Myasthenia Gravis Inebilizumab Trial

NCT ID: NCT04524273

Last Updated: 2025-02-20

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

238 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-10-15

Study Completion Date

2027-11-29

Brief Summary

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Randomized, double-blind, placebo-controlled, Phase 3, parallel-group study with optional open-label extension.

Detailed Description

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This study is a phase 3, randomized, double-blind, placebo-controlled study, to be conducted at approximately 120 study sites. Approximately 230 participants (188 acetylcholine receptor antibody positive \[AChR-Ab+\] and 42 muscle-specific tyrosine kinase antibody positive \[MuSK-Ab+\]) will be enrolled. Participants with Myasthenia Gravis (MG) who are positive for anti-AChR or anti-MuSK antibodies will be enrolled and analyzed. Patients who do not have anti-AChR or anti-MuSK antibodies will not be enrolled. Patients with Myasthenia Gravis Foundation of America (MGFA) classification II, III, or IV disease, Myasthenia Gravis Activities of Daily Living (MG-ADL) score at screening and randomization between 6 and 10 with \> 50% of this score attributed to non-ocular items, or an MG-ADL score \>=11, Quantitative Myasthenia Gravis (QMG) score \>= 11 at the time of screening and randomization, and use of a corticosteroid and/or non-steroidal immunosuppressant will be included in the study.

All subjects who complete the randomized controlled period (RCP) will have the option to enroll in a 3-year (156 weeks) open-label period.

Study acquired from Horizon in 2023.

Conditions

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Myasthenia Gravis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

A Randomized, Double-blind, Multicenter, Placebo-controlled Phase 3 Study with Open-label Period
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
This is a double-blind study in which the IV inebilizumab and the IV placebo are matching in appearance.

Study Groups

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Inebilizumab, (AChR-Ab+) MG

Participants will receive inebilizumab administered intravenously (IV) on Days 1, 15, and 183 of the RCP.

Participants who elect to enter the open label phase (OLP) will receive inebilizumab administered IV on OLP Days 1, IV placebo on OLP Day 15 (to avoid potential unblinding), and inebilizumab IV on OLP Days 183, 365, 547, 729, and 911.

Group Type EXPERIMENTAL

inebilizumab

Intervention Type DRUG

Participants will receive IV inebilizumab

Placebo, (AChR-Ab+) MG

Participants will receive placebo administered IV on Days 1, 15, and 183 of the RCP.

Participants who elect to enter the OLP will receive inebilizumab administered IV on OLP Days 1,15, 183, 365, 547, 729, and 911.

Group Type PLACEBO_COMPARATOR

IV Placebo

Intervention Type DRUG

Participants will receive IV placebo matched to inebilizumab

Inebilizumab, (MuSK-Ab+) MG

Participants will receive inebilizumab administered IV on Days 1 and 15 of the RCP.

Participants who elect to enter the OLP will receive inebilizumab administered IV on OLP Day 1, IV placebo on OLP Day 15 (to avoid potential unblinding), and inebilizumab IV on OLP Days 183, 365, 547, 729, and 911.

Group Type EXPERIMENTAL

inebilizumab

Intervention Type DRUG

Participants will receive IV inebilizumab

Placebo, (MuSK-Ab+) MG

Participants will receive placebo administered IV on Days 1 and 15 of the RCP. Participants who elect to enter the OLP will receive inebilizumab administered IV on OLP Days 1,15, 183, 365, 547, 729, and 911.

Group Type PLACEBO_COMPARATOR

IV Placebo

Intervention Type DRUG

Participants will receive IV placebo matched to inebilizumab

Interventions

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inebilizumab

Participants will receive IV inebilizumab

Intervention Type DRUG

IV Placebo

Participants will receive IV placebo matched to inebilizumab

Intervention Type DRUG

Other Intervention Names

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MEDI-551 VIB0551

Eligibility Criteria

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Inclusion Criteria

1. Diagnosis of MG with anti-AChR or anti-MuSK antibody.
2. MGFA Clinical Classification Class II, III, or IV.
3. MG-ADL score of 6 or greater at screening and at randomization with \> 50% of this score attributed to non-ocular items.
4. QMG score of 11 or greater.
5. Participants must be on:

1. Corticosteroids only, with no dose increase within 4 weeks prior to randomization, or
2. One allowed non-steroidal immunosuppressive therapy (IST), with continuous use for at least 6 months prior to randomization and no dose increase within 4 months prior to randomization, or
3. Combination of (1) corticosteroids with no dose increase within 4 weeks prior to randomization and (2) one allowed non-steroidal IST with continuous use for at least 6 months prior to randomization and no dose increase within 4 months prior to randomization.

Allowed ISTs, alone or in combination with corticosteroids, are azathioprine, mycophenolate mofetil, and mycophenolic acid.

