Placebo Controlled, Dose Escalation Study to Evaluate Safety, Pharmacokinetics & Efficacy of SAP-001 in Gout Patients

NCT ID: NCT03857165

Last Updated: 2021-10-14

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

24 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-09-24

Study Completion Date

2019-10-31

Brief Summary

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This is a Phase I, Multicenter, Randomized, Double-blind, Placebo controlled, Dose-escalation study to evaluate Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of SAP-001 in Gout Patients with Hyperuricemia. The study will be single dose ascending cohorts across three doses with a placebo control arm.

Detailed Description

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A total of 24 eligible adult subjects will be randomized in a 3:1 randomization ratio into two blinded treatment groups in the three dose cohorts with matching placebo arm. The duration of the observation would be 5 days for each subject with a single SAP-001 dosing to evaluate safety, tolerability, pharmacokinetics (PK), pharmacodynamics (PD) and efficacy of oral SAP-001 (once daily) in adults gout patients with hyperuricemia.

Conditions

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Gout, Hyperuricemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Single ascending dose with placebo control
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Double blind

Study Groups

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Low dose SAP-001

SAP-001 (Experimental drug) low dose versus placebo

Group Type EXPERIMENTAL

SAP-001

Intervention Type DRUG

SAP-001 or placebo treatment in a 3:1 randomization ratio.

Mid dose SAP-001

SAP-001 (Experimental drug) mid dose versus placebo

Group Type EXPERIMENTAL

SAP-001

Intervention Type DRUG

SAP-001 or placebo treatment in a 3:1 randomization ratio.

High dose SAP-001

SAP-001 (Experimental drug) high dose versus placebo

Group Type EXPERIMENTAL

SAP-001

Intervention Type DRUG

SAP-001 or placebo treatment in a 3:1 randomization ratio.

Interventions

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SAP-001

SAP-001 or placebo treatment in a 3:1 randomization ratio.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Male or female, between 18 and 75 years of age, inclusive.
2. Body mass index (BMI) between 19 and 42 kg/m\^2 at screening, inclusive.
3. Serum uric acid (sUA) levels ≥7.5 mg/dL at screening.
4. Patients must meet all the American College of Rheumatology scoring criteria for the classification of primary gout (Neogi et al., 2015).
5. Patients who are not taking any UA-lowering medications 1 month prior to the dose of study drug.
6. Is a nonsmoker or light smoker (smokes fewer than 10 cigarettes per day).
7. Female patients cannot be pregnant or lactating/breast-feeding and will either be postmenopausal (female patients who state they are postmenopausal should have had cessation of menses for\>1 year and have serum follicle stimulating hormone \[FSH\] levels \>40 mIU/mL and serum estradiol \< 20 pg/mL or a negative estrogen test), surgically sterile (including bilateral tubal ligation, salpingectomy \[with or without oophorectomy\], surgical hysterectomy, or bilateral oophorectomy \[with or without hysterectomy\]) for at least 3 months prior to Screening, or will agree to use, from the time of Check-in (Day -1) until 90 days following the last dose of study drug, the following forms of contraception: double-barrier method, hormonal contraceptives, barrier with spermicide, diaphragm or cervical cap with spermicide, intrauterine device, oral, implantable, or injectable contraceptives, or a sterile sexual partner. All female patients will have a negative urine or serum pregnancy test result prior to enrollment in the study.
8. Male patients will either be surgically sterile or agree to use, from the time of Check-in (Day -1) until 90 days following the last dose of study drug, the following forms of contraception: male condom with spermicide and a female partner who is sterile or agrees to use hormonal contraceptives, female condom with spermicide, diaphragm or cervical cap with spermicide, intrauterine device, oral, implantable, or injectable contraceptives. Male patients will refrain from sperm donation from the time of Check-in (Day -1) until 90 days following the last dose of study drug.
9. Is capable of understanding the written informed consent, provides signed and witnessed written informed consent, and agrees to comply with protocol requirements.

