A Study to Investigate the Efficacy, Safety and Tolerability of Remibrutinib Versus Placebo in Adult Patients With Generalized Myasthenia Gravis

NCT ID: NCT06744920

Last Updated: 2026-01-27

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

180 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-02-07

Study Completion Date

2033-02-26

Brief Summary

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A study to evaluate the efficacy, safety and tolerability of Remibrutinib versus placebo in adult patients with Generalized Myasthenia Gravis who are on stable, standard-of-care (SOC) treatment.

Detailed Description

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This study is a randomized, double-blind, placebo-controlled, multicenter, Phase III study, to evaluate the efficacy, safety and tolerability of remibrutinib in gMG patients who are on stable SOC treatment. Approximately 180 eligible participants will be randomized in a ratio of 1:1, to receive either remibrutinib or matching placebo.

The study consists of a Core Part (6-months double-blind treatment) and an Extension Part (up to 60-month open-label treatment).

Conditions

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Generalized Myasthenia Gravis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Remibrutinib arm

Core Part: Remibrutinib tablet taken orally

\[Extension Part: Open-label remibrutinib tablet taken orally\]

Group Type EXPERIMENTAL

Remibrutinib (Blinded)

Intervention Type DRUG

Remibrutinib (Blinded) active treatment

Remibrutinib (Open Label)

Intervention Type DRUG

Remibrutinib (Open Label) active treatment

Placebo arm

Core Part: Placebo tablet taken orally

\[Extension Part: Open-label remibrutinib tablet taken orally\]

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Placebo

Remibrutinib (Open Label)

Intervention Type DRUG

Remibrutinib (Open Label) active treatment

Interventions

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Remibrutinib (Blinded)

Remibrutinib (Blinded) active treatment

Intervention Type DRUG

Placebo

Placebo

Intervention Type OTHER

Remibrutinib (Open Label)

Remibrutinib (Open Label) active treatment

Intervention Type DRUG

Other Intervention Names

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LOU64 LOU064

Eligibility Criteria

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Inclusion Criteria

* Adult patients with gMG (age 18-75 years)
* Confirmed diagnosis of Myasthenia Gravis Foundation of America (MGFA) Class II-IV gMG at screening and likely not in need of a respirator for the duration of the study, as judged by the Investigator
* Documented evidence of positive serologic testing for AChR+ antibody or MuSK+ antibody at screening, OR seronegative for both AChR and MuSK antibodies at screening
* Baseline MG-ADL score ≥ 6 with ≥ 50% of the total score due to non ocular symptoms
* Participants who have been on a stable dose of standard-of-care treatment as specified in the protocol
* Able to safely swallow the study medication according to investigator clinical judgement based on a bedside swallowing test or another formal swallowing test in line with local practice, both at Screening and Baseline

Exclusion Criteria

* Prior to baseline have been treated with intravenous immunoglobulins or plasma exchange (IVIg/PLEX) in the past month, with rituximab in the past 6 months, eculizumab in the past 2 months, ravulizumab or other complement inhibitors in the past 3 months, efgartigimod or other anti-FcRn therapies in the past 3 months, or had a thymectomy in the past 6 months or a planned thymectomy during the trial period
* Women of child-bearing potential, defined as all women physiologically capable of becoming pregnant, unless they are using highly effective methods of contraception during dosing and for 1 week after stopping of study treatment
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Neuromuscular Research Center

