Randomized Global Phase 3 Study to Evaluate the Impact on NASH With Fibrosis of Obeticholic Acid Treatment

NCT ID: NCT02548351

Last Updated: 2024-10-01

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

2477 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-09-22

Study Completion Date

2023-09-15

Brief Summary

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The primary objectives of this study are to evaluate the effect of Obeticholic Acid treatment compared to placebo on 1) histological improvement and 2) liver-related clinical outcomes in patients with non-cirrhotic nonalcoholic steatohepatitis (NASH) with liver fibrosis.

Detailed Description

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Conditions

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Non Alcoholic Steatohepatitis (NASH)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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10 mg Obeticholic Acid

10 mg Obeticholic Acid daily for the remainder of the study

Group Type EXPERIMENTAL

Obeticholic Acid

Intervention Type DRUG

25 mg Obeticholic Acid

25 mg Obeticholic Acid daily for the remainder of the study

Group Type EXPERIMENTAL

Obeticholic Acid

Intervention Type DRUG

Placebo

One tablet daily for the remainder of the study

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Interventions

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Obeticholic Acid

Intervention Type DRUG

Placebo

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Histologic evidence of NASH upon central read of a liver biopsy obtained no more than 6 months before Day 1 defined by presence of all 3 key histological features of NASH according to NASH CRN criteria.
2. Histologic evidence of fibrosis stage 2 or stage 3 as defined by the NASH CRN scoring of fibrosis, or

Histologic evidence of fibrosis stage 1a or stage 1b if accompanied by ≥1 of the following risk factors:
* Obesity (BMI ≥30 kg/m2)
* Type 2 diabetes diagnosed per 2013 American Diabetes Association criteria
* ALT \>1.5× upper limit of normal (ULN).
3. For subjects with a historical biopsy, is either not taking or is on stable doses of TZDs/glitazones or vitamin E for 6 months before Day 1.
4. Stable body weight.

Exclusion Criteria

1. Model for End-stage Liver Disease (MELD) score \>12
2. ALT ≥10× ULN
3. HbA1c \>9.5%
4. Total bilirubin \>1.5 mg/dL
5. Evidence of other known forms of known chronic liver disease such as alcoholic liver disease, hepatitis B, hepatitis C, PBC, PSC, autoimmune hepatitis, Wilson disease, iron overload, alpha-1-antitrypsin deficiency, drug-induced liver injury, known or suspected hepatocellular carcinoma (HCC)
6. History of liver transplant, or current placement on a liver transplant list
7. Current or history of significant alcohol consumption
8. Prior or planned ileal resection, or prior or planned bariatric surgery
9. Histological presence of cirrhosis
10. History of biliary diversion
11. Known positivity for human immunodeficiency virus infection.
12. Acute cholecystitis or acute biliary obstruction.
13. BMI \>45 kg/m2
Minimum Eligible Age

18 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Intercept Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Sangeeta Sawhney, MD

Role: STUDY_DIRECTOR

Intercept Pharmaceuticals

Locations

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The University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Digestive Health Specialists of the Southeast

Dothan, Alabama, United States

Site Status

Institute for Liver Health DBA Arizona Liver Health

Chandler, Arizona, United States

Site Status

Arizona Liver Health - Glendale

Glendale, Arizona, United States

Site Status

St. Joseph's Hospital and Medical Center

Phoenix, Arizona, United States

Site Status

Mayo Clinic Arizona

Phoenix, Arizona, United States

Site Status

Arizona Liver Clinic - Tucson

Tucson, Arizona, United States

Site Status

Liver Wellness Center

Little Rock, Arkansas, United States

Site Status

Arkansas Gastroenterology

North Little Rock, Arkansas, United States

Site Status

GW Research Inc.

