A Study Comparing 2 Doses Of CP-690,550 Vs. Placebo For The Treatment Of Rheumatoid Arthritis In Patients On Other Background Arthritis Medications

NCT ID: NCT00856544

Last Updated: 2013-01-10

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

795 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-05-31

Study Completion Date

2011-01-31

Brief Summary

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This Phase 3 study is intended to provide evidence that CP-690,550 dosed 5 mg BID and 10 mg BID is safe and effective when used in combination with a variety of traditional disease modifying antirheumatic drugs in adult patients with rheumatoid arthritis. It is intended to confirm the benefits of CP-690,550 in improving signs and symptoms and physical function that were observed in the Phase 2 rheumatoid arthritis studies.

Detailed Description

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Conditions

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Arthritis, Rheumatoid

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Active 5 mg

Group Type EXPERIMENTAL

CP-690,550

Intervention Type DRUG

Film coated tablet, 5 mg PO BID, 1 year

Active 10 mg

Group Type EXPERIMENTAL

CP-690,550

Intervention Type DRUG

Film coated tablet, 10 mg PO BID, 1 year

Placebo Sequence 1

Placebo non-responders advance to 5 mg CP-690,550 at Month 3 visit. All patients in this treatment arm advance to 5 mg CP-690,550 at Month 6 visit.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Film coated tablet, 1 tablet PO BID, 3-6 months

Placebo Sequence 2

Placebo non-responders advance to 10 mg CP-690,550 at Month 3 visit. All patients in this treatment arm advance to 10 mg CP-690,550 at Month 6 visit.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Film coated tablet, 1 tablet PO BID, 3-6 months

Interventions

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CP-690,550

Film coated tablet, 5 mg PO BID, 1 year

Intervention Type DRUG

CP-690,550

Film coated tablet, 10 mg PO BID, 1 year

Intervention Type DRUG

Placebo

Film coated tablet, 1 tablet PO BID, 3-6 months

Intervention Type DRUG

Placebo

Film coated tablet, 1 tablet PO BID, 3-6 months

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* The patient has a diagnosis of Rheumatoid Arthritis based on the American College of Rheumatology (ACR) 1987 Revised Criteria.
* The patient has active disease as defined by both \>=4 tender or painful joints on motion and \>= 4 joints swollen; and either an erythrocyte sedimentation rate (ESR) \> 28 mm or a C-reactive protein (CRP) concentration \> 7 mg/dL.
* Patient had an inadequate response to at least one disease modifying antirheumatic drug (traditional or biologic) due to lack of efficacy or toxicity.
* Patient must remain on at least one background traditional disease modifying antirheumatic drug.
* No evidence of inadequately treated latent or active infection with Mycobacterium tuberculosis.

Exclusion Criteria

* Blood dyscrasias including confirmed: Hemoglobin \<9 g/dL or Hematocrit \<30%; White blood cell count \<3.0 x 109/L; Absolute neutrophil count \<1.2 x 109/L; Platelet count \<100 x 109/L.
* History of any other rheumatic autoimmune disease other than Sjogren's syndrome.
* No malignancy or history of malignancy.
* History of infection requiring hospitalization, parenteral antimicrobial therapy, or as otherwise judged clinically significant by the investigator, within the 6 months prior to the first dose of study drug.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Pfizer Investigational Site

Huntsville, Alabama, United States

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Jonesboro, Arkansas, United States

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Palo Alto, California, United States

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Stanford, California, United States

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Boulder, Colorado, United States

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Denver, Colorado, United States

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Danbury, Connecticut, United States

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Hamden, Connecticut, United States

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Trumbull, Connecticut, United States

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New Port Richey, Florida, United States

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Ocala, Florida, United States

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Plantation, Florida, United States

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Port Richey, Florida, United States

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Tamarac, Florida, United States

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Tampa, Florida, United States

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Decatur, Georgia, United States

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Marietta, Georgia, United States

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Maywood, Illinois, United States

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Oakbrook Terrace, Illinois, United States

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Rockford, Illinois, United States

