Phase 3 Study to Assess the Efficacy and Safety of Batoclimab as Induction and Maintenance Therapy in Adult Participants With Generalized Myasthenia Gravis

NCT ID: NCT05403541

Last Updated: 2024-08-07

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

240 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-06-27

Study Completion Date

2025-04-30

Brief Summary

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The purpose of this 4-period study is to confirm the efficacy and safety of batoclimab in participants with gMG. In Period 1, participants will be randomized 1:1:1 to receive batoclimab 680 milligrams (mg) subcutaneously (SC) once a week (QW) or 340 mg SC QW or placebo. The primary efficacy endpoint will be assessed by change in the myasthenia gravis activities of daily living (MG- ADL) score in acetylcholine receptor antibody seropositive (AChRAb+) participants. In Period 2, participants previously treated with batoclimab will be re-randomized to stay on batoclimab (340 mg SC QW or 340 mg SC every two weeks) or receive placebo treatment. The secondary endpoint of maintenance of efficacy will be assessed by change in the MG- ADL score in AChRAb+ participants. Participants demonstrating a response to batoclimab during either Period 1 or 2 may enter the long-term extension (Period 3). Participants who complete Period 3 are eligible to participate in Period 4 (Optional Long-Term extension) according to their treatment assignment in Period 3.

Detailed Description

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Conditions

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Generalized Myasthenia Gravis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors
Sponsor Staff is also masked, so the study is Quadruple-blind.

Study Groups

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Batoclimab Induction Dose 1 (Period 1)

Group Type EXPERIMENTAL

Batoclimab 680 mg SC weekly

Intervention Type DRUG

Batoclimab is a fully human anti-neonatal fragment crystallizable receptor (FcRn) monoclonal antibody

Batoclimab Induction Dose 2 (Period 1)

Group Type EXPERIMENTAL

Batoclimab 340 mg SC weekly

Intervention Type DRUG

Batoclimab is a fully human anti-neonatal fragment crystallizable receptor (FcRn) monoclonal antibody

Placebo Induction Dose (Period 1)

Group Type PLACEBO_COMPARATOR

Matching Placebo SC

Intervention Type DRUG

Placebo

Batoclimab Maintenance Dose 1 (Period 2)

Group Type EXPERIMENTAL

Batoclimab 340 mg SC weekly

Intervention Type DRUG

Batoclimab is a fully human anti-neonatal fragment crystallizable receptor (FcRn) monoclonal antibody

Batoclimab Maintenance Dose 2 (Period 2)

Group Type EXPERIMENTAL

Batoclimab 340 mg SC bi-weekly

Intervention Type DRUG

Batoclimab is a fully human anti-neonatal fragment crystallizable receptor (FcRn) monoclonal antibody

Placebo Maintenance Dose (Period 2)

Group Type PLACEBO_COMPARATOR

Matching Placebo SC

Intervention Type DRUG

Placebo

Interventions

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Batoclimab 680 mg SC weekly

Batoclimab is a fully human anti-neonatal fragment crystallizable receptor (FcRn) monoclonal antibody

Intervention Type DRUG

Batoclimab 340 mg SC weekly

Batoclimab is a fully human anti-neonatal fragment crystallizable receptor (FcRn) monoclonal antibody

Intervention Type DRUG

Matching Placebo SC

Placebo

Intervention Type DRUG

Batoclimab 340 mg SC bi-weekly

Batoclimab is a fully human anti-neonatal fragment crystallizable receptor (FcRn) monoclonal antibody

Intervention Type DRUG

Other Intervention Names

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IMVT-1401 IMVT-1401 IMVT-1401

Eligibility Criteria

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Inclusion Criteria

1. Are ≥ 18 years of age at the Screening Visit.
2. Have mild to severe gMG by Myasthenia Gravis Foundation of America (MGFA) classification Class II, III, or IVa at the Screening Visit.
3. Have a QMG score ≥ 11 at the Screening and Baseline Visits.
4. Have a MG-ADL score of ≥ 5 at the Screening and Baseline Visits.

5. Have used anti-FcRn treatment within 3 months prior to the Screening Visit or have a documented history of non-response to prior anti-FcRn treatment.

Exclusion Criteria

1. Have experienced myasthenic crisis within 3 months of the Screening Visit.
2. Have had a thymectomy performed \< 6 months prior to the Screening Visit or have a planned thymectomy during the study period.
3. Have any active or untreated malignant thymoma.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Immunovant Sciences GmbH

