FXR Effect on Severe Alcohol-Associated Hepatitis (FRESH) Study

NCT ID: NCT05639543

Last Updated: 2025-04-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

80 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-12-15

Study Completion Date

2027-04-01

Brief Summary

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The purpose of this trial is to assess dose related safety, efficacy, and pharmacokinetics (PK) of INT-787 in participants with severe alcohol-associated hepatitis (sAH).

Detailed Description

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This is a Phase 2a, randomized, double-blind, placebo-controlled, dose-escalation, proof-of-concept study to evaluate the safety, tolerability, efficacy, and PK of INT-787 in participants, initially admitted to the hospital, with severe alcohol-associated hepatitis (sAH). The study aims to demonstrate and provide rationale for the selection of optimal dose(s) of INT-787 in the target population of participants with sAH. INT-787 will be evaluated for safety and tolerability prior to dose escalation. Overall efficacy, compared to placebo, will be assessed for each dose cohort.

Additionally, PK measurements at various study timepoints will allow the Sponsor to better understand the systemic exposure of INT-787 and the relationship between exposure and efficacy and safety. Such insights in participants with more advanced liver disease will provide valuable information for future clinical trials of INT-787.

The placebo-treated participants will provide important natural history information on outcomes in this participant population with sAH treated with supportive care. The placebo-treated participants within cohorts are meant to blind the study drug administration while the data across dose cohorts will be used in the overall analysis.

Conditions

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Alcohol Associated Hepatitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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INT-787

Participants will be randomized to receive INT-787 (in Dose Escalation Cohorts \[Cohorts 1 through 4\] and Extension Phase Cohorts \[Cohorts 5 and 6\])

Group Type ACTIVE_COMPARATOR

INT-787

Intervention Type DRUG

Blinded Study Drug

Placebo

Participants will be randomized to receive matching placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo

Interventions

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INT-787

Blinded Study Drug

Intervention Type DRUG

Placebo

Placebo

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Males or females aged 18 to 65 years (inclusive)
2. Clinical diagnosis of sAH based on all the following:

1. History of ongoing excess alcohol (\>60 g/day \[male\] or \>40 g/day \[female\]) use for ≥6 months, with \<60 days of abstinence prior to the onset of jaundice
2. Serum total bilirubin \>3.0 mg/dL
3. Aspartate aminotransferase (AST) ≥50 U/L
4. AST/Aspartate aminotransferase (ALT) ratio ≥1.5
5. Onset of jaundice within prior 8 weeks
6. Cohort 1 through Cohort 4: Maddrey's Discriminant Factor (mDF) ≥32 and ≤70
7. Cohort 5 and Cohort 6: mDF ≥32
3. Cohort 1 through Cohort 4: MELD score ≥18 to ≤25 (inclusive) and Cohort 5 and Cohort 6: MELD score ≥21 to ≤30
4. Female participants must be postmenopausal, surgically sterile, or, if premenopausal (and not surgically sterile), be prepared to use ≥1 highly effective method of contraception from the initiation of Screening and for 90 days after the last dose of investigational product as follows:

* Surgical sterilization (bilateral tubal occlusion, etc.)
* Placement of an intrauterine device (IUD) or intrauterine system (e.g., intrauterine hormone-releasing system \[IUS\])
* Combined (estrogen and progesterone containing) hormonal contraceptive associated with inhibition of ovulation:

* Oral
* Intravaginal
* Transdermal
* Progesterone-only hormonal contraception associated with inhibition of ovulation:

* Oral
* Injectable
* Implantable
* Sexual abstinence: When in line with the preferred and usual lifestyle of the participant, is defined as avoiding all types of activity that could result in conception (pregnancy) from the initiation of Screening and until at least 90 days after the last dose of investigational product
6. Male participants must refrain from sperm donation from the initiation of Screening and until at least 90 days after the last dose of investigational product
7. Must provide written informed consent and agree to comply with the study protocol. In participants with hepatic encephalopathy which may impair decision-making, consent will be obtained per hospital procedures (e.g., by Legally Authorized Representative).
8. Participants must agree to participate in an alcohol use disorder program during the study period, as recommended by the local institution's addiction medicine specialists, including post-hospitalization

