A Study of Nipocalimab Administered to Adults With Generalized Myasthenia Gravis

NCT ID: NCT04951622

Last Updated: 2025-11-13

Study Results

Results available

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Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

219 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-07-15

Study Completion Date

2026-04-17

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of nipocalimab compared to placebo in participants with generalized myasthenia gravis (gMG). The purpose of the U.S. substudy is to evaluate how well it works in the body (pharmacodynamic \[PD\]) when given as an injection under the skin (subcutaneous) compared to when given through a vein (intravenous) in participants with gMG.

Detailed Description

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Conditions

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Myasthenia Gravis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Nipocalimab

Double-blind Placebo-controlled Phase: Participants will receive nipocalimab intravenous (IV) infusions once every 2 weeks (q2w) up to 24 weeks during double-blind placebo-controlled phase.

Open-label Extension (OLE) Phase: Participants who complete the double-blind placebo-controlled phase will enter the OLE phase and continue to receive nipocalimab q2w IV infusion till study end.

Group Type EXPERIMENTAL

Nipocalimab

Intervention Type DRUG

Nipocalimab will be administered as an IV infusion.

Placebo

Double-blind Placebo-controlled Phase: Participants will receive matching placebo of nipocalimab IV infusion q2w up to 24 weeks during double-blind placebo-controlled phase.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching placebo will be administered as an IV infusion.

Nipocalimab Subcutaneous (SC)

OLE Phase: Participants from Cohort 1 will receive nipocalimab subcutaneous liquid in vial (SC-LIV) qw until Week 8. Participants with gMG from Cohort 2 who have not received nipocalimab previously, will receive nipocalimab SC-LIV until Week 8. Participants who complete the 8-week treatment period will have the opportunity to continue receiving nipocalimab SC-LIV qw in the Long term extension (LTE) period.

Group Type EXPERIMENTAL

Nipocalimab SC-LIV

Intervention Type DRUG

Nipocalimab will be administered subcutaneously.

Interventions

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Nipocalimab

Nipocalimab will be administered as an IV infusion.

Intervention Type DRUG

Placebo

Matching placebo will be administered as an IV infusion.

Intervention Type DRUG

Nipocalimab SC-LIV

Nipocalimab will be administered subcutaneously.

Intervention Type DRUG

Other Intervention Names

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JNJ-80202135, M281

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of myasthenia gravis (MG) with generalized muscle weakness meeting the clinical criteria for generalized myasthenia gravis (gMG) as defined by the Myasthenia Gravis Foundation of America (MGFA) Clinical Classification Class II a/b, III a/b, or IVa/b at screening
* Myasthenia Gravis - Activities of Daily Living (MG-ADL) score of greater than or equal to (\>=) 6 at screening and baseline
* Has sufficient venous access to allow drug administration by infusion and blood sampling as per the protocol
* A woman of childbearing potential must have a negative highly sensitive serum (beta-human chorionic gonadotropin \[beta-hCG\]) at screening and a negative urine pregnancy test at Day 1 prior to administration of study intervention
* A male participant must agree not to donate sperm for the purpose of reproduction during the study and for a minimum 90 days after receiving the last administration of study intervention
* For the SC Substudy (Cohort 1): Has reasonable abdominal skin area for SC administration
* For the SC Substudy (Cohort 1): Participants must be willing to comply with maintaining their stable dose of corticosteroids and/or immunosuppressants for the initial 8 weeks of the SC substudy, that is, through the SC Week 8 visit

Exclusion Criteria

* Has any confirmed or suspected clinical immunodeficiency syndrome not related to treatment of his/her gMG, or has a family history of congenital or hereditary immunodeficiency unless confirmed absent in the participant
* Has MGFA Class I disease or presence of MG crisis (MGFA Class V) at screening, history of MG crisis within 1 month of screening, or fixed weakness (and/or 'burnt out' MG)
* Has had a thymectomy within 12 months prior to screening, or thymectomy is planned during the study
* Has known allergies, hypersensitivity, or intolerance to nipocalimab or its excipients
* Has experienced myocardial infarction, unstable ischemic heart disease, or stroke within 12 weeks of screening
* For the SC Substudy (Cohort 1): Participants who have undergone a recent tapering of their concomitant MG medication in the OLE
* For the SC Substudy (Cohort 1): Participants actively deteriorating at the SC Dose 1 visit for the SC substudy such that they meet the criteria for Clinical Deterioration
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Janssen Research & Development, LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Janssen Research & Development, LLC Clinical Trial

Role: STUDY_DIRECTOR

Janssen Research & Development, LLC

Locations

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Neuromuscular Research Center and Clinic

Paradise Valley, Arizona, United States

Site Status

HonorHealth Neurology

Scottsdale, Arizona, United States

Site Status

University of Southern California

Los Angeles, California, United States

Site Status

Stanford University

Palo Alto, California, United States

Site Status

Care Access Research

Pasadena, California, United States

Site Status

University of Colorado Anschutz Medical Campus

Aurora, Colorado, United States

Site Status

Yale New Haven Hospital

New Haven, Connecticut, United States

Site Status

FM Clinical Research, LLC South Florida Neurology Associates, P. A.

