Long Term Safety of Anifrolumab in Adult Subjects With Active Systemic Lupus Erythematosus

NCT ID: NCT02794285

Last Updated: 2023-01-13

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

559 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-06-30

Study Completion Date

2021-12-21

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to characterise long-term safety and tolerability of intravenous anifrolumab.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

This is a Phase 3, multicentre, multinational, randomised, double-blind, placebo-controlled extension study to characterising the long term safety and tolerability of of an intravenous treatment regimen of anifrolumab versus placebo in subjects with moderately to severely active systemic lupus erythematosus who completed a Phase 3 study (D3461C00004 or D3461C00005) through the 52-week double-blind treatment period.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Active Systemic Lupus Erythematosus

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Anifrolumab

Anifrolumab

Group Type EXPERIMENTAL

Anifrolumab

Intervention Type BIOLOGICAL

Anifrolumab IV administration every 4 weeks from Week 0 to Week 152 for a total of 39 doses

Placebo

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo IV administration every 4 weeks from Week 0 to Week 152 for a total of 39 doses

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Anifrolumab

Anifrolumab IV administration every 4 weeks from Week 0 to Week 152 for a total of 39 doses

Intervention Type BIOLOGICAL

Placebo

Placebo IV administration every 4 weeks from Week 0 to Week 152 for a total of 39 doses

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

1. Subjects who have qualified for and received investigational product (anifrolumab or placebo) and completed the treatment period in Studies D3461C00004 or D3461C00005 (through Week 52)
2. Adequate peripheral venous access
3. Females with an intact cervix should have documentation of a Pap smear with no documented malignancy within 90 days before Day 1/Visit 1 or 30 days following Day 1/Visit 1. Since access to a Pap smear may vary by country, the Sponsor recommends that local guidelines for obtaining Pap smears in subjects who have received immunomodulators or immunosuppressive treatment be followed.
4. Meets the following TB criteria:

1. Negative QuantiFERON®-TB Gold \[QFT-G\] test result for TB obtained from the study central laboratory at Week 52 of Studies D3461C00004 or D3461C00005; OR
2. Newly positive QFT-G test result at Week 52 of Studies D3461C00004 or D3461C00005 from the study central laboratory. A chest x-ray must be performed. If the chest x-ray shows no evidence of active TB, and the subject has no symptoms or medical history consistent with active TB, the subject must have a retest. If the retest is positive, the subject must start on prophylaxis within 30 days of randomisation but prior to the second dose of investigational product (Visit 2/Week 4); OR
3. Positive but not newly positive QFT-G test at Week 52 of Studies D3461C00004 or D3461C00005. The subject must have been diagnosed with latent TB and must have documentation confirming initiation of appropriate treatment OR initiate treatment for latent TB within 30 days of randomization, but prior to the second dose of investigational product administration (Visit 2/Week 4)
4. Newly indeterminate (confirmed on retest unless prior positive QFT G was documented, along with completed treatment for latent TB) or indeterminate but not newly indeterminate QFT-G test result at Week 52 of Studies D3461C00004 or D3461C00005 from the study central laboratory with ongoing QFT-G testing for TB according to the Study Plan
5. In the opinion of the Investigator, subject must be able to comprehend the ICF and all protocol related assessments

Exclusion Criteria

1. Receipt of any of the following within the last 60 days:

1. Azathioprine \>200 mg/day
2. Mycophenolate mofetil \>2.0 g/day /mycophenolic acid \>1.44 g/day
3. Oral, subcutaneous, or intramuscular methotrexate \>25 mg/week
4. Mizoribine \>150 mg/day
2. Receipt of any investigational product (small molecule or biologic agent other than anifrolumab) within 4 weeks or 5 half-lives prior to Day 1/Visit 1, whichever is greater
3. Receipt of any of the following:

1. Any live or attenuated vaccine within 8 weeks prior to Day 1/Visit 1 (administration of killed vaccines is acceptable, the Sponsor recommends Investigators ensure all subjects are up to date on required vaccinations, including influenza \[inactivated/recombinant\] vaccine prior to study entry)
2. Bacillus Calmette-Guerin (BCG) vaccine between the end of Studies D3461C00004 or D3461C00005 and Day 1/Visit 1
4. Active severe SLE-driven renal or neuropsychiatric disease
5. Any underlying condition that predisposes the subject to infection, including history of/current human immunodeficiency virus (HIV) infection
6. Subjects with Hepatitis B core antibody (HBcAb) positivity at enrolment of Studies D3461C00004 or D3461C00005 will be tested every 3 months for Hepatitis B virus (HBV) DNA. To remain eligible in the LTE study, subject HBV DNA levels must remain below the lower limit of quantitation as per the central laboratory.
7. Opportunistic infection requiring hospitalisation or parenteral antimicrobial treatment within 3 years of Day 1/Visit 1
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

