A Head-to-head Study Comparing the Functional Value of Two Models of Robotically Assisted Rehabilitation in SMA (Spinal Muscular Atrophy) Patients

NCT ID: NCT06322654

Last Updated: 2024-03-21

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

NA

Total Enrollment

200 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-12-21

Study Completion Date

2027-07-31

Brief Summary

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A head-to-head study comparing the functional value of two models of robotically assisted rehabilitation in patients with SMA. A single-center, randomized, single-blinded, comparative study of Robotically Assisted Verticalization versus Robotically Assisted Locomotion.

The objective of research:

The main goal of the project is to determine the optimal robotically assisted rehabilitation model for people with SMA depending on age and baseline functional status. The study consists of a head-to-head comparison of two rehabilitation models.

1. Research period: 4 years
2. Patients age: 0-21 y.o.
3. Group size: 200 patients (100 patients in each group)
4. Assignment of patients to study groups in a randomised manner

Detailed Description

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Conditions

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SMA

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

There are two research groups with 100 patients in each group.

1. Experimental: Robotically Assisted Locomotion
2. Comparison: Robotically Assisted Verticalization
Primary Study Purpose

SUPPORTIVE_CARE

Blinding Strategy

SINGLE

Investigators
Patients and their parents will not be blinded by the nature of the therapeutic procedure used after random allocation to the treatment group. Study personnel will be divided into Blinded Team and Unblinded Team to ensure objectivity of the assessment of safety and effectiveness of both strategies.

Study Groups

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Robotically Assisted Locomotion

Group Type EXPERIMENTAL

Robotically Assisted Locomotion

Intervention Type PROCEDURE

* Motor control training
* Locomotion and motor control training with elements of balance and coordination
* Verticalization training: standing frame device and vibration platform
* Cognitive therapy

Robotically Assisted Verticalization

Group Type ACTIVE_COMPARATOR

Robotically Assisted Verticalization

Intervention Type PROCEDURE

* Motor control training
* Verticalization training with Standard Frame Devices
* Locomotion and motor control training with elements of balance and coordination
* Cognitive therapy

Interventions

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Robotically Assisted Locomotion

* Motor control training
* Locomotion and motor control training with elements of balance and coordination
* Verticalization training: standing frame device and vibration platform
* Cognitive therapy

Intervention Type PROCEDURE

Robotically Assisted Verticalization

* Motor control training
* Verticalization training with Standard Frame Devices
* Locomotion and motor control training with elements of balance and coordination
* Cognitive therapy

Intervention Type PROCEDURE

Eligibility Criteria

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Inclusion Criteria

* Signing of informed consent to participate in the experiment by the participant or the participant's parent/legal guardian
* Diagnosis of SMA (spinal muscular atrophy 1-4) confirmed by genetic testing, symptomatic or pre-symptomatic
* Age between 0 and 21 years of age (will be determined on the day of starting participation in the project based on the date of birth)
* Treatment under a drug program for spinal muscular atrophy, provided that the patient has a diagnosis of spinal muscular atrophy at the date of eligibility.

Exclusion Criteria

* Cardio-respiratory disorders requiring invasive ventilation
* Advanced osteoporosis with multiple fractures prior to treatment
* Functional deterioration during the rehabilitation process in the range of scales appropriately selected for the SMA type: Prechtl, HINE, CHOP-INTEND, HFMS, RULM
* Lack of cooperation with the therapist
* Other functional indications preventing exercise
Maximum Eligible Age

21 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Wiktor Dega University Orthopedic and Rehabilitation Hospital

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Marek Jóźwiak

Role: PRINCIPAL_INVESTIGATOR

Wiktor Dega University Orthopedic and Rehabilitation Hospital

Locations

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Wiktor Dega University Orthopedic and Rehabilitation Hospital

Poznan, , Poland

Site Status RECRUITING

Countries

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Poland

Central Contacts

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Marek Jóźwiak

Role: CONTACT

696052475 ext. +48

Radosław Rutkowski

Role: CONTACT

696052475

Facility Contacts

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Marek Jóźwiak

Role: primary

696052475 ext. +48

Radosław Rutkowski

Role: backup

696052475

Other Identifiers

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2023/ABM/01/00004/P/02

Identifier Type: -

Identifier Source: org_study_id

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