Subcutaneous Anifrolumab in Adult Patients With Systemic Lupus Erythematosus

NCT ID: NCT04877691

Last Updated: 2026-01-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

367 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-06-08

Study Completion Date

2026-11-06

Brief Summary

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The purpose of this study is evaluating the efficacy and safety of SC antifrolumab in adult patients with moderate -to-severe SLE despite receiving standard therapy

Detailed Description

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This is a Phase 3, multicentre, multinational, randomised, double-blind, placebo-controlled study to evaluate the efficacy and safety of a subcutaneous treatment regimen of anifrolumab versus placebo in participants with moderately to severely active, autoantibody-positive systemic lupus erythematosus (SLE) while receiving standard of care (SOC) treatment. Participants must be taking either 1 or any combination of the following: oral glucocorticoids, antimalarial, and/or immunosuppressants. The study will be performed in adult participants of 18 to 70 years of age.

Approximately 360 participants receiving SOC treatment will be randomised in a 1:1 ratio to receive a fixed subcutaneous dose of anifrolumab or placebo administered once weekly via an accessorized prefilled syringe and with the primary endpoint evaluated at Week 52. Subjects who complete Week 52 may enter into open-label extension (OLE). All patients who enter the OLE Period will receive a fixed subcutaneous dose of anifrolumab for up to 52 weeks. Study intervention will be administered SC via an accessorised prefilled syringe (aPFS).

Conditions

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Systemic Lupus Erythematosus

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

SINGLE

Participants
Double Blind (Participant, Care Provider and Investigator) and OLE

Study Groups

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Anifrolumab

Solution for injection in aPFS

Group Type EXPERIMENTAL

Medi-546

Intervention Type DRUG

Patients will have IP administered or will self-administer IP under supervision by site staff at Week 0 and Week 1 and, for patients participating in the OLE period, at Week 52. For weekly doses coinciding with subsequent on-site visits, patients will also have IP administered or will self-administer IP under supervision by site staff, and in addition will receive a set of kits (including back-up kits) for at-home administration.

Placebo

Solution for injection in aPFS

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Solution for injection in aPFS

Interventions

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Medi-546

Patients will have IP administered or will self-administer IP under supervision by site staff at Week 0 and Week 1 and, for patients participating in the OLE period, at Week 52. For weekly doses coinciding with subsequent on-site visits, patients will also have IP administered or will self-administer IP under supervision by site staff, and in addition will receive a set of kits (including back-up kits) for at-home administration.

Intervention Type DRUG

Placebo

Solution for injection in aPFS

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Patients who have a diagnosis of pediatric or adult SLE according to the ACR 1997 revised criteria for ≥ 24 weeks prior to signing the ICF
2. To be eligible a patient must have SLEDAI-2K ≥ 6 points and "Clinical" SLEDAI-2K score ≥4 points at screening
3. BILAG2004 with at least 1 of the following:

1. BILAG2004 level A disease in ≥ 1 organ system
2. BILAG2004 level B disease in ≥ 2 organ systems
4. Physician's Global Assessment (PGA) score ≥ 1.0 on a 0 to 3 VAS at Screening
5. Antinuclear antibody, and/or Anti-dsDNA and/oranti-Smith positive at Screening,
6. Must be on stable background standard therapy with DMARD, glucocorticoids or anti-malarials alone or in combinations.

Exclusion Criteria

7. Active severe or unstable neuropsychiatric SLE
8. Active severe SLE-driven renal disease
9. History of any non-SLE disease that has required treatment with oral or parenteral corticosteroids for more than a total of 2 weeks within the last 24 weeks prior to signing the ICF.
10. History of recurrent infection requiring hospitalization and IV antibiotics (eg, 3 or more of the same type of infection over the previous 52 weeks).
11. Known history of a primary immunodeficiency, splenectomy, or any underlying condition that predisposes the patient to infection, or a positive result for human immunodeficiency virus (HIV) infection confirmed by central laboratory at Screening.
12. At Screening, confirmed positive test for hepatitis B serology and positive test for hepatitis C antibody
13. Any severe case herpes zoster infection at any time prior to Week 0 (Day 1),
14. Opportunistic infection requiring hospitalization or IV antimicrobial treatment within 3 years of randomization.
15. History of cancer, apart from:

1. Squamous or basal cell carcinoma of the skin treated with documented success of curative therapy ≥ 3 months prior to Week 0 (Day 1)
2. Cervical cancer in situ treated with apparent success with curative therapy ≥ 1 year prior to Week 0 (Day 1).
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Iqvia Pty Ltd

