Efficacy and Safety of Adalimumab in Pediatric Subjects With Moderate to Severe Ulcerative Colitis

NCT ID: NCT02065557

Last Updated: 2020-10-05

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

101 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-10-13

Study Completion Date

2020-02-07

Brief Summary

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The purpose of the study is to demonstrate the efficacy and safety, and to assess the pharmacokinetics of adalimumab administered subcutaneously (SC) in pediatric subjects with moderate to severe ulcerative colitis (UC).

Detailed Description

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Conditions

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Ulcerative Colitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Adalimumab Induction Standard Dose

Participants randomized to receive adalimumab 2.4 mg/kg (maximum dose of 160 mg) at Baseline and matching placebo at Week 1, 1.2 mg/kg (maximum dose of 80 mg) at Week 2, followed by 0.6 mg/kg (maximum dose of 40 mg) at Week 4 and Week 6.

Group Type EXPERIMENTAL

Adalimumab

Intervention Type BIOLOGICAL

Subcutaneous (SC) injection

Placebo

Intervention Type BIOLOGICAL

Subcutaneous (SC) injection

Adalimumab Induction High Dose

Participants randomized to receive adalimumab 2.4 mg/kg (maximum dose of 160 mg) at Baseline and at Week 1, 1.2 mg/kg (maximum dose of 80 mg) at Week 2, followed by 0.6 mg/kg (maximum dose of 40 mg) at Week 4 and Week 6.

Group Type EXPERIMENTAL

Adalimumab

Intervention Type BIOLOGICAL

Subcutaneous (SC) injection

Adalimumab Induction High Dose - Open Label

(After Amendment 4) participants assigned to open-label adalimumab 2.4 mg/kg (maximum dose of 160 mg) at Baseline and at Week 1, 1.2 mg/kg (maximum dose of 80 mg) at Week 2, followed by 0.6 mg/kg (maximum dose of 40 mg) at Week 4 and Week 6.

Group Type EXPERIMENTAL

Adalimumab

Intervention Type BIOLOGICAL

Subcutaneous (SC) injection

Maintenance Placebo

(Prior to Amendment 4) participants demonstrating a clinical response per PMS (defined as a decrease in PMS ≥ 2 points and ≥ 30% from Baseline) at Week 8 randomized to maintenance placebo. Participants were to continue their blinded treatment during the maintenance period until Week 52 unless they had ≥ 2 flares and got open label rescue therapy after the second flare.

Group Type PLACEBO_COMPARATOR

Adalimumab

Intervention Type BIOLOGICAL

Subcutaneous (SC) injection

Placebo

Intervention Type BIOLOGICAL

Subcutaneous (SC) injection

Adalimumab Maintenance Standard Dose

Participants demonstrating a clinical response per PMS (defined as a decrease in PMS ≥ 2 points and ≥ 30% from Baseline) at Week 8 randomized to adalimumab maintenance standard dose (0.6 mg/kg \[maximum dose of 40 mg\] every other week). Participants were to continue their blinded treatment during the maintenance period until Week 52 unless they had ≥ 2 flares and got open label rescue therapy after second flare.

Group Type EXPERIMENTAL

Adalimumab

Intervention Type BIOLOGICAL

Subcutaneous (SC) injection

Adalimumab Maintenance High Dose

Participants demonstrating a clinical response per PMS (defined as a decrease in PMS ≥ 2 points and ≥ 30% from Baseline) at Week 8 randomized to adalimumab maintenance high dose (0.6 mg/kg \[maximum dose of 40 mg\] every week). Participants were to continue their blinded treatment during the maintenance period until Week 52 unless they had ≥ 2 flares and got open label rescue therapy after second flare.

