Safety and Tolerability of Nexvax2 in Subjects With Celiac Disease

NCT ID: NCT02528799

Last Updated: 2018-12-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

38 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-08-31

Study Completion Date

2017-01-06

Brief Summary

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A randomized, double-blind, placebo-controlled, dose titration trial, stratified by Human Leukocyte Antigen (HLA)-DQ2.5 genotype in subjects with celiac disease.

Detailed Description

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This is a randomized, double-blind, placebo-controlled, study to evaluate the safety and tolerability of Nexvax2 preceded by dose titration period in patients with celiac disease currently on a gluten-free diet. The study will consist of a Screening Period, a Treatment Period, and a Follow-up Period. Eligible subjects will be enrolled in one of three cohorts according to whether they are homozygous or not homozygous for both genes coding for HLA-DQ2.5.

Conditions

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Celiac Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Nexvax2 DQ2.5 Homozygotes (Cohort 1)

Nexvax2 by ID injections for a total of 14 doses over 46 days.

Group Type EXPERIMENTAL

Nexvax2

Intervention Type BIOLOGICAL

Nexvax2 intra-dermal injections twice weekly

Nexvax2 Placebo DQ2.5 Homozygotes (Cohort 1)

Nexvax2 Placebo by ID injections for a total of 14 doses over 46 days.

Group Type PLACEBO_COMPARATOR

Nexvax2 placebo

Intervention Type BIOLOGICAL

Sodium chloride 0.9% intra-dermal injections twice weekly

Nexvax2 DQ2.5 Non-homozygotes (Cohort 2)

Nexvax2 by ID injections for a total of 14 doses over 46 days.

Group Type EXPERIMENTAL

Nexvax2

Intervention Type BIOLOGICAL

Nexvax2 intra-dermal injections twice weekly

Nexvax2 Placebo DQ2.5 Non-homozygotes (Cohort 2)

Nexvax2 Placebo by ID injections for a total of 14 doses over 46 days.

Group Type PLACEBO_COMPARATOR

Nexvax2 placebo

Intervention Type BIOLOGICAL

Sodium chloride 0.9% intra-dermal injections twice weekly

Nexvax2 DQ2.5 Non-homozygotes (Cohort 3)

Nexvax2 by ID injections for 18 doses (up to 27 doses) over 60 days (maximum of 91 days).

Group Type EXPERIMENTAL

Nexvax2

Intervention Type BIOLOGICAL

Nexvax2 intra-dermal injections twice weekly

Nexvax2 Placebo DQ2.5 Non-homozygotes (Cohort 3)

Nexvax2 Placebo by ID injections for 18 doses (up to 27 doses) over 60 days (maximum of 91 days).

Group Type PLACEBO_COMPARATOR

Nexvax2 placebo

Intervention Type BIOLOGICAL

Sodium chloride 0.9% intra-dermal injections twice weekly

Interventions

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Nexvax2

Nexvax2 intra-dermal injections twice weekly

Intervention Type BIOLOGICAL

Nexvax2 placebo

Sodium chloride 0.9% intra-dermal injections twice weekly

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

1. Subject has signed and understands the informed consent form before initiation of any study specific procedures.
2. Subject is between 18 and 70 years old (inclusive) on the date of the Screening Visit.
3. Subject has been diagnosed with celiac disease on the basis of intestinal histology showing villous atrophy according to expert guidelines current at the time of diagnosis.
4. Subject has HLA DQ2.5 genotype (HLA-DQA1\*05 and HLA-DQB1\*02).