Exclusion Criteria

1. Receipt of the following medications within the 4 weeks prior to Day 1:

1. Cyclosporine (except eye drops)
2. Tacrolimus (except topical)
3. Methotrexate
2. Current use of:

1. Corticosteroids (Prednisone \> 40 milligram (mg)/day or \> 80 mg over a 2-day period (or equivalent dose of other corticosteroids).
2. Acetylcholinesterase inhibitors (pyridostigmine) \> 480 mg/day) or unstable dose in the 2 weeks prior to Day 1.
3. Azathioprine \> 3 mg/kilogram (kg)/day
4. Mycophenolate mofetil \> 3 grams/day or mycophenolic acid \> 1440 mg/day
5. Any IST, alone or in combination with corticosteroids, except for azathioprine, mycophenolate mofetil, and mycophenolic acid.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Locations

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Viela Bio Investigative Site - 1015

Orange, California, United States

Site Status

Viela Bio Investigative Site - 1002

New Haven, Connecticut, United States

Site Status

Viela Bio Investigative Center - 1024

Washington D.C., District of Columbia, United States

Site Status

Viela Bio Investigative Site - 1005

Tampa, Florida, United States

Site Status

Viela Bio Investigative Site - 1012

Kansas City, Kansas, United States

Site Status

Viela Bio Investigative Site - 1018

Charlotte, North Carolina, United States

Site Status

Viela Bio Investigative Site - 1025

Canton, Ohio, United States

Site Status

Viela Bio Investigative Site - 1001

Cincinnati, Ohio, United States

Site Status

Viela Bio Investigative Site - 1009

Columbus, Ohio, United States

Site Status

Viela Bio Investigative Site - 1008

Pittsburgh, Pennsylvania, United States

Site Status

Viela Bio Investigative Site - 1019

Austin, Texas, United States

Site Status

Viela Bio Investigative Site - 1003

Houston, Texas, United States

Site Status

Viela Bio Investigative Site - 1014

San Antonio, Texas, United States

Site Status

Viela Bio Investigative Site - 1017

Salt Lake City, Utah, United States

Site Status

Viela Bio Investigative Site - 1004

Burlington, Vermont, United States

Site Status

Viela Bio Investigative Site - 1006

Richmond, Virginia, United States

Site Status

Viela Bio Investigative Site - 2001

Buenos Aires, , Argentina

Site Status

VielaBio Investigative Site - 2002

Buenos Aires, , Argentina

Site Status

Viela Bio Investigative Site - 2003

Buenos Aires, , Argentina

Site Status

Viela Bio Investigative Site - 5203

Grodno, , Belarus

Site Status

Viela Bio Investigative Site - 5204

Minsk, , Belarus

Site Status

Viela Bio Investigative Site - 5201

Vitebsk, , Belarus

Site Status

VielaBio Investigative Site - 2201

Porto Alegre, , Brazil

Site Status

VielaBio Investigative Site - 2203

Porto Alegre, , Brazil

Site Status

VielaBio Investigative Site - 2207

Ribeirão Preto, , Brazil

Site Status

VielaBio Investigative Site - 2206

São Paulo, , Brazil

Site Status

Viela Bio Investigative Site - 2205

São Paulo, , Brazil

Site Status

Viela Bio Investigative Site - 1102

Toronto, Ontario, Canada

Site Status

Viela Bio Investigative Site - 1101

Montreal, Quebec, Canada

Site Status

Viela Bio Investigative Site - 1103

Montreal, Quebec, Canada

Site Status

Viela Bio Investigative Site 4009

Beijing, , China

Site Status

Viela Bio Investigative Site - 4007

Beijing, , China

Site Status

Viela Bio Investigative Site 4003

Beijing, , China

Site Status

Viela Bio Investigative Site - 4005

Guiyang, , China

Site Status

Viela Bio Investigative site 4010

Hunan, , China

Site Status

Viela Bio Investigative Site - 4011

Jinan, , China

Site Status

Viela Bio Investigative Site - 4006

Shanghai, , China

Site Status

Viela Bio Investigative Site - 4008

Suzhou, , China

Site Status

Viela Bio Investigative Site - 4004

Tianjin, , China

Site Status

Viela Bio Investigative Site 4012

Xi'an, , China

Site Status

Viela Bio Investigative Site - 5601

Copenhagen, , Denmark

Site Status

Viela Bio Investigative Site - 3003

Lille, , France

Site Status

Viela Bio Investigative Site - 3001

Nice, , France

Site Status

Viela Bio Investigative Site - 3002

Strasbourg, , France

Site Status

VielaBio Investigative Site - 3101

Essen, , Germany

Site Status

Viela Bio Investigative Site - 4107

Nagpur, Maharashtra, India

Site Status

Viela Bio Investigative Site - 4113

Nagpur, Maharashtra, India

Site Status

Viela Bio Investigative Site - 4112

Hyderabad, Telangana, India

Site Status

Viela Bio Investigative Site - 4104

Bangalore, , India

Site Status

Viela Bio investigative Site - 4105

Lucknow, , India

Site Status

Viela Bio Investigative Site - 4103

Manipal, , India

Site Status

