A Study of Ustekinumab in Pediatric Participants With Moderately to Severely Active Ulcerative Colitis (UC)

NCT ID: NCT04630028

Last Updated: 2025-07-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

112 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-03-17

Study Completion Date

2025-06-05

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to evaluate: a) the efficacy of ustekinumab dosing in inducing clinical remission, b) safety profile of ustekinumab, and c) ustekinumab exposure (pharmacokinetics \[PK\]) in pediatric participants with moderately to severely active UC.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Colitis, Ulcerative

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Induction Period (I): Ustekinumab

All participants will receive a single intravenous (IV) administration of ustekinumab at induction Week 0 (I-0) based on body surface area (BSA) (milligram per meter square \[mg/m\^2\]) or weight-tiered induction dose (milligram per kilogram \[mg/kg\]).

Group Type EXPERIMENTAL

Ustekinumab Dose Based on BSA and Body Weight

Intervention Type DRUG

As per BSA and body weight Ustekinumab will be administered SC and IV.

Maintenance (M) Period: Ustekinumab once every 8 Week (q8w)

Participants will receive subcutaneous (SC) administration of ustekinumab every 8 weeks (q8w) based on BSA (mg/m\^2) or weight-tiered induction dose (mg/kg) at Weeks M-0, M-8, M-16, M-24, M-32, M-40 and matching placebo at Weeks M-12 and M-36 to maintain the blind.

Group Type EXPERIMENTAL

Ustekinumab Dose Based on BSA and Body Weight

Intervention Type DRUG

As per BSA and body weight Ustekinumab will be administered SC and IV.

Matching Placebo

Intervention Type DRUG

Placebo will be administered subcutaneously.

Maintenance (M) Period: Ustekinumab once every 12 Week (q12w)

Participants will receive SC administration of ustekinumab every 12 weeks (q12w) based on BSA (mg/m\^2) or weight-tiered induction dose (mg/kg) at Weeks M-0, M-12, M-24, M-36 and matching placebo at Weeks M-8, M-16, M-32, and M-40 to maintain the blind.

Group Type EXPERIMENTAL

Ustekinumab Dose Based on BSA and Body Weight

Intervention Type DRUG

As per BSA and body weight Ustekinumab will be administered SC and IV.

Matching Placebo

Intervention Type DRUG

Placebo will be administered subcutaneously.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Ustekinumab Dose Based on BSA and Body Weight

As per BSA and body weight Ustekinumab will be administered SC and IV.

Intervention Type DRUG

Matching Placebo

Placebo will be administered subcutaneously.

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

STELARA

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Medically stable on the basis of physical examination, medical history, and vital signs, performed at screening. Any abnormalities must be consistent with the underlying illness in the study population and this determination must be recorded in the participant's source documents and acknowledged by the investigator
* Must have had UC diagnosed prior to screening
* Have moderately to severely active UC, defined as a baseline Mayo score of 6 through 12, inclusive, with a screening Mayo endoscopy subscore greater than or equal to (\>=) 2 as determined by a central review of the video of the endoscopy
* A participant who has had extensive colitis for \>= 8 years, or disease limited to the left side of the colon for \>= 10 years, must: a) have had a full colonoscopy to assess for the presence of dysplasia within 1 year before the first administration of study intervention or b) have a full colonoscopy with surveillance for dysplasia as the baseline endoscopy during the screening period. Results from these surveillance biopsies must be negative for dysplasia (low-grade, high-grade, or indeterminant) prior to the first administration of study intervention
* Females of childbearing potential must have a negative highly sensitive urine pregnancy test at screening and at Week I-0 prior to study intervention administration

Exclusion Criteria

* Have UC limited to the rectum only or to less than (\<) 20 centimeter (cm) of the colon
* Presence or history of colonic or small bowel obstruction within 6 months prior to screening, confirmed by objective radiographic or endoscopic evidence of a stricture with resulting obstruction (dilation of the colon or small bowel proximal to the stricture on barium radiograph or an inability to traverse the stricture at endoscopy)
* Have a history of latent or active granulomatous infection, histoplasmosis, or coccidioidomycosis, or have had a nontuberculous mycobacterial infection prior to screening
* Presence or history of any malignancy including presence or history of lymphoproliferative disease including lymphoma, or signs and symptoms suggestive of possible lymphoproliferative disease, such as lymphadenopathy of unusual size or location (example, nodes in the posterior triangle of the neck, infraclavicular, epitrochlear, or periaortic areas) and monoclonal gammopathy of undetermined significance, or clinically significant hepatomegaly or splenomegaly
* Has known allergies, hypersensitivity, or intolerance to ustekinumab or its excipients
Minimum Eligible Age

2 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Janssen Research & Development, LLC

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Janssen Research & Development, LLC Clinical Trial

Role: STUDY_DIRECTOR

Janssen Research & Development, LLC

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Nemours DuPont Hospital for Children

