Evaluation of Efficacy, Safety and Tolerability of Aldafermin in a Phase 2b, Randomized, Double-blind, Placebo-controlled, Multi-center Study In Subjects With Nonalcoholic Steatohepatitis and Stage 2/3 Fibrosis (ALPINE 2/3)

NCT ID: NCT03912532

Last Updated: 2025-07-03

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

171 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-05-16

Study Completion Date

2021-03-29

Brief Summary

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This is a multi-center evaluation of NGM282 in a randomized, double-blind, placebo-controlled study administered for 24 weeks in participants with histologically confirmed NASH and F2/F3 Fibrosis.

Detailed Description

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Conditions

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NASH - Nonalcoholic Steatohepatitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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NGM282 Dose 1

Administered by subcutaneous injection

Group Type EXPERIMENTAL

NGM282

Intervention Type BIOLOGICAL

NGM282

NGM282 Dose 2

Administered by subcutaneous injection

Group Type EXPERIMENTAL

NGM282

Intervention Type BIOLOGICAL

NGM282

NGM282 Dose 3

Administered by subcutaneous injection

Group Type EXPERIMENTAL

NGM282

Intervention Type BIOLOGICAL

NGM282

Placebo

Administered by subcutaneous injection

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Placebo for NGM282

Interventions

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NGM282

NGM282

Intervention Type BIOLOGICAL

Placebo

Placebo for NGM282

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

1. Histologically confirmed NASH diagnosis as defined by the NASH CRN
2. Total liver fat content of ≥ 8% as measured by MRI-PDFF

Exclusion Criteria

1. Clinically significant acute or chronic liver disease of an etiology other than NASH
2. Evidence of drug-induced steatohepatitis secondary to amiodarone, corticosteroids, estrogens, methotrexate, tetracycline, or other medications known to cause hepatic steatosis
3. History or presence of cirrhosis (compensated or decompensated) as determined by histology and/or relevant medical complications and/or laboratory parameters
4. Prior or pending liver transplantation
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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NGM Biopharmaceuticals, Inc

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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NGM Study Director

Role: STUDY_DIRECTOR

NGM Biopharmaceuticals

Locations

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NGM Clinical Study Site

Chandler, Arizona, United States

Site Status

NGM Clinical Study Site 814

Tucson, Arizona, United States

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NGM Clinical Study Site 816

Tucson, Arizona, United States

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NGM Clinical Study Site

North Little Rock, Arkansas, United States

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NGM Clinical Study Site

Fresno, California, United States

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NGM Clinical Study Site

La Jolla, California, United States

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NGM Clinical Study Site

Los Angeles, California, United States

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NGM Clinical Study Site

Los Angeles, California, United States

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NGM Clinical Study Site

Poway, California, United States

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NGM Clinical Study Site

Rialto, California, United States

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NGM Clinical Study Site

Boca Raton, Florida, United States

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NGM Clinical Study Site

Lakewood Rch, Florida, United States

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NGM Clinical Study Site

Port Orange, Florida, United States

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NGM Clinical Study Site

Sarasota, Florida, United States

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NGM Clinical Study Site

The Villages, Florida, United States

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NGM Clinical Study Site

Chicago, Illinois, United States

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NGM Clinical Study Site

Baton Rouge, Louisiana, United States

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NGM Clinical Study Site

Baltimore, Maryland, United States

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NGM Clinical Study Site

Ann Arbor, Michigan, United States

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NGM Clinical Study Site

Flowood, Mississippi, United States

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NGM Clinical Study Site

Jackson, Mississippi, United States

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NGM Clinical Study Site

Kansas City, Missouri, United States

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NGM Clinical Study Site

St Louis, Missouri, United States

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NGM Clinical Study Site

New York, New York, United States

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NGM Clinical Study Site

Durham, North Carolina, United States

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NGM Clinical Study Site

Fayetteville, North Carolina, United States

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NGM Clinical Study Site

Germantown, Tennessee, United States

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NGM Clinical Study Site

Hermitage, Tennessee, United States

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NGM Clinical Study Site

Austin, Texas, United States

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NGM Clinical Study Site 845

Edinburg, Texas, United States

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NGM Clinical Study Site

Edinburg, Texas, United States

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NGM Clinical Study Site

Houston, Texas, United States

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NGM Clinical Study Site

San Antonio, Texas, United States

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NGM Clinical Study Site

San Antonio, Texas, United States

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NGM Clinical Study Site

Richmond, Virginia, United States

Site Status

NGM Clinical Study Site

Richmond, Virginia, United States

Site Status

NGM Clinical Study Site

San Juan, , Puerto Rico

Site Status

Countries

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United States Puerto Rico

References

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Harrison SA, Abdelmalek MF, Neff G, Gunn N, Guy CD, Alkhouri N, Bashir MR, Freilich B, Kohli A, Khazanchi A, Sheikh MY, Leibowitz M, Rinella ME, Siddiqui MS, Kipnes M, Moussa SE, Younes ZH, Bansal M, Baum SJ, Borg B, Ruane PJ, Thuluvath PJ, Gottwald M, Khan M, Chen C, Melchor-Khan L, Chang W, DePaoli AM, Ling L, Lieu HD. Aldafermin in patients with non-alcoholic steatohepatitis (ALPINE 2/3): a randomised, double-blind, placebo-controlled, phase 2b trial. Lancet Gastroenterol Hepatol. 2022 Jul;7(7):603-616. doi: 10.1016/S2468-1253(22)00017-6. Epub 2022 Mar 21.

Reference Type DERIVED
PMID: 35325622 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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18-0108

Identifier Type: -

Identifier Source: org_study_id

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