Exclusion Criteria

1. Has a history or presence of clinically significant (CS) cardiovascular, renal, pulmonary, hepatic, gallbladder or biliary tract, hematologic, gastrointestinal, endocrine, immunologic, dermatologic, neurologic, or psychiatric disease, which in the Investigator's opinion would not be suitable for the study.
2. Serum creatinine level \> 1.5 mg/dL and/or estimated glomerular filtration (eGFR) by the Modification of Diet in Renal Disease (MDRD) rate ≤60 mL/min/1.73 m2 at screening. The MDRD formula is: GFR (mL/min/1.73 m2) = 175 × (Scr)-1.154 × (Age)-0.203 × (0.742 if female) × (1.212 if African American)
3. History of stomach or intestinal surgery (except that cholecystectomy, appendectomy, and/or hernia repair will be allowed).
4. History of prescription drug abuse, illicit drug use, or alcohol abuse according to medical history within 6 months prior to the Screening visit or any alcohol use for at least 48 hours prior to dosing on Day 1.
5. Positive blood screen for human immunodeficiency virus (HIV), hepatitis B surface antigen (HbsAg), or hepatitis C (HCV) antibody.
6. Clinically significant abnormal liver function test at screening or Check-in (Day -1), defined as aspartate aminotransferase (AST) or alanine aminotransferase (ALT)\>1.5 times upper limit of normal (ULN) or total bilirubin \>ULN; or a history of clinically significant acute or chronic hepatitis (including infectious, metabolic, autoimmune, genetic, ischemic, or other forms), hepatocirrhosis, or hepatic tumors.
7. Positive screen for alcohol or drugs of abuse (except for patients with a positive drug screen test if it is a result of a prescribed medication from their physician) at Screening and Check-in (Day -1).
8. History of a gout flare that is resolved within 14 days prior to first treatment with study drug (exclusive of chronic synovitis/arthritis).
9. Has a known hypersensitivity to URAT1 inhibitors, XOIs, or related compounds.
10. Receipt of any other investigational product within 30 days prior to the dose of study drug on Day 1or planning to take an investigational agent during the study.
11. Concomitant use of or treatment with any prescription drugs, herbal products, vitamins, minerals, and over-the-counter medications within 14 days prior to Check in (Day -1). Exceptions may be made on a case by case basis following discussion and agreement between the Investigator and the Sponsor.
12. Use of any drugs or nutrients known to modulate cytochrome P450 (CYP)3A activity or any strong or moderate inhibitors or inducers of CYP3A4, starting from 14 days prior to dose administration on Day 1 until the final end of study assessments, including but not limited to the following: inhibitors such as ketoconazole, miconazole, itraconazole, fluconazole, atazanavir, erythromycin, clarithromycin, ranitidine, cimetidine, verapamil, and diltiazem and inducers such as rifampicin, rifabutin, glucocorticoids, carbamazepine, phenytoin, phenobarbital, and St. John's wort.
13. Participated in strenuous exercise from 48 hours prior to Check-in (Day -1) or during the study through the final end of study assessment.
14. Has donated or lost a significant volume (\>500 mL) of blood or plasma within 30 days prior to Check-in (Day -1).
15. Malignancy within 5 years of the screening visit.
16. Has problems understanding the protocol requirements, instructions, study related restrictions, and/or problems understanding the nature, scope, and potential consequences of participating in this clinical study.
17. Is unlikely to comply with the protocol requirements, instructions, and/or study related restrictions (e.g., uncooperative attitude, unavailable for follow up call, and/or improbability of completing the clinical study).
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Shanton Pharma Co., Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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John M Hill, MD

Role: PRINCIPAL_INVESTIGATOR

Accel Research Sites (Avail Clinical Research)

Melanie Fein

Role: PRINCIPAL_INVESTIGATOR

High Point Clinical Trials Center

Peter Winkle

Role: PRINCIPAL_INVESTIGATOR

Anaheim Clinical Trials, LLC

Locations

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Anaheim Clinical Trials, LLC

Anaheim, California, United States

Site Status

Avail - Accel Research Sites

DeLand, Florida, United States

Site Status

High Point Clinical Trials Center

High Point, North Carolina, United States

Site Status

Countries

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United States

Other Identifiers

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SAP001-1-001

Identifier Type: OTHER

Identifier Source: secondary_id

SAP-001

Identifier Type: -

Identifier Source: org_study_id