BI655130 (SPESOLIMAB) Induction Treatment in Patients With Moderate-to-severe Ulcerative Colitis

NCT ID: NCT03482635

Last Updated: 2025-10-16

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2/PHASE3

Total Enrollment

98 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-03-27

Study Completion Date

2020-05-18

Brief Summary

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This trial has two sequentially enrolling parts with different objectives. The primary objectives of this trial are

* to prove the concept of clinical activity of BI655130 (SPESOLIMAB) in patients with moderate-to-severely active ulcerative colitis who have failed previous biologic treatments and to identify efficacious and safe dose regimens in Part 1 (Phase II)
* to confirm efficacy and safety of BI655130 (SPESOLIMAB) in patients with moderate-to-severely active ulcerative colitis who have failed previous biologic treatments in Part 2 (Phase III)
* To provide, along with induction study 1368-0018 and the run-in cohort of 1368-0020, the target population to be evaluated in study 1368-0020.

Detailed Description

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Conditions

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Colitis, Ulcerative

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Group 1- Placebo Group

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

Solution for infusion

Group 2- Small Dose Group

Group Type EXPERIMENTAL

Spesolimab

Intervention Type DRUG

Solution for infusion

Group 3- Medium Dose Group

Group Type EXPERIMENTAL

Spesolimab

Intervention Type DRUG

Solution for infusion

Group 4 - High Dose Group

Group Type EXPERIMENTAL

Spesolimab

Intervention Type DRUG

Solution for infusion

Interventions

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Spesolimab

Solution for infusion

Intervention Type DRUG

Placebo

Solution for infusion

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* 18 - 75 years, at date of signing informed consent, males or females
* Diagnosis of ulcerative colitis ≥ 3 months prior to screening by clinical and endoscopic evidence corroborated by a histopathology report
* Moderate to severe activity (total MCS 6 to 12 with a RBS ≥ 1 AND an SFS ≥ 1 AND mESS ≥ 2 within 7-28 days prior to first dose)
* Endoscopic activity extending proximal to the rectum (≥ 15 cm from anal verge)
* Well-documented demonstration of inadequate response or loss of response or have had unacceptable side effects with approved doses of TNFɑ antagonists (infliximab, adalimumab, golimumab) and/or vedolizumab in the past (screening of both TNFɑ antagonists-AND-Vedolizumab failure patients will be capped once 48 randomized patients in Part 1 and 117 randomized patients in Part 2 meet this criterion; patients who have already been screened at the time of the cap will continue to be randomized into the study)

Exclusion Criteria

* Evidence of abdominal abscess at screening
* Evidence of fulminant colitis or toxic megacolon at screening
* Ileostomy, colostomy, or known fixed symptomatic stenosis of the intestine
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Boehringer Ingelheim

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Medical Research Center of Connecticut, LLC

Hamden, Connecticut, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

AdventHealth Orlando

Orlando, Florida, United States

Site Status

Emory University

Atlanta, Georgia, United States

Site Status

Atlanta Center for Gastroenterology, P.C.

Decatur, Georgia, United States

Site Status

University of Chicago

Chicago, Illinois, United States

Site Status

Columbia University Medical Center-New York Presbyterian Hospital

New York, New York, United States

Site Status

University Hospitals of Cleveland

Cleveland, Ohio, United States

Site Status

Digestive Disease Specialists Inc

Oklahoma City, Oklahoma, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

Southern Star Research Institute, LLC

San Antonio, Texas, United States

Site Status

Texas Digestive Disease Consultants - Southlake

Southlake, Texas, United States

Site Status

Hunter Holmes McGuire VA Medical Center

Richmond, Virginia, United States

Site Status

Ordensklinikum Linz GmbH - Barmherzige Schwestern

Linz, , Austria

Site Status

AKH - Medical University of Vienna

Vienna, , Austria

Site Status

UZ Leuven

Leuven, , Belgium

Site Status

Centre Hospitalier Universitaire de Liège

Liège, , Belgium

Site Status

University of Manitoba - Health Sciences Centre

Winnipeg, Manitoba, Canada

Site Status

Victoria Hospital (LHSC)

