A Study of Intravenous or Subcutaneous Methoxy Polyethylene Glycol-Epoetin Beta (RO0503821, Mircera) in Chronic Kidney Disease Patients With Renal Anemia

NCT ID: NCT00090753

Last Updated: 2012-02-14

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1228 participants

Study Classification

INTERVENTIONAL

Study Start Date

2004-10-31

Study Completion Date

2009-12-31

Brief Summary

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This study assessed the long-term efficacy, safety, and tolerability of intravenous (iv) or subcutaneous (sc) methoxy polyethylene glycol-epoetin beta in chronic kidney disease patients with renal anemia. Eligible patients were those who were receiving stable maintenance therapy with methoxy polyethylene glycol-epoetin beta or erythropoiesis stimulating agents (ESAs) in Phase II or III clinical studies. They continued to receive methoxy polyethylene glycol-epoetin beta or comparator ESAs at the same weekly dose and by the same route of administration (sc or iv) as in the qualifying studies.

Detailed Description

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Conditions

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Anemia

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Methoxy Polyethylene Glycol-Epoetin Beta

Patients received the same weekly dose of methoxy polyethylene glycol-epoetin beta via the same route of administration (iv or sc) as they received in the Phase II or Phase III study that qualified the patient for participation in this study. Methoxy polyethylene glycol-epoetin beta was administered every 2 or every 4 weeks in the initial 104-week treatment period. Patients on a 4-week dosing interval were switched to once-monthly administration in the 24-month extension phase. The dose of methoxy polyethylene glycol-epoetin beta was adjusted to maintain the patient's hemoglobin (Hb) within a target range of 11 to 13 g/dL.

Group Type EXPERIMENTAL

Methoxy Polyethylene Glycol-Epoetin Beta

Intervention Type DRUG

Methoxy polyethylene glycol-epoetin beta was provided as a sterile single-use injectable solution in 2-mL glass vials containing 1 mL solution or in single-use sterile pre-filled syringes (PFSs) containing 0.3 mL or 0.6 mL injectable solution. The injectable solution was available in vials with the following strengths: 50, 100, 200, 400, and 1000 μg/mL. The injectable solution was available in PFSs with the following strengths: 30, 40, 50, 60, 75, 100, 120, 150, 200, and 250 μg/0.3 mL; and 360 and 400 μg/0.6 mL.

Comparator ESA

Patients received the same comparator ESA \[epoetin alfa, epoetin beta, or darbepoetin alfa\] at the same weekly dose and dosing interval via the same route of administration (iv or sc) as they received in the Phase III study that qualified the patient for participation in this study. The dose of the comparator drug was adjusted to maintain the patient's Hb within a target range of 11 to 13 g/dL. Of the 480 patients in the comparator drug group, 170 received darbepoetin alfa, 134 received epoetin alfa, and 176 received epoetin beta.

Group Type ACTIVE_COMPARATOR

Epoetin alfa

Intervention Type DRUG

Epoetin alfa was provided with commercial packaging in English with country-specific labels (10,000 IU, 20,000 IU).

Epoetin beta

Intervention Type DRUG

Epoetin beta was provided with commercial packaging in English with country-specific labels (50,000 IU, 100,000 IU).

Darbepoetin alfa

Intervention Type DRUG

Darbepoetin alfa was provided with commercial packaging in English with country-specific labels (vials and PFSs in various strengths).

Interventions

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Methoxy Polyethylene Glycol-Epoetin Beta

Methoxy polyethylene glycol-epoetin beta was provided as a sterile single-use injectable solution in 2-mL glass vials containing 1 mL solution or in single-use sterile pre-filled syringes (PFSs) containing 0.3 mL or 0.6 mL injectable solution. The injectable solution was available in vials with the following strengths: 50, 100, 200, 400, and 1000 μg/mL. The injectable solution was available in PFSs with the following strengths: 30, 40, 50, 60, 75, 100, 120, 150, 200, and 250 μg/0.3 mL; and 360 and 400 μg/0.6 mL.

Intervention Type DRUG

Epoetin alfa

Epoetin alfa was provided with commercial packaging in English with country-specific labels (10,000 IU, 20,000 IU).

Intervention Type DRUG

Epoetin beta

Epoetin beta was provided with commercial packaging in English with country-specific labels (50,000 IU, 100,000 IU).

Intervention Type DRUG

Darbepoetin alfa

Darbepoetin alfa was provided with commercial packaging in English with country-specific labels (vials and PFSs in various strengths).

