Dose-Ranging Study of the Efficacy and Safety of TAK-101 for Prevention of Gluten-Specific T Cell Activation in Participants With Celiac Disease on a Gluten-Free Diet

NCT ID: NCT04530123

Last Updated: 2026-01-15

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

102 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-06-23

Study Completion Date

2026-01-08

Brief Summary

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The main aim of the study is to assess if TAK-101 can reduce gluten related symptoms and immune activation in adult participants with celiac disease (CeD) on a gluten-free diet (GFD).

Participants will receive TAK-101 and/or placebo through the vein on Day 1 and Day 8. All participants will receive active treatment at Week 24.

Detailed Description

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The drug being tested in this study is called TAK-101. TAK-101 is being tested to treat people who have celiac disease. The study has 2 cohorts planned. Cohort 1 has 1 dose level and the Cohort 2 may include 1 or 2 additional dose levels, depending on safety, tolerability, and activity observed in Cohort 1. Dosing in the Cohort 2 will be based on data from Cohort 1.

The study will enroll approximately 90 patients. In Cohort 1, approximately 45 participants will be randomly assigned in 1:2:2 ratio in one of the three arm groups which will remain undisclosed to the participant and study doctor during the study (unless there is an urgent medical need). Eligible participants in Cohort 1 will receive:

* Group A: 2 infusion doses of placebo, 1 infusion dose on Day 1 and 1 infusion dose on Day 8, followed by 1 infusion dose of 25 micrograms per kilogram (µg/kg) Gluten Epitopes (GE) TAK-101 at Week 24.
* Group B: 1 infusion dose of 25 µg/kg GE TAK-101 on Day 1 followed by 1 infusion dose of placebo on Day 8, followed by 1 infusion dose of 25 µg/kg GE TAK-101 at Week 24.
* Group C: 2 infusion doses of 25 µg/kg GE TAK-101, 1 infusion dose on Day 1 and 1 infusion dose on Day 8, followed by 1 infusion dose of 25 µg/kg GE TAK-101 at Week 24.

If it is deemed appropriate to enroll both the TAK-101 50 µg/kg GE and the 12.5 µg/kg GE dose levels in Cohort 2, approximately 45 participants may be randomly assigned in 1:2:2 ratio in Cohort 2 to receive:

* Group A: Two infusion doses of placebo, 1 infusion dose on Day 1 and 1 infusion dose on Day 8, followed by 1 infusion dose of 25 µg/kg GE TAK-101 at Week 24.
* Group D: Two infusion doses of 50 µg/kg GE TAK-101, 1 infusion dose on Day 1 and 1 infusion dose on Day 8, followed by 1 infusion dose of 50 µg/kg GE TAK-101 at Week 24.
* Group F: Two infusion doses of 12.5 µg/kg GE TAK-101, 1 infusion dose on Day 1 and 1 infusion dose on Day 8, followed by 1 infusion dose of 12.5 µg/kg GE TAK-101 at Week 24.

If it is decided not to open the second cohort at the 50 µg/kg GE dose level and if 1 2.5 µg/kg GE dose is recommended to be tested by the independent data monitoring committee (IDMC), approximately 27 participants will be randomly assigned in 1:2 ratio to receive:

* Group E: Two infusion doses of placebo, 1 infusion dose on Day 1 and 1 infusion dose on Day 8, followed by 1 infusion dose of 12.5 µg/kg GE TAK-101 at Week 24.
* Group F: Two infusion doses of 12.5 µg/kg GE TAK-101, 1 infusion dose on Day 1 and 1 infusion dose on Day 8, followed by 1 infusion dose of 12.5 µg/kg TAK-101 at Week 24.

This trial will be conducted globally. The overall time to participate in this study is approximately 34 weeks. Participants will make multiple visits to the clinic, and will be contacted by telephone OR plus a final visit after receiving their last dose of study drug for a follow-up assessment.

Conditions

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Celiac Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

PREVENTION

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Cohort 1, Group A: Placebo + Placebo + TAK-101 25 µg/kg GE

Following a single-day 3 gram (g) oral run-in gluten challenge, participants will receive TAK-101 placebo-matching intravenous (IV) infusion dose, once each on Days 1 and 8, followed by 12 g/day gluten for 3 days followed by 6 g/day gluten for 3 days starting at Week 2. Participants will then undergo single-day 3 g gluten challenges at Weeks 8, 14, and 20. A third IV infusion dose of TAK-101 25 microgram per kilogram (µg/kg) GE will be given 23 weeks after the second dose at approximately Week 24.