PRA Health Sciences

INDUSTRY

Sponsor Role collaborator

AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Kenneth Kalunian, MD

Role: PRINCIPAL_INVESTIGATOR

University of California, San Diego

Raj Tummala, MD

Role: STUDY_DIRECTOR

AstraZeneca

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Research Site

Birmingham, Alabama, United States

Site Status

Research Site

El Cajon, California, United States

Site Status

Research Site

Hemet, California, United States

Site Status

Research Site

La Jolla, California, United States

Site Status

Research Site

Los Alamitos, California, United States

Site Status

Research Site

Los Angeles, California, United States

Site Status

Research Site

San Leandro, California, United States

Site Status

Research Site

Thousand Oaks, California, United States

Site Status

Research Site

Upland, California, United States

Site Status

Research Site

Aurora, Colorado, United States

Site Status

Research Site

Denver, Colorado, United States

Site Status

Research Site

Bridgeport, Connecticut, United States

Site Status

Research Site

Brandon, Florida, United States

Site Status

Research Site

DeBary, Florida, United States

Site Status

Research Site

Miami, Florida, United States

Site Status

Research Site

Miami, Florida, United States

Site Status

Research Site

Ormond Beach, Florida, United States

Site Status

Research Site

Tampa, Florida, United States

Site Status

Research Site

Vero Beach, Florida, United States

Site Status

Research Site

Atlanta, Georgia, United States

Site Status

Research Site

Decatur, Georgia, United States

Site Status

Research Site

Lawrenceville, Georgia, United States

Site Status

Research Site

Marietta, Georgia, United States

Site Status

Research Site

Boise, Idaho, United States

Site Status

Research Site

Idaho Falls, Idaho, United States

Site Status

Research Site

Cumberland, Maryland, United States

Site Status

Research Site

Hagerstown, Maryland, United States

Site Status

Research Site

Grand Rapids, Michigan, United States

Site Status

Research Site

Minneapolis, Minnesota, United States

Site Status

Research Site

Nashua, New Hampshire, United States

Site Status

Research Site

Freehold, New Jersey, United States

Site Status

Research Site

Las Cruces, New Mexico, United States

Site Status

Research Site

Brooklyn, New York, United States

Site Status

Research Site

Great Neck, New York, United States

Site Status

Research Site

New Hyde Park, New York, United States

Site Status

Research Site

New York, New York, United States

Site Status

Research Site

New York, New York, United States

Site Status

Research Site

New York, New York, United States

Site Status

Research Site

Charlotte, North Carolina, United States

Site Status

Research Site

Charlotte, North Carolina, United States

Site Status

Research Site

Greenville, North Carolina, United States

Site Status

Research Site

Raleigh, North Carolina, United States

Site Status

Research Site

Middleburg Heights, Ohio, United States

Site Status

Research Site

Oklahoma City, Oklahoma, United States

Site Status

Research Site

Oklahoma City, Oklahoma, United States

Site Status

Research Site

Philadelphia, Pennsylvania, United States

Site Status

Research Site

Pittsburgh, Pennsylvania, United States

Site Status

Research Site

Reading, Pennsylvania, United States

Site Status

Research Site

North Charleston, South Carolina, United States

Site Status

Research Site

Memphis, Tennessee, United States

Site Status

Research Site

Memphis, Tennessee, United States

Site Status

Research Site

Amarillo, Texas, United States

Site Status

Research Site

Austin, Texas, United States

Site Status

Research Site

Austin, Texas, United States

Site Status

Research Site

Dallas, Texas, United States

Site Status

Research Site

Houston, Texas, United States

Site Status

Research Site

Houston, Texas, United States

Site Status

Research Site

Houston, Texas, United States

Site Status

Research Site

Mesquite, Texas, United States

Site Status

Research Site

Stafford, Texas, United States

Site Status

Research Site

Spokane, Washington, United States

Site Status

Research Site

Milwaukee, Wisconsin, United States

Site Status

Research Site

Mendoza, , Argentina

Site Status

Research Site

Quilmes, , Argentina

Site Status

Research Site

San Miguel de Tucumán, , Argentina

Site Status

Research Site

Fitzroy, , Australia

Site Status

Research Site

Kogarah, , Australia

Site Status

Research Site

Plovdiv, , Bulgaria

Site Status

Research Site

Plovdiv, , Bulgaria

Site Status

Research Site

Hamilton, Ontario, Canada

Site Status

Research Site

Rimouski, Quebec, Canada

Site Status

Research Site

Osorno, , Chile

Site Status

Research Site

Santiago, , Chile

Site Status

Research Site

Viña del Mar, , Chile

Site Status

Research Site

Armenia, , Colombia

Site Status

Research Site

Barranquilla, , Colombia

Site Status

Research Site

Medellín, , Colombia

