A Study of Experimental Medication BMS-986036 in Adults With Nonalcoholic Steatohepatitis (NASH) and Liver Cirrhosis

NCT ID: NCT03486912

Last Updated: 2022-10-13

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

155 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-06-12

Study Completion Date

2021-09-14

Brief Summary

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This is a study of experimental medication BMS-986036 given to adults with Nonalcoholic Steatohepatitis (NASH; the buildup of fat and inflammation in the liver that is not caused by alcohol) and liver cirrhosis (liver damage characterized by normal liver tissue being replaced by scar tissue).

Detailed Description

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Conditions

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Hepatic Cirrhosis Liver Fibrosis Nonalcoholic Fatty Liver Disease (NAFLD) Nonalcoholic Steatohepatitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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BMS-986036 Dose Level 1

Group Type EXPERIMENTAL

BMS-986036

Intervention Type DRUG

Specified dose on specified days.

BMS-986036 Dose Level 2

Group Type EXPERIMENTAL

BMS-986036

Intervention Type DRUG

Specified dose on specified days.

BMS-986036 Dose Level 3

Group Type EXPERIMENTAL

BMS-986036

Intervention Type DRUG

Specified dose on specified days.

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Specified dose on specified days.

Interventions

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BMS-986036

Specified dose on specified days.

Intervention Type DRUG

Placebo

Specified dose on specified days.

Intervention Type OTHER

Other Intervention Names

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Pegbelfermin

Eligibility Criteria

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Inclusion Criteria

* Liver biopsy performed within 6 months (26 weeks) prior to the screening period. If historical biopsy is not available, a liver biopsy will be performed during the screening period. Biopsy must be consistent with NASH and cirrhosis according to the NASH CRN classification, as assessed by the central reader
* Must be taking anti-diabetic, anti-obesity, or anti-dyslipidemic medications must have been on stable regimens for at least 3 months (12 weeks) (6 weeks for statins) prior to and during the screening period
* Participants taking vitamin E at doses greater than or equal to (\>=) 800 IU/day must have been on stable doses for at least 6 months (26 weeks) prior to and during the screening period. Vitamin E treatment (\>=800 IU/day) must not have been initiated after the qualifying liver biopsy was performed

Exclusion Criteria

* Other causes of liver disease (e.g., alcoholic liver disease, hepatitis B virus infection, chronic hepatitis C virus infection \[HCV\], autoimmune hepatitis, drug-induced hepatotoxicity, Wilson disease, α-1-antitrypsin deficiency, iron overload, and hemochromatosis); participants with HCV sustained viral response (undetectable HCV RNA) for at least 2 years prior to biopsy confirming study eligibility may be eligible
* Current or past history of hepatocellular carcinoma (HCC)
* Past or current evidence of hepatic decompensation (e.g., ascites, variceal bleeding, hepatic encephalopathy and/or spontaneous bacterial peritonitis) or liver transplantation
* Medical history of gastroesophageal varices, except if esophagogastroduodenoscopy \[EGD\] performed within 12 months prior to the Screening Period has shown \<= Grade 1 varices
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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North Alabama Health Research, LLC