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

TAK-101 placebo-matching intravenous infusion

TAK-101

Intervention Type DRUG

TAK 101 intravenous infusion

Gluten

Intervention Type DIETARY_SUPPLEMENT

Powder form (vital wheat gluten)

Cohort 1, Group B: TAK-101 25 µg/kg GE + Placebo + TAK-101 25 µg/kg GE

Following a single-day 3 g oral run-in gluten challenge, participants will receive TAK-101 25 µg/kg, IV infusion once on Day 1 followed by TAK-101 placebo-matching IV infusion, once on Day 8, followed by 12 g/day gluten for 3 days followed by 6 g/day gluten for 3 days starting at Week 2. Participants will then undergo single-day 3 g gluten challenges at Weeks 8, 14, and 20. A third IV infusion dose of TAK-101 25 µg/kg GE will be given 23 weeks after the second dose at approximately Week 24.

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

TAK-101 placebo-matching intravenous infusion

TAK-101

Intervention Type DRUG

TAK 101 intravenous infusion

Gluten

Intervention Type DIETARY_SUPPLEMENT

Powder form (vital wheat gluten)

Cohort 1, Group C: TAK-101 25 µg/kg GE + TAK-101 25 µg/kg GE + TAK-101 25 µg/kg GE

Following a single-day 3 g oral run-in gluten challenge, participants will receive TAK-101 25 µg/kg GE IV infusion, once each on Days 1 and 8, followed by 12 g/day gluten for 3 days followed by 6 g/day gluten for 3 days starting at Week 2. Participants will then undergo single-day 3 g gluten challenges at Weeks 8, 14, and 20. A third IV infusion dose of TAK-101 25 µg/kg GE will be given 23 weeks after the second dose at approximately Week 24.

Group Type EXPERIMENTAL

TAK-101

Intervention Type DRUG

TAK 101 intravenous infusion

Gluten

Intervention Type DIETARY_SUPPLEMENT

Powder form (vital wheat gluten)

Cohort 2, Group A: Placebo + Placebo + TAK-101 25 µg/kg GE

Following a single-day 3 g oral run-in gluten challenge, participants will receive TAK-101 placebo-matching IV infusion, once each on Days 1 and 8, followed by 12 g/day gluten for 3 days followed by 6 g/day gluten for 3 days starting at Week 2. Participants will then undergo single-day 3 g gluten challenges at Weeks 8, 14, and 20. A third IV infusion dose of TAK-101 25 µg/kg GE will be given 23 weeks after the second dose at approximately Week 24. Cohort 2 would start based on the results of Cohort 1.

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

TAK-101 placebo-matching intravenous infusion

TAK-101

Intervention Type DRUG

TAK 101 intravenous infusion

Gluten

Intervention Type DIETARY_SUPPLEMENT

Powder form (vital wheat gluten)

Cohort 2, Group D: TAK-101 50 µg/kg GE + TAK-101 50 µg/kg GE+ TAK-101 50 µg/kg GE

Following a single-day 3 g oral run-in gluten challenge, participants will receive TAK-101 50 µg/kg GE IV infusion, once each on Days 1 and 8, followed by 12 g/day gluten for 3 days followed by 6 g/day gluten for 3 days starting at Week 2. Participants will then undergo single-day 3 g gluten challenges at Weeks 8, 14, and 20. A third IV infusion dose of TAK-101 50 µg/kg GE will be given 23 weeks after the second dose at approximately Week 24. Cohort 2 would start based on the results of Cohort 1.

Group Type EXPERIMENTAL

TAK-101

Intervention Type DRUG

TAK 101 intravenous infusion

Gluten

Intervention Type DIETARY_SUPPLEMENT

Powder form (vital wheat gluten)

Cohort 2, Group E: Placebo + Placebo + TAK-101 12.5 µg/kg GE

Following a single-day 3 g oral run-in gluten challenge, participants will receive TAK-101 placebo-matching IV infusion, once each on Days 1 and 8, followed by 12 g/day gluten for 3 days followed by 6 g/day gluten for 3 days starting at Week 2. Participants will then undergo single-day 3 g gluten challenges at Weeks 8, 14, and 20. A third IV infusion dose of TAK-101 12.5 µg/kg GE will be given 23 weeks after the second dose at approximately Week 24. Cohort 2 would start based on the results of Cohort 1. This group would be opened only if it is decided not to open Cohort 2 at the 50 µg/kg GE dose level.

