Efficacy and Safety of Adalimumab in Subjects With Moderately to Severely Acute Ulcerative Colitis

NCT ID: NCT00385736

Last Updated: 2011-04-11

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

576 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-11-30

Study Completion Date

2010-03-31

Brief Summary

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The objective of this study is to assess the efficacy and safety of adalimumab for the induction of clinical remission in subjects with moderately to severely active ulcerative colitis.

Detailed Description

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This was a Phase 3, multicenter, randomized, double-blind (DB), placebo-controlled trial designed to evaluate the efficacy and safety of the human anti-TNF monoclonal antibody adalimumab for the induction of clinical remission in participants with moderately to severely active ulcerative colitis (UC).

Adult participants with moderate to severe UC (Mayo score of 6 to 12 points with endoscopy subscore of 2 to 3 points), confirmed by colonoscopy with biopsy or by flexible sigmoidoscopy with biopsy, were enrolled at 80 sites worldwide. The study enrolled 576 participants, including 186 participants under the original protocol and protocol Amendments 1 and 2, and 390 participants under protocol Amendments 3 and 4.

Participants enrolled in the study prior to Amendment 3 were randomized in a 1:1 ratio to receive adalimumab or placebo during the 12-week DB induction period. Participants received 4 injections of adalimumab 40 mg (160 mg) or 4 injections of placebo at Baseline (Week 0), followed by 2 injections of adalimumab 40 mg (80 mg) or 2 injections of placebo at Week 2, followed by 1 injection of adalimumab 40 mg or placebo at Weeks 4 and 6. At Week 8, participants randomized to placebo received 4 injections of adalimumab 40 mg (160 mg) followed by 2 injections of adalimumab 40 mg (80 mg) at Week 10. Participants randomized to adalimumab received 3 injections of placebo and 1 injection of adalimumab 40 mg at Week 8 and 1 injection of placebo and 1 injection of adalimumab 40 mg at Week 10. All participants continued to receive 1 injection of open-label (OL) adalimumab 40 mg every other week beginning at Week 12 up to Week 52 (or the early termination visit). Starting at Week 14, participants who had inadequate responses to treatment (as defined using partial Mayo scores) were permitted to dose escalate to adalimumab 40 mg weekly. Participants with persistent inadequate response while on weekly treatment could be discontinued from the study at the discretion of the investigator.

In August 2007, the study design was amended to incorporate an additional adalimumab induction dosing arm of 80/40 mg. Earlier that year, both 160/80-mg and 80/40-mg induction regimens had been approved in the EU as induction treatment for Crohn's disease. The adalimumab induction dosing regimen of 80/40 mg was therefore included so that both of these approved induction regimens would be evaluated for the induction of remission of UC.

Participants enrolled in the study after Amendment 3 were randomized in a 1:1:1 ratio to receive adalimumab (1 of 2 regimens) or placebo during the 8-week DB induction period. Participants received DB therapy from Baseline until Week 8 and OL therapy from Week 8 until the end of the study. In the first adalimumab dosing arm (adalimumab 80/40), participants received 2 injections of adalimumab 40 mg (80 mg) and 2 injections of placebo at Baseline followed by 1 injection of adalimumab 40 mg and 1 injection of placebo at Week 2, and 1 injection of adalimumab 40 mg every other week thereafter. In the second adalimumab DB induction dosing arm (adalimumab 160/80), participants received 4 injections of adalimumab 40 mg (160 mg) at Baseline followed by 2 injections of adalimumab 40 mg (80 mg) at Week 2, and 1 injection of adalimumab 40 mg every other week thereafter. Participants randomized to placebo received 4 injections of placebo at Baseline followed by 2 injections of placebo at Week 2, and 1 injection of placebo at Weeks 4 and 6. Beginning at Week 8, but after the Week 8 study assessments had been completed, all participants received 1 injection of OL adalimumab 40 mg every other week until Week 52 or early termination. Starting at Week 12, participants who had inadequate responses to treatment (as defined using partial Mayo scores) were permitted to dose escalate to adalimumab 40 mg weekly. Participants with persistent inadequate response while on weekly treatment could be discontinued from the study at the discretion of the investigator.

