Safety and Efficacy Study of Cenobamate in Pediatric Subjects 2-17 Years of Age With Partial-onset (Focal) Seizures

NCT ID: NCT05067634

Last Updated: 2025-09-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

140 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-01-14

Study Completion Date

2026-07-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

Primary objective: To evaluate the safety and tolerability of cenobamate in pediatric subjects 2-17 years of age with partial-onset (focal) seizures

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Secondary objectives:

* To evaluate the efficacy of cenobamate tablets and suspension in pediatric subjects with partial onset (focal) seizures
* To evaluate the pharmacokinetics of cenobamate tablets and suspension in pediatric subjects with partial onset seizures
* To evaluate the PK/pharmacodynamics of cenobamate in pediatric subjects with partial onset (focal) seizures
* Acceptability and palatability assessment (determined by a 5-point Hedonic Scale) of the oral formulation and the 12.5 mg tablets - Day 1, and Day 15

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Partial Epilepsy

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

12 to < 18 year olds

Group Type EXPERIMENTAL

Xcopri

Intervention Type DRUG

Age groups 12 to \<18 will enroll once dosing data is received from Cohort I of the PK analysis of YKP3089C039 study. Age groups 6 to \<12 will enroll once dosing data is received from Cohort IIa of the PK analysis of YKP3089C039 study. Age groups 4 to \<6 will enroll once dosing data is received from Cohort IIb of the PK analysis of YKP3089C039 study. Age groups 2 to \<4 will enroll once dosing data is received from Cohort III of the PK analysis of YKP3089C039 study.

6 to <12 years old

Group Type EXPERIMENTAL

Xcopri

Intervention Type DRUG

Age groups 12 to \<18 will enroll once dosing data is received from Cohort I of the PK analysis of YKP3089C039 study. Age groups 6 to \<12 will enroll once dosing data is received from Cohort IIa of the PK analysis of YKP3089C039 study. Age groups 4 to \<6 will enroll once dosing data is received from Cohort IIb of the PK analysis of YKP3089C039 study. Age groups 2 to \<4 will enroll once dosing data is received from Cohort III of the PK analysis of YKP3089C039 study.

4 to <6 years old

Group Type EXPERIMENTAL

Xcopri

Intervention Type DRUG

Age groups 12 to \<18 will enroll once dosing data is received from Cohort I of the PK analysis of YKP3089C039 study. Age groups 6 to \<12 will enroll once dosing data is received from Cohort IIa of the PK analysis of YKP3089C039 study. Age groups 4 to \<6 will enroll once dosing data is received from Cohort IIb of the PK analysis of YKP3089C039 study. Age groups 2 to \<4 will enroll once dosing data is received from Cohort III of the PK analysis of YKP3089C039 study.

2 to <4 years old

Group Type EXPERIMENTAL

Xcopri

Intervention Type DRUG

Age groups 12 to \<18 will enroll once dosing data is received from Cohort I of the PK analysis of YKP3089C039 study. Age groups 6 to \<12 will enroll once dosing data is received from Cohort IIa of the PK analysis of YKP3089C039 study. Age groups 4 to \<6 will enroll once dosing data is received from Cohort IIb of the PK analysis of YKP3089C039 study. Age groups 2 to \<4 will enroll once dosing data is received from Cohort III of the PK analysis of YKP3089C039 study.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Xcopri

Age groups 12 to \<18 will enroll once dosing data is received from Cohort I of the PK analysis of YKP3089C039 study. Age groups 6 to \<12 will enroll once dosing data is received from Cohort IIa of the PK analysis of YKP3089C039 study. Age groups 4 to \<6 will enroll once dosing data is received from Cohort IIb of the PK analysis of YKP3089C039 study. Age groups 2 to \<4 will enroll once dosing data is received from Cohort III of the PK analysis of YKP3089C039 study.