London, Ontario, Canada

Site Status

Sunnybrook Health Sciences Centre

Toronto, Ontario, Canada

Site Status

Universitätsklinikum Aachen, AöR

Aachen, , Germany

Site Status

Universitätsklinikum Erlangen

Erlangen, , Germany

Site Status

Universitätsklinikum Essen AöR

Essen, , Germany

Site Status

Klinikum Esslingen GmbH

Esslingen am Neckar, , Germany

Site Status

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status

Universitätsklinikum Schleswig-Holstein, Campus Kiel

Kiel, , Germany

Site Status

Universitätsklinikum Ulm

Ulm, , Germany

Site Status

Azienda Ospedaliera Universitaria di Padova

Padua, , Italy

Site Status

Istituto Clinico Humanitas

Rozzano (MI), , Italy

Site Status

Toho University Sakura Medical Center

Chiba, Sakura, , Japan

Site Status

Sapporo Tokushukai Hospital

Hokkaido, Sapporo, , Japan

Site Status

Sapporo Higashi Tokushukai Hospital

Hokkaido, Sapporo, , Japan

Site Status

Hyogo College of Medicine Hospital

Hyogo, Nishinomiya, , Japan

Site Status

Sameshima Hospital

Kagoshima, Kagoshima, , Japan

Site Status

Ofuna Chuo Hospital

Kanagawa, Kamakura, , Japan

Site Status

Tokyo Medical and Dental University

Tokyo, Bunkyo-ku, , Japan

Site Status

Kitasato Institute Hospital

Tokyo, Minato-ku, , Japan

Site Status

Tokyo Yamate Medical Center

Tokyo, Shinjuku, , Japan

Site Status

Health Center of Mother, Child and Youth Sp.z o.o.

Warsaw, , Poland

Site Status

Central Clinical Hospital MSWiA, Internal Diseases, Warsaw

Warsaw, , Poland

Site Status

FSB Instit. HC Irkutsk Scient.Cent. Sibirian Branch of Russ. Acad. Scien.

Irkutsk, , Russia

Site Status

Kirov State Med.Univ. of MoH RF

Kirov, , Russia

Site Status

Federal State Budgetary Institution " State Scientific Center of Coloproctology" MOH Russia

Moscow, , Russia

Site Status

Reg. Clin. Scientific Research Institute na Vladimiskiy

Moscow, , Russia

Site Status

The limited liability company "Clinic USI 4D"

Pyatigorsk, , Russia

Site Status

FSBMEI HPE "Military Medical Academy n.a. S.M. Kirov"

Saint Petersburg, , Russia

Site Status

Inje University Haeundae Paik Hospital

Busan, , South Korea

Site Status

Yeungnam University Medical Center

Daegu, , South Korea

Site Status

Hospital Virgen del Rocío

Seville, , Spain

Site Status

Hospital Politècnic La Fe

Valencia, , Spain

Site Status

Barnsley Hospital

Barnsley, , United Kingdom

Site Status

Doncaster Royal Infirmary

Doncaster, , United Kingdom

Site Status

Guy's Hospital

London, , United Kingdom

Site Status

Whiston Hospital

Prescot, , United Kingdom

Site Status

Countries

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United States Austria Belgium Canada Germany Italy Japan Poland Russia South Korea Spain United Kingdom

References

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Lebwohl MG, Thoma C, Haeufel T. Spesolimab use in generalised pustular psoriasis flares - Authors' reply. Lancet. 2024 Aug 31;404(10455):847-848. doi: 10.1016/S0140-6736(24)01557-5. No abstract available.

Reference Type DERIVED
PMID: 39216969 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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2017-004230-28

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

1368-0005

Identifier Type: -

Identifier Source: org_study_id

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