A Phase 2 Study For Patients With A Physician's Diagnosis Of Rheumatoid Arthritis

NCT ID: NCT00550446

Last Updated: 2013-01-03

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

386 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-09-30

Study Completion Date

2009-01-31

Brief Summary

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The purpose of this study is to determine the effectiveness and safety, over 6 months, of 5 doses of CP-690,550 for the treatment of adults with active rheumatoid arthritis. Five out of seven subjects will receive CP-690,550. One out of seven will receive adalimumab (Humira®) and one out of seven will only receive inactive substances (placebo.)

Detailed Description

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Conditions

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Arthritis, Rheumatoid

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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1

Group Type ACTIVE_COMPARATOR

Adalimumab

Intervention Type DRUG

40mg subcutaneous injections every other week for 6 injections during week 0-10 with oral placebo BID. Subjects switched to CP-690,550 at week 12.

2

Group Type EXPERIMENTAL

CP-690-550

Intervention Type DRUG

15 mg BID oral plus 6 placebo subcutaneous injections (week 0-10)

3

Group Type EXPERIMENTAL

CP-690-550

Intervention Type DRUG

10 mg BID oral plus 6 placebo subcutaneous injections (week 0-10)

4

Group Type EXPERIMENTAL

CP-690-550

Intervention Type DRUG

5 mg BID oral plus 6 placebo subcutaneous injections (week 0-10)

5

Group Type EXPERIMENTAL

CP-690,550

Intervention Type DRUG

3 mg BID PO plus 6 placebo subcutaneous injections (week 0-10)

6

Group Type EXPERIMENTAL

CP-690,550

Intervention Type DRUG

1 mg BID PO plus 6 placebo subcutaneous injections (week 0-10)

7

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo by mouth plus 6 placebo subcutaneous injections (week 0-10)

Interventions

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Adalimumab

40mg subcutaneous injections every other week for 6 injections during week 0-10 with oral placebo BID. Subjects switched to CP-690,550 at week 12.

Intervention Type DRUG

CP-690-550

15 mg BID oral plus 6 placebo subcutaneous injections (week 0-10)

Intervention Type DRUG

CP-690-550

10 mg BID oral plus 6 placebo subcutaneous injections (week 0-10)

Intervention Type DRUG

CP-690-550

5 mg BID oral plus 6 placebo subcutaneous injections (week 0-10)

Intervention Type DRUG

CP-690,550

3 mg BID PO plus 6 placebo subcutaneous injections (week 0-10)

Intervention Type DRUG

CP-690,550

1 mg BID PO plus 6 placebo subcutaneous injections (week 0-10)

Intervention Type DRUG

Placebo

Placebo by mouth plus 6 placebo subcutaneous injections (week 0-10)

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Subjects must have active rheumatoid arthritis
* Subjects must have failed at least 1 disease modifying anti-rheumatic drug (DMARD)
* Subjects must not be currently taking any DMARD other than an antimalarial

Exclusion Criteria

* Subjects who discontinued any previous TNF inhibitor therapy for either lack of benefit or safety.
* Subjects who previously received adalimumab (Humira®) therapy for any reason.
* Subjects with evidence of blood disorders, chronic infections or untreated tuberculosis
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Pfizer Investigational Site

Mesa, Arizona, United States

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Little Rock, Arkansas, United States

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Northridge, California, United States

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Palo Alto, California, United States

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Stanford, California, United States

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Tarzana, California, United States

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Upland, California, United States

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Orlando, Florida, United States

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Tampa, Florida, United States

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Morton Grove, Illinois, United States

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Rockford, Illinois, United States

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Cedar Rapids, Iowa, United States

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Wichita, Kansas, United States

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Wichita, Kansas, United States

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New Orleans, Louisiana, United States

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Hickory, North Carolina, United States

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Hickory, North Carolina, United States

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Dayton, Ohio, United States

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Duncansville, Pennsylvania, United States

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Knoxville, Tennessee, United States

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Dallas, Texas, United States

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Mesquite, Texas, United States

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Porto Alegre, Rio Grande do Sul, Brazil

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São Paulo, São Paulo, Brazil

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Pleven, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Santiago, RM, Chile

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Santiago, RM, Chile

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Providencia, Santiago, RM, Chile

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Split, , Croatia

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Zagreb, , Croatia

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Brno, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Praha 11 - Chodov, , Czechia

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Zlín, , Czechia

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Dresden, , Germany

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Hamburg, , Germany

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Hildesheim, , Germany

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Leipzig, , Germany

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Goudi, Athens, Greece

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Thessaloniki, , Greece

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Szolnok, , Hungary

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Florence, , Italy

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Genova, , Italy

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México, D.f., Mexico

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Guadalajara, Jalisco, Mexico

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Cuernavaca, Morelos, Mexico

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Metepec, State of Mexico, Mexico

