The Efficacy and Safety of Cobitolimod in Participants With Moderate to Severe Active Left-Sided Ulcerative Colitis

NCT ID: NCT04985968

Last Updated: 2023-12-27

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

171 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-11-24

Study Completion Date

2023-12-20

Brief Summary

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The purpose of the study is to evaluate the efficacy of cobitolimod treatment compared to placebo in inducing clinical remission, in participants with moderate to severe active left-sided UC and to evaluate the efficacy of cobitolimod maintenance treatment compared to placebo in inducing or maintaining clinical remission at week 52, in participants with clinical response at week 6 after induction treatment with cobitolimod.

Detailed Description

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This phase III study protocol includes an induction study for 6 weeks and a maintenance study for an additional 45 weeks.

In the induction study there will be an initial phase to explore the best dose, between cobitolimod 250 mg and cobitolimod 500 mg using adaptive design.

Conditions

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Ulcerative Colitis

Keywords

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Colitis, Ulcerative Gastrointestinal Disease Inflammatory Bowel Diseases Glucocorticosteroids Anti-Inflammatory Agents Therapeutic uses Cobitolimod Toll like receptor 9 agonist TLR9 agonist Kappaproct IDX0150 DIMS0150

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Cobitolimod 250 mg

Dose of 250 mg cobitolimod

2 treatments during induction study and subsequently every third week

Group Type EXPERIMENTAL

Cobitolimod 250 mg

Intervention Type DRUG

Rectal administration

Cobitolimod 500 mg

Dose of 500 mg cobitolimod

2 treatments during induction study and subsequently every third week

Group Type EXPERIMENTAL

Cobitolimod 500 mg

Intervention Type DRUG

Rectal administration

Placebo

Dose of Placebo

2 treatments during induction study and subsequently every third week

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Rectal administration

Interventions

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Cobitolimod 250 mg

Rectal administration

Intervention Type DRUG

Cobitolimod 500 mg

Rectal administration

Intervention Type DRUG

Placebo

Rectal administration

Intervention Type DRUG

Other Intervention Names

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Kappaproct Kappaproct

Eligibility Criteria

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Inclusion Criteria

* Male or female ≥ 18 years of age.
* Established diagnosis of UC.
* Moderate to severe active left-sided UC assessed by central reading.
* Have inadequate response, loss of response or be intolerant of at least one of the following treatments: Oral GCS, AZA/6-MP, Biologics, JAK-inhibitors, or other approved advanced therapies for UC.
* Allowed to receive a therapeutic dose of the following UC drugs during the study: Oral GCS therapy (≤20 mg prednisone or equivalent/day) , Oral 5-ASA/SP compounds, AZA/6-MP.
* Ability to understand the treatment, willingness to comply with all study requirements, and ability to provide informed consent.


* Participants are eligible to be included in the maintenance study if they have achieved clinical response at week 6 and have adhered to the protocol procedures of the induction study.

Exclusion Criteria

* Suspicion of differential diagnosis.
* Acute fulminant UC and/or signs of systemic toxicity.
* UC limited to the rectum or extending beyond the splenic flexure.
* Have failed treatment with more than three advanced therapies of two different therapeutic classes.
* Have had surgery for treatment of UC.
* History of malignancy, unless treated with no relapse of the disease and ≥ 5 years since last treatment (cured).
* History or presence of any clinically significant disorder.
* Concomitant treatment with cyclosporine, methotrexate, tacrolimus, or advanced therapies or similar immunosuppressants and immunomodulators.
* Treatment with rectal GCS, 5-ASA/SP or tacrolimus.
* Long-term treatment (\>14 days) with antibiotics or NSAIDs .
* Serious known active infection including history of latent or active tuberculosis.
* Gastrointestinal infections including positive Clostridium difficile stool assay.
* Females who are lactating or have a positive serum pregnancy test.
* Women of childbearing potential not using highly effective contraceptive methods.
* Concurrent participation in another clinical study.
* Previous exposure to cobitolimod.


* Participants will not be eligible for the maintenance study if they are not willing to comply with all further study requirements.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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InDex Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Raja Atreya, Professor

Role: PRINCIPAL_INVESTIGATOR

Friedrich-Alexander University Erlangen-Nuremberg

Locations

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Accout Center s.r.o.