Madison, Alabama, United States

Site Status

Local Institution - 0005

Chandler, Arizona, United States

Site Status

Local Institution - 0088

Phoenix, Arizona, United States

Site Status

Local Institution - 0006

Phoenix, Arizona, United States

Site Status

Local Institution - 0090

Tucson, Arizona, United States

Site Status

Kindred Medical Institute for Clinical Trials

Corona, California, United States

Site Status

Local Institution - 0092

Coronado, California, United States

Site Status

Local Institution - 0038

La Jolla, California, United States

Site Status

Local Institution - 0017

Los Angeles, California, United States

Site Status

Cedars-Sinai Medical Center

Los Angeles, California, United States

Site Status

GastroIntestinal Biosciences

Los Angeles, California, United States

Site Status

Catalina Research Institute

Montclair, California, United States

Site Status

Kaiser Permanente

Oakland, California, United States

Site Status

Diverse Research Solutions

Oxnard, California, United States

Site Status

Huntington Medical Research Institutes - HMRI Liver Center

Pasadena, California, United States

Site Status

Local Institution - 0020

Pasadena, California, United States

Site Status

Local Institution - 0073

Redwood City, California, United States

Site Status

Local Institution - 0012

Rialto, California, United States

Site Status

Local Institution - 0089

San Clemente, California, United States

Site Status

Local Institution

San Diego, California, United States

Site Status

Local Institution - 0014

San Diego, California, United States

Site Status

Local Institution - 0068

San Francisco, California, United States

Site Status

Local Institution - 0042

Bridgeport, Connecticut, United States

Site Status

Local Institution

Washington D.C., District of Columbia, United States

Site Status

Local Institution - 0079

Coral Gables, Florida, United States

Site Status

Top Medical Research

Cutler Bay, Florida, United States

Site Status

Clinical Research of Homestead

Homestead, Florida, United States

Site Status

Mayo Clinic - Jacksonville

Jacksonville, Florida, United States

Site Status

Local Institution - 0001

Lakewood Rch, Florida, United States

Site Status

Local Institution - 0003

Miami, Florida, United States

Site Status

A+ Research

Miami, Florida, United States

Site Status

IMIC Research

Miami, Florida, United States

Site Status

Sensible Healthcare

Ocoee, Florida, United States

Site Status

Local Institution - 0081

Orlando, Florida, United States

Site Status

Local Institution

Tampa, Florida, United States

Site Status

Local Institution

Atlanta, Georgia, United States

Site Status

Local Institution - 0108

Marietta, Georgia, United States

Site Status

Tandem Clinical Research

Marrero, Louisiana, United States

Site Status

Tulane University Health Sciences Center

New Orleans, Louisiana, United States

Site Status

Local Institution - 0026

New Orleans, Louisiana, United States

Site Status

Local Institution - 0010

Baltimore, Maryland, United States

Site Status

Local Institution - 0058

Catonsville, Maryland, United States

Site Status

Boston Medical Center

Boston, Massachusetts, United States

Site Status

NECCR PrimaCare Research

Fall River, Massachusetts, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

Clinical Research Professionals

Chesterfield, Missouri, United States

Site Status

Local Institution - 0031

Kansas City, Missouri, United States

Site Status

Saint Louis University

St Louis, Missouri, United States

Site Status

University at Buffalo

Buffalo, New York, United States

Site Status

Northwell Health

Manhasset, New York, United States

Site Status

Mount Sinai Hospital

New York, New York, United States

Site Status

Local Institution - 0036

New York, New York, United States

Site Status

Icahn School of Medicine at Mount Sinai

New York, New York, United States

Site Status

Local Institution - 0067

Butner, North Carolina, United States

Site Status

Local Institution - 0064

Charlotte, North Carolina, United States

Site Status

Northeast GI Research Division

Concord, North Carolina, United States

Site Status

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

Local Institution - 0009

Philadelphia, Pennsylvania, United States

Site Status

Local Institution - 0004

Pittsburgh, Pennsylvania, United States

Site Status

Local Institution

Chattanooga, Tennessee, United States

Site Status

Local Institution - 0046

Germantown, Tennessee, United States

Site Status

Local Institution - 0041

Hermitage, Tennessee, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Texas Clinical Research Institute

Arlington, Texas, United States

Site Status

Local Institution - 0066

Austin, Texas, United States

Site Status

Local Institution - 0051

Dallas, Texas, United States

Site Status

Local Institution - 0053

Dallas, Texas, United States

Site Status

Texas Digestive Disease Consultants - Dallas

Dallas, Texas, United States

Site Status

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status

Local Institution - 0084

Fort Worth, Texas, United States

Site Status

Local Institution - 0002

Houston, Texas, United States

Site Status

Local Institution - 0057

Houston, Texas, United States

Site Status

Local Institution - 0063

Houston, Texas, United States

Site Status

Local Institution - 0028

San Antonio, Texas, United States

Site Status

Local Institution - 0011

San Antonio, Texas, United States

Site Status

Local Institution - 0102

San Antonio, Texas, United States

Site Status

University of Vermont Medical Center

Burlington, Vermont, United States

Site Status

University of Virginia Health System

Charlottesville, Virginia, United States

Site Status

Inova Fairfax Hospital

Falls Church, Virginia, United States

Site Status

Gastroenterology Associates, PC

Manassas, Virginia, United States

Site Status

Local Institution - 0069

Norfolk, Virginia, United States

Site Status

The Gastroenterology Group

Reston, Virginia, United States

Site Status

Bon Secours Liver Institute of Richmond

Richmond, Virginia, United States

Site Status

Local Institution - 0077

Richmond, Virginia, United States

Site Status

Local Institution - 0050

Richmond, Virginia, United States

Site Status

Kurume University Hospital

Kurume, Fukuoka, Japan

Site Status

Local Institution - 0055

Yokohama, Kanagawa, Japan

Site Status

Local Institution - 0072

Kashihara, Nara, Japan

Site Status

Toranomon Hospital

Minato, Tokyo, Japan

Site Status

Keio University Hospital

Shinjuku-ku, Tokyo, Japan

Site Status

Fukushima Medical University Hospital

Fukushima, , Japan

Site Status

Countries

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United States Japan

References

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Abdelmalek MF, Sanyal AJ, Nakajima A, Neuschwander-Tetri BA, Goodman ZD, Lawitz EJ, Harrison SA, Jacobson IM, Imajo K, Gunn N, Halegoua-DeMarzio D, Akahane T, Boone B, Yamaguchi M, Chatterjee A, Tirucherai GS, Shevell DE, Du S, Charles ED, Loomba R. Pegbelfermin in Patients With Nonalcoholic Steatohepatitis and Compensated Cirrhosis (FALCON 2): A Randomized Phase 2b Study. Clin Gastroenterol Hepatol. 2024 Jan;22(1):113-123.e9. doi: 10.1016/j.cgh.2023.04.012. Epub 2023 Apr 23.

Reference Type DERIVED
PMID: 37088458 (View on PubMed)

Abdelmalek MF, Charles ED, Sanyal AJ, Harrison SA, Neuschwander-Tetri BA, Goodman Z, Ehman RA, Karsdal M, Nakajima A, Du S, Tirucherai GS, Klinger GH, Mora J, Yamaguchi M, Shevell DE, Loomba R. The FALCON program: Two phase 2b randomized, double-blind, placebo-controlled studies to assess the efficacy and safety of pegbelfermin in the treatment of patients with nonalcoholic steatohepatitis and bridging fibrosis or compensated cirrhosis. Contemp Clin Trials. 2021 May;104:106335. doi: 10.1016/j.cct.2021.106335. Epub 2021 Feb 28.

Reference Type DERIVED
PMID: 33657443 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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MB130-069

Identifier Type: -

Identifier Source: org_study_id

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