Intervention Type DRUG

Other Intervention Names

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RO0503821 Mircera

Eligibility Criteria

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Inclusion Criteria

* Written informed consent
* Adult patients (≥ 18 years old) with chronic renal anemia
* Maintenance erythropoietic therapy with methoxy polyethylene glycol-epoetin beta or a protocol-specified reference medication (epoetin alfa formulated with human albumin, epoetin beta or darbepoetin alfa) in one of the following studies: BA16528\[NCT00048048\], BA16285\[NCT00048035\], BA16286\[NCT00364832\], BA16736\[NCT00077597\], BA16738\[NCT00081471\], BA16739\[NCT00077610\], BA16740\[NCT00077623\], BA17283\[NCT00077766\] and BA17284\[NCT00081484\]
* Hemoglobin (Hb) concentration between 10.5 and 13.0 g/dL
* Adequate iron status defined as serum ferritin ≥ 100 ng/mL or Transferrin Saturation (TSAT)≥ 20% or percentage of hypochromic red blood cells (RBCs) \< 10%

Exclusion Criteria

* Poorly controlled hypertension
* History of epileptic seizure
* Pure red cell aplasia
* Chronic congestive heart failure \[New York Heart Association (NYHA) IV\]
* High likelihood of early withdrawal or interruption of the study
* Active malignant disease (except non-melanoma skin cancer)
* Life expectancy less than 12 months
* Pregnancy or breast-feeding
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Palma de Mallorca, , Spain

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Salamanca, , Spain

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Santander, , Spain

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Santiago de Compostela, , Spain

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Seville, , Spain

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Huddinge, , Sweden

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Karlstad, , Sweden

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Stockholm, , Sweden

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Umeå, , Sweden

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Aarau, , Switzerland

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Lausanne, , Switzerland

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Birmingham, Alabama, United States

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Mobile, Alabama, United States

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Montgomery, Alabama, United States

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Hot Springs, Arkansas, United States

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Covina, California, United States

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Encino, California, United States

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Irvine, California, United States

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Los Alamitos, California, United States

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Los Angeles, California, United States

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Los Angeles, California, United States

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Monterey Park, California, United States

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Mountain View, California, United States

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Sacramento, California, United States

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San Diego, California, United States

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San Diego, California, United States

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San Francisco, California, United States

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Stanford, California, United States

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Colorado Springs, Colorado, United States

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Denver, Colorado, United States

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Lakewood, Colorado, United States

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Stamford, Connecticut, United States

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Ocala, Florida, United States

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Pembroke Pines, Florida, United States

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Atlanta, Georgia, United States

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Augusta, Georgia, United States

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Honolulu, Hawaii, United States

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Maywood, Illinois, United States

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South Holland, Illinois, United States

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Louisville, Kentucky, United States

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Baton Rouge, Louisiana, United States

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Shreveport, Louisiana, United States

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Boston, Massachusetts, United States

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Boston, Massachusetts, United States

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Springfield, Massachusetts, United States

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Detroit, Michigan, United States

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Detroit, Michigan, United States

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Kalamazoo, Michigan, United States

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Brooklyn Center, Minnesota, United States

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Columbus, Mississippi, United States

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Tupelo, Mississippi, United States

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St Louis, Missouri, United States

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Hackensack, New Jersey, United States

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Paterson, New Jersey, United States

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Albuquerque, New Mexico, United States

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Brooklyn, New York, United States

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Flushing, New York, United States

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Great Neck, New York, United States

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Mineola, New York, United States

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New York, New York, United States

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New York, New York, United States

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Orchard Park, New York, United States

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The Bronx, New York, United States

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Chapel Hill, North Carolina, United States

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Mount Airy, North Carolina, United States

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Raleigh, North Carolina, United States

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Cincinnati, Ohio, United States

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Cleveland, Ohio, United States

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Toledo, Ohio, United States

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Oregon City, Oregon, United States

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Portland, Oregon, United States

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Portland, Oregon, United States

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Allentown, Pennsylvania, United States

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Erie, Pennsylvania, United States

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Lewistown, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Columbia, South Carolina, United States

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Orangeburg, South Carolina, United States

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Chattanooga, Tennessee, United States

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Nashville, Tennessee, United States

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Nashville, Tennessee, United States

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Austin, Texas, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Burlington, Vermont, United States

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Fairfax, Virginia, United States

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Norfolk, Virginia, United States

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Salem, Virginia, United States

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Morgantown, West Virginia, United States