Chula Vista, California, United States

Site Status

Precision Research Institute

Chula Vista, California, United States

Site Status

Southern California Research Center

Coronado, California, United States

Site Status

Citrus Valley Gastroenterology

Covina, California, United States

Site Status

TriWest Research Associates, LLC

El Cajon, California, United States

Site Status

UCSF Fresno, Clinical Research Center

Fresno, California, United States

Site Status

Fresno Clinical Research Center

Fresno, California, United States

Site Status

Scripps Clinic

La Jolla, California, United States

Site Status

University of California, San Diego

La Jolla, California, United States

Site Status

Keck Medical Center of USC

Los Angeles, California, United States

Site Status

Cedars-Sinai Medical Center

Los Angeles, California, United States

Site Status

National Research Institute, Wilshire

Los Angeles, California, United States

Site Status

Gastrointestinal Biosciences

Los Angeles, California, United States

Site Status

Veteran Affairs Great Los Angeles Healthcare System

Los Angeles, California, United States

Site Status

Stanford University

Palo Alto, California, United States

Site Status

Inland Empire Liver Foundation

Rialto, California, United States

Site Status

University of California Davis Medical Center

Sacramento, California, United States

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eStudy Site

San Diego, California, United States

Site Status

Medical Associates Research Group

San Diego, California, United States

Site Status

Kaiser Permanente

San Diego, California, United States

Site Status

California Pacific Medical Center (CPMC)

San Francisco, California, United States

Site Status

UCSF/ San Francisco General Hospital

San Francisco, California, United States

Site Status

Quest Clinical Research

San Francisco, California, United States

Site Status

University of California, San Francisco

San Francisco, California, United States

Site Status

Silicon Valley Research Institute

San Jose, California, United States

Site Status

University of Colorado Denver and Hospital

Aurora, Colorado, United States

Site Status

South Denver Gastroenterology, PC

Englewood, Colorado, United States

Site Status

Western States Clinical Research, Inc.

Wheat Ridge, Colorado, United States

Site Status

Yale University School of Medicine

New Haven, Connecticut, United States

Site Status

Integrity Clinical Research, LLC

Doral, Florida, United States

Site Status

UF Hepatology Research at CTRB

Gainesville, Florida, United States

Site Status

Nature Coast Clinical Research

Inverness, Florida, United States

Site Status

UF Health Jacksonville-Gastroenterology Emerson

Jacksonville, Florida, United States

Site Status

Mayo Clinic

Jacksonville, Florida, United States

Site Status

Florida Digestive Health Specialist Research Institute

Lakewood Rch, Florida, United States

Site Status

Sunrise Medical Research, Inc.

Lauderdale Lakes, Florida, United States

Site Status

Meridien Research

Maitland, Florida, United States

Site Status

Bruce W. Carter Miami VA Medical Center

Miami, Florida, United States

Site Status

Schiff Center for Liver Diseases

Miami, Florida, United States

Site Status

ProLive Medical Research

Miami, Florida, United States

Site Status

Janus Clinical Research, Inc.

Miami, Florida, United States

Site Status

Sensible Healthcare, LLC

Ocoee, Florida, United States

Site Status

Florida Hospital Transplant Institute

Orlando, Florida, United States

Site Status

South Florida Center of Gastroenterology, P.A.

Wellington, Florida, United States

Site Status

Florida Medical Clinic, P.A.

Zephyrhills, Florida, United States

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Summit Clinical Research, LLC

Athens, Georgia, United States

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Digestive Healthcare of Georgia

Atlanta, Georgia, United States

Site Status

Piedmont Atlanta Hospital

Atlanta, Georgia, United States

Site Status

The Emory Clinic (TEC)

Atlanta, Georgia, United States

Site Status

Gastrointestinal Specialists of Georgia

Marietta, Georgia, United States

Site Status

The Queen's Medical Center - Liver Center

Honolulu, Hawaii, United States

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Grand Teton Research Group

Idaho Falls, Idaho, United States

Site Status

Northwestern University, Feinberg School of Medicine

Chicago, Illinois, United States

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The University of Chicago Medical Center

Chicago, Illinois, United States

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Loyola University Medical Center

Maywood, Illinois, United States

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Indiana University Health University Hospital

Indianapolis, Indiana, United States

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Indianapolis Gastroenterology & Hepatology

Indianapolis, Indiana, United States

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The University of Kansas Medical Center

Kansas City, Kansas, United States

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The Medical Center of Bowling Green

Bowling Green, Kentucky, United States

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University of Kentucky Chandler Medical Center

Lexington, Kentucky, United States

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University of Louisville Medical, Clinical Trials Unit

Louisville, Kentucky, United States

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Tulane Medical Center

New Orleans, Louisiana, United States

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Ochsner Clinic Foundation

New Orleans, Louisiana, United States

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Louisiana Research Center, LLC

