A Study of Efruxifermin in Subjects With Compensated Cirrhosis Due to Nonalcoholic Steatohepatitis (NASH) (Symmetry)

NCT ID: NCT05039450

Last Updated: 2025-04-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

182 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-07-30

Study Completion Date

2025-05-31

Brief Summary

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This is a multi-center evaluation of efruxifermin (EFX) in a randomized, double-blind, placebo-controlled study in cirrhotic subjects with biopsy-proven F4 compensated NASH.

Detailed Description

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Conditions

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NASH - Nonalcoholic Steatohepatitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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EFX 28 mg (Main Study)

Group Type EXPERIMENTAL

EFX

Intervention Type DRUG

Investigational drug, Efruxifermin

EFX 50 mg (Main Study)

Group Type EXPERIMENTAL

EFX

Intervention Type DRUG

Investigational drug, Efruxifermin

Placebo (Main Study)

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo

EFX 50 mg (Cohort D)

Group Type EXPERIMENTAL

EFX

Intervention Type DRUG

Investigational drug, Efruxifermin

Placebo (Cohort D)

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo

Interventions

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EFX

Investigational drug, Efruxifermin

Intervention Type DRUG

Placebo

Placebo

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Males and non-pregnant, non-lactating females between 18-75 years of age inclusive, based on the date of signing informed consent.
* Main Study Only: Previous history or presence of Type 2 diabetes or 2 out of 4 components of metabolic syndrome (obesity, dyslipidemia, elevated blood pressure, elevated fasting glucose).
* Main Study Only: Biopsy-proven compensated cirrhosis due to NASH.
* Cohort D Only: Diagnosis of type 2 diabetes
* Cohort D Only: Use of GLP-1R agonist for at least 90 days
* Cohort D Only: Biopsy-proven liver fibrosis stages 1, 2, or 3

Exclusion Criteria

* Main Study Only: Weight loss \> 10% in the 90 days prior to screening until randomization or from the time of collection of the liver biopsy used to assess subject eligibility until randomization, whichever is longer.
* Type 1 diabetes or uncontrolled Type 2 diabetes
* Cohort D Only: Weight loss \> 5% in the 90 days prior to screening
* Cohort D Only: Presence of cirrhosis on liver biopsy
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Akero Therapeutics, Inc

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Akero Clinical Study Site

Chandler, Arizona, United States

Site Status

Akero Clinical Study Site

Glendale, Arizona, United States

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Akero Clinical Study Site

Tucson, Arizona, United States

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Akero Clinical Study Site

Tucson, Arizona, United States

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Akero Clinical Study Site

North Little Rock, Arkansas, United States

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Akero Clinical Study Site

Fresno, California, United States

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Akero Clinical Study Site

Long Beach, California, United States

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Akero Clinical Study Site

Los Angeles, California, United States

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Akero Clinical Study Site

Pasadena, California, United States

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Akero Clinical Study Site

Englewood, Colorado, United States

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Akero Clinical Study Site

Clearwater, Florida, United States

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Akero Clinical Study Site

Fort Myers, Florida, United States

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Akero Clinical Study Site

Fort Myers, Florida, United States

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Akero Clinical Study Site

Hialeah Gardens, Florida, United States

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Akero Clinical Study Site

Lakewood Rch, Florida, United States

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Akero Clinical Study Site

Miami Lakes, Florida, United States

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Akero Clinical Study Site

Ocala, Florida, United States

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Akero Clinical Study Site

Sarasota, Florida, United States

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Akero Clinical Study Site

South Bend, Indiana, United States

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Akero Clinical Study Site

Topeka, Kansas, United States

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Akero Clinical Study Site

Bastrop, Louisiana, United States

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Akero Clinical Study Site

Marrero, Louisiana, United States

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Akero Clinical Study Site

Las Vegas, Nevada, United States

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Akero Clinical Study Site

Concord, North Carolina, United States

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Akero Clinical Study Site

Fayetteville, North Carolina, United States

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Akero Clinical Study Site

Morehead City, North Carolina, United States

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Akero Clinical Study Site

Springboro, Ohio, United States

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Akero Clinical Study Site

Westlake, Ohio, United States

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Akero Clinical Study Site

Greenville, South Carolina, United States

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Akero Clinical Study Site

Greenwood, South Carolina, United States

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Akero Clinical Study Site

Summerville, South Carolina, United States

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Akero Clinical Study Site

Nashville, Tennessee, United States

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Akero Clinical Study Site

Austin, Texas, United States

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Akero Clinical Study Site

Dallas, Texas, United States

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Akero Clinical Study Site

Edinburg, Texas, United States

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Akero Clinical Study Site

Edinburg, Texas, United States

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Akero Clinical Study Site

Fort Worth, Texas, United States

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Akero Clinical Study Site

Fort Worth, Texas, United States

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Akero Clinical Study Site

Houston, Texas, United States

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Akero Clinical Study Site

Houston, Texas, United States

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Akero Clinical Study Site

San Antonio, Texas, United States

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Akero Clinical Study Site

Waco, Texas, United States

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Akero Clinical Study Site

Webster, Texas, United States

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Akero Clinical Study Site

Wichita Falls, Texas, United States

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Akero Clinical Study Site

Ogden, Utah, United States

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Akero Clinical Study Site

Richmond, Virginia, United States

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Akero Clinical Study Site

Mexico City, , Mexico

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Akero Clinical Study Site

Monterrey, , Mexico

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Akero Clinical Study Site

San Juan, , Puerto Rico

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Countries

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United States Mexico Puerto Rico

References

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Noureddin M, Rinella ME, Chalasani NP, Neff GW, Lucas KJ, Rodriguez ME, Rudraraju M, Patil R, Behling C, Burch M, Chan DC, Tillman EJ, Zari A, de Temple B, Shringarpure R, Jain M, Rolph T, Cheng A, Yale K. Efruxifermin in Compensated Liver Cirrhosis Caused by MASH. N Engl J Med. 2025 Jun 26;392(24):2413-2424. doi: 10.1056/NEJMoa2502242. Epub 2025 May 9.

Reference Type DERIVED
PMID: 40341827 (View on PubMed)

Harrison SA, Frias JP, Lucas KJ, Reiss G, Neff G, Bollepalli S, Su Y, Chan D, Tillman EJ, Moulton A, de Temple B, Zari A, Shringarpure R, Rolph T, Cheng A, Yale K. Safety and Efficacy of Efruxifermin in Combination With a GLP-1 Receptor Agonist in Patients With NASH/MASH and Type 2 Diabetes in a Randomized Phase 2 Study. Clin Gastroenterol Hepatol. 2025 Jan;23(1):103-113. doi: 10.1016/j.cgh.2024.02.022. Epub 2024 Mar 4.

Reference Type DERIVED
PMID: 38447814 (View on PubMed)

Other Identifiers

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AK-US-001-0103

Identifier Type: -

Identifier Source: org_study_id

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