Group Type EXPERIMENTAL

Adalimumab

Intervention Type BIOLOGICAL

Subcutaneous (SC) injection

Interventions

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Adalimumab

Subcutaneous (SC) injection

Intervention Type BIOLOGICAL

Placebo

Subcutaneous (SC) injection

Intervention Type BIOLOGICAL

Other Intervention Names

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Humira

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of UC for at least 12 weeks prior to screening, confirmed by endoscopy with biopsy.
* Active ulcerative colitis with a Mayo Score of 6 - 12 points and endoscopy subscore of 2 - 3 despite concurrent treatment with oral corticosteroids or immunosuppressants or both.

Exclusion Criteria

* Subject with Crohn's disease (CD) or indeterminate colitis (IC).
* Current diagnosis of fulminant colitis and/or toxic megacolon.
* Subjects with disease limited to the rectum (ulcerative proctitis) during the screening endoscopy.
* Chronic recurring infections or active tuberculosis (TB).
Minimum Eligible Age

4 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AbbVie

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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AbbVie Inc.

Role: STUDY_DIRECTOR

AbbVie

Locations

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Childrens Hospital LA /ID# 147452

Los Angeles, California, United States

Site Status

Univ California, San Francisco /ID# 120901

San Francisco, California, United States

Site Status

Arnold Palmer Hosp Children /ID# 120898

Orlando, Florida, United States

Site Status

Emory University Hospital /ID# 121858

Atlanta, Georgia, United States

Site Status

Children's Ctr Digestive, US /ID# 121855

Atlanta, Georgia, United States

Site Status

University of Chicago /ID# 120904

Chicago, Illinois, United States

Site Status

Loyola University Medical Ctr /ID# 120900

Maywood, Illinois, United States

Site Status

Indiana University /ID# 120908

Indianapolis, Indiana, United States

Site Status

Massachusetts General Hospital /ID# 124551

Boston, Massachusetts, United States

Site Status

Boston Childrens Hospital /ID# 147714

Boston, Massachusetts, United States

Site Status

Mayo Clinic - Rochester /ID# 121056

Rochester, Minnesota, United States

Site Status

Minnesota Gastroenterology P.A /ID# 120895

Saint Paul, Minnesota, United States

Site Status

Goryeb Chidlren's Hospital /ID# 121860

Morristown, New Jersey, United States

Site Status

North Shore University Hospital /ID# 120905

New Hyde Park, New York, United States

Site Status

Univ Rochester Med Ctr /ID# 127776

Rochester, New York, United States

Site Status

Multicare Institute for Research and Innovation /ID# 147716

Tacoma, Washington, United States

Site Status

Womens and Childrens Hospital /ID# 127538

Adelaide, South Australia, Australia

Site Status

Medizinische Universitat Wien /ID# 120802

Vienna, Vienna, Austria

Site Status

LKH Salzburg and Paracelsus /ID# 123457

Salzburg, , Austria

Site Status

UZ Brussel /ID# 120798

Jette, Brussels Capital, Belgium

Site Status

Cliniques Universitaires Saint Luc /ID# 120797

Woluwe-Saint-Lambert, Brussels Capital, Belgium

Site Status

Hosp Univ Enfants Reine Fabiol /ID# 120795

Brussels, , Belgium

Site Status

London Health Sciences Centre /ID# 127777

London, Ontario, Canada

Site Status

Palacky University /ID# 131388

Olomouc, , Czechia

Site Status

Univ Hosp, Plzen, CZ /ID# 120813

Pilsen, , Czechia

Site Status

Petz Aladar Megyei Oktato Korh /ID# 124323

Győr, , Hungary

Site Status

Balassa Janos County Hospital /ID# 128474

Szekszárd, , Hungary

Site Status

Soroka Medical Ctr /ID# 147338

Beersheba, , Israel

