Study of Rufinamide in Pediatric Subjects 1 to Less Than 4 Years of Age With Lennox-Gastaut Syndrome Inadequately Controlled With Other Anti-epileptic Drugs

NCT ID: NCT01405053

Last Updated: 2019-08-06

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

37 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-06-16

Study Completion Date

2015-11-02

Brief Summary

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This study was designed to evaluate the cognitive effect, safety, and pharmacokinetics (PK) of rufinamide on Lennox-Gastaut Syndrome (LGS) inadequately controlled in pediatric participants already taking other anti-epileptic drugs.

Detailed Description

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Conditions

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Lennox-Gastaut Syndrome

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Rufinamide

Group Type ACTIVE_COMPARATOR

Rufinamide

Intervention Type DRUG

Rufinamide up to 45 mg/kg/day, in 2 divided doses, administered as oral suspension (40 mg/mL) as an add-on to the subject's existing regimen of 1-3 antiepileptic drugs (AEDs)

Any other approved AED

Group Type ACTIVE_COMPARATOR

Any other approved Antiepileptic Drug

Intervention Type DRUG

Any other approved AED: any other approved AED of the investigator's choice as an add-on to the subject's existing regimen of 1-3 anti-epileptic drugs (AEDs)

Interventions

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Rufinamide

Rufinamide up to 45 mg/kg/day, in 2 divided doses, administered as oral suspension (40 mg/mL) as an add-on to the subject's existing regimen of 1-3 antiepileptic drugs (AEDs)

Intervention Type DRUG

Any other approved Antiepileptic Drug

Any other approved AED: any other approved AED of the investigator's choice as an add-on to the subject's existing regimen of 1-3 anti-epileptic drugs (AEDs)

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Clinical diagnosis of LGS, which might include the presence of a slow background electroencephalogram (EEG) rhythm, slow spikes-waves pattern (less than 3 Hz), the presence of polyspikes; care should be taken not to include benign myoclonic epilepsy of infancy, atypical benign partial epilepsy (pseudo-Lennox syndrome), or continuous spike-waves of slow sleep (CSWS).
2. On a fixed and documented dose of one to three concomitant regionally approved antiepileptic drugs (AEDs) for a minimum of 4 weeks prior to randomization with an inadequate response to treatment.
3. Consistent seizure documentation (i.e., no uncertainty of the presence of seizures) during the pre-randomization phase.

Key Exclusion:

1. Familial short QT syndrome
2. Prior treatment with rufinamide within 30 days of baseline visit or discontinuation of rufinamide treatment due to safety issues related to rufinamide
Minimum Eligible Age

1 Year

Maximum Eligible Age

3 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Eisai Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Alexis Arzimanoglou Arzimanoglou

Role: PRINCIPAL_INVESTIGATOR

Hopital Femme-Mere-Enfant Service D'Epilepsie -5eme etage 59 Boulevard Pinel Bron, France

Locations

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San Diego, California, United States

Site Status

Aurora, Colorado, United States

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Washington D.C., District of Columbia, United States

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Gulf Breeze, Florida, United States

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Miami, Florida, United States

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Tampa, Florida, United States

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Wellington, Florida, United States

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Augusta, Georgia, United States

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Chicago, Illinois, United States

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Lexington, Kentucky, United States

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Shreveport, Louisiana, United States

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Lebanon, New Hampshire, United States

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Gibbsboro, New Jersey, United States

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Rochester, New York, United States

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Akron, Ohio, United States

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Akson, Ohio, United States

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Columbus, Ohio, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Austin, Texas, United States

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San Antonio, Texas, United States

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Norfolk, Virginia, United States

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Calgary, Alberta, Canada

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Edmonton, Alberta, Canada

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Toronto, Ontario, Canada

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Saskatoon, , Canada

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Bron, , France

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Marseille, , France

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Paris, , France

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Ambelokipi Athens, , Greece

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Pátrai, , Greece

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Pendeli Athens, , Greece

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Thessaloniki, , Greece

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Mantova, MN, Italy

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Calambrone, PI, Italy

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Pisa, PI, Italy

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Pavia, PV, Italy

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Mantova, , Italy

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Roma, , Italy

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Salerno, , Italy

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Elblag, , Poland

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Gdansk, , Poland

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Kielce, , Poland

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Poznan, , Poland

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Rzeszów, , Poland

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Warsaw, , Poland

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Cape Town, , South Africa

Site Status

Countries

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United States Canada France Greece Italy Poland South Africa

References

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Brigo F, Jones K, Eltze C, Matricardi S. Anti-seizure medications for Lennox-Gastaut syndrome. Cochrane Database Syst Rev. 2021 Apr 7;4(4):CD003277. doi: 10.1002/14651858.CD003277.pub4.

Reference Type DERIVED
PMID: 33825230 (View on PubMed)

Auvin S, Williams B, McMurray R, Kumar D, Perdomo C, Malhotra M. Novel seizure outcomes in patients with Lennox-Gastaut syndrome: Post hoc analysis of seizure-free days in rufinamide Study 303. Epilepsia Open. 2019 Mar 13;4(2):275-280. doi: 10.1002/epi4.12314. eCollection 2019 Jun.

Reference Type DERIVED
PMID: 31168494 (View on PubMed)

Arzimanoglou A, Ferreira J, Satlin A, Olhaye O, Kumar D, Dhadda S, Bibbiani F. Evaluation of long-term safety, tolerability, and behavioral outcomes with adjunctive rufinamide in pediatric patients (>/=1 to <4 years old) with Lennox-Gastaut syndrome: Final results from randomized study 303. Eur J Paediatr Neurol. 2019 Jan;23(1):126-135. doi: 10.1016/j.ejpn.2018.09.010. Epub 2018 Sep 27.

Reference Type DERIVED
PMID: 30309816 (View on PubMed)

Arzimanoglou A, Ferreira JA, Satlin A, Mendes S, Williams B, Critchley D, Schuck E, Hussein Z, Kumar D, Dhadda S, Bibbiani F. Safety and pharmacokinetic profile of rufinamide in pediatric patients aged less than 4 years with Lennox-Gastaut syndrome: An interim analysis from a multicenter, randomized, active-controlled, open-label study. Eur J Paediatr Neurol. 2016 May;20(3):393-402. doi: 10.1016/j.ejpn.2015.12.015. Epub 2016 Jan 11.

Reference Type DERIVED
PMID: 26805435 (View on PubMed)

Other Identifiers

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E2080-G000-303

Identifier Type: -

Identifier Source: org_study_id

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