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

TAK-101 placebo-matching intravenous infusion

TAK-101

Intervention Type DRUG

TAK 101 intravenous infusion

Gluten

Intervention Type DIETARY_SUPPLEMENT

Powder form (vital wheat gluten)

Cohort 2, Group F: TAK-101 12.5 µg/kg GE + TAK-101 12.5 µg/kg GE + TAK-101 12.5 µg/kg GE

Following a single-day 3 g oral run-in gluten challenge, participants will receive TAK-101 12.5 µg/kg GE IV infusion, once each on Days 1 and 8, followed by 12 g/day gluten for 3 days followed by 6 g/day gluten for 3 days starting at Week 2. Participants will then undergo single-day 3 g gluten challenges at Weeks 8, 14, and 20. A third IV infusion dose of TAK-101 12.5 µg/kg GE will be given 23 weeks after the second dose at approximately Week 24. Cohort 2 would start based on the results of Cohort 1.

Group Type EXPERIMENTAL

TAK-101

Intervention Type DRUG

TAK 101 intravenous infusion

Gluten

Intervention Type DIETARY_SUPPLEMENT

Powder form (vital wheat gluten)

Interventions

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Placebo

TAK-101 placebo-matching intravenous infusion

Intervention Type DRUG

TAK-101

TAK 101 intravenous infusion

Intervention Type DRUG

Gluten

Powder form (vital wheat gluten)

Intervention Type DIETARY_SUPPLEMENT

Eligibility Criteria

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Inclusion Criteria

1. Biopsy-confirmed CeD that is well-controlled, defined as mild or with no ongoing signs or symptoms felt to be related to active CeD and with immunoglobulin A (IgA) tissue transglutaminase (tTG) \<2 × upper limit of normal (ULN) and IgG deamidated gliadin peptide (DGP) \<3 × ULN.

Note: Participants may be retested for IgA tTG and IgG DGP to meet eligibility criteria at the discretion of the investigator. Intermittent symptoms would not exclude participants from participation as long as symptoms are generally well controlled in the opinion of the investigator, and as long as symptoms are back to baseline for 2 weeks before the run-in gluten challenge.
2. Must be able to maintain a gluten-free diet (GFD) for ≥6 months.
3. Must be HLA-DQ2.5 and/or HLA-DQ8 positive during screening laboratory testing.

Exclusion Criteria

1. Has received any investigational compound within 12 weeks (84 days) or 5 half-lives, whichever is longer, before signing of the informed consent form (ICF).
2. Has received TAK-101 in a previous clinical study.
3. Has presence of other inflammatory gastrointestinal (GI) disorders or systemic autoimmune diseases, that either have the potential to cause persistent GI symptoms similar to CeD or are not well controlled without the use of excluded medications.

* Examples of conditions that are exclusionary include: inflammatory bowel disease, eosinophilic gastroenteritis or colitis, and microscopic colitis requiring treatment in the 6 months before screening.
* Examples of conditions that may be permissible after discussion with the medical monitor/or sponsor include: systemic autoimmune disease such as scleroderma, psoriatic or rheumatoid arthritis, lupus that is stable and without GI involvement, well controlled autoimmune thyroid disease, well controlled type 1 diabetes or proton pump inhibitor -responsive eosinophilic esophagitis in symptomatic and histologically confirmed remission.
4. Has known or suspected refractory CeD or ulcerative jejunitis.
5. Has known or suspected allergy to wheat, such as hypersensitivity and/or anaphylaxis including wheat-dependent-exercise induced anaphylaxis (WDEIA). If there is a possible history of urticaria, angioedema, or anaphylaxis to wheat, investigators should perform testing for wheat anti-Immunoglobulin (anti-IgE) antibodies or refer to an allergist for evaluation prior to enrollment to rule out any of these allergies.
6. Ongoing systemic immunosuppressant, systemic (oral or IV) corticosteroid treatment, or has received treatment with systemic immunosuppressants or corticosteroids in the 12 weeks before run-in gluten challenge.
7. Has known or suspected clinically significant liver disease or positive test result for hepatitis B or C.
8. Has intolerable symptoms after the run-in gluten challenge and is unwilling to undergo subsequent post treatment gluten challenges.
9. Has known allergy to or intolerance of TAK-101 or any of its ingredients or excipients. Also, any subject with a symptomatic allergic reaction that is confirmed by laboratory serology such as elevated tryptase levels following the administration of TAK-101 will be excluded from future dosing.
10. Has a current diagnosis of active malignancy or malignancy diagnosed in the 5 years prior to screening or is receiving ongoing treatment for malignancy.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Takeda

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

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One of a Kind Clinical Research Center LLC

Scottsdale, Arizona, United States

Site Status

Gastroenterology and Liver Institute

Escondido, California, United States

Site Status

Cadena Care Institute, Inc.

