Open-Label Extension of Zilucoplan in Subjects With Generalized Myasthenia Gravis

NCT ID: NCT04225871

Last Updated: 2026-01-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

200 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-12-23

Study Completion Date

2026-06-02

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The RAISE-XT study is an open-label extension study to evaluate the long-term efficacy, safety, and tolerability of zilucoplan in subjects with gMG who have previously participated in a qualifying Ra Pharmaceuticals sponsored zilucoplan study.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Generalized Myasthenia Gravis

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

0.3 mg/kg zilucoplan (RA101495)

Group Type EXPERIMENTAL

zilucoplan (RA101495)

Intervention Type DRUG

Daily subcutaneous (SC) injection

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

zilucoplan (RA101495)

Daily subcutaneous (SC) injection

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Completion of a qualifying zilucoplan study

Exclusion Criteria

* With the exception of a prior zilucoplan trial, participation in another concurrent clinical trial involving an experimental therapeutic intervention (participation in observational studies and/or registry studies is permitted)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

UCB Biopharma SRL

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

UCB Cares

Role: STUDY_DIRECTOR

001 844 599 2273

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Mg0011 41

Mobile, Alabama, United States

Site Status

Mg0011 116

Phoenix, Arizona, United States

Site Status

Mg0011 31

Irvine, California, United States

Site Status

MG0011 4

Los Angeles, California, United States

Site Status

Mg0011 220

Pasadena, California, United States

Site Status

Mg0011 160

San Francisco, California, United States

Site Status

Mg0011 24

New Haven, Connecticut, United States

Site Status

Mg0011 27

Washington D.C., District of Columbia, United States

Site Status

Mg0011 25

Tampa, Florida, United States

Site Status

Mg0011 135

Augusta, Georgia, United States

Site Status

Mg0011 188

Glenview, Illinois, United States

Site Status

Mg0011 156

Indianapolis, Indiana, United States

Site Status

Mg0011 32

Kansas City, Kansas, United States

Site Status

Mg0011 33

Detroit, Michigan, United States

Site Status

Mg0011 49

East Lansing, Michigan, United States

Site Status

Mg0011 134

Columbia, Missouri, United States

Site Status

Mg0011 117

Las Vegas, Nevada, United States

Site Status

Mg0011 30

Buffalo, New York, United States

Site Status

Mg0011 123

Great Neck, New York, United States

Site Status

Mg0011 23

New York, New York, United States

Site Status

Mg0011 47

New York, New York, United States

Site Status

Mg0011 22

Chapel Hill, North Carolina, United States

Site Status

Mg0011 122

Cleveland, Ohio, United States

Site Status

Mg0011 38

Columbus, Ohio, United States

Site Status

Mg0011 40

Pittsburgh, Pennsylvania, United States

Site Status

Mg0011 128

Charleston, South Carolina, United States

Site Status

Mg0011 28

Cordova, Tennessee, United States

Site Status

Mg0011 131

Austin, Texas, United States

Site Status

Mg0011 19

Dallas, Texas, United States

Site Status

Mg0011 39

Salt Lake City, Utah, United States

Site Status

Mg0011 164

Charlottesville, Virginia, United States

Site Status

Mg0011 154

Seattle, Washington, United States

Site Status

Mg0011 45

Milwaukee, Wisconsin, United States

Site Status

Mg0011 11

Montreal, , Canada

Site Status

Mg0011 204

Lille, , France

Site Status

Mg0011 118

Nice, , France

Site Status

Mg0011 105

Paris, , France

Site Status

Mg0011 137

Strasbourg, , France

Site Status

Mg0011 150

Göttingen, , Germany

Site Status

Mg0011 129

Tübingen, , Germany

Site Status

Mg0011 132

Milan, , Italy

Site Status

Mg0011 126

Roma, , Italy

Site Status

Mg0011 151

Chiba, , Japan

Site Status

Mg0011 136