Shreveport, Louisiana, United States

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Investigative Clinical Research

Annapolis, Maryland, United States

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Mercy Medical Center

Baltimore, Maryland, United States

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Johns Hopkins Hospital

Baltimore, Maryland, United States

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Walter Reed National Military Medical Center

Bethesda, Maryland, United States

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Massachusetts General Hospital

Boston, Massachusetts, United States

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Boston Medical Center

Boston, Massachusetts, United States

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Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

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Lahey Hospital & Medical Center

Burlington, Massachusetts, United States

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University of Massachusetts Medical School

Worcester, Massachusetts, United States

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Henry Ford Health System

Detroit, Michigan, United States

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Gastroenterology Associates of Western Michigan, d.b.a West Michigan Clinical Research

Wyoming, Michigan, United States

Site Status

Huron Gastroenterology Associates/Center for Digestive Care

Ypsilanti, Michigan, United States

Site Status

Minnesota Gastroenterology

Minneapolis, Minnesota, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

Southern Therapy and Advanced Research, LLC

Jackson, Mississippi, United States

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Kansas City VA Medical Center

Kansas City, Missouri, United States

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Kansas City Research Institute

Kansas City, Missouri, United States

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Saint Louis University Gastroenterology & Hepatology

St Louis, Missouri, United States

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Washington University School of Medicine - Gastroenterology

St Louis, Missouri, United States

Site Status

CHI Health Alegent Creighton Clinic Gastroenterology

Omaha, Nebraska, United States

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AGA Clinical Research Associates, LLC

Egg Harbor, New Jersey, United States

Site Status

Amici Clinical Research

Martinsville, New Jersey, United States

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Amici GI - LLC

Martinsville, New Jersey, United States

Site Status

Rutgers University New Jersey Medical School

Newark, New Jersey, United States

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Saint Joseph's Regional Medical Center

Paterson, New Jersey, United States

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AccumetRx Clinical research / UGNM

Albuquerque, New Mexico, United States

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University at Buffalo, Clinical and Translational Research Center

Buffalo, New York, United States

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Mount Sinai Beth Israel

New York, New York, United States

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Concorde Medical Group PLLC

New York, New York, United States

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New York University (NYU) Langone Medical Center

New York, New York, United States

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Weill Cornell Medical College

New York, New York, United States

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Icahn School of Medicine at Mt. Sinai

New York, New York, United States

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Columbia University Medical Center

New York, New York, United States

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University of Rochester Medical Center

Rochester, New York, United States

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Montefiore Medical Center

The Bronx, New York, United States

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Asheville Gastroenterology Associates, PA

Asheville, North Carolina, United States

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University of North Carolina at Chapel Hill, School of Medicine

Chapel Hill, North Carolina, United States

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Center for Liver Disease

Charlotte, North Carolina, United States

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Charlotte Gastroenterology & Hepatology

Charlotte, North Carolina, United States

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Duke University Medical Center

Durham, North Carolina, United States

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Cumberland Research Associates, LLC

Fayetteville, North Carolina, United States

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Carolinas Center for Liver Disease/Carolinas HeatlhCare System

Huntersville, North Carolina, United States

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Digestive Health Specialists, PA

Winston-Salem, North Carolina, United States

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Consultants for Clinical Research

Cincinnati, Ohio, United States

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University of Cincinnati

Cincinnati, Ohio, United States

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University Hospitals Case Medical Center

Cleveland, Ohio, United States

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MetroHealth Medical Center

Cleveland, Ohio, United States

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The Ohio State University Wexner Medical Center

Columbus, Ohio, United States

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INTEGRIS Baptist Medical Center

Oklahoma City, Oklahoma, United States

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Doylestown Health Gastroenterology

Doylestown, Pennsylvania, United States

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Hillmont GI, pc

Flourtown, Pennsylvania, United States

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The Pennsylvania State University and The Milton S. Hershey Medical Center

Hershey, Pennsylvania, United States

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Hillmont G.I. - Lansdale Office

Lansdale, Pennsylvania, United States

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Drexel University

Philadelphia, Pennsylvania, United States

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Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, United States