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Springfield, Illinois, United States

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Springfield, Illinois, United States

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Vernon Hills, Illinois, United States

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Evansville, Indiana, United States

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Indianapolis, Indiana, United States

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Wichita, Kansas, United States

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Lexington, Kentucky, United States

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Leominster, Massachusetts, United States

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Worcester, Massachusetts, United States

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Edina, Minnesota, United States

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Lincoln, Nebraska, United States

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Albany, New York, United States

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Orchard Park, New York, United States

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Rochester, New York, United States

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Asheville, North Carolina, United States

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Charlotte, North Carolina, United States

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Bethlehem, Pennsylvania, United States

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Wyomissing, Pennsylvania, United States

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Greenville, South Carolina, United States

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Knoxville, Tennessee, United States

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Austin, Texas, United States

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Dallas, Texas, United States

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Seattle, Washington, United States

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Tacoma, Washington, United States

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Tacoma, Washington, United States

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Clarksburg, West Virginia, United States

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Campsie, New South Wales, Australia

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Cairns, Queensland, Australia

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Maroochydore, Queensland, Australia

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Woodville, South Australia, Australia

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Malvern East, Victoria, Australia

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Shenton Park, Western Australia, Australia

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Viña del Mar, Región de Valparaíso, Chile

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Santiago, RM, Chile

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Santiago, RM, Chile

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Providencia, Santiago, RM, Chile

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Viña del Mar, , Chile

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Hefei, Anhui, China

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Hefei, Anhui, China

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Guangzhou, Guangdong, China

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Guangzhou, Guangdong, China

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Wuhan, Hubei, China

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Changsha, Hunan, China

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Nanjing, Jiangsu, China

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Suzhou, Jiangsu, China

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Jinan, Shandong, China

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Qingdao, Shandong, China

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Xi’an, Shanxi, China

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Chengdu, Sichuan, China

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Hangzhou, Zhejiang, China

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Beijing, , China

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Beijing, , China

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Beijing, , China

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Shanghai, , China

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Shanghai, , China

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Shanghai, , China

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Tianjin, , China

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Barranquilla, Atlántico, Colombia

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Bogota, Cundinamarca, Colombia

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Bucaramanga, Santander Department, Colombia

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Opatija, , Croatia

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Zagreb, , Croatia

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Frederiksberg, , Denmark

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Helsinki, , Finland

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Hyvinkää, , Finland

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Tampere, , Finland

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Berlin, , Germany

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Dresden, , Germany

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Hamburg, , Germany

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Leipzig, , Germany

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Nuremberg, , Germany

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Rheine, , Germany

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Maroussi Athens, , Greece

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Putrajaya, Kuala Lumpur, Malaysia

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Seremban, Negeri Sembilan, Malaysia

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Batu Caves, Selangor, Malaysia

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Subang Jaya, Selangor, Malaysia

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Torreón, Coahuila, Mexico

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Morelia, Michoacán, Mexico

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Cuernavaca, Morelos, Mexico

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México, Querétaro, Mexico

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Mérida, Yucatán, Mexico

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Bialystok, , Poland

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Bialystok, , Poland

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Kościan, , Poland

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Poznan, , Poland

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Torun, , Poland

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Moscow, , Russia

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Moscow, , Russia

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Petrozavodsk, , Russia

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Nové Zámky, , Slovakia

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Poprad, , Slovakia

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Považská Bystrica, , Slovakia

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Rimavská Sobota, , Slovakia

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Senica, , Slovakia

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Žilina, , Slovakia

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A Coruña, A Coruña, Spain

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Santiago de Compostela, A Coruña, Spain

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Madrid, Madrid, Spain

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Málaga, Malaga, Spain

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Seville, Sevilla, Spain

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Falun, , Sweden

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Gothenburg, , Sweden

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Uppsala, , Sweden

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Rajathevee, Bangkok, Thailand

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Amphoe Muang, Chiang Mai, Thailand

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Muang District, Khonkaen, Thailand

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Metropolitan Borough of Wirral, Merseyside, United Kingdom