Šahy, , Slovakia

Site Status

Inje University Haeundae Paik Hospital

Busan, , South Korea

Site Status

Kyungpook National University Hospital

Daegu, , South Korea

Site Status

CLINIQ s.r.o.

Bratislava, , Slovakia

Site Status

Amicis Research Center

Granada Hills, California, United States

Site Status

Allameh Medical Corporation

Mission Viejo, California, United States

Site Status

Prospective Research Innovations Inc.

Rancho Cucamonga, California, United States

Site Status

Valiance Clinical Research

Tarzana, California, United States

Site Status

RecioMed Clinical Research Network, Inc.

Boynton Beach, Florida, United States

Site Status

MB & V Medical Research

Doral, Florida, United States

Site Status

A+ Research, Inc.

Miami, Florida, United States

Site Status

SouthCoast Research Center, Inc

Miami, Florida, United States

Site Status

I.V.A.M. Clinical & Investigational Center LLC

Miami, Florida, United States

Site Status

D&H National Research Centers, Inc.

Miami, Florida, United States

Site Status

Medical Professionals Clinical Research Center

Miami, Florida, United States

Site Status

Gastroenterology Group Of Naples

Naples, Florida, United States

Site Status

Alliance Clinical Research - Gastroenterology

Tampa, Florida, United States

Site Status

Cotton O'Neil Clinical Research Center

Topeka, Kansas, United States

Site Status

Clinical Research Institute of Michigan

Troy, Michigan, United States

Site Status

Lenox Hill Hospital

New York, New York, United States

Site Status

Carolina Digestive Health Associates, PA

Charlotte, North Carolina, United States

Site Status

Carolina Research

Greenville, North Carolina, United States

Site Status

Peters Medical Research

High Point, North Carolina, United States

Site Status

Dayton Gastroenterology

Beavercreek, Ohio, United States

Site Status

Digestive Health Associates of Texas, PA

Carrollton, Texas, United States

Site Status

Clinical Research Solution: Digestive Health Associates

Houston, Texas, United States

Site Status

Baylor College of Medicine - Gastroeneterology

Houston, Texas, United States

Site Status

Gastroenterology Associates of Northern Virginia

Fairfax, Virginia, United States

Site Status

Wisconsin Center For Advanced Research

Milwaukee, Wisconsin, United States

Site Status

Monash Health

Clayton, , Australia

Site Status

St Vincent's Hospital Melbourne

Fitzroy, , Australia

Site Status

The Alfred Hospital

Melbourne, , Australia

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Royal Melbourne Hospital

Parkville, , Australia

Site Status

Mater Health Services

South Brisbane, , Australia

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Princess Alexandra Hospital

Woolloongabba, , Australia

Site Status

MedUn Innsbruck

Innsbruck, , Austria

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LKH Klagenfurt

Klagenfurt, , Austria

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Universitätsklinikum Salzburg

Salzburg, , Austria

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Akh Wien

Vienna, , Austria

Site Status

UZ Antwerpen

Antwerp, , Belgium

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Imelda Ziekenhuis

Bonheiden, , Belgium

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Erasme University Hospital

Brussels, , Belgium

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Universitair Ziekenhuis Gent

Ghent, , Belgium

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AZ Groeninge - Campus Kennedylaan

Kortrijk, , Belgium

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AZ Delta

Roeselare, , Belgium

Site Status

University Clinical Centre of the Republic of Srpska - Gastroenterology

Banja Luka, , Bosnia and Herzegovina

Site Status

The University Hospital Foca

Foča, , Bosnia and Herzegovina

Site Status

Clinical Center University of Sarajevo - Gastroenterology

Sarajevo, , Bosnia and Herzegovina

Site Status

General Hospital "Prim.dr.Abdulah Nakas"

Sarajevo, , Bosnia and Herzegovina

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Polyclinic Dr. Al-Tawil

Sarajevo, , Bosnia and Herzegovina

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Opca Bolnica Tesanj

Tešanj, , Bosnia and Herzegovina

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Plava Medical Group

Tuzla, , Bosnia and Herzegovina

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Cantonal Hospital Zenica

Zenica, , Bosnia and Herzegovina

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Instituto Goiano de Gastroenterologia e Endoscopia Digestiva Ltda

