A Study To Evaluate Efficacy, Safety, Pharmacokinetics, And Pharmacodynamics Of Satralizumab In Patients With Generalized Myasthenia Gravis

NCT ID: NCT04963270

Last Updated: 2025-02-28

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

188 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-10-19

Study Completion Date

2024-09-02

Brief Summary

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This study will evaluate the efficacy, safety, pharmacokinetics, and pharmacodynamics of satralizumab compared with placebo in participants with generalized myasthenia gravis (gMG).

Detailed Description

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Conditions

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Generalized Myasthenia Gravis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Satralizumab

Participants will receive Satralizumab at Weeks 0, 2, 4, and Q4W thereafter. Adolescent patients who first enter the study in the OLE period will receive satralizumab SC loading doses at Week 0, 2, and 4 in the OLE, followed by maintenance doses Q4W thereafter and will remain on stable background therapy until Week 24 of the OLE.

Group Type EXPERIMENTAL

Satralizumab

Intervention Type DRUG

Satralizumab will be administered as a subcutaneous injection

Placebo

Participants will receive placebo at Weeks 0, 2, 4, and Q4W thereafter

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Satralizumab placebo will be administered as a subcutaneous injection

Interventions

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Satralizumab

Satralizumab will be administered as a subcutaneous injection

Intervention Type DRUG

Placebo

Satralizumab placebo will be administered as a subcutaneous injection

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Signed Informed Consent Form
* For adolescent patients: Informed Consent Form for study participation signed by the parents or a legal guardian, and patient assent obtained, as per local requirements
* Ability to comply with the study protocol procedures
* Confirmed diagnosis of gMG (anti-AChR, anti-MuSK or anti-LRP4 present at screening)
* A total MG-ADL score of ≥ 5 points at screening with more than 50% of this score attributed to non-ocular items
* MGFA severity Class II-IV
* Ongoing gMG treatment at a stable dose
* For female patients of childbearing potential: agreement to remain abstinent (refrain from heterosexual intercourse) or use adequate contraception during the treatment period and for at least 3 months after the final dose of satralizumab.

Exclusion Criteria

* History of thymectomy within 12 months prior to screening
* Ocular MG (MGFA Class I) and myasthenic crisis (MGFA Class V) within the last 3 months prior to screening
* Known disease other than gMG that would interfere with the course and conduct of the study
* Positive screening tests for hepatitis B virus (HBV) and hepatitis C virus (HCV)
* Evidence of latent or active tuberculosis (excluding patients receiving chemoprophylaxis for latent tuberculosis infection)
* Receipt of live or live attenuated vaccine within 6 weeks prior to baseline
* Pregnant or breastfeeding, or intending to become pregnant during the study or within 3 months after the last dose
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Chugai Pharmaceutical

INDUSTRY

Sponsor Role collaborator

Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Keck School of Medicine of USC

Los Angeles, California, United States

Site Status

University of California Irvine - Manchester Pavilion

Orange, California, United States

Site Status

SC3 Research Group, Inc

Pasadena, California, United States

Site Status

Medical Faculty Associates Inc.

Washington D.C., District of Columbia, United States

Site Status

University of Chicago Hospital

Chicago, Illinois, United States

Site Status

Prairie Education and Research

O'Fallon, Illinois, United States

Site Status

Hospital Italiano

CABA, , Argentina

Site Status

Hospital Ramos Mejía

CABA, , Argentina

Site Status

Hospital Britanico

Ciudad Autonoma Bs As, , Argentina

Site Status

Fundación Scherbovsky

Mendoza, , Argentina

Site Status

INECO Neurociencias Orono

Rosario, , Argentina

Site Status

Concord Repatriation General Hospital

Concord, New South Wales, Australia

Site Status

Hospital Sao Lucas - PUCRS

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Hospital das Clinicas - UNICAMP

Campinas, São Paulo, Brazil

Site Status

Faculdade de Medicina do ABC - FMABC

Santo André, São Paulo, Brazil

Site Status

Hospital Sao Paulo

São Paulo, São Paulo, Brazil

Site Status

MUCH - Montreal Neurological Institute & Hospital

Montreal, Quebec, Canada

Site Status

Beijing Tongren Hospital

Beijing, , China

Site Status

Beijing Tiantan Hospital,Capital Medical University

Beijing, , China

Site Status

The First Hospital of Jilin University

Changchun, , China

Site Status

West China Hospital - Sichuan University

Chengdu, , China

Site Status

The Affiliated Hospital of Guizhou Medical University

Guiyang, , China

Site Status

Sir Run Run Shaw Hospital

Hangzhou, , China

Site Status

The First Affiliated Hospital Of Shandong First Medical University

Jinan, , China

Site Status

Huashan Hospital, Fudan University

Shanghai, , China

Site Status

Children's Hospital of Fudan University

Shanghai, , China

Site Status

Tianjin Medical University General Hospital

Tianjin, , China

Site Status

Tongji Hospital Tongji Medical College Huazhong University of Science and Technology