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Thomas Jefferson University

Philadelphia, Pennsylvania, United States

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Einstein Healthcare Network

Philadelphia, Pennsylvania, United States

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UPMC

Pittsburgh, Pennsylvania, United States

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University Gastroenterology

Providence, Rhode Island, United States

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Prisma Health- Upstate Gastroenterology and Liver Center

Greenville, South Carolina, United States

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Rapid City Medical Center

Rapid City, South Dakota, United States

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WR-Clinsearch, LLC

Chattanooga, Tennessee, United States

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Gastro One

Germantown, Tennessee, United States

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Associates in Gastroenterology, PLC

Hermitage, Tennessee, United States

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Clinical Research Solutions

Jackson, Tennessee, United States

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East Tennesse Research Institute

Johnson City, Tennessee, United States

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Methodist Healthcare, University Hospital

Memphis, Tennessee, United States

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Nashville Gastrointestinal Specialists

Nashville, Tennessee, United States

Site Status

Quality Medical Research, PLLC

Nashville, Tennessee, United States

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Vanderbilt University Medical Center

Nashville, Tennessee, United States

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Texas Clinical Research Institute

Arlington, Texas, United States

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The Liver Institute at Methodist Dallas Medical Center

Dallas, Texas, United States

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Liver Center of Texas

Dallas, Texas, United States

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Texas Digestive Disease Consultants

Dallas, Texas, United States

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UT Southwestern Medical Center

Dallas, Texas, United States

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MedResearch, Inc.

El Paso, Texas, United States

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Brooke Army Medical Center

Fort Sam Houston, Texas, United States

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Baylor Scott & White All Saints Medical Center

Fort Worth, Texas, United States

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Texas Digestive Disease Consultants

Fort Worth, Texas, United States

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Baylor College of Medicine Ben Taub General Hospital

Houston, Texas, United States

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Baylor College of Medicine

Houston, Texas, United States

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Houston Methodist Hospital

Houston, Texas, United States

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Liver Associates of Texas, P.A.

Houston, Texas, United States

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The University of Texas Health Science Center at Houston-Medical School IM-Division of Gastroenterology, Hepatology & Nutrition

Houston, Texas, United States

Site Status

Centex Studies, Inc.

Houston, Texas, United States

Site Status

Centex Studies, Inc.

McAllen, Texas, United States

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American Research Corporation at the Texas Liver Institute

San Antonio, Texas, United States

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Gastroenterology Consultants of San Antonio

San Antonio, Texas, United States

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Texas Digestive Disease Consultants - San Marcos

San Marcos, Texas, United States

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University of Utah Hospital

Salt Lake City, Utah, United States

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The University of Vermont Medical Center - Smith 2

Burlington, Vermont, United States

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University of Virginia Health System

Charlottesville, Virginia, United States

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Inova Fairfax Medical Campus

Falls Church, Virginia, United States

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Digestive and Liver Disease Specialists

Norfolk, Virginia, United States

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Bon Secours St. Mary's Hospital

Richmond, Virginia, United States

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McGuire DVAMC GI

Richmond, Virginia, United States

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Virginia Commonwealth University Clinical Research Services Unit (CRSU)

Richmond, Virginia, United States

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Virginia Mason - Seattle Medical Center

Seattle, Washington, United States

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Swedish Organ Transplant and Liver Center

Seattle, Washington, United States

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Liver Institute Northwest

Seattle, Washington, United States

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University of Washington Medical Center

Seattle, Washington, United States

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University of Wisconsin Hospital & Clinics

Madison, Wisconsin, United States

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Royal Adelaide Hospital Gastroenterology and Hepatology Dept.

Adelaide, , Australia

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Flinders Medical Centre

Bedford Park, , Australia

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AW Morrow Gastroenterology and Liver Centre Royal Prince Alfred Hospital

Camperdown, , Australia

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Monash Health - Monash Medical Centre

Clayton, , Australia

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Gallipoli Medical Research Foundation

Greenslopes, , Australia

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Austin Hospital

Heidelberg, , Australia

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Royal Brisbane and Women's Hospital

Herston, , Australia

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Nepean Hospital

Kingswood, , Australia

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The Alfred Hospital, Department of Gastroenterology

Melbourne, , Australia

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Fiona Stanley Hospital

Murdoch, , Australia

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The Royal Melbourne Hospital