Goiânia, , Brazil

Site Status

Hospital de Clinicas de Porto Alegre - Centro de Pesquisa Clinica

Porto Alegre, , Brazil

Site Status

Ufrj - Hospital Universitario Clementino Fraga Filho

Rio de Janeiro, , Brazil

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Praxis Pesquisa Medica

Santo André, , Brazil

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CEMEC - Centro Multidisciplinar de Estudos Clinicos

São Bernardo do Campo, , Brazil

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Kaiser Clinica

São José do Rio Preto, , Brazil

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MUMC - Hamilton Health Sciences

Hamilton, , Canada

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Installation Hospital Maisonneuve-Rosemont

Montreal, , Canada

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Royal University Hospital

Saskatoon, , Canada

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Opca bolnica Bjelovar

Bjelovar, , Croatia

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Clinical Hospital Osijek

Osijek, , Croatia

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Opca bolnica Pula

Pula, , Croatia

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Zadar General Hospital

Zadar, , Croatia

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Poliklinika Solmed

Zagreb, , Croatia

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University Hospital Centre Zagreb

Zagreb, , Croatia

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Aalborg University Hospital

Aalborg, , Denmark

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Aarhus University Hospital

Aarhus, , Denmark

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Herlev Hospital

Herlev, , Denmark

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Hillerod Hospital

Hillerød, , Denmark

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Lillebælt Hospital Vejle

Vejle, , Denmark

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CHRU de Lille - Hôpital Claude Huriez

Lille, , France

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CHRU Montpellier-Hopital Saint Eloi - Hepato-gastro-enterologie

Montpellier, , France

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CHU de Nancy Brabois

Nancy, , France

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CHU de Nice - Hôpital de l'Archet II - Gastro-Entérologie, Hépatologie

Nice, , France

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Hopital Bichat - Gastroenterology

Paris, , France

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Hopital Saint Antoine

Paris, , France

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Centre Hospitalier Lyon Sud

Pierre-Bénite, , France

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Centre Hospitalier Universitaire de Poitiers

Poitiers, , France

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CHU de Saint Etienne, Hôpital Nord - Service de Gastroentérologie

Saint-Etienne, , France

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CHU Amiens - Hopital Sud - Service Hepato-Gastroenterolog

Salouël, , France

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Centre Hospitalier Universitaire de Toulouse - Hopital Rangueil

Toulouse, , France

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JSC " Evex Hospitals"

Batumi, , Georgia

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LTD Israel-Georgian Medical Research Clinic Helsicore

Tbilisi, , Georgia

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Universitätsklinikum Augsburg

Augsburg, , Germany

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Charité - Universitätsmedizin Berlin KöR

Berlin, , Germany

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University Hospital Cologne AöR

Cologne, , Germany

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MVZ Sanaklinikum Duisburg

Duisburg, , Germany

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Universitätsklinikum Erlangen

Erlangen, , Germany

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Agaplesion Markus Krankenhaus

Frankfurt am Main, , Germany

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Klinikum der Johann Wolfgang Goethe-Universität - Medizinische Klinik I

Frankfurt am Main, , Germany

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Universitätsklinikum Freiburg

Freiburg im Breisgau, , Germany

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Uniklinik Halle (Saale)

Halle, , Germany

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Gastroenterology Outpatient Clinic Prof. Dr. med. Ehehalt

Heidelberg, , Germany

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University Hospital Schleswig-Holstein

Kiel, , Germany

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Universitätsmedizin Mannheim

Mannheim, , Germany

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Medius Klinik Nürtingen

Nürtingen, , Germany

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Universitätsklinikum Rostock

Rostock, , Germany

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Universitätsklinikum Ulm

Ulm, , Germany

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Internistische Praxis Weyhe

Weyhe, , Germany

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Clinexpert Egészségügyi Szolgáltató És Kereskedelmi Kft.

Budapest, , Hungary

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Pannónia Magánorvosi Centrum Kft

Budapest, , Hungary

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Semmelweis Egyetem Altalanos Orvostudomanyi Kar Sebeszeti, Transzplantacios es Gasztroenterologiai Klinika

Budapest, , Hungary

Site Status

Semmelweis Egyetem Altalanos Orvostudomanyi Kar

Budapest, , Hungary

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SzTE Szt-Gy A Orvostud Kar Bel Klin

Szeged, , Hungary

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The Barzilai Medical Center

Ashkelon, , Israel

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The Edith Wolfson Medical Center

Holon, , Israel

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Hadassah Medical Organization, Hadassah Medical Center, Ein-

