A Study to Evaluate the Safety, Tolerability, PK, and PD Properties of PRX-115 in Adult Volunteers With Elevated Uric Acid Levels

NCT ID: NCT05745727

Last Updated: 2025-02-11

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

64 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-03-23

Study Completion Date

2025-02-06

Brief Summary

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This is a Phase 1, double-blind, placebo-controlled, single ascending dose study in participants with elevated uric acid levels. This study will be conducted in approximately 64 adult male and female participants in the dose escalation phase.

Detailed Description

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Participants will be assigned to 1 of 8 sequential dosing cohorts, each composed of 8 participants (6 active + 2 placebo) who will receive a single dose of PRX-115 or placebo by intravenous (IV) infusion.

Conditions

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Gout

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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PRX-115

Participants will receive a single dose of PRX-115 by IV infusion

Group Type EXPERIMENTAL

PRX-115

Intervention Type DRUG

Escalating doses of PRX-115 will be given in different cohorts i.e., Cohorts 1 through 8

Placebo

Participants will receive a single dose of placebo by IV infusion

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Escalating doses of Placebo will be given in different cohorts i.e., Cohorts 1 through 8

Interventions

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PRX-115

Escalating doses of PRX-115 will be given in different cohorts i.e., Cohorts 1 through 8

Intervention Type DRUG

Placebo

Escalating doses of Placebo will be given in different cohorts i.e., Cohorts 1 through 8

Intervention Type DRUG

Other Intervention Names

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Escalating doses of PRX-115 Placebo to match

Eligibility Criteria

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Inclusion Criteria

1. Males or females 18 to 65 years of age, inclusive.
2. Serum uric acid greater than 6.0 mg/dL (0.35 mmol/L) at the Screening visit.
3. Body mass index within the range 18.5 to 40 kg/m\^2, inclusive, at the Screening visit.
4. Women of childbearing potential may be included only if they have a negative beta human chorionic gonadotropin (β-hCG) test result at Screening.
5. Men and women of childbearing potential and their partners should use double barrier contraception.

Exclusion Criteria

1. Has any condition known to have arthritis as a clinical manifestation
2. Had greater than or equal to 1 gout flare in the last year prior to either Screening or Day -1.
3. Has clinical evidence of subcutaneous tophi at either Screening or Day -1.
4. Estimated glomerular filtration rate (eGFR) value less than or equal to 60 mL/min/1.73m\^2
5. History of significant renal disease, and/or presence of renal stones at either Screening or Day -1.
6. Has a history of anaphylaxis, severe allergic reactions, or severe atopy.
7. History of autoimmune disorders, and/or participant is immunocompromised or treated with immunosuppressive medications.
8. Has evidence of cardiovascular or cerebrovascular disease.
9. History of congestive heart failure, New York Heart Association Class III or IV.
10. BP outside the range of 90 to 150 mm Hg for systolic or 50 to 95 mm Hg for diastolic.
11. Participants with hypertension who are not on stable medication for at least 6 months.
12. Has uncontrolled type 2 diabetes
13. Concurrent treatment with urate lowering drugs (ULDs).
14. Prior exposure to any experimental or marketed uricase (eg, rasburicase \[Elitek, Fasturtec\], pegloticase \[Krystexxa®\], pegadricase \[SEL-212\]).
15. Glucose-6-phosphate dehydrogenase (G6PD) deficiency or known catalase deficiency.
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Protalix

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Mark Marshall, Dr.

Role: PRINCIPAL_INVESTIGATOR

New Zealand Clinical Research

Locations

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New Zealand Clinical Research

Grafton, Auckland, New Zealand

Site Status

New Zealand Clinical Research

Christchurch, Christchurch, New Zealand

Site Status

Countries

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New Zealand

Other Identifiers

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PB115-SAD-101

Identifier Type: -

Identifier Source: org_study_id

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