Parkville, , Australia

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Westmead Hospital

Westmead, , Australia

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Universitätsklinik für Innere Medizin I Innsbruck

Innsbruck, , Austria

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Klinikum Klagenfurt am Wörthersee

Klagenfurt, , Austria

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Ordensklinikum Linz GmbH

Linz, , Austria

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Uniklinikum Salzburg

Salzburg, , Austria

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Medizinische Universität Wien

Vienna, , Austria

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UZ Antwerpen

Edegem, Antwerpen, Belgium

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ULB Hȏpital Erasme - Gastroenterology

Brussels, Brabant, Belgium

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UZ Leuven Campus Gathuisberg Hepatology Department

Leuven, Vlaams-Brabant, Belgium

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AZ Sint-Jan Brugge Oostende

Bruges, , Belgium

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UCL Saint-Luc - Hepatology Department

Brussels, , Belgium

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Ziekenhuis Oost-Limburg (ZOL)

Genk, , Belgium

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UZ Gent Gastroenterology Department

Ghent, , Belgium

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AZ Nikolaas

Sint-Niklaas, , Belgium

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London Health Sciences Centre University Hospital

London, Ontario, Canada

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University of Calgary Liver Unit

Calgary, , Canada

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GI Research

Edmonton, , Canada

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University of Alberta

Edmonton, , Canada

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Centre de Recherche du Centre Hospitalier de l'Universite de Montreal

Montreal, , Canada

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The Research Institute of the McGill University Health Centre

Montreal, , Canada

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Toronto Center for Liver Disease

Toronto, , Canada

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Toronto Liver Centre

Toronto, , Canada

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LAIR Centre

Vancouver, , Canada

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Gordon and Leslie Diamond Health Care Centre

Vancouver, , Canada

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GIRI - GI Research Institute

Vancouver, , Canada

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PerCuro Clinical Research Ltd.

Victoria, , Canada

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John Buhler Research Centre

Winnipeg, , Canada

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Aalborg University Hospital

Aalborg, , Denmark

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Aarhus University Hospital Medicinsk Hepatogastroenterologisk Afdeling

Aarhus, , Denmark

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Copenhagen University Hospital Hvidovre

Hvidovre, , Denmark

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Odense University Hospital

Odense, , Denmark

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Helsinki University Hospital

Helsinki, , Finland

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Turku University Hospital

Turku, , Finland

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CHU Amiens Picardie

Amiens, , France

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CHU Angers-Service d'Hepato-Gastroenterologie

Angers, , France

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Centre hospitalier Pierre Oudot

Bourgoin, , France

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CHU Beaujon-Service d'Hépatologie

Clichy, , France

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Hôpital Henri Mondor - Service d'hépatologie

Créteil, , France

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CHU Grenoble

Grenoble, , France

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CHRU Hôpital Claude Huriez

Lille, , France

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Hôpital de la Croix Rousse

Lyon, , France

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Hôpital Saint Joseph

Marseille, , France

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Hôpital de l'Archet II-CHU Nice

Nice, , France

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Service d'Hepato-Gastroenterologie CHR Orleans - La Source

Orléans, , France

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Hospital Saint Antoine Department of Hepatology

Paris, , France

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Hôpital de la Pitié Salpétrère

Paris, , France

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Hôpital Cochin

Paris, , France

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Hopital Haut-Lévêque-Hépatogastroentérologie-Bât USN

Pessac, , France

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CHU de Rouen

Rouen, , France

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CHU Toulouse - Hopital de Purpan

Toulouse, , France

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CHU de Nancy - Hôpital de Brabois adultes

Vandœuvre-lès-Nancy, , France

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Hopital Paul Brousse

Villejuif, , France

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Universitätsklinikum Heidelberg Medizinischen Klinik IV Gastroenterologie und Hepatologie

Heidelberg, Baden-Wurttemberg, Germany

Site Status

Friedrich-Alexander-Universität Erlangen Medizinische Klinik 1

Erlangen, Bavaria, Germany

Site Status

Universitätsmedizin Mainz, I. Med. Klinik und Poliklinik

Mainz, Rhineland-Palatinate, Germany

Site Status

Universitätsklinikum Leipzig Klinik für Gastroenterologie und Rheumatologie-Sektion Hepatologie