Jerusalem, , Israel

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Shaare Zedek Medical Center

Jerusalem, , Israel

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Galilee Medical Center (Western Galilee Hospital)

Nahariya, , Israel

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Kaplan Medical Center

Rehovot, , Israel

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ASST Papa Giovanni XXIII - Cardiologia - Bergamo

Bergamo, , Italy

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AO Brotzu

Cagliari, , Italy

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Universita degli Studi di Firenze - Azienda Ospedaliero - Un

Florence, , Italy

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IRCCS Ospedale San Raffaele

Milan, , Italy

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Azienda Ospedaliera San Gerardo

Monza, , Italy

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AOU di Padova

Padua, , Italy

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Azienda Ospedaliera Universitaria Policlinico Tor Vergata (P

Roma, , Italy

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Policlinico Universitario Agostino Gemelli

Roma, , Italy

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Policlinico Universitario Campus Biomedico

Rome, , Italy

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A.O. Ordine Mauriziano Di Torino

Torino, , Italy

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AOU S. Maria della Misericordia

Udine, , Italy

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Universita degli Studi dell'Insubria - Ospedale di Circolo e

Varese, , Italy

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Hospital of Lithuanian University of Health Sciences Kauno Klinikos

Kaunas, , Lithuania

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Klaipeda Seamen's Hospital

Klaipėda, , Lithuania

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Republic Klaipeda Hospital

Klaipėda, , Lithuania

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ENDOMED s.r.o.

Košice, , Slovakia

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Panevezio ligonine

Panevezys, , Lithuania

Site Status

Vilniaus Universiteto ligonines Santariskiu Klinikos

Vilnius, , Lithuania

Site Status

Instituto de Investigaciones Aplicadas a la Neurociencia A.C.

Durango, , Mexico

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Clinicos Asociados Bocm, S.C.

Mexico City, , Mexico

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Medical Care and Research S. A. de C. V

Mérida, , Mexico

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Centro Regiomontano de Estudios Clinicos Roma SC

Monterrey, , Mexico

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Clinical Research Institute S.C.

Tlalnepantla, , Mexico

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Radboud University Medical Center

Nijmegen, , Netherlands

Site Status

Ålesund Hospital, Møre & Romsdal Hospital trust, Dept. of Medicine, div of Gastroenterology and the Clinical research unit HMR

Ålesund, , Norway

Site Status

Akershus Universitetssykehus

Lørenskog, , Norway

Site Status

Universitetssykehuset Nord-Norge Tromsø, Gastrolab, Medisinsk poliklinikk, B8

Tromsø, , Norway

Site Status

Vestfold Hjertesenter As

Tønsberg, , Norway

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MPS - MED sp. z o.o.

Grudziądz, , Poland

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MZ Badania Slowik Zymla Spolka jawna

Knurów, , Poland

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Centrum Medyczne Plejady

Krakow, , Poland

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Centrum Medyczne PROMED

Krakow, , Poland

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Krakowskie Centrum Medyczne Sp. z o.o.

Krakow, , Poland

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Szpital Zakonu Bonifratrow Sw. Jana Bozego w Lodzi

Lodz, , Poland

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Klinika Badawcza Centrum Badawcze Panaceum Agnieszka Brzezicka, Magdalena Lenkiewicz Sp. z o.o.

Malbork, , Poland

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Twoja Przychodnia - Opolskie Centrum Medyczne

Opole, , Poland

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Medicome Sp. z o.o.

Oświęcim, , Poland

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Szpital Kliniczny im. Heliodora Swiecickiego Uniwersytetu Medycznego im. Karola Marcinkowskiego w Poznaniu

Poznan, , Poland

Site Status

ETG Skierniewice

Skierniewice, , Poland

Site Status

KO-MED Centra Kliniczne Staszow

Staszów, , Poland

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Twoja Przychodnia - SCM

Szczecin, , Poland

Site Status

GASTROMED Kopoń, Zmudziński i Wspólnicy spółka jawna, Specjalistyczne Centrum Gastrologii i Endoskopii, Specjalistyczne Gabinety Lekarskie

Torun, , Poland

Site Status

Bodyclinic sp. z o.o. sp.k.

