Observational Study of the Use of Pegloticase (KRYSTEXXA®) in Refractory Chronic Gout

NCT ID: NCT01466166

Last Updated: 2019-01-11

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

188 participants

Study Classification

OBSERVATIONAL

Study Start Date

2011-11-15

Study Completion Date

2017-06-30

Brief Summary

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The primary purpose of this study is to observe patients being treated with pegloticase in a standard healthcare setting in order to evaluate the frequency and severity of infusion reactions, anaphylaxis and immune complex related events. Additionally, serious adverse events associated with pegloticase therapy will be identified.

Detailed Description

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This was a Phase 4, multicenter, open-label, single-arm observational study of pegloticase 8 mg administered intravenously every 2 weeks in adult hyperuricemic patients with gout refractory to conventional therapy. Study duration is approximately 63 weeks, including 51 weeks of treatment and 12 weeks of follow-up.

The design of this study follows the FDA-approved Full Prescribing Information for the use of pegloticase and allows for capturing additional data related to the safety and efficacy of pegloticase within the standard healthcare setting.

Conditions

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Refractory Chronic Gout

Study Design

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Observational Model Type

CASE_ONLY

Study Time Perspective

PROSPECTIVE

Study Groups

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Pegloticase

Participants received pegloticase 8 mg by intravenous (IV) infusion every 2 weeks for up to 1 year, as prescribed by their treating physician.

Pegloticase

Intervention Type BIOLOGICAL

Pegloticase 8 mg intravenous every 2 weeks

Interventions

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Pegloticase

Pegloticase 8 mg intravenous every 2 weeks

Intervention Type BIOLOGICAL

Other Intervention Names

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KRYSTEXXA®

Eligibility Criteria

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Inclusion Criteria

* Adults (age 18 years or more) with chronic gout refractory to conventional therapy, defined as patients who have failed to normalize SUA and whose signs and symptoms are inadequately controlled with xanthine oxidase inhibitors at the maximum medically appropriate dose, or for whom these drugs are contraindicated.
* Patients who have made the decision, along with their treating physician, to begin treatment with KRYSTEXXA.
* Patients who are willing and able to give informed consent and adhere to visit/protocol schedules.

Exclusion Criteria

* Glucose-6-phosphate dehydrogenase (G6PD) deficiency
* Non-compensated congestive heart failure
* Pregnancy or breast feeding
* Prior treatment with pegloticase or another recombinant uricase
* Known allergy to urate oxidase
* Prior treatment or concomitant therapy with a polyethylene glycol (PEG)-conjugated drug
* Recipient of an investigational drug within 4 weeks prior to study drug administration or plans to take an investigational agent during the study
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Horizon Pharma Rheumatology LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Jeffery Nieves, PharmD

Role: STUDY_DIRECTOR

Horizon Pharma Rheumatology LLC

Locations

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Rheumatology Associates, PC

Birmingham, Alabama, United States

Site Status

UAB Rheumatology

Birmingham, Alabama, United States

Site Status

Saadat Ansari, MD, LLC

Huntsville, Alabama, United States

Site Status

Medvin Clinical Research

Covina, California, United States

Site Status

Alliance Clinical Research, LLC

Laguna Hills, California, United States

Site Status

Advanced Medical Research, LLC

Lakewood, California, United States

Site Status

Pacific Arthritis Care Center

Los Angeles, California, United States

Site Status

R Srinivasan, MD, Inc

Monterey Park, California, United States

Site Status

Brigid Freyne, MD, Inc

Murrieta, California, United States

Site Status

Alliance Clinical Research

Poway, California, United States

Site Status

Denver Nephrologists, PC

Denver, Colorado, United States

Site Status

New England Research Associates, LLC

Trumbull, Connecticut, United States

Site Status

Howard University Hospital

Washington D.C., District of Columbia, United States

Site Status

Washington DC Veteran's Affairs Medical Center

Washington D.C., District of Columbia, United States

Site Status

Bay Area Arthritis and Osteoporosis

Brandon, Florida, United States

Site Status

Countryside Arthritis Center

Clearwater, Florida, United States

Site Status

Science and Research Institute, Inc

Jupiter, Florida, United States

Site Status

A & O Research Center

Miami, Florida, United States

Site Status

Arthritis Research of Florida, Inc.

Palm Harbor, Florida, United States

Site Status

Family Clinical Trials, LLC

Pembroke Pines, Florida, United States

Site Status

Jedidiah Clinical Research

Tampa, Florida, United States

Site Status

Midtown Medical Center

Tampa, Florida, United States

Site Status

Global Research Partners & Consultants, Inc.