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Constanța, Constanța County, Romania

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Iași, Iaşi, Romania

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Bucharest, , Romania

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Piešťany, , Slovakia

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Žilina, , Slovakia

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Seoul, , South Korea

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Seoul, , South Korea

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Kharkiv, , Ukraine

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Kyiv, , Ukraine

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Lviv, , Ukraine

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Vinnitsa, , Ukraine

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Zaporizhzhia, , Ukraine

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Countries

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United States Brazil Bulgaria Chile Croatia Czechia Germany Greece Hungary Italy Mexico Romania Slovakia South Korea Ukraine

References

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Hetland ML, Strangfeld A, Bonfanti G, Soudis D, Deuring JJ, Edwards RA. Machine learning prediction and explanatory models of serious infections in patients with rheumatoid arthritis treated with tofacitinib. Arthritis Res Ther. 2024 Aug 27;26(1):153. doi: 10.1186/s13075-024-03376-9.

Reference Type DERIVED
PMID: 39192350 (View on PubMed)

Wright GC, Mysler E, Kwok K, Cadatal MJ, Germino R, Yndestad A, Kinch CD, Ogdie A. Impact of Race on the Efficacy and Safety of Tofacitinib in Rheumatoid Arthritis: Post Hoc Analysis of Pooled Clinical Trials. Rheumatol Ther. 2024 Oct;11(5):1135-1164. doi: 10.1007/s40744-024-00677-y. Epub 2024 Jul 3.

Reference Type DERIVED
PMID: 38958913 (View on PubMed)

Charles-Schoeman C, Hyde C, Guan S, Parikh N, Wang J, Shahbazian A, Stockert L, Andrews J. Relationship Between Paraoxonase-1 Genotype and Activity, and Major Adverse Cardiovascular Events and Malignancies in Patients With Rheumatoid Arthritis Receiving Tofacitinib. J Rheumatol. 2023 Jul 15:jrheum.2023-0112. doi: 10.3899/jrheum.2023-0112. Online ahead of print.

Reference Type DERIVED
PMID: 37453736 (View on PubMed)

Kristensen LE, Danese S, Yndestad A, Wang C, Nagy E, Modesto I, Rivas J, Benda B. Identification of two tofacitinib subpopulations with different relative risk versus TNF inhibitors: an analysis of the open label, randomised controlled study ORAL Surveillance. Ann Rheum Dis. 2023 Jul;82(7):901-910. doi: 10.1136/ard-2022-223715. Epub 2023 Mar 17.

Reference Type DERIVED
PMID: 36931693 (View on PubMed)

Hansen KE, Mortezavi M, Nagy E, Wang C, Connell CA, Radi Z, Litman HJ, Adami G, Rossini M. Fracture in clinical studies of tofacitinib in rheumatoid arthritis. Ther Adv Musculoskelet Dis. 2022 Dec 27;14:1759720X221142346. doi: 10.1177/1759720X221142346. eCollection 2022.

Reference Type DERIVED
PMID: 36601090 (View on PubMed)

Curtis JR, Yamaoka K, Chen YH, Bhatt DL, Gunay LM, Sugiyama N, Connell CA, Wang C, Wu J, Menon S, Vranic I, Gomez-Reino JJ. Malignancy risk with tofacitinib versus TNF inhibitors in rheumatoid arthritis: results from the open-label, randomised controlled ORAL Surveillance trial. Ann Rheum Dis. 2023 Mar;82(3):331-343. doi: 10.1136/ard-2022-222543. Epub 2022 Dec 5.

Reference Type DERIVED
PMID: 36600185 (View on PubMed)

Winthrop KL, Yndestad A, Henrohn D, Danese S, Marsal S, Galindo M, Woolcott JC, Jo H, Kwok K, Shapiro AB, Jones TV, Diehl A, Su C, Panes J, Cohen SB. Influenza Adverse Events in Patients with Rheumatoid Arthritis, Ulcerative Colitis, or Psoriatic Arthritis in the Tofacitinib Clinical Development Programs. Rheumatol Ther. 2023 Apr;10(2):357-373. doi: 10.1007/s40744-022-00507-z. Epub 2022 Dec 17.

Reference Type DERIVED
PMID: 36526796 (View on PubMed)

Winthrop KL, Curtis JR, Yamaoka K, Lee EB, Hirose T, Rivas JL, Kwok K, Burmester GR. Clinical Management of Herpes Zoster in Patients With Rheumatoid Arthritis or Psoriatic Arthritis Receiving Tofacitinib Treatment. Rheumatol Ther. 2022 Feb;9(1):243-263. doi: 10.1007/s40744-021-00390-0. Epub 2021 Dec 6.