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Site Number -1022

Phoenix, Arizona, United States

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Site Number -1029

Scottsdale, Arizona, United States

Site Status

Site Number -1002

Carlsbad, California, United States

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Site Number -1009

Irvine, California, United States

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Site Number - 1012

Olive View, California, United States

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Site Number -1032

San Francisco, California, United States

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Site Number - 1027

Aurora, Colorado, United States

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Site Number - 1025

New Haven, Connecticut, United States

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Site Number -1017

Boca Raton, Florida, United States

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Site Number -1007

Clearwater, Florida, United States

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Site Number -1010

Maitland, Florida, United States

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Site Number - 1020

Miami, Florida, United States

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Site Number -1019

Orlando, Florida, United States

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Site Number - 1028

Port Charlotte, Florida, United States

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Site Number - 1015

Tampa, Florida, United States

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Site Number -1011

Fairway, Kansas, United States

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Site Number -1003

Lexington, Kentucky, United States

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Site Number -1013

East Lansing, Michigan, United States

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Site Number - 1024

Minneapolis, Minnesota, United States

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Site Number - 1021

Buffalo, New York, United States

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Site Number - 1018

Chapel Hill, North Carolina, United States

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Site Number - 1008

Durham, North Carolina, United States

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Site Number -1004

Cleveland, Ohio, United States

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Site Number -1006

Portland, Oregon, United States

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Site Number - 1023

Philadelphia, Pennsylvania, United States

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Site Number - 1030

Charleston, South Carolina, United States

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Site Number - 1026

Memphis, Tennessee, United States

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Site Number -1001

Austin, Texas, United States

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Site Number -1016

Dallas, Texas, United States

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Site Number - 1034

Houston, Texas, United States

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Site Number - 1014

Round Rock, Texas, United States

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Site Number -1031

Murray, Utah, United States

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Site Number -1005

Charlottesville, Virginia, United States

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Site Number - 5002

Buenos Aires, , Argentina

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Site Number - 5001

Buenos Aires, , Argentina

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Site Number - 5003

Rosario, , Argentina

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Site Number - 5501

Ribeirão Preto, , Brazil

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Site Number- 5503

Rio de Janeiro, , Brazil

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Site Number -2001

Edmonton, Alberta, Canada

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Site Number - 2003

Vancouver, British Columbia, Canada

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Site Number - 2002

Toronto, Ontario, Canada

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Site Number - 2004

Montreal, Quebec, Canada

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Site Number -8002

Tbilisi, , Georgia

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Site Number -8004

Tbilisi, , Georgia

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Site Number -8001

Tbilisi, , Georgia

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Site Number -8003

Tbilisi, , Georgia

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Site Number - 8005

Tbilisi, , Georgia

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Site Number - 6507

Berlin, , Germany

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Site Number - 6506

Bochum, , Germany

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Site Number - 6501

Hamburg, , Germany

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Site Number - 6503

Jena, , Germany

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Site Number -6504

Leipzig, , Germany

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Site Number -6502

Würzburg, , Germany

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Site Number -7553

Budapest, , Hungary

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Site Number - 7552

Kistarcsa, , Hungary

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Site Number - 6004

Bergamo, , Italy

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Site Number -6006

Brescia, , Italy

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Site Number - 6002

Genova, , Italy

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Site Number - 6003

Milan, , Italy

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Site Number - 6007

Napoli, , Italy

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Site Number -6001

Napoli, , Italy

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Site Number -6005

Roma, , Italy

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Site Number - 4020

Asahikawa-shi, , Japan

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Site Number - 4014

Fuchu-shi, , Japan

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Site Number - 4002

Hanamaki-shi, , Japan

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Site Number - 4013

Higashimatsushima, , Japan

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Site Number - 4006

Kagawa, , Japan

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Site Number - 4009

Kawasaki-shi, , Japan

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Site Number - 4012

Koriyama-shi, , Japan

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Site Number - 4007

Koshigaya-shi, , Japan

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Site Number - 4011

Matsuyama, , Japan

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Site Number - 4008

Miyagi, , Japan

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Site Number - 4003

Narita-shi, , Japan

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Site Number - 4010

Osaka, , Japan

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Site Number - 4004

Osaka, , Japan

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Site Number - 4001

Osaka, , Japan

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Site Number - 4005

Tokyo, , Japan

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Site Number - 4018

Toyama, , Japan

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Site Number - 4016

Yokohama, , Japan

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Site Number - 4019

Yokohama, , Japan

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Site Number - 4015

Yokohama, , Japan

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Site Number - 4017

Yonago-shi, , Japan

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Site Number - 2601

Mexico City, , Mexico

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Site Number - 3007

Gdansk, , Poland

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Site Number -3001

Katowice, , Poland

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Site Number -3004

Krakow, , Poland

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Site Number - 3003

Krakow, , Poland

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Site Number -3002

Krakow, , Poland

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Site Number - 3008

Lublin, , Poland

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Site Number -3006

Poznan, , Poland

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Site Number - 3005

Warsaw, , Poland

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Site Number -7502

Constanța, , Romania

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Site Number -7501

Târgu Mureş, , Romania

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Site Number -7503

Timișoara, , Romania

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Site Number - 9001

Belgrade, , Serbia

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Site Number - 9002

Niš, , Serbia

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Site Number -4505

Daegu, , South Korea

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Site Number -4501

Seoul, , South Korea

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Site Number -3502

Barcelona, , Spain

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Site Number -3505

Barcelona, , Spain

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Site Number -3504

Córdoba, , Spain

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Site Number -3501

Madrid, , Spain

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Site Number -3503

Madrid, , Spain

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Site Number - 7001

Liverpool, , United Kingdom

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Site Number - 7002

Sheffield, , United Kingdom

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Countries

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United States Argentina Brazil Canada Georgia Germany Hungary Italy Japan Mexico Poland Romania Serbia South Korea Spain United Kingdom

References

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Benatar M, Wiendl H, Nowak R, Zheng Y, Macias W. Batoclimab as induction and maintenance therapy in patients with myasthenia gravis: rationale and study design of a phase 3 clinical trial. BMJ Neurol Open. 2024 Jan 10;6(1):e000536. doi: 10.1136/bmjno-2023-000536. eCollection 2024.

Reference Type DERIVED
PMID: 38268752 (View on PubMed)

Other Identifiers

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IMVT-1401-3101

Identifier Type: -

Identifier Source: org_study_id

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