A Study of ALN-HSD in Healthy Adult Subjects and Adult Patients With Nonalcoholic Steatohepatitis (NASH)

NCT ID: NCT04565717

Last Updated: 2024-05-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

TERMINATED

Clinical Phase

PHASE1

Total Enrollment

6 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-10-09

Study Completion Date

2023-12-21

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to evaluate the safety and tolerability of single ascending doses of ALN-HSD in healthy participants (Part A) and multiple doses of ALN-HSD in patients with NASH (Parts B and C).

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Nonalcoholic Steatohepatitis NASH

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Parts A\&B: Quadruple (Participant, Care Provider, Investigator, Outcomes Assessor); Part C: Open label

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Part A: ALN-HSD

Participants will be administered a single dose of ALN-HSD.

Group Type EXPERIMENTAL

ALN-HSD

Intervention Type DRUG

ALN-HSD will be administered by subcutaneous (SC) injection.

Part A: Placebo

Participants will be administered a single dose of ALN-HSD-matching placebo.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Normal saline (0.9% NaCl) matching volume of ALN-HSD doses will be administered SC.

Part B: ALN-HSD

Participants will be administered multiple doses of ALN-HSD.

Group Type EXPERIMENTAL

ALN-HSD

Intervention Type DRUG

ALN-HSD will be administered by subcutaneous (SC) injection.

Part B: Placebo

Participants will be administered multiple doses of ALN-HSD-matching placebo.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Normal saline (0.9% NaCl) matching volume of ALN-HSD doses will be administered SC.

Part C: ALN-HSD

Participants will be administered multiple doses of ALN-HSD.

Group Type EXPERIMENTAL

ALN-HSD

Intervention Type DRUG

ALN-HSD will be administered by subcutaneous (SC) injection.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

ALN-HSD

ALN-HSD will be administered by subcutaneous (SC) injection.

Intervention Type DRUG

Placebo

Normal saline (0.9% NaCl) matching volume of ALN-HSD doses will be administered SC.

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Part A Only

* Has body mass index (BMI) ≥18 kg/m\^2 and ≤28 kg/m\^2
* Has normal 12-lead electrocardiogram (ECG)
* Parts B and C Only:

* Has BMI ≥18 kg/m\^2 and ≤40 kg/m\^2
* Has a diagnosis of NASH documented in the patient's medical history or a clinical suspicion of NASH based on defined study criteria
* Has screening liver biopsy with NASH activity score (NAS) score of ≥3 per NASH Clinical Research Network (CRN) criteria

Exclusion Criteria

* Parts A, B and C:

* Has any clinical safety laboratory result considered clinically significant and unacceptable by the Investigator
* Has known active human immunodeficiency virus (HIV), hepatitis B virus (HBV), or hepatitis C virus (HCV) infection
* Has known history or evidence of drug abuse, within 12 months prior to screening
* Has evidence of other forms of known chronic liver disease
* Has recently received an investigational agent
* Has any uncontrolled or serious disease, medical or surgical condition that my interfere with participation or data interpretation
* Has excessive alcohol intake for ≥ 3 months during past year
* Has history of intolerance to SC injection(s)
* Has international normalized ratio (INR) \>1.2
* Has platelet count \<140x10\^9/L
* Part A Only

* Has systolic blood pressure (BP) \>140 mmHg and diastolic \>90 mmHg;
* Has used certain prescription drugs within last 14 days prior to screening
* Has used certain over the counter (OTC) medication within 7 days prior to screening
* Has estimated glomerular filtration rate (GFR) \<90 mL/min/1.73m\^2 at screening
* Parts B and C Only

* Has abnormal ECG
* Has changes in certain prescription medications defined in the protocol within the specified timeframe prior to screening
* Has GFR\<45ml/min/1.73m\^2
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Alnylam Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Medical Director

Role: STUDY_DIRECTOR

Alnylam Pharmaceuticals

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Clinical Trial Site

Fleming Island, Florida, United States

Site Status

Clinical Trial Site

Marrero, Louisiana, United States

Site Status

Clinical Trial Site

Baltimore, Maryland, United States

Site Status

Clinical Trial Site

Hermitage, Tennessee, United States

Site Status

Clinical Trial Site

San Antonio, Texas, United States

Site Status

Clinical Trial Site

San Antonio, Texas, United States

Site Status

Clinical Trial Site

San Antonio, Texas, United States

Site Status

Clinical Trial Site

Brussels, , Belgium

Site Status

Clinical Trial Site

Sofia, , Bulgaria

Site Status

Clinical Trial Site

Balçova, , Turkey (Türkiye)

Site Status

Clinical Trial Site

Izmir, , Turkey (Türkiye)

Site Status

Clinical Trial Site

Edinburgh, , United Kingdom

Site Status

Clinical Trial Site

London, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Belgium Bulgaria Turkey (Türkiye) United Kingdom

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2020-000847-29

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

ALN-HSD-001

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Phase 2b Study of GSK4532990 in Adults With NASH
NCT05583344 ACTIVE_NOT_RECRUITING PHASE2