Warsaw, , Poland

Site Status

Centralny Szpital Kliniczny MSWiA w Warszawie

Warsaw, , Poland

Site Status

Centrum Zdrowia Matki, Dziecka i Mlodziezy

Warsaw, , Poland

Site Status

PlanetMed

Wroclaw, , Poland

Site Status

ETG Zamosc

Zamość, , Poland

Site Status

Hospital Prof. Doutor Fernando Fonseca (HFF) (Hospital Amadora Sintra)

Amadora, , Portugal

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Hospital de Braga

Braga, , Portugal

Site Status

GASTROMEDIC, s.r.o.

Nové Zámky, , Slovakia

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Hospital Beatriz Angelo (HBA)

Loures, , Portugal

Site Status

Centro Hospitalar de Entre o Douro e Vouga (CHEDV)- Hospital São Sebastião

Santa Maria da Feira, , Portugal

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Sana Monitoring

Bucharest, , Romania

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Spitalul Clinic Colentina

Bucharest, , Romania

Site Status

Spitalul Clinic Judetean de Urgenta Cluj-Napoca

Cluj-Napoca, , Romania

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Spitalul Clinic Judetean de Urgenta "Sf. Spiridon" Iasi

Iași, , Romania

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Spitalul Clinic Judetean Mures

Târgu Mureş, , Romania

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Cabinet Particular Policlinic Algomed

Timișoara, , Romania

Site Status

Clinic Center of Serbia

Belgrade, , Serbia

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Clinical Hospital Center "Dr. Dragisa Misovic"

Belgrade, , Serbia

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Euromedik Hospital

Belgrade, , Serbia

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Zvezdara University Medical Center

Belgrade, , Serbia

Site Status

Clinical Center Kragujevac - Center for Gastroenterohepatology

Kragujevac, , Serbia

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General Hospital Dr Djordje Joanovic

Zrenjanin, , Serbia

Site Status

General hospital Zrenjanin

Zrenjanin, , Serbia

Site Status

FNsP F.D.R. Banska Bystrica

Banská Bystrica, , Slovakia

Site Status

Hanyang University Guri Hospital

Guri-si, , South Korea

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Kyung Hee University Hospital

Seoul, , South Korea

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Seoul National University Bundang Hospital

Seoul, , South Korea

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Seoul National University Hospital

Seoul, , South Korea

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Kyung Hee University Hospital - Internal Medicine

Soeul, , South Korea

Site Status

Kyung Hee University Hospital

Soeul, , South Korea

Site Status

The Catholic University of Korea, St. Vincent's Hospital

Suwon, , South Korea

Site Status

Yonsei University, Wonju Severance Christian Hospital

Wŏnju, , South Korea

Site Status

Örebro Univ. Hospital

Örebro, , Sweden

Site Status

Karolinska Universitetssjukhuset - Gastroenterology

Stockholm, , Sweden

Site Status

Uppsala University Hospital, Akademiska

Uppsala, , Sweden

Site Status

Hacettepe University Medical Faculty - Hematology

Ankara, , Turkey (Türkiye)

Site Status

Istanbul University Medical Faculty

Istanbul, , Turkey (Türkiye)

Site Status

Mersin Universtiy Medical Faculty

Mersin, , Turkey (Türkiye)

Site Status

Northern Care Alliance NHS Foundation Trust-Fairfield General Hospital - Gastroenterology

Bury, , United Kingdom

Site Status

Accellacare Warwickshire Quality Research Site

Coventry, , United Kingdom

Site Status

County Durham and Darlington NHS Foundation Trust (CDDFT) - Darlington Memorial Hospital

Darlington, , United Kingdom

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Glasgow Royal Infirmary

Glasgow, , United Kingdom

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North West London Hospitals NHS Trust

Harrow, , United Kingdom

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Central Middlesex Hospital

London, , United Kingdom

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Kings College Hospital

London, , United Kingdom

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Accellacare North London

Northwood, , United Kingdom

Site Status

Accellacare Limited/Accellacare of South London

Orpington, , United Kingdom

Site Status

Royal Berkshire Hospital

Reading, , United Kingdom

Site Status

Countries

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United States Australia Austria Belgium Bosnia and Herzegovina Brazil Canada Croatia Denmark France Georgia Germany Hungary Israel Italy Lithuania Mexico Netherlands Norway Poland Portugal Romania Serbia Slovakia South Korea Sweden Turkey (Türkiye) United Kingdom

Other Identifiers

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CSUC-01/21

Identifier Type: -

Identifier Source: org_study_id