Exclusion Criteria

1. Subject has not been maintained on a gluten-free diet for at least 1 year.
2. Celiac Dietary Adherence Test at screening indicates non-compliance to gluten-free diet (score \>12).
3. Serum levels of both recombinant human transglutaminase (tTG)-specific immunoglobulin-A (IgA) and deamidated gliadin peptide (DGP)-specific immunoglobulin-G (IgG) are elevated above the manufacturer's upper limit of normal. The elevation of one or other of the serology test for tTG IgA and DGP IgG is not an exclusion.
4. Subject has uncontrolled complications of celiac disease or a medical condition which, in the opinion of the investigator, would impact the immune response or pose an increased risk to the subject.
5. Subject is or has been using an immuno-modulatory or immune suppressing medical treatment during the 2 months prior to Screening, for example azathioprine, methotrexate, or biological
6. Subject is female and premenopausal or perimenopausal and has a male partner who is not sterile, unless she is sterile, or she practices true abstinence, or unless throughout the entire study period and for 30 days after study drug discontinuation she is using a medically acceptable method of contraception.
7. Subject is male with a premenopausal or perimenopausal female partner who is not sterile, unless he is sterile, or he practices true abstinence, or unless throughout the entire study period and for 30 days after study drug discontinuation he is using a medically acceptable method of contraception, or unless his female partner is using a medically acceptable method of contraception.
8. Subject is unable and/or unwilling to comply with study requirements.
9. Subject has taken oral or parenteral corticosteroids within the previous six weeks prior to Screening. Topical or inhaled corticosteroids are acceptable.
10. Subject has received an experimental therapy within 30 days prior to Screening.
11. Subject has previously been enrolled and dosed in a clinical trial with Nevax2.
12. Subject has any of the following laboratory abnormalities at Screening:

* Alanine aminotransferase (ALT), aspartate aminotransferase (AST), or alkaline phosphatase (ALP) ≥ 2 × the upper limit of normal (ULN)
* Hemoglobin \<10 g/dL
* Platelet count \<100 × 109/L
* White blood cell count (WBC) outside the normal range and judged clinically significant by the investigator
* Direct bilirubin outside the normal range
* Any other clinically significant abnormal laboratory values, as determined by the investigator
13. Subject is lactating, is known to be pregnant, has a positive pregnancy test at Screening or Treatment Day, intends to become pregnant, or is nursing.
14. Subject has a history or presence of any medically significant condition considered by the investigator to have the potential to adversely affect participation in the study and/or interpretation of the study results.
15. Subject has a history of severe allergic reactions (e.g., swelling of the mouth and throat, difficulty breathing, hypotension, or shock) that require medical intervention.
16. Subject has donated blood ≤ 56 days prior to Screening and plans to donate blood within 5 weeks after study completion.
17. Subject has a clinically relevant abnormality on electrocardiogram (ECG), as determined by the investigator.
18. Other unspecified reasons that in the opinion of the investigator or the sponsor make the subject unsuitable for enrollment.
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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ImmusanT, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Robert P. Anderson, MB ChB, PhD

Role: STUDY_CHAIR

ImmusanT, Inc.

Locations

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Q-Pharm Pty Ltd.

Herston, Queensland, Australia

Site Status

CMAX, A Division of IDT Australia Ltd

Adelaide, South Australia, Australia

Site Status

Linear Clinical Research

Nedlands, , Australia

Site Status

Auckland Clinical Studies Ltd

Auckland, , New Zealand

Site Status

Countries

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Australia New Zealand

References

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Daveson AJM, Ee HC, Andrews JM, King T, Goldstein KE, Dzuris JL, MacDougall JA, Williams LJ, Treohan A, Cooreman MP, Anderson RP. Epitope-Specific Immunotherapy Targeting CD4-Positive T Cells in Celiac Disease: Safety, Pharmacokinetics, and Effects on Intestinal Histology and Plasma Cytokines with Escalating Dose Regimens of Nexvax2 in a Randomized, Double-Blind, Placebo-Controlled Phase 1 Study. EBioMedicine. 2017 Dec;26:78-90. doi: 10.1016/j.ebiom.2017.11.018. Epub 2017 Nov 22.

Reference Type DERIVED
PMID: 29191561 (View on PubMed)

Related Links

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Other Identifiers

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U1111-1173-7522

Identifier Type: OTHER

Identifier Source: secondary_id

Nexvax2-1004

Identifier Type: -

Identifier Source: org_study_id