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

1. Have a diagnosis of epilepsy with partial-onset (focal) seizures (POS) with or without secondarily generalized seizures according to the International League Against Epilepsy's (ILAE) Classification of Epileptic Seizures. A diagnosis should have been established at least 12 months prior to Visit 1 (Screening) by clinical history and an electroencephalogram (EEG) that is consistent with the diagnosis; normal interictal EEGs will be allowed provided that the participant meets the other diagnosis criterion (i.e., clinical history)
2. Male or female participant, from age 2 to less than 18 years at the time of informed consent/assent (dates including informed consent in YKP3089C039)
3. Have a minimum weight of 10.0 kilograms (kg) (22.0 pounds \[lb\])
4. Have had a brain imaging (e.g., magnetic resonance imaging \[MRI\] scan or computed tomography (CT) within 10 years before Visit 1 (Screening) that ruled out a progressive cause of epilepsy.
5. For subjects new to Study YKP3089C040, participants must have had at least 1 POS seizure during the 28-day Baseline Period. Only simple POS with motor signs, complex POS, and complex POS with secondary generalization are counted toward this inclusion for POS
6. Are currently being treated with stable doses of 1 to a maximum of 3 approved antiepileptic drugs (AEDs). Doses must be stable for at least 4 weeks before to Visit 1 (Screening). A vagal nerve stimulator \[VNS\] will not be counted as one of the 3 allowed AEDs but the settings should be stable for at least 4 weeks prior to Visit 1 (Screening).
7. Investigator believes subject could benefit from new or continued exposure to study drug
9. Subjects receiving felbamate as a concomitant AED must meet the following criteria:

1. Have a 12-month history of felbamate use and a history of a fixed dosing regimen for a minimum of 60 days prior to Visit 1 (Screening).
2. No prior or known history of hepatotoxicity or hematologic disorder due to felbamate.
10. Subjects following a ketogenic diet will be allowed as long as the diet has been stable for at least 30 days prior to Visit 1 (Screening) and will remain stable for the duration of the study

Exclusion Criteria

1. Females who are breastfeeding or pregnant at Screening or Baseline.
2. Current or history of pseudo-seizures (psychogenic nonepileptic seizures) within approximately 2 years before Visit 1 (Screening).
3. Have a history of status epilepticus that required hospitalization during the 6 months before Visit 1 (Screening).
4. Have an unstable psychiatric diagnosis that may confound participants' ability to participate in the study or that may prevent completion of the protocol-specified tests (e.g., significant suicide risk, including suicidal behavior and ideation within 6 months before Visit 1 (Screening), current psychotic disorder, acute mania).
5. Any suicidal ideation with intent, with or without a plan within 6 months before Visit 2 \[i.e., answering "Yes" to questions 4 or 5 on the Suicidal Ideation section of the Columbia-Suicide Severity Rating Scale (C-SSRS) in participants aged 6 and above, if able\].
6. Are scheduled and/or confirmed to have epilepsy surgery within 6 months after Visit 1 (Screening); however, those who have previously documented "failed" epilepsy surgery will be allowed.
7. Evidence of clinically significant disease (e.g., cardiac, respiratory, gastrointestinal, renal disease) that in the opinion of the investigator(s) could affect the participant's safety or interfere with the study assessments.
8. Presence of only nonmotor simple partial seizures or primary generalized epilepsies.
9. Evidence of moderate or severe renal insufficiency as defined by estimated glomerular filtration rates (eGFRs) of 31 to \< 60 "milliliters per minute (mL/min)" and \< 30 mL/min, respectively.
10. Evidence of significant active hepatic disease. Stable elevation of liver enzymes, alanine aminotransferase (ALT) and aspartate aminotransferase (AST) due to concomitant medication(s), will be allowed if they are less than 3 times the upper limit of normal (ULN).
11. Evidence of significant active hematological disease; white blood cell (WBC) count equal or less than 2500/µL (2.50 1E+09/liter \[L\]) or an absolute neutrophil count equal or less than 1000/µL (1.00 1E+09/L).
12. Subjects with Familial short QT syndrome.
13. Clinically significant electrocardiogram (ECG) abnormality, including prolonged corrected QT interval (QTc) defined as greater than 450 milliseconds (msec) or shortened corrected QT interval (QTc) defined as less than 340 msec.
14. Have a progressive central nervous system (CNS) disease, including degenerative CNS diseases and progressive tumors.
15. Subject has a history of any serious drug-induced hypersensitivity reaction (including, but not limited to, Stevens Johnson syndrome, toxic epidermal necrolysis, or DRESS) or any drug-related rash requiring hospitalization.
16. History of AED-associated rash that involved conjunctiva or mucosae.
17. History of more than one non-serious drug-related hypersensitivity reaction that required discontinuation of the medication.
18. Concomitant use of vigabatrin. Participants who took vigabatrin in the past must be off vigabatrin for at least 5 months before Visit 1 (Screening) and with documentation showing no evidence of a vigabatrin-associated clinically significant abnormality in a visual perimetry test.
19. A history of intermittent use of rescue benzodiazepines (i.e., 1 to 2 doses over a 24-hour period is considered a 1-time rescue) more than once within the 30 days prior to Visit 1(Screening).
20. A VNS implanted less than 5 months before Visit 1 (Screening) or changes in parameter less than 4 weeks before Visit 1 (or thereafter during the study).
21. History of or a concomitant medical condition that in the opinion of the investigator(s) would preclude the participant's participation in a clinical study or compromise the participant's ability to safely complete the study.
22. Have participated in a study involving administration of an investigational drug or device within 4 weeks before Visit 1 (Screening), or within approximately 5 half-lives of the previous investigational compound, whichever is longer.
23. Participants with rare hereditary problems of galactose intolerance, the Lapp lactase deficiency or glucose-galactose malabsorption.
24. For subjects new to Study YKP3089C040 previous exposure to cenobamate or sensitivity/allergy to components of the oral suspension.
Minimum Eligible Age

