A Study of Safety, Tolerability, Pharmacodynamics, and Pharmacokinetics of KAN-101 in Celiac Disease (ACeD-it)

NCT ID: NCT05574010

Last Updated: 2025-05-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

TERMINATED

Clinical Phase

PHASE1/PHASE2

Total Enrollment

126 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-11-15

Study Completion Date

2025-05-19

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This study is to evaluate the Pharmacodynamic (PD), safety, tolerability, Pharmacokinetic (PK), and plasma biomarker response of KAN-101 in participants with Celiac Disease (CeD).

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

The study is a 3-part, multicenter Phase 1b/2 study of KAN-101 in participants with Celiac Disease (CeD) on a gluten free diet (GFD). The 3 parts include:

* Part A - Open-label, multiple ascending dose
* Part B - Double-blind, placebo-controlled, parallel design
* Part C - Double-blind, placebo-controlled, parallel design

Part A is a Phase 1b, open-label, multiple ascending dose (MAD) study design to assess the safety, tolerability, and pharmacokinetics (PK) of KAN-101 in adult participants (18 to 70 years inclusive) with histology-confirmed CeD. Up to 12 participants who meet study inclusion/exclusion criteria will receive 1 of 2 dose levels of KAN-101. The overall study duration will be about 56 days, including up to 28 days of screening, 7 days of treatment and 21 days of follow up. There will be a gluten challenge test (GC) on Day 15.

Parts B and C are Phase 2, double-blind, placebo-controlled, parallel design study to characterize the biomarker response following GC, safety, tolerability, and PK of KAN-101 in adult participants with histology-confirmed CeD. Approximately 16 participants (4 participants per dose group) will be enrolled in Part B and 104 participants (26 participants per dose group) enrolled into Part C. Participants will be randomized 1:1:1:1 and stratified by participation in a biopsy substudy to 4 treatment groups: placebo and 3 treatment groups with KAN-101 doses based on information obtained from Part A.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Celiac Disease

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Part A: This part of the study is an open label with up to 6 participants in each dose cohort. There will be 2 dose cohorts.

Part B and Part C: These parts of the study have a randomized, double- blinded, placebo-controlled, parallel study design.
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors
Part A is open label Part B and Part C are a double-blinded study. Study participants and their caregivers, investigators and other site staff, and sponsor staff involved in the study team will be blinded.

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Cohort 1 in Part A

All eligible Part A participants will receive 3 intravenous (IV) infusions of KAN-101 Dose 1

Group Type EXPERIMENTAL

Cohort 1 in Part A

Intervention Type DRUG

Dose 1 KAN-101 Intravenous (IV) infusion

Cohort 2 in Part A

All eligible Part A participants will receive 3 intravenous (IV) infusions of KAN-101 Dose 2

Group Type EXPERIMENTAL

Cohort 2 in Part A

Intervention Type DRUG

Dose 2 KAN-101 Intravenous (IV) infusion

Group 1 in Part B and Part C

All eligible Part B and Part C participants will receive 3 intravenous (IV) infusions of placebo

Group Type PLACEBO_COMPARATOR

Placebo: Group 1 in Part B and Part C

Intervention Type OTHER

Placebo Intravenous (IV) infusion

Group 2 in Part B and Part C

All eligible Part B and Part C participants will receive 3 intravenous (IV) infusions of KAN-101 Dose 3

Group Type EXPERIMENTAL

Group 2 in Part B and Part C

Intervention Type DRUG

Dose 3 KAN-101 Intravenous (IV) infusion

Group 3 in Part B and Part C

All eligible Part B and Part C participants will receive 3 intravenous (IV) infusions of KAN-101 Dose 4

Group Type EXPERIMENTAL

Group 3 in Part B and Part C

Intervention Type DRUG

Dose 4 KAN-101 Intravenous (IV) infusion

Group 4 in Part B and Part C

All eligible Part B and Part C participants will receive 3 intravenous (IV) infusions of KAN-101 Dose 5