Leipzig, Saxony, Germany

Site Status

Universitatsklinikum Aachen, RWTH Aachen, Medizinische Klinik III

Aachen, , Germany

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Charite Universitätsmedizin Campus Virchow

Berlin, , Germany

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St. Josef-Hospital, Ruhr University Bochum

Bochum, , Germany

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University Hosptial Cologne Clinics for Gastroenterology and Hepatology

Cologne, , Germany

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University Hospital Essen

Essen, , Germany

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Katholische Kliniken Ruhrhalbinsel GmbH

Essen, , Germany

Site Status

Universitätsklinikum Hamburg- Eppendorf

Hamburg, , Germany

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Medizinische Hochschule Hannover

Hanover, , Germany

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Gastroenterologische Gemeinschaftspraxis

Herne, , Germany

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Hepato-Gastroenterology Center Kiel

Kiel, , Germany

Site Status

EUGASTRO GmbH

Leipzig, , Germany

Site Status

Krankenhaus Barmherzige Bruder Innere Medizin I - Gastroenterologie

Munich, , Germany

Site Status

Universitätsklinikum Würzburg

Würzburg, , Germany

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Egyesitett Szent Istvan és Szent Laszlo

Budapest, , Hungary

Site Status

Pecsi Tudomanyegyetem Klinikai Kozpont, I. sz

Budapest, , Hungary

Site Status

Kenezy Gyula Korhaz es Rendelointezet

Debrecen, , Hungary

Site Status

Soroka Medical Center Division of Internal Medicine

Beersheba, , Israel

Site Status

Rambam Medical Center Center for Liver diseases

Haifa, , Israel

Site Status

Carmel Medical Center

Haifa, , Israel

Site Status

Shaarei Zedek Medical Center

Jerusalem, , Israel

Site Status

Hadassah Ein Kerem MC

Jerusalem, , Israel

Site Status

West Galilee Hospital

Nahariya, , Israel

Site Status

Holy Family Medical Center

Nazareth, , Israel

Site Status

Rabin Medical Center, Liver Institute

Petah Tikva, , Israel

Site Status

Sheba Medical Center

Ramat Gan, , Israel

Site Status

Sourasky Tel-Aviv Medical Center

Tel Aviv, , Israel

Site Status

Universita di Bologna - DIMEC

Bologna, , Italy

Site Status

University di Bologna - Dipartimento di Scienze Mediche e Chirurgiche - DIMEC

Bologna, , Italy

Site Status

Ospedale san Giuseppe - Multimedica

Milan, , Italy

Site Status

Fondazione IRCCS Ca Granda Ospedale

Milan, , Italy

Site Status

Azienda Socio-Sanitaria Territoriale (ASST) Santi Paolo e Carlo

Milan, , Italy

Site Status

Fondazione IRCCS Ca Grande Ospedale

Milan, , Italy

Site Status

AOU di Modena Ospedale Civile

Modena, , Italy

Site Status

Azienda Ospedaliera Universitaria Policlinico

Napoli, , Italy

Site Status

Policlinico Paolo Giaccone di Palermo

Palermo, , Italy

Site Status

Policlinico University Campus Biomedico

Rome, , Italy

Site Status

Istituto Clinico Humanitas

Rozzano, , Italy

Site Status

A.O.U. Città della Salute e della Scienza di Torino

Torino, , Italy

Site Status

NZ Liver Transplant Unit

Grafton, Auckland, New Zealand

Site Status

Middlemore Hospital

Auckland, , New Zealand

Site Status

Centrum Badan Klinicznych PI-House Sp. z o.o.

Gdansk, , Poland

Site Status

Uniwersyteckie Centrum Kliniczne im. Prof K. Gibinskiego Slaskiego Uniwersytetu Medycznego w Katowicach

Katowice, , Poland

Site Status

Wojewodzki Specjalistyczny Szpital im. Dr WI. Bieganskiego

Lodz, , Poland

Site Status

Samodzielny Publiczny Szpital Kliniczny Nr 1

Lublin, , Poland

Site Status

Centrum Badan Klinicznych Piotr Napora

Wroclaw, , Poland

Site Status

Centro Hospitalar do Baixo Vouga, E.P.E.