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Cannock, Staffs, United Kingdom

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Solihull, West Midlands, United Kingdom

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Newcastle upon Tyne, , United Kingdom

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Caracas, DC/ Municipio Libertados, Venezuela

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Caracas, Distrito Federal, Venezuela

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Countries

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United States Australia Chile China Colombia Croatia Denmark Finland Germany Greece Malaysia Mexico Poland Russia Slovakia Spain Sweden Thailand United Kingdom Venezuela

References

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Curtis JR, Yamaoka K, Chen YH, Bhatt DL, Gunay LM, Sugiyama N, Connell CA, Wang C, Wu J, Menon S, Vranic I, Gomez-Reino JJ. Malignancy risk with tofacitinib versus TNF inhibitors in rheumatoid arthritis: results from the open-label, randomised controlled ORAL Surveillance trial. Ann Rheum Dis. 2023 Mar;82(3):331-343. doi: 10.1136/ard-2022-222543. Epub 2022 Dec 5.

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Winthrop KL, Yndestad A, Henrohn D, Danese S, Marsal S, Galindo M, Woolcott JC, Jo H, Kwok K, Shapiro AB, Jones TV, Diehl A, Su C, Panes J, Cohen SB. Influenza Adverse Events in Patients with Rheumatoid Arthritis, Ulcerative Colitis, or Psoriatic Arthritis in the Tofacitinib Clinical Development Programs. Rheumatol Ther. 2023 Apr;10(2):357-373. doi: 10.1007/s40744-022-00507-z. Epub 2022 Dec 17.

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Dikranian AH, Gonzalez-Gay MA, Wellborne F, Alvaro-Gracia JM, Takiya L, Stockert L, Paulissen J, Shi H, Tatulych S, Curtis JR. Efficacy of tofacitinib in patients with rheumatoid arthritis stratified by baseline body mass index: an analysis of pooled data from phase 3 studies. RMD Open. 2022 May;8(1):e002103. doi: 10.1136/rmdopen-2021-002103.

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Bartlett SJ, Bingham CO, van Vollenhoven R, Murray C, Gruben D, Gold DA, Cella D. The impact of tofacitinib on fatigue, sleep, and health-related quality of life in patients with rheumatoid arthritis: a post hoc analysis of data from Phase 3 trials. Arthritis Res Ther. 2022 Apr 5;24(1):83. doi: 10.1186/s13075-022-02724-x.

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Charles-Schoeman C, Burmester G, Nash P, Zerbini CA, Soma K, Kwok K, Hendrikx T, Bananis E, Fleischmann R. Efficacy and safety of tofacitinib following inadequate response to conventional synthetic or biological disease-modifying antirheumatic drugs. Ann Rheum Dis. 2016 Jul;75(7):1293-301. doi: 10.1136/annrheumdis-2014-207178. Epub 2015 Aug 14.

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Cohen S, Radominski SC, Gomez-Reino JJ, Wang L, Krishnaswami S, Wood SP, Soma K, Nduaka CI, Kwok K, Valdez H, Benda B, Riese R. Analysis of infections and all-cause mortality in phase II, phase III, and long-term extension studies of tofacitinib in patients with rheumatoid arthritis. Arthritis Rheumatol. 2014 Nov;66(11):2924-37. doi: 10.1002/art.38779.

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Kremer J, Li ZG, Hall S, Fleischmann R, Genovese M, Martin-Mola E, Isaacs JD, Gruben D, Wallenstein G, Krishnaswami S, Zwillich SH, Koncz T, Riese R, Bradley J. Tofacitinib in combination with nonbiologic disease-modifying antirheumatic drugs in patients with active rheumatoid arthritis: a randomized trial. Ann Intern Med. 2013 Aug 20;159(4):253-61. doi: 10.7326/0003-4819-159-4-201308200-00006.

Reference Type DERIVED
PMID: 24026258 (View on PubMed)

Related Links

Other Identifiers

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A3921046

Identifier Type: -

Identifier Source: org_study_id

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