A Study of Efruxifermin in Subjects With Histologically Confirmed Nonalcoholic Steatohepatitis (NASH)

NCT ID: NCT03976401

Last Updated: 2022-08-04

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

110 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-05-28

Study Completion Date

2022-01-10

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This is a multi-center evaluation of efruxifermin (EFX) in a randomized, double-blind, placebo-controlled study administered for 16 weeks in subjects with biopsy proven F1 - F4 NASH.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

NASH - Nonalcoholic Steatohepatitis

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

EFX Dose 1

Main Study

Group Type EXPERIMENTAL

EFX

Intervention Type DRUG

Administered by subcutaneous injection

EFX Dose 2

Main Study

Group Type EXPERIMENTAL

EFX

Intervention Type DRUG

Administered by subcutaneous injection

EFX Dose 3

Main Study

Group Type EXPERIMENTAL

EFX

Intervention Type DRUG

Administered by subcutaneous injection

Placebo

Main Study

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Administered by subcutaneous injection

EFX Dose (Cohort C)

Group Type EXPERIMENTAL

EFX

Intervention Type DRUG

Administered by subcutaneous injection

Placebo (Cohort C)

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Administered by subcutaneous injection

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

EFX

Administered by subcutaneous injection

Intervention Type DRUG

Placebo

Administered by subcutaneous injection

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Males and non-pregnant, non-lactating females between 18 - 80 years of age inclusive, based on the date of the screening visit.
* Main Study only: Body mass index (BMI) \> 25 kg/m\^2 (unless the patient has biopsy-proven NASH documented within the last 2 years).
* Main Study only: Must have confirmation of ≥ 10% liver fat content on magnetic resonance imaging- proton density fat fraction (MRI-PDFF) at screening.
* Main Study only: Biopsy-proven NASH. Must have had a liver biopsy within 180 days of randomization with fibrosis stage 1 to 3 and a non-alcoholic fatty liver disease (NAFLD) activity score (NAS) of ≥ 4 with at least a score of 1 in each of the following NAS components:

* Steatosis (scored 0 to 3),
* Ballooning degeneration (scored 0 to 2), and
* Lobular inflammation (scored 0 to 3)
* Cohort C only: FibroScan® measurement \> 13.1 kPa.
* Cohort C only: Cirrhosis due to NASH. Liver biopsy consistent with F4 fibrosis according to the NAS system, confirmed by the central or local reader.

Exclusion Criteria

* Weight gain or loss \> 5% in the 3 months prior to randomization or \> 10% in the 6 months prior to screening.
* Type 1 and insulin-dependent Type 2 diabetes.
* Poorly controlled hypertension (blood pressure \> 160/100).
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Akero Therapeutics, Inc

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Akero Clinical Study Site

Tucson, Arizona, United States

Site Status

Akero Clinical Study Site

Little Rock, Arkansas, United States

Site Status

Akero Clinical Study Site

Huntington Park, California, United States

Site Status

Akero Clinical Study Site

Los Angeles, California, United States

Site Status

Akero Clinical Study Site

Los Angeles, California, United States

Site Status

Akero Clinical Study Site

Panorama City, California, United States

Site Status

Akero Clinical Study Site

Poway, California, United States

Site Status

Akero Clinical Study Site

Boca Raton, Florida, United States

Site Status

Akero Clinical Study Site

Lakewood Rch, Florida, United States

Site Status

Akero Clinical Study Site

Miami, Florida, United States

Site Status

Akero Clinical Study Site

New Port Richey, Florida, United States

Site Status

Akero Clinical Study Site

Ocoee, Florida, United States

Site Status

Akero Clinical Study Site

Port Orange, Florida, United States

Site Status

Akero Clinical Study Site

Sarasota, Florida, United States

Site Status

Akero Clinical Study Site

Baton Rouge, Louisiana, United States

Site Status

Akero Clinical Study Site

Marrero, Louisiana, United States

Site Status

Akero Clinical Study Site

Kansas City, Missouri, United States

Site Status

Akero Clinical Study Site

Berlin, New Jersey, United States

Site Status

Akero Clinical Study Site

Chattanooga, Tennessee, United States

Site Status

Akero Clinical Study Site

Cedar Park, Texas, United States

Site Status

Akero Clinical Study Site

Dallas, Texas, United States

Site Status

Akero Clinical Study Site

Edinburg, Texas, United States

Site Status

Akero Clinical Study Site

Fort Worth, Texas, United States

Site Status

Akero Clinical Study Site

San Antonio, Texas, United States

Site Status

Akero Clinical Study Site

San Antonio, Texas, United States

Site Status

Akero Clinical Study Site

Webster, Texas, United States

Site Status

Akero Clinical Study Site

San Juan, , Puerto Rico

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Puerto Rico

References

Explore related publications, articles, or registry entries linked to this study.

Alkhouri N, Beyer C, Shumbayawonda E, Andersson A, Yale K, Rolph T, Chung RT, Vuppalanchi R, Cusi K, Loomba R, Pansini M, Dennis A. Decreases in cT1 and liver fat content reflect treatment-induced histological improvements in MASH. J Hepatol. 2025 Mar;82(3):438-445. doi: 10.1016/j.jhep.2024.08.031. Epub 2024 Sep 25.

Reference Type DERIVED
PMID: 39326675 (View on PubMed)

Harrison SA, Ruane PJ, Freilich B, Neff G, Patil R, Behling C, Hu C, Shringarpure R, de Temple B, Fong E, Tillman EJ, Rolph T, Cheng A, Yale K. A randomized, double-blind, placebo-controlled phase IIa trial of efruxifermin for patients with compensated NASH cirrhosis. JHEP Rep. 2022 Aug 23;5(1):100563. doi: 10.1016/j.jhepr.2022.100563. eCollection 2023 Jan.

Reference Type DERIVED
PMID: 36644237 (View on PubMed)

Harrison SA, Ruane PJ, Freilich BL, Neff G, Patil R, Behling CA, Hu C, Fong E, de Temple B, Tillman EJ, Rolph TP, Cheng A, Yale K. Efruxifermin in non-alcoholic steatohepatitis: a randomized, double-blind, placebo-controlled, phase 2a trial. Nat Med. 2021 Jul;27(7):1262-1271. doi: 10.1038/s41591-021-01425-3. Epub 2021 Jul 8.

Reference Type DERIVED
PMID: 34239138 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan: Main Study

View Document

Document Type: Statistical Analysis Plan: Cohort C

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

AK-US-001-0101

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Phase 2b Study of GSK4532990 in Adults With NASH
NCT05583344 ACTIVE_NOT_RECRUITING PHASE2