A Study of Tofacitinib in Patients With Ulcerative Colitis in Stable Remission

NCT ID: NCT03281304

Last Updated: 2023-03-21

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE4

Total Enrollment

140 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-11-16

Study Completion Date

2022-03-18

Brief Summary

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This study is a follow up study for subjects with Ulcerative Colitis (UC) in stable remission designed to evaluate flexible dosing of CP-690,550.

Detailed Description

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Conditions

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Ulcerative Colitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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CP-690,550 5 mg

CP-690,550 5 mg tablet by mouth twice a day (BID)

Group Type EXPERIMENTAL

CP-690,500 5 mg

Intervention Type DRUG

CP-690,550 5 mg tablet BID

CP-690,550 10 mg

CP-690,550 10 mg BID

Group Type EXPERIMENTAL

CP-690,550 10 mg

Intervention Type DRUG

CP-690,550 10 mg tablet BID

Interventions

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CP-690,500 5 mg

CP-690,550 5 mg tablet BID

Intervention Type DRUG

CP-690,550 10 mg

CP-690,550 10 mg tablet BID

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Currently enrolled in Study A3921139 receiving CP-690,550 10 mg BID for at least 2 years consecutively.
* In stable remission on CP-690,550 10 mg BID
* Agree to use highly effective contraception
* Negative pregnancy test
* Comply with visits, treatments, lab tests, diary and other study procedures
* Signed and dated informed consent document.

Exclusion Criteria

* Subjects who were initially assigned to tofacitinib 10 mg BID at baseline of Study A3921139 whose tofacitinib dose was reduced to 5 mg BID due to safety or efficacy.
* Presence of indeterminate colitis, microscopic colitis, ischemic colitis, infectious colitis or findings suggestive of Crohn's disease
* Likely to require surgery for ulcerative colitis during study
* Expected to receive any prohibited medication
* Expected to receive live or attenuated virus vaccination during study
* Women who are pregnant or breastfeeding or planning to become pregnant during the study
* Evidence of colonic malignancy or any dysplasia
* Acute or chronic medical or psychiatric condition that may increase risk of participation
* Investigator site staff member
* Subjects likely to be uncooperative or unable to comply with study procedures
* Participation in other studies involving investigational drugs during study
* Subjects with any of the following risk factors for pulmonary embolism at baseline as defined by EMA's PRAC:

* has heart failure;
* has inherited coagulation disorders;
* has had venous thromboembolism, either deep venous thrombosis or pulmonary embolism;
* is taking combined hormonal contraceptives or hormone replacement therapy;
* has malignancy (association is strongest with cancers other than non-melanoma skin cancers);
* is undergoing major surgery
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Surgicare of Mobile

Mobile, Alabama, United States

Site Status

Alabama Medical Group, P.C.

Mobile, Alabama, United States

Site Status

Clinical Applications Laboratories, Inc.

San Diego, California, United States

Site Status

Bristol Hospital

Bristol, Connecticut, United States

Site Status

Connecticut Clinical Research Institute

Bristol, Connecticut, United States

Site Status

Central Connecticut Endoscopy Center

Plainville, Connecticut, United States

Site Status

Advanced Medical Research Center

Port Orange, Florida, United States

Site Status

Florida Medical Clinic, P.A.

Zephyrhills, Florida, United States

Site Status

Cotton-O'Neil Clinical Research Center, Digestive Health

Topeka, Kansas, United States

Site Status

Chevy Chase Endoscopy Center

Chevy Chase, Maryland, United States

Site Status

MGG Group Co., Inc., Chevy Chase Clinical Research

Chevy Chase, Maryland, United States

Site Status

Clinical Research Institute of Michigan, LLC

Chesterfield, Michigan, United States

Site Status

Eastside Endoscopy Center

Macomb, Michigan, United States

Site Status

Clinical Research Institute of Michigan, LLC

Troy, Michigan, United States

Site Status

NYU Langone Long Island Clinical Research Associates

Lake Success, New York, United States

Site Status

Columbia University Irving Medical Center

New York, New York, United States

Site Status

Columbia University Medical Center Research Pharmacy/ Milstein Hospital

New York, New York, United States

Site Status

Great Lakes Gastroenterology Research, LLC

Mentor, Ohio, United States

Site Status

Memorial Hermann Hospital

Houston, Texas, United States

Site Status

The University of Texas Health Science Center at Houston (UTHealth)- McGovern Medical School