Wuhan, , China

Site Status

Tangdu Hospital

Xi'an, , China

Site Status

Aarhus Universitetshospital

Aarhus N, , Denmark

Site Status

Rigshospitalet

København Ø, , Denmark

Site Status

CHU Bordeaux

Bordeaux, , France

Site Status

APHP Raymond Poincare

Garches, , France

Site Status

Hopital Timone Adultes

Marseille, , France

Site Status

CHU de Nantes - Hotel Dieu

Nantes, , France

Site Status

CHU Nice - Hôpital Pasteur 2

Nice, , France

Site Status

St. Josef-Hospital, Klinik für Neurologie

Bochum, , Germany

Site Status

Universitätsklinikum Essen (AöR)

Essen, , Germany

Site Status

Universitätsklinikum Münster

Münster, , Germany

Site Status

Azienda Ospedaliera A. Cardarelli

Napoli, Campania, Italy

Site Status

Fond. Istituto Neurologico C.Besta

Milan, Lombardy, Italy

Site Status

A.R.N.A.S. Civico Di Cristina Benfratelli

Palermo, Sicily, Italy

Site Status

Ospedale Cà Foncello

Treviso, Veneto, Italy

Site Status

Juntendo University Hospital

Bunkyō City, , Japan

Site Status

Chiba University Hospital

Chiba-shi, Chiba, , Japan

Site Status

General Hanamaki Hospital

Hanamaki, Iwate, , Japan

Site Status

Sapporo Medical University Hospital

Hokkaido, , Japan

Site Status

NHO Hokkaido Medical Center

Hokkaido, , Japan

Site Status

St. Marianna University Hospital

Kanagawa, , Japan

Site Status

International University of Health and Welfare Narita Hospital

Narita, Chiba, , Japan

Site Status

Kindai University Hospital

Osaka, , Japan

Site Status

Seirei Hamamatsu General Hospital

Shizuoka, , Japan

Site Status

Osaka University Hospital

Suita, , Japan

Site Status

Tokyo Medical And Dental University, Medical Hospital

Tokyo, , Japan

Site Status

Tokyo Medical University Hospital

Tokyo, , Japan

Site Status

Klinika Neurologii Doros?ych, Uniwersyteckie Centrum Kliniczne

Gda?sk, , Poland

Site Status

Zespol Poradni Specjalistycznych - Poradnia Neurologiczna

Krakow, , Poland

Site Status

Krakowska Akademia Neurologii Sp z o.o. Centrum Neurologii K

Krakow, , Poland

Site Status

Indywidualna Praktyka Lekarska Prof. Dr Hab. N. Med. Konrad Rejdak.

Lublin, , Poland

Site Status

Krasnoyarsk State Medical Academy

Krasnoyarsk, Krasnoyarsk Krai, Russia

Site Status

Novosibirsk State Regional Clinical Hospital

Novosibirsk, , Russia

Site Status

Kyungpook National University Chilgok Hospital

Daegu, , South Korea

Site Status

Pusan National University Yangsan Hospital

Gyeongsangnam-do, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Korea University Anam Hospital

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Hospital Universitari de Bellvitge

L'Hospitalet de Llobregat, Barcelona, Spain

Site Status

Clinica Universitaria de Navarra

Pamplona, Navarre, Spain

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Hospital Universitario la Fe

Valencia, , Spain

Site Status

Taipei Veterans General Hospital-Neurology

Taipei, , Taiwan

Site Status

Chang Gung Medical Foundation Linkou Branch

Taoyuan, , Taiwan

Site Status

Hacettepe University Medical Faculty

Ankara, , Turkey (Türkiye)

Site Status

Ege University Medical Faculty

Izmir, , Turkey (Türkiye)

Site Status

Kocaeli University Hospital

Kocaeli, , Turkey (Türkiye)

Site Status

Ondokuz Mayis Univ. Med. Fac.

Samsun, , Turkey (Türkiye)

Site Status

Countries

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United States Argentina Australia Brazil Canada China Denmark France Germany Italy Japan Poland Russia South Korea Spain Taiwan Turkey (Türkiye)

References

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Habib AA, Zhao C, Aban I, Franca MC Jr, Jose JG, Zu Horste GM, Klimiec-Moskal E, Pulley MT, Tavolini D, Krumova P, Lennon-Chrimes S, Smith J, Thanei GA, Blondeau K, Vodopivec I, Wolfe GI, Murai H. Safety and efficacy of satralizumab in patients with generalised myasthenia gravis (LUMINESCE): a randomised, double-blind, multicentre, placebo-controlled phase 3 trial. Lancet Neurol. 2025 Feb;24(2):117-127. doi: 10.1016/S1474-4422(24)00514-3.

Reference Type DERIVED
PMID: 39862880 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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WN42636

Identifier Type: -

Identifier Source: org_study_id

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