For the analysis of efficacy parameters during the DB Period through Week 8, only participants randomized under Protocol Amendment 3 or later were considered ("Efficacy Analysis Set - Induction" in the participant flow). For the analysis of efficacy parameters during the OL Period through Week 52, all randomized participants (under any version of the protocol) who received at least 1 dose of study drug were considered ("Efficacy Analysis Set - Maintenance" in the participant flow). For the analysis of safety parameters, all participants who received at least 1 dose of study drug were considered ("Safety Analysis Set" in the participant flow).

Twelve ranked secondary variables during the DB Period through Week 8 were to be tested in a hierarchical order to account for multiple testing. These variables are identified as "Ranked Secondary Endpoints" in the results section below. Additionally, non-ranked secondary variables during the OL Period through Week 52 were tested and are presented after the ranked secondary endpoints in the results section below.

Conditions

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Ulcerative Colitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Adalimumab 80/40

Group Type EXPERIMENTAL

adalimumab

Intervention Type BIOLOGICAL

Prefilled syringe, 40 mg (loading dose then every other week dosing). 80 mg at Week 0, 40 mg at Week 2, and 40 mg every other week starting at Week 4.

Adalimumab 160/80/40

Group Type EXPERIMENTAL

adalimumab

Intervention Type BIOLOGICAL

Prefilled syringe, 40 mg (loading dose then every other week dosing). 160 mg at Week 0, 80 mg at Week 2, and 40 mg every other week starting at Week 4.

Placebo

Group Type PLACEBO_COMPARATOR

placebo

Intervention Type BIOLOGICAL

Placebo for 40 mg syringe. Matching placebo for loading dose and every other week dosing. Subjects received placebo at Weeks 0, 2, 4, and 6, followed by 160 mg adalimumab at Week 8, 80 mg adalimumab at Week 10, and 40 mg adalimumab eow thereafter (prior to Amendment 3) or 40 mg adalimumab eow starting at Week 8 (after Amendment 3).

Interventions

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adalimumab

Prefilled syringe, 40 mg (loading dose then every other week dosing). 80 mg at Week 0, 40 mg at Week 2, and 40 mg every other week starting at Week 4.

Intervention Type BIOLOGICAL

adalimumab

Prefilled syringe, 40 mg (loading dose then every other week dosing). 160 mg at Week 0, 80 mg at Week 2, and 40 mg every other week starting at Week 4.

Intervention Type BIOLOGICAL

placebo

Placebo for 40 mg syringe. Matching placebo for loading dose and every other week dosing. Subjects received placebo at Weeks 0, 2, 4, and 6, followed by 160 mg adalimumab at Week 8, 80 mg adalimumab at Week 10, and 40 mg adalimumab eow thereafter (prior to Amendment 3) or 40 mg adalimumab eow starting at Week 8 (after Amendment 3).

Intervention Type BIOLOGICAL

Other Intervention Names

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ABT-D2E7 Humira ABT-D2E7 Humira

Eligibility Criteria

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Inclusion Criteria

1. Male and female participants \>= 18 years of age
2. Diagnosis of ulcerative colitis for greater than 90 days prior to Baseline
3. Diagnosis of active ulcerative colitis confirmed by colonoscopy with biopsy or flexible sigmoidoscopy with biopsy during the Screening Period, with exclusion of infection
4. Active UC with a Mayo score of 6 to 12 points and endoscopy subscore of 2 to 3 points, despite concurrent treatment with at least 1 of the following (oral corticosteroids or immunosuppressants or both as defined below):

* Stable oral corticosteroid dose (prednisone dose of \>= 20 mg/day or equivalent) for at least 14 days prior to Baseline or stable oral corticosteroid dose (prednisone of \< 20 mg/day) for at least 40 days prior to Baseline.

and/or
* At least a consecutive 90 day course of azathioprine or 6-mercaptopurine (6 MP) prior to Baseline, with a dose of azathioprine \>= 1.5 mg/kg/day or 6 MP \>= 1 mg/kg/day (rounded to the nearest available tablet formulation), or a dose that is the highest tolerated by the participant (e.g., due to leukopenia, elevated liver enzymes, nausea) during that time. Participant was to be on a stable dose for at least 28 days prior to Baseline.