Phoenix, Arizona, United States

Site Status RECRUITING

Honor Health Research Institute

Scottsdale, Arizona, United States

Site Status RECRUITING

Fullerton Neuro and Headache Ctr

Fullerton, California, United States

Site Status RECRUITING

University Of Southern California

Los Angeles, California, United States

Site Status RECRUITING

Univ Cali Irvine ALS Neuromuscular

Orange, California, United States

Site Status RECRUITING

SFM Clinical Research LLC

Boca Raton, Florida, United States

Site Status RECRUITING

Homestead Assoc In Research Inc

Homestead, Florida, United States

Site Status RECRUITING

AdventHealth

Orlando, Florida, United States

Site Status RECRUITING

Neurological Services of Orlando PA

Orlando, Florida, United States

Site Status RECRUITING

Mid Atlantic Epilepsy and Sleep Ctr

Bethesda, Maryland, United States

Site Status RECRUITING

Michigan State University-Department of Neurology

East Lansing, Michigan, United States

Site Status RECRUITING

Dent Neurological Institute

Buffalo, New York, United States

Site Status RECRUITING

Univ of Cincinnati Medical Center

Cincinnati, Ohio, United States

Site Status RECRUITING

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

Houston Methodist Hospital

Houston, Texas, United States

Site Status RECRUITING

UT Health Science Center

Houston, Texas, United States

Site Status RECRUITING

University of WA Division of Cardio

Seattle, Washington, United States

Site Status RECRUITING

Center for Neurological Disorders G

Greenfield, Wisconsin, United States

Site Status RECRUITING

Novartis Investigative Site

Rosario, Santa Fe Province, Argentina

Site Status RECRUITING

Novartis Investigative Site

Kogarah, New South Wales, Australia

Site Status RECRUITING

Novartis Investigative Site

Fitzroy, Victoria, Australia

Site Status RECRUITING

Novartis Investigative Site

Southport, , Australia

Site Status RECRUITING

Novartis Investigative Site

Leuven, Vlaams Brabant, Belgium

Site Status RECRUITING

Novartis Investigative Site

London, Ontario, Canada

Site Status RECRUITING

Novartis Investigative Site

Ottawa, Ontario, Canada

Site Status RECRUITING

Novartis Investigative Site

Guangzhou, Guangdong, China

Site Status RECRUITING

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Shijiazhuang, Hebei, China

Site Status RECRUITING

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Wuhan, Hubei, China

Site Status RECRUITING

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Wuxi, Jiangsu, China

Site Status RECRUITING

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Changchun, Jilin, China

Site Status RECRUITING

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Shanghai, , China

Site Status RECRUITING

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Shanghai, , China

Site Status RECRUITING

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Bordeaux, , France

Site Status RECRUITING

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Nice, , France

Site Status RECRUITING

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Paris, , France

Site Status RECRUITING

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Toulouse, , France

Site Status RECRUITING

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Kutaisi, , Georgia

Site Status RECRUITING

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Tbilisi, , Georgia

Site Status RECRUITING

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Tbilisi, , Georgia

Site Status RECRUITING

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Mangalore, Karnataka, India

Site Status RECRUITING

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Nashik, Maharashtra, India

Site Status RECRUITING

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New Delhi, National Capital Territory of Delhi, India

Site Status RECRUITING

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Ludhiana, Punjab, India

Site Status RECRUITING

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Vellore, Tamil Nadu, India

Site Status RECRUITING

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Hyderabad, Telangana, India

Site Status RECRUITING

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Bergamo, BG, Italy

Site Status RECRUITING

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Sapporo, Hokkaido, Japan

Site Status RECRUITING

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Sapporo, Hokkaido, Japan

Site Status RECRUITING

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Nishinomiya, Hyōgo, Japan

Site Status RECRUITING

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Hanamaki, Iwate, Japan

Site Status RECRUITING

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Sendai, Miyagi, Japan

Site Status RECRUITING

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Suita, Osaka, Japan

Site Status RECRUITING

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Higashi-Matsuyama, Saitama, Japan

Site Status RECRUITING

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Koshigaya, Saitama, Japan

Site Status RECRUITING

Novartis Investigative Site

Shinjuku Ku, Tokyo, Japan

Site Status RECRUITING

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Chiba, , Japan

Site Status RECRUITING

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Fukushima, , Japan

Site Status RECRUITING

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Hiroshima, , Japan

Site Status RECRUITING

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Lublin, Lublin Voivodeship, Poland