Reference Type DERIVED
PMID: 34870800 (View on PubMed)

Cohen SB, Tanaka Y, Mariette X, Curtis JR, Lee EB, Nash P, Winthrop KL, Charles-Schoeman C, Wang L, Chen C, Kwok K, Biswas P, Shapiro A, Madsen A, Wollenhaupt J. Long-term safety of tofacitinib up to 9.5 years: a comprehensive integrated analysis of the rheumatoid arthritis clinical development programme. RMD Open. 2020 Oct;6(3):e001395. doi: 10.1136/rmdopen-2020-001395.

Reference Type DERIVED
PMID: 33127856 (View on PubMed)

Panaccione R, Isaacs JD, Chen LA, Wang W, Marren A, Kwok K, Wang L, Chan G, Su C. Characterization of Creatine Kinase Levels in Tofacitinib-Treated Patients with Ulcerative Colitis: Results from Clinical Trials. Dig Dis Sci. 2021 Aug;66(8):2732-2743. doi: 10.1007/s10620-020-06560-4. Epub 2020 Aug 20.

Reference Type DERIVED
PMID: 32816215 (View on PubMed)

Suzuki M, Shoji S, Miyoshi S, Krishnaswami S. Model-Based Comparison of Dose-Response Profiles of Tofacitinib in Japanese Versus Western Rheumatoid Arthritis Patients. J Clin Pharmacol. 2020 Feb;60(2):198-208. doi: 10.1002/jcph.1514. Epub 2019 Sep 12.

Reference Type DERIVED
PMID: 31512746 (View on PubMed)

Mariette X, Chen C, Biswas P, Kwok K, Boy MG. Lymphoma in the Tofacitinib Rheumatoid Arthritis Clinical Development Program. Arthritis Care Res (Hoboken). 2018 May;70(5):685-694. doi: 10.1002/acr.23421. Epub 2018 Apr 2.

Reference Type DERIVED
PMID: 28941219 (View on PubMed)

Cohen SB, Tanaka Y, Mariette X, Curtis JR, Lee EB, Nash P, Winthrop KL, Charles-Schoeman C, Thirunavukkarasu K, DeMasi R, Geier J, Kwok K, Wang L, Riese R, Wollenhaupt J. Long-term safety of tofacitinib for the treatment of rheumatoid arthritis up to 8.5 years: integrated analysis of data from the global clinical trials. Ann Rheum Dis. 2017 Jul;76(7):1253-1262. doi: 10.1136/annrheumdis-2016-210457. Epub 2017 Jan 31.

Reference Type DERIVED
PMID: 28143815 (View on PubMed)

Wallenstein GV, Kanik KS, Wilkinson B, Cohen S, Cutolo M, Fleischmann RM, Genovese MC, Gomez Reino J, Gruben D, Kremer J, Krishnaswami S, Lee EB, Pascual-Ramos V, Strand V, Zwillich SH. Effects of the oral Janus kinase inhibitor tofacitinib on patient-reported outcomes in patients with active rheumatoid arthritis: results of two Phase 2 randomised controlled trials. Clin Exp Rheumatol. 2016 May-Jun;34(3):430-42. Epub 2016 Apr 28.

Reference Type DERIVED
PMID: 27156561 (View on PubMed)

Charles-Schoeman C, Burmester G, Nash P, Zerbini CA, Soma K, Kwok K, Hendrikx T, Bananis E, Fleischmann R. Efficacy and safety of tofacitinib following inadequate response to conventional synthetic or biological disease-modifying antirheumatic drugs. Ann Rheum Dis. 2016 Jul;75(7):1293-301. doi: 10.1136/annrheumdis-2014-207178. Epub 2015 Aug 14.

Reference Type DERIVED
PMID: 26275429 (View on PubMed)

Cohen S, Radominski SC, Gomez-Reino JJ, Wang L, Krishnaswami S, Wood SP, Soma K, Nduaka CI, Kwok K, Valdez H, Benda B, Riese R. Analysis of infections and all-cause mortality in phase II, phase III, and long-term extension studies of tofacitinib in patients with rheumatoid arthritis. Arthritis Rheumatol. 2014 Nov;66(11):2924-37. doi: 10.1002/art.38779.

Reference Type DERIVED
PMID: 25047021 (View on PubMed)

Fleischmann R, Cutolo M, Genovese MC, Lee EB, Kanik KS, Sadis S, Connell CA, Gruben D, Krishnaswami S, Wallenstein G, Wilkinson BE, Zwillich SH. Phase IIb dose-ranging study of the oral JAK inhibitor tofacitinib (CP-690,550) or adalimumab monotherapy versus placebo in patients with active rheumatoid arthritis with an inadequate response to disease-modifying antirheumatic drugs. Arthritis Rheum. 2012 Mar;64(3):617-29. doi: 10.1002/art.33383.

Reference Type DERIVED
PMID: 21952978 (View on PubMed)

Related Links

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Other Identifiers

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A3921035

Identifier Type: -

Identifier Source: org_study_id

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