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Clayton, , Australia

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Gosford, , Australia

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Liverpool, , Australia

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Parkville, , Australia

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Perth, , Australia

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Sydney, , Australia

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Woolloongabba, , Australia

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Graz, , Austria

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Aalst, , Belgium

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Brussels, , Belgium

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Edegem, , Belgium

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Ghent, , Belgium

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Hasselt, , Belgium

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Leuven, , Belgium

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Liège, , Belgium

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Liberec, , Czechia

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Ostrava, , Czechia

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Pilsen, , Czechia

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Aalborg, , Denmark

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Odense, , Denmark

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Roskilde, , Denmark

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HUS, , Finland

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Tampere, , Finland

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Bayonne, , France

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Bois-Guillaume, , France

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Bordeaux, , France

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Boulogne, , France

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Cabestany, , France

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Caen, , France

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Chambéry, , France

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Colmar, , France

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Hyères, , France

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La Tronche, , France

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Limoges, , France

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Lyon, , France

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Montpellier, , France

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Nantes, , France

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Nîmes, , France

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Paris, , France

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Perpignan, , France

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Poitiers, , France

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Saint-Germain-en-Laye, , France

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Saint-Ouen, , France

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Salouël, , France

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Tarbes, , France

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Thionville, , France

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Toulouse, , France

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Tours, , France

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Bad Hersfeld, , Germany

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Berlin, , Germany

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Dortmund, , Germany

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Erlangen, , Germany

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München, , Germany

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Nuremberg, , Germany

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Stuttgart, , Germany

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Villingen-Schwenningen, , Germany

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Wiesbaden, , Germany

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Wiesloch, , Germany

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Wuppertal, , Germany

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Alexandroupoli, , Greece

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Ioannina, , Greece

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Larissa, , Greece

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Piraeus, , Greece

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Thessaloniki, , Greece

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Budapest, , Hungary

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Budapest, , Hungary

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Debrecen, , Hungary

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Miskolc, , Hungary

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Pécs, , Hungary

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Bergamo, , Italy

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Cagliari, , Italy

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Cremona, , Italy

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Cuneo, , Italy

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Genova, , Italy

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Lecco, , Italy

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Livorno, , Italy

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Lodi, , Italy

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Messina, , Italy

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Mestre, , Italy

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Modena, , Italy

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Pavia, , Italy

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Prato, , Italy

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Reggio Calabria, , Italy

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S Fermo Della Battaglia, , Italy

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Venezia, , Italy

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Cuernavaca, , Mexico

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Mexico City, , Mexico

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Heerlen, , Netherlands

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Trondheim, , Norway

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Panama City, , Panama

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Gdansk, , Poland

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Gdynia, , Poland

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Kielce, , Poland

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Krakow, , Poland

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Lodz, , Poland

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Poznan, , Poland

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Rzeszów, , Poland

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Szczecin, , Poland

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Warsaw, , Poland

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Wołomin, , Poland

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Wroclaw, , Poland

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Setúbal, , Portugal

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Ponce, , Puerto Rico

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Moscow, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Cape Town, , South Africa

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Durban, , South Africa

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Soweto, , South Africa

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A Coruña, , Spain

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Alcorcón, , Spain

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Alicante, , Spain

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Almería, , Spain

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Badalona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Bilbao, , Spain

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Córdoba, , Spain

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L'Hospitalet de Llobregat, , Spain

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Lleida, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Málaga, , Spain

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Oviedo, , Spain

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Palma de Mallorca, , Spain

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Lausanne, , Switzerland

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Taichung, , Taiwan

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Taipei, , Taiwan

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Bangkok, , Thailand

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Bangkok, , Thailand

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Bangkok, , Thailand

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Bangkok, , Thailand

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Chiang Mai, , Thailand

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Chon Buri, , Thailand

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Phitsanulok, , Thailand

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Belfast, , United Kingdom

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Cambridge, , United Kingdom

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Carshalton, , United Kingdom

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Dundee, , United Kingdom

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Exeter, , United Kingdom

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Glasgow, , United Kingdom

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Leicester, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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Salford, , United Kingdom

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Swansea, , United Kingdom

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Countries

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United States Australia Austria Belgium Czechia Denmark Finland France Germany Greece Hungary Italy Mexico Netherlands Norway Panama Poland Portugal Puerto Rico Russia South Africa Spain Sweden Switzerland Taiwan Thailand United Kingdom

Other Identifiers

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BH18387

Identifier Type: -

Identifier Source: org_study_id

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