Exclusion Criteria

1. Participants taking products containing obeticholic acid in the 30 days prior to randomization
2. Participants taking \>2 doses of systemic corticosteroids within 30 days prior to randomization.
3. Participants who have been inpatient at a referral hospital for \>7 days prior to transfer.
4. Pregnancy, planned pregnancy, potential for pregnancy (e.g., unwillingness to use effective birth control during the study), or current or planned breast feeding.
5. Abstinence from alcohol consumption for \>2 months before Day 1.
6. AST or ALT \>400 U/L.
7. Cohort 1 through Cohort 4: mDF \<32 or \>70.
8. Cohort 5 and Cohort 6: mDF \<32
9. Cohort 1 through Cohort 4: MELD score \<18 or \>25.
10. Cohort 5 and Cohort 6: MELD \<21 or \>30
11. Other causes of liver disease including chronic hepatitis B (hepatitis B surface antigen \[HBsAg\] positive), chronic hepatitis C virus (HCV) RNA positive, drug-induced liver injury (DILI), biliary obstruction, and autoimmune liver disease.
12. Current or previous history of hepatocellular carcinoma (HCC)
13. History of liver transplantation or currently listed for liver transplant
14. Untreated infection (e.g., has not initiated appropriate medical treatment for infection)
15. Known positivity for human immunodeficiency virus infection
16. Uncontrolled gastrointestinal (GI) bleeding or controlled GI bleeding that was associated with shock or required transfusion of more than 3 units of blood within 7 days of Screening.
17. Kidney injury defined as a serum creatinine \>133 μmol/L (\>1.5 mg/dL) or the requirement for renal replacement therapy whether prior to or after study screening.
18. Portal vein thrombosis
19. Acute pancreatitis or acute gallbladder disease (e.g., cholecystitis)
20. Severe, on-going associated disease (e.g., cardiac failure, acute myocardial infarction, severe cardiac arrhythmias, severe pulmonary disease, neurologic disease)
21. Malignancy within the 2 years prior to Screening, with the exception of specific cancers that have been cured by surgical resection (e.g., basal cell skin cancer). Participants under evaluation for possible malignancy are not eligible.
22. Positive urine drug screen (amphetamines, barbiturates, benzodiazepines, cocaine, and opiates) except tetrahydrocannabinol or in the setting of documented prescription medications (e.g., opiates, benzodiazepines, amphetamines, barbiturates), which also include medications prescribed as part of in-patient management. Participants being treated for alcohol withdrawal may be exempt for this reason, verify with Medical Monitor.
23. Participated in a clinical research study and received any active investigational product being evaluated for the treatment of sAH within 3 months before Day 1
24. Participation in a study of another investigational medicine or device within 30 days before Screening
25. Any other condition or clinical laboratory result that, in the opinion of the Investigator, might confound the results, or would impede compliance or hinder completion of the study
26. Participants treated in the Dose Escalation Phase (Cohort 1 through Cohort 4) are not eligible for enrollment into an Extension Cohort (Cohort 5 and Cohort 6), and participants treated in Cohort 5 are not eligible for enrollment into Cohort 6.
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Intercept Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Stanford Healthcare