Boca Raton, Florida, United States

Site Status

University of Florida Health Jacksonville

Jacksonville, Florida, United States

Site Status

Medsol Clinical Research Center Inc

Port Charlotte, Florida, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

Augusta University

Augusta, Georgia, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

St. Elizabeth Medical Center

Boston, Massachusetts, United States

Site Status

Lahey Hospital & Medical Center

Burlington, Massachusetts, United States

Site Status

Washington University School Of Medicine

St Louis, Missouri, United States

Site Status

Duke University School of Medicine

Durham, North Carolina, United States

Site Status

University of Cincinnati

Cincinnati, Ohio, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

The Ohio State University

Columbus, Ohio, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Wesley Neurology

Cordova, Tennessee, United States

Site Status

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status

University of Vermont

Burlington, Vermont, United States

Site Status

Melbourne Neurology Group

North Melbourne, , Australia

Site Status

Gold Coast University Hospital

Southport, , Australia

Site Status

ULB Hôpital Erasme

Anderlecht, , Belgium

Site Status

AZ Sint Jan Brugge Oostende AV

Bruges, , Belgium

Site Status

Cliniques Universitaires Saint Luc

Brussels, , Belgium

Site Status

AZ Sint-Lucas

Ghent, , Belgium

Site Status

University Hospitals Leuven

Leuven, , Belgium

Site Status

The Ottawa Hospital Research Institute

Ottawa, Ontario, Canada

Site Status

Toronto General Hospital

Toronto, Ontario, Canada

Site Status

McGill University

Montreal, Quebec, Canada

Site Status

Beijing Tiantan Hospital, Capital Medical University

Beijing, , China

Site Status

Xuanwu Hospital ,Capital Medical University

Beijing, , China

Site Status

Beijing Hospital

Beijing, , China

Site Status

The First Bethune Hospital of Jilin University

Changchun, , China

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Xiangya Hospital Central South University

Changsha, , China

Site Status

West China Hospital of Sichuan University

Chengdu, , China

Site Status

Fujian Medical University Union Hospital

Fuzhou, , China

Site Status

The First Affiliated Hospital of Guangzhou University of Traditional Chinese Medicine

Guangzhou, , China

Site Status

Sir Run Run Shaw Hospital Zhejiang University School of Medicine

Hangzhou, , China

Site Status

Qianfoshan hospital of Shandong Province

Jinan, , China

Site Status

Qilu Hospital of Shandong University

Jinan, , China

Site Status

Huashan Hospital Fudan University

Shanghai, , China

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Tianjin Medical University General Hospital

Tianjin, , China

Site Status

The Second Affiliated Hospital of Air Force Medical University - Tangdu Hospital

Xi'an, , China

Site Status

Neurologie a rehabilitace Skopalíkova

Brno, , Czechia

Site Status

Fakultni nemocnice Brno

Brno, , Czechia

Site Status

Vseobecna Fakultní Nemocnice

Prague, , Czechia

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Aalborg University Hospital

Aalborg, , Denmark

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Rigshospitalet

København Ø, , Denmark

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Hopital Pierre Wertheimer

Bron, , France

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CHU Grenoble

Grenoble, , France

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Hopital de la Pitie Salpetriere

Paris, , France

Site Status

Hopital PASTEUR

Provence-Alpes-Côte d'Azur, , France

Site Status

NeuroCure Clinical Research Center

Berlin, , Germany

Site Status

Universitatsmedizin Gottingen

Göttingen, , Germany

Site Status

Universitaetsklinikum Leipzig

Leipzig, , Germany

Site Status

Universitatsklinikum Schleswig Holstein Campus Lubeck

Lübeck, , Germany

Site Status

Universitatsklinikum Ulm

Ulm, , Germany

Site Status

DKD HELIOS Klinik Wiesbaden, Fachbereich Neurologie

Wiesbaden, , Germany

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U.O.P.I. di Psichiatria

Catania, , Italy

Site Status

Fondazione Istituto G. Giglio

Cefalù, , Italy

Site Status

Istituto Neurologico Carlo Besta

Milan, , Italy

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Azienda Ospedaliera Univ.- Università Degli studi della Campania - Luigi Vanvitelli

Napoli, , Italy

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IRCCS C. Mondino, Istituto Neurologico Nazionale, Fondazione

Pavia, , Italy

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Azienda ospedaliera Sant'Andrea di Roma- Università di Roma La Sapienza

Roma, , Italy

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Policlinico Universitario Agostino Gemelli

Roma, , Italy

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Chiba University Hospital

Chiba, , Japan

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General Hanamaki Hospital

Hanamaki, , Japan

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Hiroshima University Hospital