Poway, California, United States

Site Status

Asthma and Allergy Associates, PC

Colorado Springs, Colorado, United States

Site Status

GCP Clinical Research, LLC

Tampa, Florida, United States

Site Status

Agile Clinical Research Trials

Atlanta, Georgia, United States

Site Status

Lemah Creek Clinical Research

Burr Ridge, Illinois, United States

Site Status

Gastroenterology Associates, PA

Rockford, Illinois, United States

Site Status

Rockford Gastroenterology Associates, Ltd.

Rockford, Illinois, United States

Site Status

Berkshire Medical Center

New Albany, Indiana, United States

Site Status

Gastroenterology Health Partners, PLLC

New Albany, Indiana, United States

Site Status

Boston Specialists

Boston, Massachusetts, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status

Berkshire Medical Center, Inc.

Pittsfield, Massachusetts, United States

Site Status

Clinical Research Institute of Michigan, LLC

Chesterfield, Michigan, United States

Site Status

Wellness Clinical Research

Chesterfield, Michigan, United States

Site Status

Mayo Clinic - Rochester

Rochester, Minnesota, United States

Site Status

Albuquerque Clinical Trials, Inc.

Albuquerque, New Mexico, United States

Site Status

Basil Clinical

Inwood, New York, United States

Site Status

Mount Sinai

New York, New York, United States

Site Status

Columbia University Medical Center. New York Presbyterian Hospital

New York, New York, United States

Site Status

East Carolina Gastroenterology, PA

Jacksonville, North Carolina, United States

Site Status

GI Alliance-Rhode Island

Providence, Rhode Island, United States

Site Status

Amel Med LLC

Georgetown, Texas, United States

Site Status

Care Access Research - Salt Lake City

Ogden, Utah, United States

Site Status

Royal Melbourne Hospital

Parkville, AU, Australia

Site Status

Emeritus Research, Sydney

Botany, NS, Australia

Site Status

Coral Sea Clinical Research Institute

North Mackay, Queensland, Australia

Site Status

Princess Alexandra Hospital

Woolloongabba, Queensland, Australia

Site Status

Emeritus Research, Melbourne

Camberwell, Victoria, Australia

Site Status

The Northern Hospital

Epping, Victoria, Australia

Site Status

St John of God Midland

Midland, Western Australia, Australia

Site Status

St Vincent's Hospital Melbourne

Fitzroy, , Australia

Site Status

Mater Hospital Brisbane

South Brisbane, , Australia

Site Status

Gastroenterology and Internal Medicine Research Institute (GIRI)

Edmonton, Alberta, Canada

Site Status

PerCuro Clinical Research Ltd.

Victoria, British Columbia, Canada

Site Status

McMaster University

Hamilton, Ontario, Canada

Site Status

Scott Shulman Medicine Professional Corporation

North Bay, Ontario, Canada

Site Status

DIEX Recherche Quebec Inc.

Québec, Quebec, Canada

Site Status

Silverdale Medical

Silverdale, Auckland, New Zealand

Site Status

Optimal Clinical Trials - North

Auckland, AU, New Zealand

Site Status

Southern Clinical Trials Totara

New Lynn, AU, New Zealand

Site Status

Momentum Clinical Research Dunedin

Dunedin, OT, New Zealand

Site Status

P3 Research Limited (Wellington)

Wellington, OT, New Zealand

Site Status

Capital, Coast and Hutt Valley - Wellington Regional Hospital

Boulcott, WG, New Zealand

Site Status

Lakeland Clinical Trials Wellington

Upper Hutt, WG, New Zealand

Site Status

Optimal Clinical Trials - Central

Grafton, , New Zealand

Site Status

Countries

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United States Australia Canada New Zealand

Related Links

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https://clinicaltrials.takeda.com/study-detail/5f8339975a55120029fe7d9c?idFilter=%5B%22TAK-079-1004%22%2C%22TAK-101-2001%22%5D

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Other Identifiers

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U1111-1253-8169

Identifier Type: REGISTRY

Identifier Source: secondary_id

TAK-101-2001

Identifier Type: -

Identifier Source: org_study_id

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