Palo Alto, California, United States

Site Status RECRUITING

Clinical Translational Research Site

Miami, Florida, United States

Site Status RECRUITING

Tampa General Medical Group

Tampa, Florida, United States

Site Status RECRUITING

Rush University Medical Center

Chicago, Illinois, United States

Site Status RECRUITING

Mercy Medical Center

Baltimore, Maryland, United States

Site Status RECRUITING

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status RECRUITING

UMass Memorial Medical Center

Worcester, Massachusetts, United States

Site Status RECRUITING

Henry Ford Health System

Detroit, Michigan, United States

Site Status RECRUITING

Mayo Clinic

Rochester, Minnesota, United States

Site Status RECRUITING

Rutgers-New Jersey Medical School

Newark, New Jersey, United States

Site Status WITHDRAWN

Northwell Health Center for Liver Disease and Transplantation

Manhasset, New York, United States

Site Status RECRUITING

Columbia University Medical Center/New York Presbyterian Hospital

New York, New York, United States

Site Status RECRUITING

Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status RECRUITING

Vanderbilt Digestive Disease Center

Nashville, Tennessee, United States

Site Status RECRUITING

The Liver Institute at Methodist Dallas Medical Center

Dallas, Texas, United States

Site Status RECRUITING

Parkland Health and Hospital System

Dallas, Texas, United States

Site Status RECRUITING

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status RECRUITING

Baylor College of Medicine

Houston, Texas, United States

Site Status NOT_YET_RECRUITING

University of Utah Hospital

Salt Lake City, Utah, United States

Site Status RECRUITING

VCU Health Clinical Research Services Unit

Richmond, Virginia, United States

Site Status RECRUITING

CHU Angers

Angers, France, France

Site Status RECRUITING

Hopital Beaujon

Clichy, , France

Site Status RECRUITING

Hopital Claude Huriez

Lille, , France

Site Status RECRUITING

Hopital Pitie Salpetriere

Paris, , France

Site Status RECRUITING

Hopital Rangueil

Toulouse, , France

Site Status RECRUITING

Cambridge University NHS Foundation Trust

Cambridge, , United Kingdom

Site Status RECRUITING

Royal Free Hospital

London, , United Kingdom

Site Status RECRUITING

Imperial College Healthcare NHS Trust

London, , United Kingdom

Site Status RECRUITING

King's College Hospital

London, , United Kingdom

Site Status RECRUITING

University Hospitals Plymouth NHS Trust

Plymouth, , United Kingdom

Site Status RECRUITING

Countries

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United States France United Kingdom

Central Contacts

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Steven Lauder

Role: CONTACT

858-652-6800

Thomas Capozza

Role: CONTACT

646-747-1000

Facility Contacts

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Stanford Healthcare

Role: primary

Stanford Healthcare

Clinical Translational Research Site

Role: primary

Tampa General Medical Group

Role: primary

Rush University Medical Center

Role: primary

Mercy Medical Center

Role: primary

Beth Israel Deaconess Medical Center

Role: primary

Anne Foley

Role: primary

Henry Ford Health System

Role: primary

Mayo Clinic Hospital

Role: primary

Northwell Health Center for Liver Disease and Transplantation

Role: primary

Columbia University Medical Center/ New York Presbyterian Hospital

Role: primary

Columbia University Medical

Hospital of the University of Pennsylvania

Role: primary

Medical University of South Carolina

Role: primary

Vanderbilt Digestive Disease Center

Role: primary

The Liver Institute at Methodist Dallas Medical Center

Role: primary

Parkland Health Hospital System

Role: primary

University of Texas Southwestern Medical Center

Role: primary

Megha Bhongade

Role: primary

University of Utah Hospital

Role: primary

University of Utah Hospital

VCU Health Clinical Research Services Unit

Role: primary

CHU Angers

Role: primary

Hopital Beaujon

Role: primary

Hopital Claude Huriez

Role: primary

Hopital Pitie Salpetriere

Role: primary

Hopital Rangueil

Role: primary

Cambridge University NHS Foundation Trust

Role: primary

Royal Free Hospital

Role: primary

Royal Free Hospital

Imperial College Healthcare NHS Trust

Role: primary

Andrew Ayers

Role: primary

2032997615

University Hospitals Plymouth NHS Trust

Role: primary

Other Identifiers

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787-201

Identifier Type: -

Identifier Source: org_study_id

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