Wilmington, Delaware, United States

Site Status

Children's Center for Digestive Health Care

Atlanta, Georgia, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

Morristown Memorial Hospital

Morristown, New Jersey, United States

Site Status

Levine Childrens at Atrium Health

Charlotte, North Carolina, United States

Site Status

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status

Penn State Hershey Children's Hospital

Hershey, Pennsylvania, United States

Site Status

Cook Childrens Medical Center

Fort Worth, Texas, United States

Site Status

Pediatric Specialists Of Virginia

Fairfax, Virginia, United States

Site Status

Universitair Kinderziekenhuis Koningin Fabiola

Brussels, , Belgium

Site Status

Cliniques Universitaires Saint Luc

Brussels, , Belgium

Site Status

UZ Gent

Ghent, , Belgium

Site Status

UZ Brussel

Jette, , Belgium

Site Status

UZ Leuven

Leuven, , Belgium

Site Status

Universitätsklinikum Aachen

Aachen, , Germany

Site Status

Charite-Universitätsmedizin Berlin - Berlin

Berlin, , Germany

Site Status

Universitatsklinikum Erlangen

Erlangen, , Germany

Site Status

Universitatsklinikum Essen

Essen, , Germany

Site Status

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status

Dr. von Haunersches Kinderspital

Munich, , Germany

Site Status

KUNO Klinik St. Hedwig

Regensburg, , Germany

Site Status

Universitatsklinikum Ulm

Ulm, , Germany

Site Status

Semmelweis Egyetem

Budapest, , Hungary

Site Status

Debreceni Egyetem Klinikai Kozpont

Debrecen, , Hungary

Site Status

Borsod Abauj Zemplen Varmegyei Kozponti Korhaz es Egyetemi Oktato Korhaz

Miskolc, , Hungary

Site Status

Szabolcs Szatmar Bereg Varmegyei Oktatokorhaz

Nyíregyháza, , Hungary

Site Status

Szegedi Tudományegyetem, Gyermekgyógyászati Klinika és Gyermekegészségügyi Centrum

Szeged, , Hungary

Site Status

Shamir Medical Center Assaf Harofeh

Be’er Ya‘aqov, , Israel

Site Status

Rambam Medical Center

Haifa, , Israel

Site Status

Carmel Medical Center

Haifa, , Israel

Site Status

Shaare Zedek Medical Center

Jerusalem, , Israel

Site Status

Schneider Children's Medical Center

Petah Tikva, , Israel

Site Status

Sheba Medical Center

Ramat Gan, , Israel

Site Status

Juntendo University Hospital

Bunkyō City, , Japan

Site Status

Gunma University Hospital

Gunma, , Japan

Site Status

Kindai University Nara Hospital

Ikoma, , Japan

Site Status

Kurume University Hospital

Kurume, , Japan

Site Status

Saitama Childrens Medical Center

Saitama Shi, , Japan

Site Status

Miyagi Children's Hospital

Sendai, , Japan

Site Status

National Center for Child Health and Development

Setagaya Ku, , Japan

Site Status

Jichi Medical University Hospital

Shimotsuke, , Japan

Site Status

Mie University Hospital

Tsu, , Japan

Site Status

Szpital im. M. Kopernika

Gdansk, , Poland

Site Status

Uniwersytecki Szpital Dzieciecy w Krakowie

Krakow, , Poland

Site Status

Korczowski Bartosz Gabinet Lekarski

Rzeszów, , Poland

Site Status

GASTROMED Sp. z o.o.

Torun, , Poland

Site Status

WIP Warsaw IBD Point Profesor Kierkus

Warsaw, , Poland

Site Status

Instytut Pomnik Centrum Zdrowia Dziecka

Warsaw, , Poland

Site Status

Kazan State Medical University

Kazan', , Russia

Site Status

Russian National Research Medical University named after N.I.Pirogov

Moscow, , Russia

Site Status

FSBI 'Scientific Centre of Children Health' of the Russian Academy of Medical Sciences

Moscow, , Russia

Site Status

Privolzhsky Research Medical University of Ministry of Health of Russian Federation

Nizhny Novgorod, , Russia

Site Status

Saratov State Medical University

Saratov, , Russia

Site Status

Yaroslavl Regional Children's Clinical Hospital

Yaroslavl, , Russia

Site Status

Birmingham Children's Hospital

Birmingham, , United Kingdom

Site Status

University Hospitals Bristol and Weston NHS Foundation Trust

Bristol, , United Kingdom

Site Status

Cambridge University Hospitals NHS Foundation Trust

Cambridge, , United Kingdom

Site Status

Royal London Hospital

London, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Belgium Germany Hungary Israel Japan Poland Russia United Kingdom

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

CNTO1275PUC3001

Identifier Type: OTHER

Identifier Source: secondary_id

2019-004224-38

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2023-504977-19-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

CR108865

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.