Group Type EXPERIMENTAL

Group 4 in Part B and Part C

Intervention Type DRUG

Dose 5 KAN-101 Intravenous (IV) infusion

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Cohort 1 in Part A

Dose 1 KAN-101 Intravenous (IV) infusion

Intervention Type DRUG

Cohort 2 in Part A

Dose 2 KAN-101 Intravenous (IV) infusion

Intervention Type DRUG

Placebo: Group 1 in Part B and Part C

Placebo Intravenous (IV) infusion

Intervention Type OTHER

Group 2 in Part B and Part C

Dose 3 KAN-101 Intravenous (IV) infusion

Intervention Type DRUG

Group 3 in Part B and Part C

Dose 4 KAN-101 Intravenous (IV) infusion

Intervention Type DRUG

Group 4 in Part B and Part C

Dose 5 KAN-101 Intravenous (IV) infusion

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

KAN-101 KAN-101 Placebo KAN-101 KAN-101 KAN-101

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Previous diagnosis of celiac disease based on histology and positive celiac serology
* HLA-DQ2.5 genotype
* Gluten-free diet for at least 12 months
* Negative or weak positive for transglutaminase IgA and negative or weak positive for DGP-IgA/IgG during screening

Exclusion Criteria

* Refractory celiac disease
* HLA-DQ8 genotype
* Previous oral gluten challenge within 12 months
* Selective IgA deficiency
* Diagnosis of Type-1 diabetes
* Active gastrointestinal diseases
* History of dermatitis herpetiformis
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Pfizer

INDUSTRY

Sponsor Role collaborator

Kanyos Bio, Inc., a wholly-owned subsidiary of Anokion SA

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Study Director

Role: STUDY_DIRECTOR

Anokion SA

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Anaheim Clinical Trials, LLC

Anaheim, California, United States

Site Status

GCP Research

St. Petersburg, Florida, United States

Site Status

Agile Clinical Research Trials

Sandy Springs, Georgia, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

Sneeze, Wheeze & Itch Associates, LLC

Normal, Illinois, United States

Site Status

Indiana University Health University Hospital

Indianapolis, Indiana, United States

Site Status

University of Iowa

Iowa City, Iowa, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

Prism Research LLC dba Nucleus Network

Saint Paul, Minnesota, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Quality Clinical Research

Omaha, Nebraska, United States

Site Status

Celiac Disease Center at Columbia University

New York, New York, United States

Site Status

North Carolina Clinical Research

Raleigh, North Carolina, United States

Site Status

Aventiv Research, Inc. d/b/a Centricity Research

Columbus, Ohio, United States

Site Status

Great Lakes Gastroenterology Research, LLC

Mentor, Ohio, United States

Site Status

Northshore Gastroenterology Research, LLC

Westlake, Ohio, United States

Site Status

Penn State Milton S. Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

The University of Texas Health Science Center at Houston

Houston, Texas, United States

Site Status

Digestive Research of Central Texas

Waco, Texas, United States

Site Status

Advanced Research Institute

Ogden, Utah, United States

Site Status

Velocity Clinical Research, Salt Lake City

West Jordan, Utah, United States

Site Status

Campbelltown Hospital

Campbelltown, New South Wales, Australia

Site Status

Wesley Research Institute

Auchenflower, Queensland, Australia

Site Status

Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status

Box Hill Hospital

Box Hill, Victoria, Australia

Site Status

The Royal Melbourne Hospital

Parkville, Victoria, Australia

Site Status

St John of God Midland Public and Private Hospitals

Midland, Western Australia, Australia

Site Status

PCRN Trials

Takapuna, Auckland, New Zealand

Site Status

P3 Research - Tauranga

Tauranga, Bay of Plenty, New Zealand

Site Status

P3 Research - Dunedin

Dunedin, Otago, New Zealand

Site Status

P3 Research - Palmerston North

Paraparaumu, Wellington Region, New Zealand

Site Status

Optimal Clinical Trials

Auckland, , New Zealand

Site Status

Waikato Hospital

Hamilton, , New Zealand

Site Status

P3 Research - Wellington

Wellington, , New Zealand

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Australia New Zealand

References

Explore related publications, articles, or registry entries linked to this study.

Murray JA, Wassaf D, Dunn K, Arora S, Winkle P, Stacey H, Cooper S, Goldstein KE, Manchanda R, Kontos S, Grebe KM. Safety and tolerability of KAN-101, a liver-targeted immune tolerance therapy, in patients with coeliac disease (ACeD): a phase 1 trial. Lancet Gastroenterol Hepatol. 2023 Aug;8(8):735-747. doi: 10.1016/S2468-1253(23)00107-3. Epub 2023 Jun 14.

Reference Type BACKGROUND
PMID: 37329900 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

KAN-101-02

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Study of Latiglutenase in T1D/CD Patients
NCT04839575 TERMINATED PHASE2
Study of Enzyme Supplements to Treat Celiac Disease
NCT00962182 COMPLETED PHASE1/PHASE2