Houston, Texas, United States

Site Status

Christus Trinity Mother Frances Endoscopy Center

Tyler, Texas, United States

Site Status

Tyler Research Institute, LLC

Tyler, Texas, United States

Site Status

Alpine Medical Group

Salt Lake City, Utah, United States

Site Status

Wasatch Clinical Research, LLC

Salt Lake City, Utah, United States

Site Status

UZ Leuven (University Hospital Leuven), Campus Gasthuisberg

Leuven, , Belgium

Site Status

London Health Sciences Centre - University Hospital

London, Ontario, Canada

Site Status

Royal University Hospital

Saskatoon, Saskatchewan, Canada

Site Status

Nemocnice Strakonice a.s.

Strakonice, , Czechia

Site Status

CHU Hotel Dieu

Nantes, , France

Site Status

CHU de Bordeaux Hopital Haut Leveque

Pessac, , France

Site Status

Universitaetsklinikum Schleswig-Holstein

Kiel, , Germany

Site Status

Szent Janos Korhaz és Eszak-budai Egyesitett Korhazak

Budapest, , Hungary

Site Status

Pannonia Maganorvosi Centrum Kft.

Budapest, , Hungary

Site Status

Bekes Megyei Kozponti Korhaz Pandy Kalman Tagkorhaz Endoszkopos Laboratorium

Gyula, , Hungary

Site Status

Università "Magna Graecia" di Catanzaro

Catanzaro, CZ, Italy

Site Status

Aichi Medical University Hospital

Nagakute, Aichi-ken, Japan

Site Status

Fukuoka University Chikushi Hospital

Chikushino-shi, Fukuoka, Japan

Site Status

Kurume University Hospital

Kurume, Fukuoka, Japan

Site Status

Hokkaido P.W.F.A.C Sapporo-Kosei General Hospital

Sapporo, Hokkaido, Japan

Site Status

Osaka Medical and Pharmaceutical University Hospital

Takatsuki-shi, Osaka, Japan

Site Status

Shiga University of Medical Science Hospital

Ōtsu, Shiga, Japan

Site Status

Tokyo Medical And Dental University Hospital, Faculty of Medicine

Bunkyo-ku, Tokyo, Japan

Site Status

Tokai University Hachioji Hospital

Hachiōji, Tokyo, Japan

Site Status

Kitasato University Kitasato Institute Hospital

Minato-ku, Tokyo, Japan

Site Status

Showa University Hospital

Shinagawa-ku, Tokyo, Japan

Site Status

Toho University Sakura Medical Center

Chiba, , Japan

Site Status

Hiroshima University Hospital

Hiroshima, , Japan

Site Status

Osaka Metropolitan University Hospital

Osaka, , Japan

Site Status

Keio University Hospital

Tokyo, , Japan

Site Status

Academic Medical Centre

Amsterdam, , Netherlands

Site Status

North Shore Hospital (Waitemata District Health Board)

Takapuna, Auckland, New Zealand

Site Status

Christchurch Hospital (Canterbury District Health Board)

Christchurch, , New Zealand

Site Status

Southern District Health Board

Dunedin, , New Zealand

Site Status

Endoskopia Sp. z o.o.

Sopot, , Poland

Site Status

Lexmedica

Wroclaw, , Poland

Site Status

Federal State Budgetary Institution "State Scientific Centre of Coloproctology

Moscow, , Russia

Site Status

LLC Novosibirskiy Gastrocenter

Novosibirsk, , Russia

Site Status

Federal State Budgetary Scientific Institution "Scientific Research Institute of Physiology

Novosibirsk, , Russia

Site Status

Clinical Centre of Serbia, Clinic for Gastroenterology and Hepatology

Belgrade, , Serbia

Site Status

Clinical Hospital Centre Zvezdara

Belgrade, , Serbia

Site Status

Military Medical Academy, Clinic for Gastroenterology and Hepatology

Belgrade, , Serbia

Site Status

Clinical Center Kragujevac

Kragujevac, , Serbia

Site Status

General Hospital "Djordje Joanovic"

Zrenjanin, , Serbia

Site Status

Medak s.r.o.

Bratislava, , Slovakia

Site Status

KM Management spol. s.r.o.

