Efficacy and Safety of Bimagrumab/BYM338 at 52 Weeks on Physical Function, Muscle Strength, Mobility in sIBM Patients

NCT ID: NCT01925209

Last Updated: 2017-08-11

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2/PHASE3

Total Enrollment

251 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-09-26

Study Completion Date

2016-01-06

Brief Summary

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This study evaluated the efficacy, safety and tolerability of multiple doses of bimagrumab/BYM338 vs placebo, when administered intravenously (i.v.), on physical function, muscle strength, and mobility in patients with sporadic inclusion body myositis (sIBM).

Detailed Description

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Conditions

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Sporadic Inclusion Body Myositis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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BYM338/bimagrumab 10 mg/kg

Participants received study medication with BYM338 at 10 mg/kg from Day 1 to Week 52 and up to Week 104, administered by intravenous (i.v.) infusion every 4 weeks.

Group Type EXPERIMENTAL

BYM338/bimagrumab

Intervention Type DRUG

BYM338, a 150 mg/mL concentrate for solution for i.v. infusion, was provided in colorless glass vials with a rubber stopper and aluminum flip-off caps.

BYM338/bimagrumab 3 mg/kg

Participants received study medication with BYM338 at 3 mg/kg from Day 1 to Week 52 and up to Week 104, administered by i.v. infusion every 4 weeks.

Group Type EXPERIMENTAL

BYM338/bimagrumab

Intervention Type DRUG

BYM338, a 150 mg/mL concentrate for solution for i.v. infusion, was provided in colorless glass vials with a rubber stopper and aluminum flip-off caps.

BYM338/bimagrumab 1 mg/kg

Participants received study medication with BYM338 at 1 mg/kg from Day 1 to Week 52 and up to Week 104, administered by i.v. infusion every 4 weeks.

Group Type EXPERIMENTAL

BYM338/bimagrumab

Intervention Type DRUG

BYM338, a 150 mg/mL concentrate for solution for i.v. infusion, was provided in colorless glass vials with a rubber stopper and aluminum flip-off caps.

Placebo

Participants received matching placebo to BYM338 from Day 1 to Week 52 and up to Week 104, administered by i.v. infusion every 4 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching placebo to BYM338 was provided in colorless glass vials with a rubber stopper and aluminum flip-off caps.

Interventions

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BYM338/bimagrumab

BYM338, a 150 mg/mL concentrate for solution for i.v. infusion, was provided in colorless glass vials with a rubber stopper and aluminum flip-off caps.

Intervention Type DRUG

Placebo

Matching placebo to BYM338 was provided in colorless glass vials with a rubber stopper and aluminum flip-off caps.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Diagnosed with sporadic inclusion body myositis;
* Must be able to walk (assistive aids allowed, including intermittent use of wheelchair);

Exclusion Criteria

* Must not have other conditions that significantly limit ability to move around;
* Must not be using corticosteroids. Must not have used systemic corticosteroid (at daily dose \>=10mg prednisone) for the past 3 months;
* Must meet cardiovascular requirements;
* Must not be pregnant or nursing;
* Must not have a chronic active infection (e.g., HIV, hepatitis B or C, tuberculosis, etc.);
Minimum Eligible Age

36 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Novartis Investigative Site

Phoenix, Arizona, United States

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Orange, California, United States

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Sacramento, California, United States

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Miami, Florida, United States

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Kansas City, Kansas, United States

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Baltimore, Maryland, United States

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Boston, Massachusetts, United States

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Boston, Massachusetts, United States

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Columbus, Ohio, United States

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Portland, Oregon, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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St Leonards, New South Wales, Australia

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Cauldfield, Victoria, Australia

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Nedlands, Western Australia, Australia

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Brussels, , Belgium

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Edegem, , Belgium

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Ghent, , Belgium

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Copenhagen, , Denmark

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Paris, , France

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Brescia, BS, Italy

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Rome, Lazio, Italy

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Messina, ME, Italy

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Milan, MI, Italy

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Padua, PD, Italy

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Nagoya, Aichi-ken, Japan

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Kumamoto, Kumamoto, Japan

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Sendai, Miyagi, Japan

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Osaka, Osaka, Japan

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Tokushima, Tokushima, Japan

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Kodaira, Tokyo, Japan

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Wakayama, Wakayama, Japan

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Amsterdam, , Netherlands

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Leiden, , Netherlands

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Zurich, , Switzerland

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Salford, Manchester, United Kingdom

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London, , United Kingdom

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Novartis Investigative Site

Newcastle upon Tyne, , United Kingdom

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Countries

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United States Australia Belgium Denmark France Italy Japan Netherlands Switzerland United Kingdom

References

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Hanna MG, Badrising UA, Benveniste O, Lloyd TE, Needham M, Chinoy H, Aoki M, Machado PM, Liang C, Reardon KA, de Visser M, Ascherman DP, Barohn RJ, Dimachkie MM, Miller JAL, Kissel JT, Oskarsson B, Joyce NC, Van den Bergh P, Baets J, De Bleecker JL, Karam C, David WS, Mirabella M, Nations SP, Jung HH, Pegoraro E, Maggi L, Rodolico C, Filosto M, Shaibani AI, Sivakumar K, Goyal NA, Mori-Yoshimura M, Yamashita S, Suzuki N, Katsuno M, Murata K, Nodera H, Nishino I, Romano CD, Williams VSL, Vissing J, Auberson LZ, Wu M, de Vera A, Papanicolaou DA, Amato AA; RESILIENT Study Group. Safety and efficacy of intravenous bimagrumab in inclusion body myositis (RESILIENT): a randomised, double-blind, placebo-controlled phase 2b trial. Lancet Neurol. 2019 Sep;18(9):834-844. doi: 10.1016/S1474-4422(19)30200-5.

Reference Type DERIVED
PMID: 31397289 (View on PubMed)

Other Identifiers

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CBYM338B2203

Identifier Type: -

Identifier Source: org_study_id

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