INDUSTRY

Sponsor Role collaborator

AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Research Site

Birmingham, Alabama, United States

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Paradise Valley, Arizona, United States

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Phoenix, Arizona, United States

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El Cajon, California, United States

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Fullerton, California, United States

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Hemet, California, United States

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La Mesa, California, United States

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Los Angeles, California, United States

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Menifee, California, United States

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Upland, California, United States

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Aurora, Colorado, United States

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Brandon, Florida, United States

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Clearwater, Florida, United States

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Clearwater, Florida, United States

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Miami, Florida, United States

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Tampa, Florida, United States

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Tampa, Florida, United States

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Idaho Falls, Idaho, United States

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Flint, Michigan, United States

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Lansing, Michigan, United States

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Newark, New Jersey, United States

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Las Cruces, New Mexico, United States

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Brooklyn, New York, United States

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Manhasset, New York, United States

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New York, New York, United States

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Potsdam, New York, United States

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Charlotte, North Carolina, United States

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Charlotte, North Carolina, United States

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Oklahoma City, Oklahoma, United States

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Pittsburgh, Pennsylvania, United States

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Reading, Pennsylvania, United States

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Memphis, Tennessee, United States

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Grapevine, Texas, United States

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Ciudad de Buenos Aires, , Argentina

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La Plata, , Argentina

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Mendoza, , Argentina

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Pergamino, , Argentina

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Quilmes, , Argentina

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Rosario, , Argentina

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Salta, , Argentina

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San Isidro, , Argentina

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San Juan, , Argentina

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San Miguel de Tucumán, , Argentina

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San Miguel de Tucumán, , Argentina

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San Miguel de Tucumán, , Argentina

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Kardzhali, , Bulgaria

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Pleven, , Bulgaria

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Plovdiv, , Bulgaria

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Sevlievo, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Osorno, , Chile

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Santiago, , Chile

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Santiago, , Chile

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Santiago, , Chile

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Santiago, , Chile

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Santiago, , Chile

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Santiago, , Chile

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Valdivia, , Chile

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Barranquilla, , Colombia

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Barranquilla, , Colombia

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Bogotá, , Colombia

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Bucaramanga, , Colombia

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Chía, , Colombia

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Montería, , Colombia

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Berlin, , Germany

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Cologne, , Germany

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Leipzig, , Germany

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Tübingen, , Germany

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Budapest, , Hungary

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Budapest, , Hungary

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Gyula, , Hungary

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Székesfehérvár, , Hungary

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Veszprém, , Hungary

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Chiba, , Japan

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Chūōku, , Japan

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Hamamatsu, , Japan

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Hiroshima, , Japan

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Itabashi-ku, , Japan

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Kita-gun, , Japan

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Kitakyushu-shi, , Japan

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Meguro-ku, , Japan

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Meguro-ku, , Japan

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Nagasaki, , Japan

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Nagoya, , Japan

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Nagoya, , Japan

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Okayama, , Japan

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Sagamihara-shi, , Japan

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Sasebo-shi, , Japan

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Sendai, , Japan

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Shinjuku-ku, , Japan

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Chihuahua City, , Mexico

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Culiacán, , Mexico

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Durango, , Mexico

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Guadalajara, , Mexico

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Guadalajara, , Mexico

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Guadalajara, , Mexico

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Mexicali, , Mexico

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Mérida, , Mexico

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Mérida, , Mexico

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México, , Mexico

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México, , Mexico

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México, , Mexico

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Quezon City, , Philippines

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Katowice, , Poland

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Kościan, , Poland

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Krakow, , Poland

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Krakow, , Poland

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Krakow, , Poland

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Lodz, , Poland

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Lublin, , Poland

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Nowa Sól, , Poland

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Ustroń, , Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Wroclaw, , Poland

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Barcelona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Madrid, , Spain

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Santiago de Compostela, , Spain

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Seville, , Spain

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Valencia, , Spain

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Muang, , Thailand

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Rachathewi, , Thailand

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Odesa, , Ukraine

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Vinnytsia, , Ukraine

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Vinnytsia, , Ukraine

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Zaporizhzhia, , Ukraine

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Doncaster, , United Kingdom

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Leeds, , United Kingdom

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London, , United Kingdom

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Countries

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United States Argentina Bulgaria Chile Colombia Germany Hungary Japan Mexico Philippines Poland Spain Thailand Ukraine United Kingdom

Other Identifiers

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SZA64400

Identifier Type: -

Identifier Source: secondary_id

2020-004529-22

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

D3465C00001

Identifier Type: -

Identifier Source: org_study_id

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