A Study to Evaluate the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of Satralizumab in Participants With Myelin Oligodendrocyte Glycoprotein Antibody-associated Disease

NCT ID: NCT05271409

Last Updated: 2025-12-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

152 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-08-30

Study Completion Date

2028-12-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The main objective of this study is to evaluate the efficacy of satralizumab compared with placebo based on time from randomization to the first occurrence of an adjudicated MOGAD relapse in the double-blind (DB) treatment period. Participants who experience an adjudicated relapse or complete the DB period can enter open-label extension (OLE) period. After the primary clinical cutoff date (CCOD), additional adolescent participants may be enrolled directly into the OLE period.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Myelin Oligodendrocyte Glycoprotein Antibody-Associated Disease (MOGAD)

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Satralizumab

In the DB treatment period, participants will receive satralizumab at Weeks 0, 2, 4 (loading doses) and maintenance doses every 4 weeks (Q4W) thereafter. In the OLE period, all participants will receive open-label treatment with satralizumab. Additional adolescent participants will be directly enrolled in the OLE period to receive satralizumab.

Group Type EXPERIMENTAL

Satralizumab

Intervention Type DRUG

Study drug will be administered by subcutaneous (SC) injection in the abdominal or femoral region after all other study-related procedures have been performed at a site visit.

Placebo

In the DB treatment period, participants will receive satralizumab matching placebo at Weeks 0, 2, 4 (loading doses) and maintenance doses Q4W thereafter. In the OLE period, all participants will receive open label treatment with satralizumab.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Placebo will be administered by SC injection in the abdominal or femoral region after all other study-related procedures have been performed at a site visit.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Satralizumab

Study drug will be administered by subcutaneous (SC) injection in the abdominal or femoral region after all other study-related procedures have been performed at a site visit.

Intervention Type DRUG

Placebo

Placebo will be administered by SC injection in the abdominal or femoral region after all other study-related procedures have been performed at a site visit.

Intervention Type OTHER

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Participants who are aged \>=12 years at the time of signing Informed Consent Form
* Confirmed diagnosis of MOGAD with a history of \>=1 MOGAD relapse in the 12 months prior to screening or \>=2 attacks in the 24 months prior to screening
* Expanded Disability Status Scale (EDSS) score of 0-6.5 at screening
* High-contrast visual acuity (HCVA) better than 20/800 in each eye at screening
* Participants receiving either no or ongoing chronic immunosuppressant treatment (IST) for MOGAD at the time of screening
* For women of childbearing potential: participants who agree to remain abstinent or use adequate contraception during the treatment period and for at least 3 months after the final dose of satralizumab

Exclusion Criteria

* Presence of aquaporin-4-antibodies immunoglobin G (AQP4-IgG) in the serum
* History of anti-N-methyl-d-aspartate receptor (NMDAR) encephalitis
* Any concomitant disease other than MOGAD that may require treatment with ISTs or oral corticosteroids (OCS) or intravenous (IV) corticosteroids at doses \> 20 milligrams (mg) prednisone equivalent per day for \>21 days during the study
* Participants who are pregnant or breastfeeding, or intending to become pregnant during the study or within 3 months after the final dose of satralizumab
* Participants with active or presence of recurrent bacterial, viral, fungal, mycobacterial infection, or other infection at baseline
* Participants with evidence of latent or active tuberculosis (excluding patients receiving chemoprophylaxis for latent tuberculosis infection)
* Participants with positive screening tests for hepatitis B and C
* Receipt of live or live attenuated vaccine within 6 weeks prior to baseline
* History of severe allergic reaction to a biologic agent
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Chugai Pharmaceutical

INDUSTRY

Sponsor Role collaborator

Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status RECRUITING

Mayo Clinic- Scottsdale

Scottsdale, Arizona, United States

Site Status WITHDRAWN

University of California Irvine - Manchester Pavilion

Irvine, California, United States

Site Status RECRUITING

University of Colorado - Anschutz Medical Campus (University of Colorado Health Sciences Center)

