Safety and Effectiveness of Acthar Gel in Participants With Rheumatoid Arthritis

NCT ID: NCT02919761

Last Updated: 2020-03-31

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE4

Total Enrollment

259 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-11-07

Study Completion Date

2019-02-13

Brief Summary

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This is a 2-part study to examine the effect of Acthar Gel in adult participants with rheumatoid arthritis (RA) with persistently active disease even after receiving two other treatments intended to modify the disease.

Part 1 is an Open Label Period in which all eligible participants receive Acthar Gel for 12 weeks. After these 12 weeks of treatment with Acthar Gel, participants will be evaluated for treatment response using the DAS28-ESR.

Participants who have achieved low disease activity (LDA) will enter a double-blind randomized maintenance period (Part 2) and be randomized in a 1:1 ratio to receive either Acthar Gel or matching placebo for an additional 12 weeks.

A single participant might be involved in the trial for as many as 32 weeks.

Detailed Description

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Conditions

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Arthritis, Rheumatoid

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Part 1: Single Group; Part 2: Parallel
Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators
Part 1: Open Label ; Part 2: Double-blind

Study Groups

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Part 1: All Enrolled Participants

All participants receive Acthar Gel 1 mL twice weekly for 12 weeks

Group Type EXPERIMENTAL

Acthar Gel

Intervention Type DRUG

80 Units Acthar Gel per 1 mL for subcutaneous injection

Part 2: Acthar Gel

Participants receive Acthar Gel 1 mL twice weekly for an additional 12 weeks

Group Type EXPERIMENTAL

Acthar Gel

Intervention Type DRUG

80 Units Acthar Gel per 1 mL for subcutaneous injection

Part 2: Placebo

Participants receive Placebo 1 mL twice weekly for an additional 12 weeks

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching placebo 1 mL for subcutaneous injection

Interventions

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Acthar Gel

80 Units Acthar Gel per 1 mL for subcutaneous injection

Intervention Type DRUG

Placebo

Matching placebo 1 mL for subcutaneous injection

Intervention Type DRUG

Other Intervention Names

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Acthar H.P. Acthar Gel Matching Placebo

Eligibility Criteria

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Inclusion Criteria

* Male or nonpregnant, nonlactating female subjects
* Meets criteria for definite rheumatoid arthritis as defined by 2010 American College of Rheumatology (ACR)/European League Against Rheumatism (EULAR) classification at screening
* Has active disease defined as a score of \>3.2 on DAS28-ESR prior to study drug administration despite dual-DMARD treatment
* Is on a stable dose of ≤ 20 mg per week of methotrexate for at least 8 weeks AND a stable dose of an allowed DMARD for at least 24 weeks prior to the screening visit
* May also be on a stable dose of 10 mg or less of prednisone or other the dose equivalent of another corticosteroid for 4 weeks prior to study drug administration

Exclusion Criteria

* Has current rheumatoid disease or inflammatory joint disease other than RA
* Has any history of use of adrenocorticotropic hormone (ACTH) for the treatment of RA
* Has taken B-cell mediated therapies in the 6 months prior to screening
* Has hepatitis B, hepatitis C, history of tuberculosis (TB) or other contraindication as per the United States (US) Prescribing Information for Acthar
* Has history of Type 1 or Type 2 diabetes
* Has any clinically significant infection
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Mallinckrodt

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Team Leader

Role: STUDY_DIRECTOR

Mallinckrodt Pharmaceutical

Locations

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East Bay Rheumatology Medical Group

San Leandro, California, United States

Site Status

Inland Rheumatology Clinical Trials

Upland, California, United States

Site Status

Orthopedic Research Institute

Boynton Beach, Florida, United States

Site Status

Clinical Research of West Florida

Clearwater, Florida, United States

Site Status

Southeastern Integrated Medical, PL, d/b/a Florida Medical Research

Gainesville, Florida, United States

Site Status

Indago Research and Health Center

Hialeah, Florida, United States

Site Status

Homestead Associates in Research

Homestead, Florida, United States

Site Status

Pharmax Research Clinic

Miami, Florida, United States

Site Status

Suncoast Research Group, LLC

Miami, Florida, United States

Site Status

San Marcus Research Clinic

Miami Lakes, Florida, United States

Site Status

Suncoast Clinical Research

New Port Richey, Florida, United States

Site Status

Omega Research Consultants-DeBary

Orlando, Florida, United States

Site Status

Millennium Research

Ormond Beach, Florida, United States

Site Status

Clinical Research of West Florida

Tampa, Florida, United States

Site Status

Arthritis & Rheumatology of Georgia, PC

Atlanta, Georgia, United States

Site Status

Arthritis Research and Treatment Center

Stockbridge, Georgia, United States

Site Status

Arthritis and Diabetes Clinic, Inc.