Concurrent therapy was not required for participants who were previously treated with corticosteroids or immunosuppressants (azathioprine or 6-MP) during the previous 5 years and, in the judgment of the investigator, have failed to respond to or could not tolerate their treatment.
5. Had to be able to self-administer or has caregiver who can reliably administer subcutaneous injections.
6. Had to be able and willing to give written informed consent and to comply with the requirements of this study protocol.
7. Female had to be either not of childbearing potential, defined as postmenopausal for at least 1 year or surgically sterile (bilateral tubal ligation, bilateral oophorectomy or hysterectomy), or of childbearing potential and practicing an approved method of birth control throughout the study and for 150 days after last dose of study drug. Examples of approved methods of birth control included the following:

* Condoms, sponge, foams, jellies, diaphragm or intrauterine device
* Oral, parenteral or intravaginal contraceptives for 90 days prior to study drug administration
* A vasectomized partner
8. The results of the serum pregnancy test performed at the Screening Visit and urine pregnancy test performed at the Baseline Visit had to be negative.
9. Judged to be in generally good health as determined by the principal investigator

Exclusion Criteria

1. History of subtotal colectomy with ileorectostomy or colectomy with ileoanal pouch, Koch pouch, or ileostomy for ulcerative colitis or is planning bowel surgery.
2. Received infliximab or any other anti-TNF agent or any biological therapy in the past.
3. Received previous treatment with adalimumab or previous participation in an adalimumab clinical study.
4. Received cyclosporine, tacrolimus, or mycophenolate mofetil within 30 days prior to Baseline.
5. Received intravenous corticosteroids within 14 days prior to Screening or during the Screening Period.
6. Received therapeutic enema or suppository, other than required for endoscopy, within 14 days prior to the Screening endoscopy and during the remainder of the Screening Period.
7. Current diagnosis of fulminant colitis and/or toxic megacolon.
8. Participants with disease limited to the rectum (ulcerative proctitis).
9. Current diagnosis of indeterminate colitis.
10. Current diagnosis and/or history of Crohn's disease.
11. Currently receiving total parenteral nutrition.
12. Discontinued use of azathioprine or 6-MP within 28 days of Baseline.
13. Discontinued use of corticosteroid within 14 days of Baseline.
14. Participants using aminosalicylates for less than 90 days prior to Baseline, not on a stable dose for at least 28 days prior to Baseline, or discontinued use within 28 days of Baseline.
15. Participants with positive Clostridium difficile stool assay.
16. Infections requiring treatment with intravenous (IV) antibiotics, IV antivirals, or IV antifungals within 30 days prior to Baseline or oral antibiotics, oral antivirals, or oral antifungals within 14 days prior to Baseline.
17. History of malignancy other than a successfully treated non-metastatic cutaneous squamous cell or basal cell carcinoma and/or localized carcinoma in situ of the cervix. If the Screening colonoscopy/flexible sigmoidoscopy showed evidence of dysplasia or a malignancy, the participant was not to be enrolled in the study.
18. History of listeria, histoplasmosis, chronic or active hepatitis B infection, human immunodeficiency virus, immunodeficiency syndrome, central nervous system demyelinating disease, or untreated tuberculosis (TB).
19. Female participants who was pregnant or breast-feeding or considering becoming pregnant during the study. There should be at least a 150-day period between the last dose of study drug and either conception or initiation of breast-feeding in women of childbearing potential.
20. Poorly controlled medical condition(s), such as uncontrolled diabetes, unstable ischemic heart disease, moderate to severe congestive heart failure, recent cerebrovascular accident and any other condition, which in the opinion of the investigator, would put the participant at risk by participation in the protocol.
21. Received any investigational agent within 30 days or 5 half lives prior to Baseline (whichever is longer).
22. History of clinically significant drug or alcohol abuse during the previous year.
23. Participants with known hypersensitivity to the excipients of adalimumab as stated in the label.
24. Participants with any prior exposure to Tysabri® (natalizumab).
25. Participants currently taking both budesonide and prednisone (or equivalent) simultaneously.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Abbott