Nitra, , Slovakia

Site Status

Gastro I., s.r.o., Gastroenterologicka ambulancia

Prešov, , Slovakia

Site Status

Kingsbury Hospital

Claremont, CAPE TOWN, South Africa

Site Status

Wits Clinical Research (WCR) Bara Site, Chris Hani Baragwanath Academic Hospital

Soweto, Johannesburg, Gauteng, South Africa

Site Status

Chris Hani Baragwanath Academic Hospital

Soweto, Johannesburg, South Africa

Site Status

Endocare Research Centre

Paarl, Western Cape, South Africa

Site Status

Panorama Mediclinic

Panorama, Western Cape, South Africa

Site Status

Hanyang University Guri Hospital

Gyeonggi-do, , South Korea

Site Status

Kyung Hee University Hospital

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

Regional Municipal Non-Profit Enterprise "Chernivtsi Regional Clinical Hospital" Surgery Departm

Chernivtsi, , Ukraine

Site Status

Kyiv Municipal Clinical Hospital #18

Kyiv, , Ukraine

Site Status

MI Uzhgorod Regional Hospital

Uzhhorod, , Ukraine

Site Status

Vinnytsia Regional Clinical Hospital for War Veterans, Therapeutics Dept. No. 2

Vinnytsia, , Ukraine

Site Status

University Hospitals Bristol NHS Foundation Trust

Bristol, AVON, United Kingdom

Site Status

Countries

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United States Belgium Canada Czechia France Germany Hungary Italy Japan Netherlands New Zealand Poland Russia Serbia Slovakia South Africa South Korea Spain Ukraine United Kingdom

References

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Torres J, D'Haens GR, Regueiro M, Santana G, Panes J, Vermeire S, Gardiner S, Kulisek N, Modesto I, Su C, Lawendy N, Mundayat R, Paulissen J, Dubinsky MC. Potential predictors of efficacy outcomes following tofacitinib dose reduction in patients with ulcerative colitis in stable remission: a post hoc analysis of outcomes from the RIVETING study. Therap Adv Gastroenterol. 2025 Feb 27;18:17562848251318849. doi: 10.1177/17562848251318849. eCollection 2025.

Reference Type DERIVED
PMID: 40028509 (View on PubMed)

Panes J, D'Haens GR, Sands BE, Ng SC, Lawendy N, Kulisek N, Guo X, Wu J, Vranic I, Panaccione R, Vermeire S. Analysis of tofacitinib safety in ulcerative colitis from the completed global clinical developmental program up to 9.2 years of drug exposure. United European Gastroenterol J. 2024 Jul;12(6):793-801. doi: 10.1002/ueg2.12584. Epub 2024 May 22.

Reference Type DERIVED
PMID: 38778549 (View on PubMed)

Rubin DT, Torres J, Regueiro M, Reinisch W, Prideaux L, Kotze PG, Tan FH, Gardiner S, Mundayat R, Cadatal MJ, Ng SC. Association Between Smoking Status and the Efficacy and Safety of Tofacitinib in Patients with Ulcerative Colitis. Crohns Colitis 360. 2024 Jan 20;6(1):otae004. doi: 10.1093/crocol/otae004. eCollection 2024 Jan.

Reference Type DERIVED
PMID: 38425446 (View on PubMed)

Sandborn WJ, D'Haens GR, Sands BE, Panaccione R, Ng SC, Lawendy N, Kulisek N, Modesto I, Guo X, Mundayat R, Su C, Vranic I, Panes J. Tofacitinib for the Treatment of Ulcerative Colitis: An Integrated Summary of up to 7.8 Years of Safety Data from the Global Clinical Programme. J Crohns Colitis. 2023 Apr 3;17(3):338-351. doi: 10.1093/ecco-jcc/jjac141.

Reference Type DERIVED
PMID: 36124702 (View on PubMed)

Winthrop KL, Vermeire S, Long MD, Panes J, Ng SC, Kulisek N, Mundayat R, Lawendy N, Vranic I, Modesto I, Su C, Melmed GY. Long-term Risk of Herpes Zoster Infection in Patients With Ulcerative Colitis Receiving Tofacitinib. Inflamm Bowel Dis. 2023 Jan 5;29(1):85-96. doi: 10.1093/ibd/izac063.

Reference Type DERIVED
PMID: 35648151 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://pmiform.com/clinical-trial-info-request?StudyID=A3921288

To obtain contact information for a study center near you, click here.

Other Identifiers

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RIVETING STUDY

Identifier Type: OTHER

Identifier Source: secondary_id

2017-002274-39

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

A3921288

Identifier Type: -

Identifier Source: org_study_id

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