Hanamaki-shi, , Japan

Site Status

Mg0011 179

Kita-gun, , Japan

Site Status

Mg0011 153

Meguro-ku, , Japan

Site Status

Mg0011 146

Nagasaki, , Japan

Site Status

Mg0011 169

Narita, , Japan

Site Status

Mg0011 152

Sapporo, , Japan

Site Status

Mg0011 144

Sendai, , Japan

Site Status

Mg0011 163

Shinjuku-ku, , Japan

Site Status

Mg0011 141

Tokyo, , Japan

Site Status

Mg0011 140

Bergen, , Norway

Site Status

Mg0011 143

Oslo, , Norway

Site Status

Mg0011 195

Katowice, , Poland

Site Status

Mg0011 213

Katowice, , Poland

Site Status

Mg0011 192

Krakow, , Poland

Site Status

Mg0011 193

Krakow, , Poland

Site Status

Mg0011 211

Krakow, , Poland

Site Status

Mg0011 214

Lodz, , Poland

Site Status

Mg0011 205

Lublin, , Poland

Site Status

Mg0011 194

Nowa Sól, , Poland

Site Status

Mg0011 209

Poznan, , Poland

Site Status

Mg0011 201

Warsaw, , Poland

Site Status

Mg0011 210

Zabrze, , Poland

Site Status

Mg0011 133

Barcelona, , Spain

Site Status

Mg0011 168

Barcelona, , Spain

Site Status

Mg0011 138

Bilbao, , Spain

Site Status

Mg0011 119

Oxford, , United Kingdom

Site Status

Mg0011 130

Sheffield, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Canada France Germany Italy Japan Norway Poland Spain United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Weiss MD, Freimer M, Leite MI, Maniaol A, Utsugisawa K, Bloemers J, Boroojerdi B, Howard E, Savic N, Howard JF Jr. Improvement of fatigue in generalised myasthenia gravis with zilucoplan. J Neurol. 2024 May;271(5):2758-2767. doi: 10.1007/s00415-024-12209-3. Epub 2024 Feb 24.

Reference Type RESULT
PMID: 38400914 (View on PubMed)

de la Borderie G, Chimits D, Boroojerdi B, Brock M, Duda PW, Grimson F, Mahoney P, Strimenopoulou F, Cutter G, Aban I, Brauner S, Petersson M, Howard JF Jr, Bennett N. Maintenance of zilucoplan efficacy in patients with generalised myasthenia gravis up to 24 weeks: a model-informed analysis. Ther Adv Neurol Disord. 2024 Sep 21;17:17562864241279125. doi: 10.1177/17562864241279125. eCollection 2024.

Reference Type RESULT
PMID: 39314260 (View on PubMed)

Hewamadduma C, Freimer M, Genge A, Leite MI, Utsugisawa K, Vu T, Boroojerdi B, Grimson F, Savic N, Vanderkelen M, Howard JF Jr; RAISE-XT study team. Changes in corticosteroid and non-steroidal immunosuppressive therapy with long-term zilucoplan treatment in generalized myasthenia gravis. J Neurol. 2025 Jun 12;272(7):457. doi: 10.1007/s00415-025-13113-0.

Reference Type RESULT
PMID: 40504283 (View on PubMed)

Howard JF Jr, Bresch S, Farmakidis C, Freimer M, Genge A, Hewamadduma C, Hinton J, Hussain Y, Juntas-Morales R, Kaminski HJ, Maniaol A, Mantegazza R, Masuda M, Nowak RJ, Sivakumar K, Smilowski M, Utsugisawa K, Vu T, Weiss MD, Zajda M, Bloemers J, Boroojerdi B, Brock M, de la Borderie G, Duda PW, Vanderkelen M, Leite MI; RAISE-XT Study Team*. Long-term safety and efficacy of zilucoplan in patients with generalized myasthenia gravis: interim analysis of the RAISE-XT open-label extension study. Ther Adv Neurol Disord. 2024 Apr 17;17:17562864241243186. doi: 10.1177/17562864241243186. eCollection 2024.

Reference Type DERIVED
PMID: 38638673 (View on PubMed)

Howard JF Jr, Bresch S, Genge A, Hewamadduma C, Hinton J, Hussain Y, Juntas-Morales R, Kaminski HJ, Maniaol A, Mantegazza R, Masuda M, Sivakumar K, Smilowski M, Utsugisawa K, Vu T, Weiss MD, Zajda M, Boroojerdi B, Brock M, de la Borderie G, Duda PW, Lowcock R, Vanderkelen M, Leite MI; RAISE Study Team. Safety and efficacy of zilucoplan in patients with generalised myasthenia gravis (RAISE): a randomised, double-blind, placebo-controlled, phase 3 study. Lancet Neurol. 2023 May;22(5):395-406. doi: 10.1016/S1474-4422(23)00080-7.

Reference Type DERIVED
PMID: 37059508 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2024-512399-37

Identifier Type: REGISTRY

Identifier Source: secondary_id

U1111-1306-6625

Identifier Type: OTHER

Identifier Source: secondary_id

RA101495-02.302

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.