INDUSTRY

Sponsor Role lead

Responsible Party

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Abbott

Principal Investigators

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Roopal Thakkar, MD

Role: STUDY_DIRECTOR

Abbott

Locations

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Site Ref # / Investigator 2080

Birmingham, Alabama, United States

Site Status

Site Ref # / Investigator 6034

Mobile, Alabama, United States

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Site Ref # / Investigator 5100

Fayetteville, Arkansas, United States

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Site Ref # / Investigator 5390

Orange, California, United States

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Site Ref # / Investigator 5392

San Diego, California, United States

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Site Ref # / Investigator 2245

Bridgeport, Connecticut, United States

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Site Ref # / Investigator 2240

Gainesville, Florida, United States

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Site Ref # / Investigator 2230

South Miami, Florida, United States

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Site Ref # / Investigator 5393

Atlanta, Georgia, United States

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Site Ref # / Investigator 2231

Atlanta, Georgia, United States

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Site Ref # / Investigator 2498

Chicago, Illinois, United States

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Site Ref # / Investigator 2078

Chevy Chase, Maryland, United States

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Site Ref # / Investigator 2238

Silver Springs, Maryland, United States

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Site Ref # / Investigator 1971

Boston, Massachusetts, United States

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Site Ref # / Investigator 2246

Rochester, Minnesota, United States

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Site Ref # / Investigator 2243

Kansas City, Missouri, United States

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Site Ref # / Investigator 2247

Mexico, Missouri, United States

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Site Ref # / Investigator 2233

Lincoln, Nebraska, United States

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Site Ref # / Investigator 2236

Cedar Knolls, New Jersey, United States

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Site Ref # / Investigator 2072

New York, New York, United States

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Site Ref # / Investigator 2241

Charlotte, North Carolina, United States

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Site Ref # / Investigator 2232

Raleigh, North Carolina, United States

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Site Ref # / Investigator 11801

Wilmington, North Carolina, United States

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Site Ref # / Investigator 2074

Cincinnati, Ohio, United States

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Site Ref # / Investigator 2126

Cleveland, Ohio, United States

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Site Ref # / Investigator 6090

Germantown, Tennessee, United States

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Site Ref # / Investigator 2076

Nashville, Tennessee, United States

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Site Ref # / Investigator 2229

Bellevue, Washington, United States

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Site Ref # / Investigator 2077

Milwaukee, Wisconsin, United States

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Site Ref # / Investigator 4936

Graz, , Austria

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Site Ref # / Investigator 6224

Hall in Tirol, , Austria

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Site Ref # / Investigator 3830

Innsbruck, , Austria

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Site Ref # / Investigator 7508

Linz, , Austria

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Site Ref # / Investigator 3829

Salzburg, , Austria

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Site Ref # / Investigator 4937

Vienna, , Austria

Site Status

Site Ref # / Investigator 3831

Vienna, , Austria

Site Status

Site Ref # / Investigator 3861

Bonheiden, , Belgium

Site Status

Site Ref # / Investigator 3859

Liège, , Belgium

Site Status

Site Ref # / Investigator 3862

Roeselare, , Belgium

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Site Ref # / Investigator 2224

Calgary, Alberta, Canada

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Site Ref # / Investigator 2227

Edmonton, Alberta, Canada

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Site Ref # / Investigator 2226

Vancouver, British Columbia, Canada

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Site Ref # / Investigator 2223

Winnipeg, Manitoba, Canada

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Site Ref # / Investigator 2138

Toronto, Ontario, Canada

Site Status

Site Ref # / Investigator 3858

Brno, , Czechia

Site Status

Site Ref # / Investigator 3856

Olomouc, , Czechia

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Site Ref # / Investigator 3857

Ostrava, , Czechia

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Site Ref # / Investigator 3854

Prague, , Czechia

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Site Ref # / Investigator 3855

Prague, , Czechia

Site Status

Site Ref # / Investigator 3832

Berlin, , Germany

Site Status

Site Ref # / Investigator 13983

Essen, , Germany

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Site Ref # / Investigator 3834

Jena, , Germany

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Site Ref # / Investigator 3833

