A Phase 3 Study of Obexelimab in Patients With IgG4-Related Disease

NCT ID: NCT05662241

Last Updated: 2026-02-04

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

194 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-01-09

Study Completion Date

2029-02-15

Brief Summary

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This study aims to examine the efficacy and safety of obexelimab for the prevention of flare of IgG4-related disease (IgG4-RD)

Detailed Description

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This study consists of a 1-year randomized control period (RCP), followed by an additional 3-year open label extension (OLE) period.

To enter the Screening Period (Day -28 to Day -1), patients must have active IgG4-RD signs/symptoms (i.e., flare) that require steroid therapy. On Day 1, patients will be randomized in a ratio of 1:1 to receive either obexelimab or placebo administered as subcutaneous (SC) injections. All patients will begin a steroid taper on Day 1 to discontinuation by Week 8.

Patients will be monitored for flares during scheduled in clinic visits and any unscheduled visits. The primary endpoint is time to first IgG4-RD flare that requires initiation of rescue therapy in the opinion of the investigator and the Adjudication Committee (AC).

Following the 52-week RCP, patients will have the opportunity to continue in an OLE period where all patients will receive obexelimab. During the OLE, a subset of patients may be eligible to participate in a sub-study evaluating the immune response to vaccination while receiving obexelimab treatment. Patients who do not wish to enroll into the OLE period will return for an in-clinic safety follow-up visit 8 weeks after the Week 52 visit (i.e., Week 60).

Including screening and follow-up, the maximum duration of participation in this study for an individual patient is 224 weeks (i.e., 28-day screening, 52-week RCP, 156-week OLE, and a 12-week follow-up).

Conditions

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IgG4 Related Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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ZB012

Obexelimab administered as an SC injection.

Group Type EXPERIMENTAL

Obexelimab

Intervention Type DRUG

Obexelimab is a monoclonal antibody that co-engages CD19 and FcγRIIb to inhibit B cell activity

Placebo

Placebo administered as an SC injection.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Placebo

Interventions

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Obexelimab

Obexelimab is a monoclonal antibody that co-engages CD19 and FcγRIIb to inhibit B cell activity

Intervention Type DRUG

Placebo

Placebo

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

1. Males and females, ≥ 18 years of age
2. Clinical diagnosis of IgG4-RD
3. Patients must meet the 2019 ACR/EULAR Classification Criteria for IgG4-RD
4. Patients must have active IgG4-RD signs/symptoms (i.e., flare) that require the initiation of GC therapy or the increase in background long-term GC therapy

Exclusion Criteria

1. Has disease in only 1 organ system whose primary manifestation is fibrosis
2. Has received prednisone equivalent given orally at a dose greater than 60 mg/day within the 4 weeks prior to screening or during screening
3. Has received a non-biologic, disease-modifying anti-rheumatological drug or immunosuppressive agent other than GCs within the 2 weeks prior to screening
4. Has received an investigational treatment or direct medical intervention on another clinical study within 12 weeks or \< 5 half-lives of the investigational treatment, whichever is shorter, prior to screening
5. Has received live vaccine or live therapeutic infectious agent within the 2 weeks prior to screening
6. Active tuberculosis or high risk for tuberculosis; hepatitis C infection in absence of curative treatment; evidence of hepatitis B infection
7. Use of B cell depleting or targeting agents within 6 months of randomization
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bristol-Myers Squibb

INDUSTRY

Sponsor Role collaborator

Zenas BioPharma (USA), LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Stanford Medicine

Stanford, California, United States

Site Status

GI PROS Research - Dedicated Research Facility

Naples, Florida, United States

Site Status

Emory Univeristy

Atlanta, Georgia, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Henry Ford Hospital

Detroit, Michigan, United States

Site Status

Hospital Italiano de Buenos Aires

Buenos Aires, , Argentina

Site Status

Artus Health Centre

Vancouver, British Columbia, Canada

Site Status

Center for Clinical Research (Nova Scotia Health)

Halifax, Nova Scotia, Canada

Site Status

Centre Hospitalier Universitaire de Sherbrooke CHUS

Sherbrooke, Quebec, Canada

Site Status

Chinese PLA General Hospital

Beijing, Beijing Municipality, China

Site Status

Peking Union Medical College Hospital

Beijing, Beijing Municipality, China

Site Status

Peking University First Hospital

Beijing, Beijing Municipality, China

Site Status

The Second Hospital of Hebei Medical University

Shijiazhuang, Hebei, China

Site Status

Tongji Hospital, Tongji Medical College of Huazhong University of Science and Technology