Aurora, Colorado, United States

Site Status RECRUITING

Medstar Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status RECRUITING

University of Florida College of Medicine Gainesville

Gainesville, Florida, United States

Site Status RECRUITING

Nemours Children's Clinic - of the Nemours Foundation

Jacksonville, Florida, United States

Site Status RECRUITING

Meridian Clinical Research, LLC

Savannah, Georgia, United States

Site Status WITHDRAWN

Northwestern University

Chicago, Illinois, United States

Site Status WITHDRAWN

Consultants in Neurology Ltd

Northbrook, Illinois, United States

Site Status WITHDRAWN

Johns Hopkins

Baltimore, Maryland, United States

Site Status RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

Memorial Healthcare Institute for Neurosciences and Multiple Sclerosis

Owosso, Michigan, United States

Site Status RECRUITING

Mayo Clinic - Rochester

Rochester, Minnesota, United States

Site Status RECRUITING

Washington University School of Medicine in St. Louis

St Louis, Missouri, United States

Site Status RECRUITING

NYU Langone

New York, New York, United States

Site Status RECRUITING

Duke University Medical Center

Durham, North Carolina, United States

Site Status WITHDRAWN

University of Cincinnati

Cincinnati, Ohio, United States

Site Status ACTIVE_NOT_RECRUITING

Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status RECRUITING

OhioHealth Research Institute

Columbus, Ohio, United States

Site Status WITHDRAWN

Premier Neurology

Greenville, South Carolina, United States

Site Status COMPLETED

Baylor College of Medicine

Houston, Texas, United States

Site Status WITHDRAWN

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status COMPLETED

Brain and Mind Research Institute

Camperdown, New South Wales, Australia

Site Status RECRUITING

John Hunter Hospital

New Lambton, New South Wales, Australia

Site Status RECRUITING

Sydney Children's Hospital

Randwick, New South Wales, Australia

Site Status RECRUITING

Royal North Shore Hospital

St Leonards, New South Wales, Australia

Site Status WITHDRAWN

Box Hill Hospital

Box Hill, Victoria, Australia

Site Status WITHDRAWN

Monash Medical Centre

Clayton, Victoria, Australia

Site Status RECRUITING

St Vincent's Hospital Melbourne

Fitzroy, Victoria, Australia

Site Status WITHDRAWN

Royal Melbourne Hospital

Parkville, Victoria, Australia

Site Status WITHDRAWN

Perron Institute for Neurological and Translational Science

Nedlands, Western Australia, Australia

Site Status RECRUITING

Instituto de Neurologia de Curitiba

Curitiba, Paraná, Brazil

Site Status RECRUITING

Instituto do Cerebro do Rio Grande do Sul

Porto Alegre, Rio Grande do Sul, Brazil

Site Status RECRUITING

Centro de Pesquisas Clinicas

São Paulo, São Paulo, Brazil

Site Status RECRUITING

Hospital Universitario Gaffree e Guinle

Rio de Janeiro, , Brazil

Site Status RECRUITING

London Health Sciences Centre Uni Campus

London, Ontario, Canada

Site Status RECRUITING

Children's Hospital of Eastern Ontario

Ottawa, Ontario, Canada

Site Status RECRUITING

Unity Health Toronto - St. Michael's Hospital

Toronto, Ontario, Canada

Site Status WITHDRAWN

The Hospital for Sick Children

Toronto, Ontario, Canada

Site Status RECRUITING

MUCH - Montreal Neurological Institute & Hospital

Montreal, Quebec, Canada

Site Status RECRUITING

Hopital Pierre Wertheimer

Bron, , France

Site Status RECRUITING

CH de Bicêtre

Le Kremlin-Bicêtre, , France

Site Status RECRUITING

CHU de Toulouse - Hôpital Purpan

Toulouse, , France

Site Status RECRUITING

NeuroCure Clinical Research Center (NCRC)