Kiel, , Germany

Site Status

Site Ref # / Investigator 3878

Mainz, , Germany

Site Status

Site Ref # / Investigator 3897

Munich, , Germany

Site Status

Site Ref # / Investigator 3852

Budapest, , Hungary

Site Status

Site Ref # / Investigator 3850

Budapest, , Hungary

Site Status

Site Ref # / Investigator 3849

Győr, , Hungary

Site Status

Site Ref # / Investigator 3876

Bologna, , Italy

Site Status

Site Ref # / Investigator 3848

Milan, , Italy

Site Status

Site Ref # / Investigator 3845

Palermo, , Italy

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Site Ref # / Investigator 6232

Rome, , Italy

Site Status

Site Ref # / Investigator 3846

Rome, , Italy

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Site Ref # / Investigator 3873

Eindhoven, , Netherlands

Site Status

Site Ref # / Investigator 3875

Leiden, , Netherlands

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Site Ref # / Investigator 8061

Lodz, , Poland

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Site Ref # / Investigator 13804

Sopot, , Poland

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Site Ref # / Investigator 8055

Warsaw, , Poland

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Site Ref # / Investigator 2392

Ponce, , Puerto Rico

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Site Ref # / Investigator 2393

San Juan, , Puerto Rico

Site Status

Site Ref # / Investigator 3839

Banská Bystrica, , Slovakia

Site Status

Site Ref # / Investigator 3838

Bratislava, , Slovakia

Site Status

Site Ref # / Investigator 3841

Bratislava, , Slovakia

Site Status

Site Ref # / Investigator 3842

Nitra, , Slovakia

Site Status

Site Ref # / Investigator 14721

Prešov, , Slovakia

Site Status

Site Ref # / Investigator 14521

Trenčín, , Slovakia

Site Status

Site Ref # / Investigator 3840

Trnava, , Slovakia

Site Status

Site Ref # / Investigator 8503

Gothenburg, , Sweden

Site Status

Site Ref # / Investigator 8504

Linköping, , Sweden

Site Status

Site Ref # / Investigator 8502

Lund, , Sweden

Site Status

Countries

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United States Austria Belgium Canada Czechia Germany Hungary Italy Netherlands Poland Puerto Rico Slovakia Sweden

References

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Reinisch W, Sandborn WJ, Panaccione R, Huang B, Pollack PF, Lazar A, Thakkar RB. 52-week efficacy of adalimumab in patients with moderately to severely active ulcerative colitis who failed corticosteroids and/or immunosuppressants. Inflamm Bowel Dis. 2013 Jul;19(8):1700-9. doi: 10.1097/MIB.0b013e318281f2b7.

Reference Type DERIVED
PMID: 23665965 (View on PubMed)

Reinisch W, Sandborn WJ, Hommes DW, D'Haens G, Hanauer S, Schreiber S, Panaccione R, Fedorak RN, Tighe MB, Huang B, Kampman W, Lazar A, Thakkar R. Adalimumab for induction of clinical remission in moderately to severely active ulcerative colitis: results of a randomised controlled trial. Gut. 2011 Jun;60(6):780-7. doi: 10.1136/gut.2010.221127. Epub 2011 Jan 5.

Reference Type DERIVED
PMID: 21209123 (View on PubMed)

Ryan C, Sobell JM, Leonardi CL, Lynde CW, Karunaratne M, Valdecantos WC, Hendrickson BA. Safety of Adalimumab Dosed Every Week and Every Other Week: Focus on Patients with Hidradenitis Suppurativa or Psoriasis. Am J Clin Dermatol. 2018 Jun;19(3):437-447. doi: 10.1007/s40257-017-0341-6.

Reference Type DERIVED
PMID: 29380251 (View on PubMed)

Feagan BG, Sandborn WJ, Lazar A, Thakkar RB, Huang B, Reilly N, Chen N, Yang M, Skup M, Mulani P, Chao J. Adalimumab therapy is associated with reduced risk of hospitalization in patients with ulcerative colitis. Gastroenterology. 2014 Jan;146(1):110-118.e3. doi: 10.1053/j.gastro.2013.09.032. Epub 2013 Sep 22.

Reference Type DERIVED
PMID: 24067881 (View on PubMed)

Other Identifiers

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2006-002781-20

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

M06-826

Identifier Type: -

Identifier Source: org_study_id

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