Safety and Efficacy of Andecaliximab (GS-5745) in Adults With Moderately to Severely Active Ulcerative Colitis

NCT ID: NCT02520284

Last Updated: 2019-04-10

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2/PHASE3

Total Enrollment

165 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-09-30

Study Completion Date

2016-11-30

Brief Summary

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The primary objectives of this study are as follows: 1) To evaluate the efficacy of andecaliximab to induce endoscopy, rectal bleeding, and stool frequency (EBS) clinical remission at Week 8 (Cohort 1); 2) To evaluate the efficacy of andecaliximab to maintain EBS clinical remission at Week 52 (Cohort 2); and 3) To evaluate the safety and tolerability of andecaliximab. The study will consist of 3 parts: Induction Phase (Cohort 1), Maintenance Phase (Cohort 2), and an optional Extended Treatment Phase.

Detailed Description

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Conditions

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Ulcerative Colitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Andecaliximab Every 2 Weeks

Participants will receive andecaliximab 150 mg administered via subcutaneous (SC) injection alternating with matching placebo weekly for a total of 4 doses of andecaliximab. Based on Week 8 assessment results, participants will either continue in Blinded Maintenance Treatment phase or will be offered Open-Label andecaliximab 150 mg administered via SC injection weekly for up to Week 51.

Group Type EXPERIMENTAL

Andecaliximab

Intervention Type BIOLOGICAL

Andecaliximab 150 mg administered via SC injection

Placebo

Intervention Type BIOLOGICAL

Placebo matched to andecaliximab administered via SC injection

Andecaliximab Weekly

Participants will receive andecaliximab 150 mg administered via SC injection once weekly for a total of 8 doses. Based on Week 8 assessment results, participants will either continue in Blinded Maintenance Treatment phase or will be offered Open-Label andecaliximab 150 mg administered via SC injection weekly for up to Week 51.

Group Type EXPERIMENTAL

Andecaliximab

Intervention Type BIOLOGICAL

Andecaliximab 150 mg administered via SC injection

Placebo

Participants will receive placebo matched to andecaliximab administered via SC injection once weekly for a total of 8 doses. Based on Week 8 assessment results, participants will either continue in Blinded Maintenance Treatment phase or will be offered Open-Label andecaliximab 150 mg administered via SC injection weekly for up to Week 51.

Group Type PLACEBO_COMPARATOR

Andecaliximab

Intervention Type BIOLOGICAL

Andecaliximab 150 mg administered via SC injection

Placebo

Intervention Type BIOLOGICAL

Placebo matched to andecaliximab administered via SC injection

Interventions

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Andecaliximab

Andecaliximab 150 mg administered via SC injection

Intervention Type BIOLOGICAL

Placebo

Placebo matched to andecaliximab administered via SC injection

Intervention Type BIOLOGICAL

Other Intervention Names

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GS-5745

Eligibility Criteria

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Inclusion Criteria

* Ulcerative Colitis (UC) confirmed on endoscopy
* Moderately to severely active UC (Mayo Score 6-12)
* May be receiving oral 5-aminosalicylate (ASA), oral corticosteroid, azathioprine, 6-mercaptopurine (MP), or methotrexate
* Treatment failure with at least one of the following agents received: corticosteroids, immunomodulators, tumor necrosis factor-alpha (TNFα) antagonists, vedolizumab

Exclusion Criteria

* Diagnose of Crohn's disease or indeterminate colitis
* Pregnant or lactating females
* Any chronic medical condition (including, but not limited to cardiac or pulmonary disease, alcohol or drug abuse)
* Exhibit severe UC / clinically significant active infection
* History of malignancy in the last 5 years
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gilead Study Director

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

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Dothan, Alabama, United States

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Wheat Ridge, Colorado, United States

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Lauderdale Lakes, Florida, United States

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Miramar, Florida, United States

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Winter Park, Florida, United States

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Zephyrhills, Florida, United States

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Chicago, Illinois, United States

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Topeka, Kansas, United States

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Louisville, Kentucky, United States

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Monroe, Louisiana, United States

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Ann Arbor, Michigan, United States

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Plymouth, Minnesota, United States

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St Louis, Missouri, United States

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Egg Harbor, New Jersey, United States

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New York, New York, United States

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Chapel Hill, North Carolina, United States

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Charlotte, North Carolina, United States

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Mentor, Ohio, United States

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Rochester, Ohio, United States

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Germantown, Tennessee, United States

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Hermitage, Tennessee, United States

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Arlington, Texas, United States

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Baytown, Texas, United States

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Houston, Texas, United States

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Irving, Texas, United States

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San Antonio, Texas, United States

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Southlake, Texas, United States

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Charlottesville, Virginia, United States

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Chesapeake, Virginia, United States

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Norfolk, Virginia, United States

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Richmond, Virginia, United States

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Seattle, Washington, United States

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Wauwatosa, Wisconsin, United States

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Footscray, , Australia

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Herston, , Australia

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Malvern, , Australia

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Melbourne, , Australia

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Ghent, , Belgium

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Leuven, , Belgium

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Mouscron, , Belgium

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Pleven, , Bulgaria

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Victoria, British Columbia, Canada

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Vaughan, Ontario, Canada

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Hradec Králové, , Czechia

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Nantes, , France

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Békéscsaba, , Hungary

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Budapest, , Hungary

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Debrecen, , Hungary

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Dublin, Leinster, Ireland

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Rozzano, , Italy

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San Giovanni Rotondo, , Italy

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Daugavpils, , Latvia

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Amsterdam, , Netherlands

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Christchurch, Canterbury, New Zealand

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Auckland, , New Zealand

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Wellington, , New Zealand

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Bialystok, , Poland

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Krakow, , Poland

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Lublin, , Poland

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Piaseczno, , Poland

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Poznan, , Poland

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Sopot, , Poland

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Środa Wielkopolska, , Poland

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Tychy, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Bucharest, , Romania

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Timișoara, , Romania

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Moscow, , Russia

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Novosibirsk, , Russia

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Rostov-on-Don, , Russia

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Saint Petersburg, , Russia

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Trenčín, , Slovakia

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Claremont, Western Cape, South Africa

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Seoul, , South Korea

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Suwon, , South Korea

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Basel, , Switzerland

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Bern, , Switzerland

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Taichung, , Taiwan

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Kharkiv, , Ukraine

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Kyiv, , Ukraine

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Lviv, , Ukraine

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Odesa, , Ukraine

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Vinnitsa, , Ukraine

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Cambridge, , United Kingdom

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Oxford, , United Kingdom

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Prescot, , United Kingdom

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Countries

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United States Australia Belgium Bulgaria Canada Czechia France Hungary Ireland Italy Latvia Netherlands New Zealand Poland Romania Russia Slovakia South Africa South Korea Switzerland Taiwan Ukraine United Kingdom

Other Identifiers

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2014-005217-24

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GS-US-326-1100

Identifier Type: -

Identifier Source: org_study_id

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