Hiroshima, , Japan

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Teikyo University Hospital

Itabashi Ku, , Japan

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St Marianna University Hospital

Kawasaki Shi, , Japan

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Kagawa University Hospital

Kita Gun, , Japan

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Kumamoto University Hospital

Kumamoto, , Japan

Site Status

Iwate Medical University Hospital

Morioka, , Japan

Site Status

National Hospital Organization Nagoya Medical Center

Nagoya, , Japan

Site Status

Niigata City General Hospital

Niigata, , Japan

Site Status

Hyogo College of Medicine Hospital

Nishinomiya-Shi, , Japan

Site Status

Sapporo Medical University Hospital

Sapporo, , Japan

Site Status

Hokkaido Medical Center

Sapporo, , Japan

Site Status

National Hospital Organization Sendai Medical Center

Sendai, , Japan

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Tokushima University Hospital

Tokushima, , Japan

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Tokyo Medical University Hospital

Tokyo, , Japan

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iBiomed Research Unit

Aguascalientes, , Mexico

Site Status

Consultorio Dr. Miguel Cortes

Cuernavaca, , Mexico

Site Status

Hospital Civil de Guadalajara Fray Antonio Alcalde

Guadalajara, , Mexico

Site Status

Neurocentrum Bydgoszcz Sp Z O O

Bydgoszcz, , Poland

Site Status

NZOZ Wielospecjalistyczna Poradnia Lekarska 'Synapsis'

Katowice, , Poland

Site Status

Centrum Neurologii Klinicznej Krakowska Akademia Neurologii

Krakow, , Poland

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Prywatny Gabinet Lekarski

Lublin, , Poland

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Centrum Medyczne NeuroProtect

Warsaw, , Poland

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Pusan National University Hospital

Busan, , South Korea

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Kyungpook National University Chilgok Hospital

Daegu, , South Korea

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Kyungpook National University Hospital

Daegu, , South Korea

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Severance Hospital Yonsei University Health System

Seoul, , South Korea

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Hosp. Gral. Univ. de Alicante

Alicante, , Spain

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Hosp. de La Santa Creu I Sant Pau

Barcelona, , Spain

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Hosp Univ Vall D Hebron

Barcelona, , Spain

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Hosp Clinic de Barcelona

Barcelona, , Spain

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Hosp. Univ. de Basurto

Bilbao, , Spain

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Hosp. Virgen Macarena

Seville, , Spain

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Hosp. Virgen Del Rocio

Seville, , Spain

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Hosp. Univ. I Politecni La Fe

Valencia, , Spain

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Karlstad Central Hospital

Karlstad, , Sweden

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Karolinska Universitetssjukhuset Solna

Stockholm, , Sweden

Site Status

China Medical University Hospital

Taichung, , Taiwan

Site Status

Shin Kong Wu Ho Su Memorial Hospital

Taipei, , Taiwan

Site Status

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status

Countries

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Colombia Russia Turkey (Türkiye) United Kingdom United States Australia Belgium Canada China Czechia Denmark France Germany Italy Japan Mexico Poland South Korea Spain Sweden Taiwan

References

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Antozzi C, Fitzgibbon M. An evaluation of nipocalimab for the treatment of generalized myasthenia gravis. Expert Opin Biol Ther. 2025 Sep 30:1-12. doi: 10.1080/14712598.2025.2561935. Online ahead of print.

Reference Type DERIVED
PMID: 41021216 (View on PubMed)

Raborn A, Savord A, Houts CR, Pease S, Scippa K, Ramchandren S. Psychometric analysis of the Neuro-QoL Fatigue in generalized Myasthenia Gravis (gMG) using data from a phase 3 trial. Qual Life Res. 2025 Sep;34(9):2577-2589. doi: 10.1007/s11136-025-03998-9. Epub 2025 Jun 14.

Reference Type DERIVED
PMID: 40515798 (View on PubMed)

Antozzi C, Vu T, Ramchandren S, Nowak RJ, Farmakidis C, Bril V, De Bleecker J, Yang H, Minks E, Park JS, Grudniak M, Smilowski M, Sevilla T, Hoffmann S, Sivakumar K, Suzuki Y, Youssef E, Sanga P, Karcher K, Zhu Y, Sheehan JJ, Sun H; Vivacity-MG3 Study Group. Safety and efficacy of nipocalimab in adults with generalised myasthenia gravis (Vivacity-MG3): a phase 3, randomised, double-blind, placebo-controlled study. Lancet Neurol. 2025 Feb;24(2):105-116. doi: 10.1016/S1474-4422(24)00498-8.

Reference Type DERIVED
PMID: 39862879 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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MOM-M281-011

Identifier Type: OTHER

Identifier Source: secondary_id

2020-005732-29

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2023-504152-97-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

CR109046

Identifier Type: -

Identifier Source: org_study_id