Viela Bio Investigative Site - 4102

Nashik, , India

Site Status

Viela Bio Investigative Site - 4109

Pune, , India

Site Status

Viela Bio Investigative Site - 4101

Surat, , India

Site Status

Viela Bio Investigative Site - 3204

Milan, , Italy

Site Status

Viela Bio Investigative Site - 3203

Milan, , Italy

Site Status

Viela Bio Investigative Site - 3201

Pavia, , Italy

Site Status

Viela Bio Investigative Site - 3202

Rome, , Italy

Site Status

Viela Bio Investigative Site - 4402

Chiba, , Japan

Site Status

Viela Bio Investigative Site - 4410

Chiba, , Japan

Site Status

Viela Bio Investigative Site 4409

Fukuoka, , Japan

Site Status

Viela Bio Investigative Site - 4401

Hanamaki, , Japan

Site Status

VielaBio Investigative Site - 4408

Hokkaido, , Japan

Site Status

Viela Bio Investigative Site - 4406

Hyōgo, , Japan

Site Status

Viela Bio Investigative Site 4405

Miyagi, , Japan

Site Status

Viela Bio Investigative Site - 4413

Moriguchi, , Japan

Site Status

VielaBio Investigative Site - 4407

Morioka, , Japan

Site Status

Viela Bio Investigative Site - 4404

Saitama, , Japan

Site Status

Viela Bio Investigative Site - 3302

Katowice, , Poland

Site Status

Viela Bio Investigative Site - 3303

Katowice, , Poland

Site Status

Viela Bio Investigative Site - 3301

Krakow, , Poland

Site Status

Med Polonia Sp. z o.o - 3311

Poznan, , Poland

Site Status

Viela Bio Investigative Site - 3310

Warsaw, , Poland

Site Status

Viela Bio Investigative Site - 5313

Barnaul, Altayskiy Kray, Russia

Site Status

Viela Bio Investigative Site - 5303

Barnaul, , Russia

Site Status

Viela Bio Investigative Site - 5302

Nizhny Novgorod, , Russia

Site Status

Viela Bio Investigative Site - 5304

Novosibirsk, , Russia

Site Status

Viela Bio Investigative Site - 5311

Rostov-on-Don, , Russia

Site Status

Viela Bio Investigative Site - 5309

Rostov-on-Don, , Russia

Site Status

Viela Bio Investigative Site - 5308

Saint Petersburg, , Russia

Site Status

Viela Bio Investigative Site - 5305

Samara, , Russia

Site Status

Viela Bio Investigative Site - 5312

Ufa, , Russia

Site Status

Viela Bio Investigative Site - 4202

Seoul, , South Korea

Site Status

Viela Bio Investigative Site - 4203

Seoul, , South Korea

Site Status

Viela Bio Investigative Site - 4201

Seoul, , South Korea

Site Status

Viela Bio Investigative Site - 3403

Badalona, , Spain

Site Status

Viela Bio Investigative Site - 3402

Barcelona, , Spain

Site Status

Viela Bio Investigative Site - 3404

Córdoba, , Spain

Site Status

Viela Bio investigative Site - 4605

Kaohsiung City, , Taiwan

Site Status

Viela Bio Investigative Site 4608

New Taipei City, , Taiwan

Site Status

Viela Bio Investigative Site - 4606

Tainan City, , Taiwan

Site Status

Viela Bio Investigative Site - 4604

Taipei, , Taiwan

Site Status

Viela Bio Investigative Site - 4603

Taipei, , Taiwan

Site Status

Viela Bio Investigative Site -4607

Taipei, , Taiwan

Site Status

Viela Bio Investigative Site - 4602

Taoyuan, , Taiwan

Site Status

Viela Bio Investigative Site - 3903

Ankara, , Turkey (Türkiye)

Site Status

Viela Bio Investigative Site - 3901

Izmir, , Turkey (Türkiye)

Site Status

Viela Bio Investigative Site - 3902

Izmir, , Turkey (Türkiye)

Site Status

Viela Bio Investigative Site - 3905

Kocaeli, , Turkey (Türkiye)

Site Status

Viela Bio Investigative Site - 5103

Dnipro, , Ukraine

Site Status

Viela Bio Investigative Site - 5108

Dnipro, , Ukraine

Site Status

Viela Bio Investigative Site - 5105

Ivano-Frankivsk, , Ukraine

Site Status

Viela Bio Investigative Site - 5104

Lutsk, , Ukraine

Site Status

Viela Bio Investigative Site - 5106

Vinnytsia, , Ukraine

Site Status

Countries

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United States Argentina Belarus Brazil Canada China Denmark France Germany India Italy Japan Poland Russia South Korea Spain Taiwan Turkey (Türkiye) Ukraine

References

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Nowak RJ, Benatar M, Ciafaloni E, Howard JF Jr, Leite MI, Utsugisawa K, Vissing J, Rojavin M, Li Q, Tang F, Wu Y, Rampal N, Cheng S; MINT Investigators. A Phase 3 Trial of Inebilizumab in Generalized Myasthenia Gravis. N Engl J Med. 2025 Jun 19;392(23):2309-2320. doi: 10.1056/NEJMoa2501561. Epub 2025 Apr 8.

Reference Type DERIVED
PMID: 40202593 (View on PubMed)

Related Links

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http://www.amgentrials.com

AmgenTrials clinical trials website

Other Identifiers

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VIB0551.P3.S1

Identifier Type: -

Identifier Source: org_study_id

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