Site Status RECRUITING

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Lublin, Lublin Voivodeship, Poland

Site Status RECRUITING

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Krakow, POL, Poland

Site Status RECRUITING

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Bydgoszcz, Woj Kujawsko Pomorskie, Poland

Site Status RECRUITING

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Bydgoszcz, , Poland

Site Status RECRUITING

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Katowice, , Poland

Site Status RECRUITING

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Lodz, , Poland

Site Status RECRUITING

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Lublin, , Poland

Site Status RECRUITING

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Lublin, , Poland

Site Status RECRUITING

Novartis Investigative Site

Poznan, , Poland

Site Status RECRUITING

Novartis Investigative Site

Skorzewo, , Poland

Site Status RECRUITING

Novartis Investigative Site

Warsaw, , Poland

Site Status RECRUITING

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Warsaw, , Poland

Site Status RECRUITING

Novartis Investigative Site

Brasov, , Romania

Site Status RECRUITING

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Bucharest, , Romania

Site Status RECRUITING

Novartis Investigative Site

Sibiu, , Romania

Site Status RECRUITING

Novartis Investigative Site

Seoul, Korea, South Korea

Site Status RECRUITING

Novartis Investigative Site

Busan, , South Korea

Site Status RECRUITING

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Seoul, , South Korea

Site Status RECRUITING

Novartis Investigative Site

Seoul, , South Korea

Site Status RECRUITING

Novartis Investigative Site

L'Hospitalet de Llobregat, Barcelona, Spain

Site Status RECRUITING

Novartis Investigative Site

Lleida, , Spain

Site Status RECRUITING

Novartis Investigative Site

Madrid, , Spain

Site Status RECRUITING

Novartis Investigative Site

Málaga, , Spain

Site Status RECRUITING

Novartis Investigative Site

Valencia, , Spain

Site Status RECRUITING

Novartis Investigative Site

Kaohsiung City, , Taiwan

Site Status RECRUITING

Novartis Investigative Site

Tainan, , Taiwan

Site Status RECRUITING

Novartis Investigative Site

Taipei, , Taiwan

Site Status RECRUITING

Novartis Investigative Site

Taipei, , Taiwan

Site Status RECRUITING

Novartis Investigative Site

Taoyuan District, , Taiwan

Site Status RECRUITING

Countries

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United States Argentina Australia Belgium Canada China France Georgia India Italy Japan Poland Romania South Korea Spain Taiwan

Central Contacts

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Novartis Pharmaceuticals

Role: CONTACT

1-888-669-6682

Novartis Pharmaceuticals

Role: CONTACT

+41613241111

Facility Contacts

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Lucia Rodriguez

Role: primary

Kristy Osgood

Role: primary

480-323-3990

Alexandra Vasquez

Role: primary

714-738-0800

Nasrin Ahmed

Role: primary

323-865-3900

Karina Bjazevic

Role: primary

714-456-2332

Gabrielle Demaria

Role: primary

561-939-0300

Daydene Ordaz

Role: primary

305-246-0873

Samuel Pierre Louis

Role: primary

+1 407 303 6729

Tanya Palafox

Role: primary

941-400-4578

Arkady Barber

Role: primary

Aubrey Alexander

Role: primary

Anna Mattle

Role: primary

716-887-4799

Kaiya Payne

Role: primary

513-475-8730

Gabriela Niizawa

Role: primary

412-692-4920

Delrose Vernon

Role: primary

713-441-9484

Christina Grun Hayes

Role: primary

Kaycie Opiyo

Role: primary

206-685-1048

Emily Barraza

Role: primary

Other Identifiers

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2023-510026-32

Identifier Type: OTHER

Identifier Source: secondary_id

CLOU064O12301

Identifier Type: -

Identifier Source: org_study_id

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