A Study of Rozanolixizumab in Pediatric Study Participants With Moderate to Severe Generalized Myasthenia Gravis

NCT ID: NCT06149559

Last Updated: 2025-11-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2/PHASE3

Total Enrollment

12 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-06-14

Study Completion Date

2026-08-17

Brief Summary

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The purpose of the study is to assess the safety and tolerability of subcutaneous (sc) administration of rozanolixizumab in pediatric participants aged ≥2 to \<18 years with generalized Myasthenia Gravis (gMG).

Detailed Description

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Conditions

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Generalized Myasthenia Gravis

Keywords

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Generalized Myasthenia Gravis gMG rozanolixizumab pediatric

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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rozanolixizumab

Study participants will receive pre-defined doses of rozanolixizumab for 6 weeks.

Group Type EXPERIMENTAL

rozanolixizumab

Intervention Type DRUG

rozanolixizumab solution for injection

Interventions

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rozanolixizumab

rozanolixizumab solution for injection

Intervention Type DRUG

Other Intervention Names

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UCB7665

Eligibility Criteria

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Inclusion Criteria

* Study participant must be ≥2 to \<18 years of age inclusive, at the time of signing the informed consent/assent according to local regulation
* Study participant must have a documented diagnosis of generalized Myasthenia Gravis (gMG) at Screening that includes a record confirming the presence of MG specific autoantibodies to acetylcholine receptor (AChR) or muscle-specific kinase (MuSK) prior to Screening
* Study participant has Myasthenia Gravis Foundation of America (MGFA) Clinical Classification II to IVa at Screening
* Study participant has received existing conventional treatment(s) for gMG (eg, pyridostigmine, corticosteroids, and/or immune suppressants) prior to Screening
* Study participant has had an unsatisfactory clinical response or worsening of gMG symptoms and is in need of additional therapy (for example, plasma exchange (PEX) or treatment with intravenous immunoglobulin (IVIg))

Exclusion Criteria

* Study participant with severe weakness affecting oropharyngeal or respiratory muscles, or who has myasthenic crisis or impending crisis at Screening or Baseline
* Study participant has a known hypersensitivity to any components of the Investigational Medicinal Product (IMP) or other anti-neonatal-Fc receptor (FcRn) medications
* Study participant with any active or untreated thymoma
* Study participant has a history of thymectomy within 6 months prior to Screening
* Study participant has a clinically relevant active infection (eg, sepsis, pneumonia, or abscess) in the opinion of the Investigator, or had a serious infection (resulting in hospitalization or requiring parenteral antibiotic treatment) within 6 weeks prior to the first dose of IMP
* Study participant has received a live vaccination within 4 weeks prior to Baseline or intends to have a live vaccination during the course of the study
Minimum Eligible Age

2 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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UCB Biopharma SRL

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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UCB Cares

Role: STUDY_DIRECTOR

001 844 599 2273

Locations

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Mg0006 50574

Denton, Texas, United States

Site Status WITHDRAWN

Mg0006 40290

Bologna, , Italy

Site Status RECRUITING

Mg0006 40144

Milan, , Italy

Site Status RECRUITING

Mg0006 40733

Napoli, , Italy

Site Status RECRUITING

Mg0006 20340

Fuchu-shi, , Japan

Site Status RECRUITING

Mg0006 20339

Ōbu, , Japan

Site Status RECRUITING

Mg0006 20343

Sagamihara, , Japan

Site Status RECRUITING

Mg0006 40734

Lodz, , Poland

Site Status RECRUITING

Mg0006 40155

Warsaw, , Poland

Site Status RECRUITING

Mg0006 20081

Taipei, , Taiwan

Site Status RECRUITING

Mg0006 20095

Taipei, , Taiwan

Site Status RECRUITING

Mg0006 40836

Kocaeli, , Turkey (Türkiye)

Site Status RECRUITING

Countries

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United States Italy Japan Poland Taiwan Turkey (Türkiye)

Central Contacts

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UCB Cares

Role: CONTACT

Phone: 1-844-599-2273

Email: [email protected]

UCB Cares

Role: CONTACT

Phone: 001 844 599 2273

Email: [email protected]

Other Identifiers

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2022-502074-16-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

U1111-1285-0787

Identifier Type: OTHER

Identifier Source: secondary_id

MG0006

Identifier Type: -

Identifier Source: org_study_id