2 Years

Maximum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

SK Life Science, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Marc Kamin, MD

Role: STUDY_DIRECTOR

SK Life Science, Inc.

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Phoenix Children's Hospital

Phoenix, Arizona, United States

Site Status RECRUITING

Lucile Packard Children's Hospital Stanford

Palo Alto, California, United States

Site Status RECRUITING

University of California Davis Health

Sacramento, California, United States

Site Status TERMINATED

Connecticut Children's Medical Center

Hartford, Connecticut, United States

Site Status RECRUITING

Augusta University Medical Center

Augusta, Georgia, United States

Site Status TERMINATED

Clinical Integrative Research Center of Atlanta

Sandy Springs, Georgia, United States

Site Status RECRUITING

Meridian Clinical Research - Savannah Neurology Specialists

Savannah, Georgia, United States

Site Status TERMINATED

Kentucky Clinic

Lexington, Kentucky, United States

Site Status TERMINATED

Mid-Atlantic Epilepsy and Sleep Center

Bethesda, Maryland, United States

Site Status RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status WITHDRAWN

Spectrum Health Hospitals Helen DeVos Children's Hospital

Grand Rapids, Michigan, United States

Site Status RECRUITING

Mayo Clinic - Rochester

Rochester, Minnesota, United States

Site Status RECRUITING

University of Missouri Health Care - Women's and Children's Hospital

Columbia, Missouri, United States

Site Status TERMINATED

Northeast Regional Epilepsy Group

Hackensack, New Jersey, United States

Site Status RECRUITING

Northeast Regional Epilepsy Group - Morristown

Morristown, New Jersey, United States

Site Status RECRUITING

Boston Children's Health Physicians - Neurology at Hawthorne

Hawthorne, New York, United States

Site Status RECRUITING

Duke University Hospital

Durham, North Carolina, United States

Site Status RECRUITING

Akron Children's Hospital NeuroDevelopmental Science Center/Pediatric Neurology

Akron, Ohio, United States

Site Status TERMINATED

Cincinnati Children's Hospital

Cincinnati, Ohio, United States

Site Status RECRUITING

Cleveland Clinic Main Campus

Cleveland, Ohio, United States

Site Status RECRUITING

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status TERMINATED

Le Bonheur Children's Hospital

Memphis, Tennessee, United States

Site Status RECRUITING

Child Neurology Consultants of Austin

Austin, Texas, United States

Site Status RECRUITING

Scottish Rite for Children

Dallas, Texas, United States

Site Status TERMINATED

MultiCare Institute - Mary Bridge Children's Neurology

Tacoma, Washington, United States

Site Status RECRUITING

Austin Health

Heidelberg, , Australia

Site Status RECRUITING

Royal Children's Hospital Melbourne

Parkville, , Australia

Site Status RECRUITING

Sydney Children's Hospital - Randwick

Randwick, , Australia

Site Status RECRUITING

Children's Health Queensland Hospital and Health Service

South Brisbane, , Australia

Site Status RECRUITING

Charite University Hospital

Berlin, , Germany

Site Status RECRUITING

Diakonie Kork

Kehl, , Germany

Site Status TERMINATED

Universitätsklinikum Schleswig-Holstein - Campus Kiel

Kiel, , Germany

Site Status TERMINATED

Neurologische Klinik und Poliklinik Interdisziplinäres Epilepsiezentrum München

Munich, , Germany

Site Status RECRUITING