Monroe, Louisiana, United States

Site Status

June DO, PC

Lansing, Michigan, United States

Site Status

Physician Research Collaboration, LLC

Lincoln, Nebraska, United States

Site Status

DJL Clinical Research

Charlotte, North Carolina, United States

Site Status

Columbia Arthritis Center

Columbia, South Carolina, United States

Site Status

West Tennessee Research Institute

Jackson, Tennessee, United States

Site Status

Ramesh C. Gupta, MD

Memphis, Tennessee, United States

Site Status

Northwest Med Care

Cypress, Texas, United States

Site Status

Rheumatic Disease Clinical Research Center

Houston, Texas, United States

Site Status

Accurate Clinical Research

Houston, Texas, United States

Site Status

Laila Hassan, MD, PA

Houston, Texas, United States

Site Status

Pioneer Research Solutions

Houston, Texas, United States

Site Status

Southwest Rheumatology Research

Mesquite, Texas, United States

Site Status

Sun Research Institute

San Antonio, Texas, United States

Site Status

Aprillus Asistencia e Investigación

Ciudad Autónoma de Buenos Aires, Buenos Aires, Argentina

Site Status

DIM Clínica Privada

Ramos Mejía, Buenos Aires, Argentina

Site Status

Centro de Investigaciones Reumatológicas

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status

Centro Polivalente de Asistencia e Investigación Clínica CER San Juan

San Juan, , Argentina

Site Status

Centro de Investigacion del Noroeste, S.C.

Tijuana, Estado de Baja California, Mexico

Site Status

Antiguo Hospital Civil de Guadalajara Fray Antonio Alcalde

Guadalajara, Jalisco, Mexico

Site Status

Clinica de Investigacion en Reumatologia y Obesidad

Guadalajara, Jalisco, Mexico

Site Status

Investigacion Biomedica para el Desarrollo de Farmacos S.A. de C.V.

Zapopan, Jalisco, Mexico

Site Status

Hospital De Jesus

Mexico City, Mexico City, Mexico

Site Status

Consultorio de Reumatología

Mexico City, Mexico City, Mexico

Site Status

Consultorio Privado del Dr. Miguel Cortes Hernandez

Cuernavaca, Morelos, Mexico

Site Status

Hospital Universitario Dr. José Eleuterio Gonzalez

Monterrey, Nuevo León, Mexico

Site Status

Centro de Estudios Clínicos y Especialidades Médicas

Monterrey, Nuevo León, Mexico

Site Status

Centro de Alta Especialidad en Reumatologia e Investigación del Potosí

San Luis Potosí City, San Luís Potosí, Mexico

Site Status

Centro Especializado en Investigación Clínica

Boca del Río, Veracruz, Mexico

Site Status

Centro Peninsular de Investigacion Clinica S.C.P.

Mérida, Yucatán, Mexico

Site Status

Instituto de Investigaciones Aplicadas a la Neurociencia A.C.

Durango, , Mexico

Site Status

Phylasis Clinicas Research S de RL de CV

Estado de México, , Mexico

Site Status

SMIQ

Querétaro, , Mexico

Site Status

Centro de Atención e Investigación Cardiovascular del Potosí, S.C.

San Luis Potosí City, , Mexico

Site Status

INBIOMEDYC Toluca

Toluca, , Mexico

Site Status

Unidad de Enfermedades Reumaticas y Cronico Degenerativas

Torreón, , Mexico

Site Status

Clinica Santa Monica

Lima, , Peru

Site Status

Hospital Nacional Cayetano Heredia

Lima, , Peru

Site Status

ABK Reuma S.R.L. - Medicentro Biociencias

Pueblo Libre, , Peru

Site Status

Clinica Vesalio

San Borja, , Peru

Site Status

Hospital de Apoyo Maria Auxiliadora

San Juán de Miraflores, , Peru

Site Status

Clínica Médica Cayetano Heredia

San Martín de Porres, , Peru

Site Status

Mindful Medical Research

San Juan, , Puerto Rico

Site Status

Countries

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United States Argentina Mexico Peru Puerto Rico

References

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Fleischmann R, Furst DE. Safety of repository corticotropin injection as an adjunctive therapy for the treatment of rheumatoid arthritis. Expert Opin Drug Saf. 2020 Aug;19(8):935-944. doi: 10.1080/14740338.2020.1779219. Epub 2020 Jun 16.

Reference Type DERIVED
PMID: 32497440 (View on PubMed)

Fleischmann R, Furst DE, Connolly-Strong E, Liu J, Zhu J, Brasington R. Repository Corticotropin Injection for Active Rheumatoid Arthritis Despite Aggressive Treatment: A Randomized Controlled Withdrawal Trial. Rheumatol Ther. 2020 Jun;7(2):327-344. doi: 10.1007/s40744-020-00199-3. Epub 2020 Mar 17.

Reference Type DERIVED
PMID: 32185745 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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MNK14294063

Identifier Type: -

Identifier Source: org_study_id

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