Wuhai, Hubei, China

Site Status

Yantai Yuhuangding Hospital

Yantai, Shandong, China

Site Status

Renji Hospital, Shanghai Jiaotong University School of Medicine

Shanghai, Shanghai Municipality, China

Site Status

Shanxi Bethune Hospital

Taiyuan, Shanxi, China

Site Status

West China Hospital of Sichuan University

Chengdu, Sichuan, China

Site Status

Haut-Lévèque Hospital Usn Building South Hospital Group

Pessac, Bordeaux, France

Site Status

Hôpitaux Universitaires de Marseille Timone

Saint-Pierre, Marseille, France

Site Status

Hôpital Beaujon

Paris, , France

Site Status

Hôpital de la Pitié Salpétrière

Paris, , France

Site Status

LMU Klinikum der Universität München

München, Bavaria, Germany

Site Status

Universitätsklinikum Ulm

Ulm, , Germany

Site Status

Ospedale San Giovanni Bosco

Turin, Piedmont, Italy

Site Status

Azienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia

Brescia, , Italy

Site Status

Azienda Ospedaliera Universitaria Meyer Istituto di Ricovero e Cura a Carattere Scientifico

Florence, , Italy

Site Status

Ospedale San Raffaele S.r.l. - PPDS

Milan, , Italy

Site Status

University of Verona

Verona, , Italy

Site Status

Hospital of University of Occupational and Environmental Health

Kitakyushu, Fukuoka, Japan

Site Status

Kanazawa Medical University Hospital

Kokura, Fukuoka, Japan

Site Status

Kanazawa University Hospital

Kanazawa, Ishikawa-ken, Japan

Site Status

Kagawa University Hospital

Hiragi, Kagawa-ken, Japan

Site Status

Shinshu University Hospital

Matsumoto, Nagano, Japan

Site Status

Osaka Metropolitan University Hospital

Osaka, Osaka, Japan

Site Status

Tokyo Metropolitan Cancer and Infectious Diseases Center Komagome Hospital

Bunkyō-Ku, Tokyo, Japan

Site Status

The Institute of Medical Science, The University of Tokyo Hospital

Minato-ku, Tokyo, Japan

Site Status

Keio University Hospital

Shinjuku-Ku, Tokyo, Japan

Site Status

Toyama University Hospital

Toyama, Toyama, Japan

Site Status

Kansai Medical University Hospital

Hirakata, , Japan

Site Status

Hiroshima University Hospital

Hiroshima, , Japan

Site Status

St. Marianna University Hospital

Kawasaki, , Japan

Site Status

Tokyo Medical Center Hospital

Meguro City, , Japan

Site Status

Nagaoka Red Cross Hospital

Nagaoka, , Japan

Site Status

Nagasaki University Hospital

Nagasaki, , Japan

Site Status

Kita-Harima Medical Center

Ono, , Japan

Site Status

Tazuke Kofukai Medical Research Institute Kitano Hospital

Osaka, , Japan

Site Status

Sapporo Medical University Hospital

Sapporo, , Japan

Site Status

Fujita Health University Hospital

Shinjuku-Ku, , Japan

Site Status

Instituto Nacional de Ciencias Medicas y Nutricion Salvador Zubiran

Mexico City, Mexico City, Mexico

Site Status

Centro de Alta Especialidad En Reumatologia E Investigacion Del Potosi SC

San Luis Potosí City, , Mexico

Site Status

Narodowy Instytut Geriatrii, Reumatologii i Rehabilitacji im. Prof. Dr hab. Med. Eleonory Reicher

Warsaw, Masovian Voivodeship, Poland

Site Status

Szpital Uniwersytecki Nr 2 im. Dr Jana Biziela w Bydgoszczy

Bydgoszcz, , Poland

Site Status

Seoul National University Hospital

Seoul, Seoul, South Korea

Site Status

Ajou University Hospital

Suwon, , South Korea

Site Status

Hospital Universitario Ramón y Cajal

Madrid, Madrid, Spain

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Vall d'Hebron University Hospital

Barcelona, , Spain

Site Status

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status

Chang Gung Medical Foundation Kaohsiung Chang Gung Memorial Hospital

Kaohsiung City, , Taiwan

Site Status

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status

Linkou Chang Gung Memorial Hospital

Taoyuan District, , Taiwan

Site Status

Hacettepe University Faculty of Medicine

Altındağ, Ankara, Turkey (Türkiye)

Site Status

Marmara University Pendik Training and Research Hospital

Pendik, Istanbul, Turkey (Türkiye)

Site Status

John Radcliffe Hospital

Oxford, , United Kingdom

Site Status

Countries

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United States Argentina Canada China France Germany Italy Japan Mexico Poland South Korea Spain Taiwan Turkey (Türkiye) United Kingdom

Other Identifiers

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ZB012-03-001

Identifier Type: -

Identifier Source: org_study_id

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