Aveiro, , Portugal

Site Status

Ulsba, Epe

Beja, , Portugal

Site Status

Hospital da Senhora da Oliveira - Guimarães

Guimarães, , Portugal

Site Status

Centro Hospitalar Lisboa Ocidental

Lisbon, , Portugal

Site Status

Centro Hospitalar de Lisboa Norte, EPE - Hosp. de Santa Maria

Lisbon, , Portugal

Site Status

Klinical Investigations Group, LLC

San Juan, , Puerto Rico

Site Status

Ave Ponce De Leon #715

San Juan, , Puerto Rico

Site Status

Fundacion de Investigacion

San Juan, , Puerto Rico

Site Status

University Medical Centar Zvezdara

Belgrade, , Serbia

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Clinical Hospital Center Bezanijska Kosa

Belgrade, , Serbia

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Clinical Center Nis

Niš, , Serbia

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Hospital Universitari Son Espases

Palma de Mallorca, Balearic Islands, Spain

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Hospital Universitario Puerta de Hierro Majadahonda

Majadahonda, Madrid, Spain

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Hospital Universitario Fundación Alcorcon

Alcorcón, , Spain

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Hospital General y Universitario de Alicante

Alicante, , Spain

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Hospital del Mar Gastroenterology Department

Barcelona, , Spain

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Hospital Universitario Vall d'Hebron

Barcelona, , Spain

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Hospital Clinic(o) de Barcelona

Barcelona, , Spain

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Hospital Universitario Donostia

Donostia / San Sebastian, , Spain

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Complejo Asistencial Universitario de Leon

León, , Spain

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Hospital Universitario Ramón y Cajal

Madrid, , Spain

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Hospital Universitario La Paz

Madrid, , Spain

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Hospital (Universitario) Virgen de la Victoria

Málaga, , Spain

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Hospital (Universitario) Marqués de Valdecilla

Santander, , Spain

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Hospital Clinico Universitario de Santiago

Santiago de Compostela, , Spain

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Hospital Universitario Virgen del Rocio

Seville, , Spain

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Hospital Clinico Universitario de Valencia

Valencia, , Spain

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Consorcio Hospital General Universitario

Valencia, , Spain

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Hospital Universitario La Fe.

Valencia, , Spain

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Hospital Universitario Miguel Servet

Zaragoza, , Spain

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Sahlgrenska University Hospital

Gothenburg, , Sweden

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Universitetsjukhuset Linkoping

Linköping, , Sweden

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Karolinska University Hospital

Stockholm, , Sweden

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UVCM Hepatologie

Bern, , Switzerland

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Epatocentro Ticino

Lugano, , Switzerland

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Hospital of St. Gallen

Sankt Gallen, , Switzerland

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University Clinic of Gastroenterology & Hepatology

Zurich, , Switzerland

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Royal Cornwall Hospital

Truro, Cornwall, United Kingdom

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Royal Bournemouth Hospital

Bournemouth, Dorset, United Kingdom

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Queen Alexandra Hospital

Portsmouth, Hampshire, United Kingdom

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Norfolk and Norwich University Hospitals

Norwich, Norfolk, United Kingdom

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John Radcliffe Hospital

Headington, Oxford, United Kingdom

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Royal Surrey NHS Foundation Trust

Guildford, Surrey, United Kingdom

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Institute of Biomedical Research

Birmingham, , United Kingdom

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Bradford Royal Infirmary

Bradford, , United Kingdom

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University Hospital Bristol NHS Foundation Trust

Bristol, , United Kingdom

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Cambridge University Hospital

Cambridge, , United Kingdom

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University Hospitals Coventry & Warwickshire

Coventry, , United Kingdom

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Glasgow Royal Infirmary, NHS Greater

Glasgow, , United Kingdom

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Gastroenterology Department Hull Royal Infirmary

Hull, , United Kingdom

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University Hospital Aintree

Liverpool, , United Kingdom

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Royal London Hospital

London, , United Kingdom

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Institute for Liver and Digestive Health

London, , United Kingdom

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Guy's and St. Thomas NHS Foundation Trust

London, , United Kingdom

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St. Mary's Hospital

London, , United Kingdom

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Central Manchester University Hospital NHS Foundation Trust Manchester Royal Infirmary