Berlin, , Germany

Site Status ACTIVE_NOT_RECRUITING

St. Josef-Hospital, Klinik für Neurologie

Bochum, , Germany

Site Status ACTIVE_NOT_RECRUITING

Vestische Kinder- und Jugendklinik Datteln

Datteln, , Germany

Site Status RECRUITING

Universitätsklinikum Düsseldorf

Düsseldorf, , Germany

Site Status ACTIVE_NOT_RECRUITING

Neurology UKSH Campus Kiel

Kiel, , Germany

Site Status ACTIVE_NOT_RECRUITING

Universitätsklinikum Mannheim

Mannheim, , Germany

Site Status ACTIVE_NOT_RECRUITING

Klinikum Großhadern, LMU

Munich, , Germany

Site Status ACTIVE_NOT_RECRUITING

Hadassah University Hospital Ein Kerem

Jerusalem, , Israel

Site Status RECRUITING

Ospedale Pediatrico Bambino Gesù

Rome, Lazio, Italy

Site Status RECRUITING

IRCCS Ospedale San Raffaele

Milan, Lombardy, Italy

Site Status RECRUITING

Fondazione IRCCS Istituto Neurologico Carlo Besta

Milan, Lombardy, Italy

Site Status RECRUITING

Fondazione Istituto Neurologico Mondino IRCCS

Pavia, Lombardy, Italy

Site Status RECRUITING

Azienda Sanitaria Ospedaliera S. Luigi Gonzaga

Orbassano, Piedmont, Italy

Site Status RECRUITING

AOU Policlinico V. Emanuele - P.O G. Rodolico

Catania, Sicily, Italy

Site Status RECRUITING

Azienda Ospedaliera Universitaria Integrata Verona

Verona, Veneto, Italy

Site Status RECRUITING

Chiba University Hospital

Chiba, , Japan

Site Status RECRUITING

Kyushu University Hospital

Fukuoka, , Japan

Site Status RECRUITING

Southern Tohoku Medical Clinic

Fukushima, , Japan

Site Status RECRUITING

Kobe University Hospital

Hyōgo, , Japan

Site Status RECRUITING

Kitasato University Hospital

Kanagawa, , Japan

Site Status RECRUITING

Tohoku University Hospital

Miyagi, , Japan

Site Status RECRUITING

Tohoku Medical and Pharmaceutical University Hospital

Miyagi, , Japan

Site Status RECRUITING

The University of Osaka Hospital

Osaka, , Japan

Site Status RECRUITING

Saitama Medical Center

Saitama, , Japan

Site Status RECRUITING

The Jikei University Hospital

Tokyo, , Japan

Site Status RECRUITING

Juntendo University Hospital

Tokyo, , Japan

Site Status RECRUITING

Tokyo Medical University Hospital

Tokyo, , Japan

Site Status RECRUITING

Keio University Hospital

Tokyo, , Japan

Site Status RECRUITING

Tokyo Women's Medical University Hospital

Tokyo, , Japan

Site Status WITHDRAWN

Wielospecjalistyczna Poradnia Lekarska Synapsis

Katowice, , Poland

Site Status RECRUITING

Szpital Uniwersytecki w Krakowie

Krakow, , Poland

Site Status RECRUITING

Centrum Medyczne "MEDYK"

Rzeszów, , Poland

Site Status RECRUITING

Klinika Neurologii I Wydzialu Lekarskiego WUM w Warszawie

Warsaw, , Poland

Site Status RECRUITING

Instytut Pomnik Centrum Zdrowia Dziecka

Warsaw, , Poland

Site Status RECRUITING

SPSK nr 1

Zabrze, , Poland

Site Status RECRUITING

National Cancer Center

Goyang-si, , South Korea

Site Status RECRUITING

Seoul National University Hospital

Seoul, , South Korea

Site Status ACTIVE_NOT_RECRUITING

Samsung Medical Center

Seoul, , South Korea

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

China United States Australia Brazil Canada France Germany Israel Italy Japan Poland South Korea

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

Reference Study ID Number: WN43194 https://forpatients.roche.com/

Role: CONTACT

Phone: 888-662-6728 (U.S.)

Email: [email protected]

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2021-003192-34

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2023-507196-22-00

Identifier Type: CTIS

Identifier Source: secondary_id

WN43194

Identifier Type: -

Identifier Source: org_study_id