Site Status

Assaf Harofeh Medical Center /ID# 147791

Be’er Ya‘aqov, , Israel

Site Status

Rambam Health Care Campus /ID# 120827

Haifa, , Israel

Site Status

Shaare Zedek Medical Center /ID# 120830

Jerusalem, , Israel

Site Status

Schneider Childrens Med Ctr /ID# 120821

Petah Tikva, , Israel

Site Status

Sheba Medical Center /ID# 124324

Ramat Gan, , Israel

Site Status

Kaplan Medical Center /ID# 150245

Rehovot, , Israel

Site Status

Kurume University Hospital /ID# 125476

Kurume-shi, Fukuoka, Japan

Site Status

Gunma University Hospital /ID# 126345

Maebashi, Gunma, Japan

Site Status

Hokkaido P.W.F.A.C. Sapporo-Kosei General Hospital /ID# 124482

Sapporo, Hokkaido, Japan

Site Status

The Hospital of Hyogo College of Medicine /ID# 131665

Nishinomiya-shi, Hyōgo, Japan

Site Status

Saiseikai Yokohamashi Tobu /ID# 124486

Yokohama, Kanagawa, Japan

Site Status

Yokohama City Univ Medical Ctr /ID# 147763

Yokohama, Kanagawa, Japan

Site Status

Miyagi Children's Hospital /ID# 125475

Sendai, Miyagi, Japan

Site Status

Saitama Children's Medical Center /ID# 124485

Saitama-shi, Saitama, Japan

Site Status

Juntendo University Hospital /ID# 124536

Bunkyo-ku, Tokyo, Japan

Site Status

National Center for Child Health and Development /ID# 125203

Setagaya-ku, Tokyo, Japan

Site Status

Osaka General Medical Center /ID# 124535

Osaka, , Japan

Site Status

Canterbury District Health Boa /ID# 120837

Christchurch, , New Zealand

Site Status

Uni Szpital Dzieciecy w Krakowie /ID# 120915

Krakow, Lesser Poland Voivodeship, Poland

Site Status

Centrum Zdrowia MDM /ID# 120910

Warsaw, Masovian Voivodeship, Poland

Site Status

Gabinet Lekarski Bartosz Korcz /ID# 120916

Rzeszów, , Poland

Site Status

Samodzielny Publiczny Szpital /ID# 120839

Wroclaw, , Poland

Site Status

Polish Mothers Memorial Hosp /ID# 148497

Lodz, Łódź Voivodeship, Poland

Site Status

FN s poliklinikou F.D. Rooseve /ID# 120847

Banská Bystrica, , Slovakia

Site Status

Univerzitna Nemocnica Bratislava /ID# 120842

Bratislava, , Slovakia

Site Status

Univerzitna nemocnica Martin /ID# 120844

Martin, Žilina Region, Slovakia

Site Status

Hospital Univ Vall d'Hebron /ID# 120856

Barcelona, , Spain

Site Status

Hospital Infantil Universitario Nino Jesus /ID# 121862

Madrid, , Spain

Site Status

The Royal London Hospital /ID# 120861

London, London, City of, United Kingdom

Site Status

The Royal Free Hospital /ID# 123142

London, London, City of, United Kingdom

Site Status

Royal Hosp for Sick Children /ID# 120864

Glasgow, , United Kingdom

Site Status

Manchester Royal Infirmary, Ma /ID# 120862

Manchester, , United Kingdom

Site Status

Countries

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United States Australia Austria Belgium Canada Czechia Hungary Israel Japan New Zealand Poland Slovakia Spain United Kingdom

References

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Croft NM, Faubion WA Jr, Kugathasan S, Kierkus J, Ruemmele FM, Shimizu T, Mostafa NM, Venetucci M, Finney-Hayward T, Sanchez Gonzalez Y, Bereswill M, Lazar A, Turner D. Efficacy and safety of adalimumab in paediatric patients with moderate-to-severe ulcerative colitis (ENVISION I): a randomised, controlled, phase 3 study. Lancet Gastroenterol Hepatol. 2021 Aug;6(8):616-627. doi: 10.1016/S2468-1253(21)00142-4. Epub 2021 Jun 19.

Reference Type DERIVED
PMID: 34153231 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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2013-003032-77

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

M11-290

Identifier Type: -

Identifier Source: org_study_id

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