Universitätsklinikum Tübingen

Tübingen, , Germany

Site Status TERMINATED

Bethesda Gyermekkorhaz

Budapest, , Hungary

Site Status RECRUITING

Országos Klinikai Idegtudományi Intézet, Neurológiai Osztály

Budapest, , Hungary

Site Status RECRUITING

Semmelweis University Dept. Of Paediatrics

Budapest, , Hungary

Site Status RECRUITING

Servus Salvus Egészségügyi Szolgáltató Kft.

Budapest, , Hungary

Site Status RECRUITING

Debreceni Egyetem Klinikai Központ

Debrecen, , Hungary

Site Status RECRUITING

Niepubliczny Zaklad Opieki Zdrowotnej - Centrum Neurologii Dzieciecej i Leczenia Padaczki

Kielce, , Poland

Site Status RECRUITING

Centrum Medyczne Plejady

Krakow, , Poland

Site Status RECRUITING

Wojewódzki Specjalistyczny Szpital Dziecięcy im. św. Ludwika w Krakowie

Krakow, , Poland

Site Status TERMINATED

Chungbuk National University Hospital

Cheonju, , South Korea

Site Status RECRUITING

Korea University Guro Hospital

Seoul, , South Korea

Site Status RECRUITING

Seoul National University Hospital

Seoul, , South Korea

Site Status RECRUITING

Severance Hospital

Seoul, , South Korea

Site Status RECRUITING

SMG-SNU Boramae Medical Center

Seoul, , South Korea

Site Status RECRUITING

Ajou University Hospital

Suwon, , South Korea

Site Status RECRUITING

Hospital Sant Joan de Déu Barcelona

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitari Vall d'Hebrón

Barcelona, , Spain

Site Status RECRUITING

Hospital Infantil Universitario Niño Jesús

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario La Paz

Madrid, , Spain

Site Status TERMINATED

Clinica Universidad de Navarra - Pamplona

Pamplona, , Spain

Site Status TERMINATED

Instituto de Investigación Sanitaria de la Fundación Ramón Domínguez

Santiago de Compostela, , Spain

Site Status TERMINATED

Hospital Universitario Virgen del Rocío

Seville, , Spain

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

United States Australia Germany Hungary Poland South Korea Spain

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

Meagan Whritner

Role: CONTACT

201-431-7812

Sunita Misra, MD, PhD

Role: CONTACT

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Role: primary

602-933-0970

Role: primary

650-497-8000

Role: primary

860-837-7500

Role: primary

678-705-7341

Arkady Barber

Role: primary

301-530-9744

Role: primary

616-267-2500

Role: primary

507-284-2511

Role: primary

201-343-6676

Role: primary

914-768-3970

Role: primary

919-668-0477

Susan Fong

Role: primary

Role: primary

216-444-8012

Role: primary

901-287-5207

Role: primary

512-494-4024

Steven Phillips

Role: primary

Role: primary

+49 89 440072685

Role: primary

36301806632

Role: primary

36306894248

Role: primary

36304330361

Role: primary

36 70 945 0368

Role: primary

48604091678

Role: primary

48608336668

Role: primary

+82-43-269-6537

Role: primary

+82 1577-9966

Role: primary

+82 1588-5700

Role: primary

02-870-2177

Role: primary

+82-31-219-4252

Role: primary

+34 936009733

Role: primary

+34 934 89 30 00

Role: primary

+34 915 03 59 00

Role: primary

34 955 013 767

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

YKP3089C040

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Pediatric Epilepsy Study
NCT00050947 COMPLETED PHASE3
Pediatric Epilepsy Study
NCT00050934 COMPLETED PHASE3
An Open-label Study of XEN1101 in Epilepsy
NCT05718817 ENROLLING_BY_INVITATION PHASE3