Manchester, , United Kingdom

Site Status

The Newcastle Upon Tyne Hospitals NHS Foundation Trust

Newcastle upon Tyne, , United Kingdom

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Nottingham Digestive Diseases and Biomedical Research Unit

Nottingham, , United Kingdom

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Derriford Hospital

Plymouth, , United Kingdom

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Countries

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United States Australia Austria Belgium Canada Denmark Finland France Germany Hungary Israel Italy New Zealand Poland Portugal Puerto Rico Serbia Spain Sweden Switzerland United Kingdom

References

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Sanyal AJ, Loomba R, Anstee QM, Ratziu V, Kowdley KV, Rinella ME, Harrison SA, Resnick MB, Capozza T, Sawhney S, Shelat N, Younossi ZM. Utility of pathologist panels for achieving consensus in NASH histologic scoring in clinical trials: Data from a phase 3 study. Hepatol Commun. 2023 Dec 22;8(1):e0325. doi: 10.1097/HC9.0000000000000325. eCollection 2024 Jan 1.

Reference Type DERIVED
PMID: 38126958 (View on PubMed)

Rinella ME, Dufour JF, Anstee QM, Goodman Z, Younossi Z, Harrison SA, Loomba R, Sanyal AJ, Bonacci M, Trylesinski A, Natha M, Shringarpure R, Granston T, Venugopal A, Ratziu V. Non-invasive evaluation of response to obeticholic acid in patients with NASH: Results from the REGENERATE study. J Hepatol. 2022 Mar;76(3):536-548. doi: 10.1016/j.jhep.2021.10.029. Epub 2021 Nov 15.

Reference Type DERIVED
PMID: 34793868 (View on PubMed)

Younossi ZM, Stepanova M, Nader F, Loomba R, Anstee QM, Ratziu V, Harrison S, Sanyal AJ, Schattenberg JM, Barritt AS, Noureddin M, Bonacci M, Cawkwell G, Wong B, Rinella M; RandomizEd Global Phase 3 Study to Evaluate the Impact on NASH with FibRosis of Obeticholic Acid TreatmEnt (REGENERATE) Study Investigators. Obeticholic Acid Impact on Quality of Life in Patients With Nonalcoholic Steatohepatitis: REGENERATE 18-Month Interim Analysis. Clin Gastroenterol Hepatol. 2022 Sep;20(9):2050-2058.e12. doi: 10.1016/j.cgh.2021.07.020. Epub 2021 Jul 15.

Reference Type DERIVED
PMID: 34274514 (View on PubMed)

Younossi ZM, Ratziu V, Loomba R, Rinella M, Anstee QM, Goodman Z, Bedossa P, Geier A, Beckebaum S, Newsome PN, Sheridan D, Sheikh MY, Trotter J, Knapple W, Lawitz E, Abdelmalek MF, Kowdley KV, Montano-Loza AJ, Boursier J, Mathurin P, Bugianesi E, Mazzella G, Olveira A, Cortez-Pinto H, Graupera I, Orr D, Gluud LL, Dufour JF, Shapiro D, Campagna J, Zaru L, MacConell L, Shringarpure R, Harrison S, Sanyal AJ; REGENERATE Study Investigators. Obeticholic acid for the treatment of non-alcoholic steatohepatitis: interim analysis from a multicentre, randomised, placebo-controlled phase 3 trial. Lancet. 2019 Dec 14;394(10215):2184-2196. doi: 10.1016/S0140-6736(19)33041-7. Epub 2019 Dec 5.

Reference Type DERIVED
PMID: 31813633 (View on PubMed)

Ratziu V, Sanyal AJ, Loomba R, Rinella M, Harrison S, Anstee QM, Goodman Z, Bedossa P, MacConell L, Shringarpure R, Shah A, Younossi Z. REGENERATE: Design of a pivotal, randomised, phase 3 study evaluating the safety and efficacy of obeticholic acid in patients with fibrosis due to nonalcoholic steatohepatitis. Contemp Clin Trials. 2019 Sep;84:105803. doi: 10.1016/j.cct.2019.06.017. Epub 2019 Jun 29.

Reference Type DERIVED
PMID: 31260793 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

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Other Identifiers

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747-303

Identifier Type: -

Identifier Source: org_study_id

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