stroke or Traumatic Brain Injury. The study will be conducted in the U.S.A., approximately 128 adult subjects from approximately 30 study centers will be randomly assigned (1:1:1:1) to one of four treatment groups. The study consists of a 21-day screening period, a treatment visit and follow-up visits.

The protocol was amended and the study was completed with fewer subjects than described in the initial protocol due to impact of COVID-19 on enrollment.

Detailed Description

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Subjects will be randomly assigned to DAXI for Injection 250 U, DAXI for Injection 375 U, DAXI for Injection 500 U, or placebo group, respectively. Eligible subjects will have ULS characterized by a primary aggregate posture

Conditions

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Upper Limb Spasticity

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Eligible subjects will be randomized (1:1:1:1) to one of four treatment groups: Group 1: DAXI 250 U (N=32); Group 2: DAXI 375 U (N=32); Group 3: DAXI 500 U (N=32); Group 4: Placebo (N=32).
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Double Blinded. The subject, Sponsor, and study site research personnel will be blinded to the identity of the subject's assigned treatment.

Study Groups

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DAXI 250 U

DAXI for injection for the treatment of Upper Limb Spasticity (ULS) in Adults with 250 U dose

Group Type EXPERIMENTAL

DAXI for injection 250 U

Intervention Type BIOLOGICAL

DaxibotulinumtoxinA for injection is a sterile, white to off-white lyophilized product containing the active ingredient, daxibotulinumtoxinA, and inactive ingredients to be reconstituted with sterile, non-preserved, 0.9% sodium chloride solution saline

DAXI 375 U

DAXI for injection for the treatment of Upper Limb Spasticity (ULS) in Adults with 375 U

Group Type EXPERIMENTAL

DAXI for injection 375 U

Intervention Type BIOLOGICAL

DaxibotulinumtoxinA for injection is a sterile, white to off-white lyophilized product containing the active ingredient, daxibotulinumtoxinA, and inactive ingredients to be reconstituted with sterile, non-preserved, 0.9% sodium chloride solution saline.

DAXI 500 U

DAXI for injection for the treatment of Upper Limb Spasticity (ULS) in Adults with 500 U

Group Type EXPERIMENTAL

DAXI for injection 500 U

Intervention Type BIOLOGICAL

DaxibotulinumtoxinA for injection is a sterile, white to off-white lyophilized product containing the active ingredient, daxibotulinumtoxinA, and inactive ingredients to be reconstituted with sterile, non-preserved, 0.9% sodium chloride solution saline

Placebo

Placebo group

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Placebo is a sterile lyophilized product consisting of inactive ingredients without the neurotoxin to be reconstituted with sterile, non-preserved 0.9% sodium chloride solution.

Interventions

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DAXI for injection 250 U

DaxibotulinumtoxinA for injection is a sterile, white to off-white lyophilized product containing the active ingredient, daxibotulinumtoxinA, and inactive ingredients to be reconstituted with sterile, non-preserved, 0.9% sodium chloride solution saline

Intervention Type BIOLOGICAL

DAXI for injection 375 U

DaxibotulinumtoxinA for injection is a sterile, white to off-white lyophilized product containing the active ingredient, daxibotulinumtoxinA, and inactive ingredients to be reconstituted with sterile, non-preserved, 0.9% sodium chloride solution saline.

Intervention Type BIOLOGICAL

DAXI for injection 500 U

DaxibotulinumtoxinA for injection is a sterile, white to off-white lyophilized product containing the active ingredient, daxibotulinumtoxinA, and inactive ingredients to be reconstituted with sterile, non-preserved, 0.9% sodium chloride solution saline

Intervention Type BIOLOGICAL

Placebo

Placebo is a sterile lyophilized product consisting of inactive ingredients without the neurotoxin to be reconstituted with sterile, non-preserved 0.9% sodium chloride solution.

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* 18 to 75 years of age
* Written informed consent including authorization to release health information
* Focal upper limb spasticity (ULS) after a stroke (as defined by WHO criteria) or traumatic brain injury (TBI), last stroke or TBI \> 24 weeks prior to Screening
* ULS with the primary aggregate posture
* Moderate to severe ULS with a MAS score ≥ 2 at the elbow, wrist, and finger flexors
* Moderate to severe functional disability (Disability Assessment Score \[DAS\] score ≥2) on the principal target of treatment
* Has sufficient cognitive and communication ability to be able to give informed consent

Exclusion Criteria

* Upper limb spasticity attributable to an etiology other than stroke or TBI.
* Bilateral upper limb paresis or quadriplegia.
* Initiated in physiotherapy of the upper extremities ≤ 30 days prior to Screening or planned to start physiotherapy of the upper extremities during the course of the study.
* Previous or planned treatment of the spastic upper limb with phenol, alcohol injection, or surgery
* Profound muscular atrophy or fixed contracture leading to marked limitation on range of motion
* Prior treatment with intrathecal baclofen
* Any neuromuscular neurologic conditions (amyotrophic lateral sclerosis, Lambert- Eaton, myasthenia gravis)
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Revance Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Rancho Research Institute at Rancho Los Amigos National Rehab Center

Downey, California, United States

Site Status

The Parkinsons and Movement Disorder Institute

Fountain Valley, California, United States

Site Status

Collaborative Neuroscience Network LLC

Long Beach, California, United States

Site Status

SC3 Research

Pasadena, California, United States

Site Status

Yale University

Fairfield, Connecticut, United States

Site Status

Waterbury Neurologists

Middlebury, Connecticut, United States

Site Status

Ki Health Partners LLC DBA New England Institute for Clinical Research

Stamford, Connecticut, United States

Site Status

MedStar National Rehabilitation Hospital

Washington D.C., District of Columbia, United States

Site Status

Parkinsons Disease and Movement Disorders Center

Boca Raton, Florida, United States

Site Status

NW FL Clinical Research Group, LLC

Gulf Breeze, Florida, United States

Site Status

Infinity Clinical Research

Hollywood, Florida, United States

Site Status

Parkinsons Disease Treatment Center of Southwest Florida

Port Charlotte, Florida, United States

Site Status

Shirley Ryan AbilityLab

Chicago, Illinois, United States

Site Status

Kansas Institute of Research

Overland Park, Kansas, United States

Site Status

William Beaumont Hospital

Royal Oak, Michigan, United States

Site Status

Rusk Rehabilitation Hospital

Columbia, Missouri, United States

Site Status

Icahn School of Medicine at Mount Sinai

New York, New York, United States

Site Status

Weill Cornell Medical College

New York, New York, United States

Site Status

Carolinas Rehabilitation

Charlotte, North Carolina, United States

Site Status

Wake Forest University School of Medicine

Salem, North Carolina, United States

Site Status

MossRehab

Elkins Park, Pennsylvania, United States

Site Status

University of Pittsburgh School of Medicine

Pittsburgh, Pennsylvania, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

North Texas Institute of Neurology and Headache

Frisco, Texas, United States

Site Status

University of Texas Health Science Center at Houston

Houston, Texas, United States

Site Status

University of Utah

Salt Lake City, Utah, United States

Site Status

Countries

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United States

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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1820203

Identifier Type: -

Identifier Source: org_study_id

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