Calhoun, Georgia, United States

Site Status

Arthritis Research & Treatment Center

Stockbridge, Georgia, United States

Site Status

University of Chicago Medical Center

Chicago, Illinois, United States

Site Status

Diagnostic Rheumatology and Research PC

Indianapolis, Indiana, United States

Site Status

Physicians' Clinic of Iowa, P.C.

Cedar Rapids, Iowa, United States

Site Status

Central Kentucky Research Associates of Kentucky

Mount Sterling, Kentucky, United States

Site Status

Research Integrity, LLC

Owensboro, Kentucky, United States

Site Status

Horizon Research Group of Opelousas, LLC

Eunice, Louisiana, United States

Site Status

Arthritis and Diabetes Clinic, Inc.

Monroe, Louisiana, United States

Site Status

Walter Reed National Military Medical Center

Bethesda, Maryland, United States

Site Status

Klein & Associates MD, PA.

Hagerstown, Maryland, United States

Site Status

The Center for Rheumatology and Bone Research

Wheaton, Maryland, United States

Site Status

Clinical Pharmacology Study Groups

Worcester, Massachusetts, United States

Site Status

Reliant Medical Group, Inc.

Worcester, Massachusetts, United States

Site Status

University of Michigan Health System

Ann Arbor, Michigan, United States

Site Status

Caro Health Plaza

Caro, Michigan, United States

Site Status

Infusion Associates

Grand Rapids, Michigan, United States

Site Status

Justus J. Fiechtner, MD, PC

Lansing, Michigan, United States

Site Status

Shores Rheumatology, PC

Saint Clair Shores, Michigan, United States

Site Status

Saint Paul Rheumatology, PA

Eagan, Minnesota, United States

Site Status

Kansas City Internal Medicine

Kansas City, Missouri, United States

Site Status

Arthritis Medical Clinic

Las Vegas, Nevada, United States

Site Status

Rheumatology Associates of North Jersey

Teaneck, New Jersey, United States

Site Status

Rheumatology Associates of Long Island

Smithtown, New York, United States

Site Status

NorthEast Rheumatology

Concord, North Carolina, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

Physicians East, PA

Greenville, North Carolina, United States

Site Status

Shanahan Rheumatology and Immunotherapy, PLLC

Raleigh, North Carolina, United States

Site Status

Specialty Medical Clinic and Research Center

Sanford, North Carolina, United States

Site Status

Southern Ohio Rheumatology

Portsmouth, Ohio, United States

Site Status

Keystone Pain Institute, Ilumina Clinical Associates

Altoona, Pennsylvania, United States

Site Status

Penn State Milton S. Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

Low Country Rheumatology

Charleston, South Carolina, United States

Site Status

Acme Research L.L.C.

Orangeburg, South Carolina, United States

Site Status

Ramesh C. Gupta, M.D.

Memphis, Tennessee, United States

Site Status

Austin Regional Clinic

Austin, Texas, United States

Site Status

Dr. Raj Marwah

El Paso, Texas, United States

Site Status

Diagnostic Clinic of Houston

Houston, Texas, United States

Site Status

Rheumatic Disease Clinical Research Center

Houston, Texas, United States

Site Status

Arthritis Clinic of Northern Virginia, P.C.

Arlington, Virginia, United States

Site Status

Arthritis & Osteoporosis Center of North Virginia

Manassas, Virginia, United States

Site Status

Sentara Rheumatology Specialists

Norfolk, Virginia, United States

Site Status

Apex Clinical Research

Kennewick, Washington, United States

Site Status

Mountain State Clinical Research

Clarksburg, West Virginia, United States

Site Status

Rheumatic Disease Center, LLP

Glendale, Wisconsin, United States

Site Status

Countries

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United States

References

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Sundy JS, Baraf HS, Yood RA, Edwards NL, Gutierrez-Urena SR, Treadwell EL, Vazquez-Mellado J, White WB, Lipsky PE, Horowitz Z, Huang W, Maroli AN, Waltrip RW 2nd, Hamburger SA, Becker MA. Efficacy and tolerability of pegloticase for the treatment of chronic gout in patients refractory to conventional treatment: two randomized controlled trials. JAMA. 2011 Aug 17;306(7):711-20. doi: 10.1001/jama.2011.1169.

Reference Type BACKGROUND
PMID: 21846852 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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M0401

Identifier Type: -

Identifier Source: org_study_id

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