Site Status

Research Site

Bordeaux, , France

Site Status

Research Site

Lille, , France

Site Status

Research Site

Montpellier, , France

Site Status

Research Site

Paris, , France

Site Status

Research Site

Paris, , France

Site Status

Research Site

Pessac, , France

Site Status

Research Site

Berlin, , Germany

Site Status

Research Site

Frankfurt am Main, , Germany

Site Status

Research Site

Hamburg, , Germany

Site Status

Research Site

Jena, , Germany

Site Status

Research Site

Kirchheim, , Germany

Site Status

Research Site

Mainz Am Rhein, , Germany

Site Status

Research Site

Budapest, , Hungary

Site Status

Research Site

Debrecen, , Hungary

Site Status

Research Site

Szeged, , Hungary

Site Status

Research Site

Zalaegerszeg, , Hungary

Site Status

Research Site

Haifa, , Israel

Site Status

Research Site

Haifa, , Israel

Site Status

Research Site

Jerusalem, , Israel

Site Status

Research Site

Kfar Saba, , Israel

Site Status

Research Site

Tel Aviv, , Israel

Site Status

Research Site

Chiba, , Japan

Site Status

Research Site

Chūōku, , Japan

Site Status

Research Site

Fukuoka, , Japan

Site Status

Research Site

Fukuoka, , Japan

Site Status

Research Site

Hiroshima, , Japan

Site Status

Research Site

Kitakyushu-shi, , Japan

Site Status

Research Site

Kurashiki-shi, , Japan

Site Status

Research Site

Meguro-ku, , Japan

Site Status

Research Site

Meguro-ku, , Japan

Site Status

Research Site

Nagasaki, , Japan

Site Status

Research Site

Omura-shi, , Japan

Site Status

Research Site

Sapporo, , Japan

Site Status

Research Site

Sasebo-shi, , Japan

Site Status

Research Site

Sendai, , Japan

Site Status

Research Site

Shinjuku-ku, , Japan

Site Status

Research Site

Kaunas, , Lithuania

Site Status

Research Site

Klaipėda, , Lithuania

Site Status

Research Site

Chihuahua City, , Mexico

Site Status

Research Site

León, , Mexico

Site Status

Research Site

Mexico City, , Mexico

Site Status

Research Site

Mérida, , Mexico

Site Status

Research Site

México, , Mexico

Site Status

Research Site

San Luis Potosí City, , Mexico

Site Status

Research Site

Arequipa, , Peru

Site Status

Research Site

Lima, , Peru

Site Status

Research Site

Lima, , Peru

Site Status

Research Site

Lima, , Peru

Site Status

Research Site

Lima, , Peru

Site Status

Research Site

Lima, , Peru

Site Status

Research Site

Bialystok, , Poland

Site Status

Research Site

Bydgoszcz, , Poland

Site Status

Research Site

Kościan, , Poland

Site Status

Research Site

Krakow, , Poland

Site Status

Research Site

Lublin, , Poland

Site Status

Research Site

Nadarzyn, , Poland

Site Status

Research Site

Starachowice, , Poland

Site Status

Research Site

Szczecin, , Poland

Site Status

Research Site

Ustroń, , Poland

Site Status

Research Site

Warsaw, , Poland

Site Status

Research Site

Brasov, , Romania

Site Status

Research Site

Bucharest, , Romania

Site Status

Research Site

Cluj-Napoca, , Romania

Site Status

Research Site

Galati, , Romania

Site Status

Research Site

Târgu Mureş, , Romania

Site Status

Research Site

Smolensk, , Russia

Site Status

Research Site

Tolyatti, , Russia

Site Status

Research Site

Vladimir, , Russia

Site Status

Research Site

Yaroslavl, , Russia

Site Status

Research Site

Cape Town, , South Africa

Site Status

Research Site

Johannesburg, , South Africa

Site Status

Research Site

Stellenbosch, , South Africa

Site Status

Research Site

Daejeon, , South Korea

Site Status

Research Site

Gwangju, , South Korea

Site Status

Research Site

Jeju City, , South Korea

Site Status

Research Site

Seoul, , South Korea

Site Status

Research Site

Seoul, , South Korea

Site Status

Research Site

Seoul, , South Korea

Site Status

Research Site

Suwon, , South Korea

Site Status

Research Site

Barcelona, , Spain

Site Status

Research Site

Getafe, , Spain

Site Status

Research Site

Mérida, , Spain

Site Status

Research Site

Servilla, , Spain

Site Status

Research Site

Vigo, , Spain

Site Status

Research Site

Kaohsiung City, , Taiwan

Site Status

Research Site

Taichung, , Taiwan

Site Status

Research Site

Taipei, , Taiwan

Site Status

Research Site

Kyiv, , Ukraine

Site Status

Research Site

Kyiv, , Ukraine

Site Status

Research Site

Lviv, , Ukraine

Site Status

Research Site

Ternopil, , Ukraine

Site Status

Research Site

Uzhhorod, , Ukraine

Site Status

Research Site

Vinnytsia, , Ukraine

Site Status

Research Site

Zaporizhzhia, , Ukraine

Site Status

Research Site

Doncaster, , United Kingdom

Site Status

Research Site

Leeds, , United Kingdom

Site Status

Research Site

London, , United Kingdom

Site Status

Research Site

Manchester, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Argentina Australia Bulgaria Canada Chile Colombia France Germany Hungary Israel Japan Lithuania Mexico Peru Poland Romania Russia South Africa South Korea Spain Taiwan Ukraine United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Strand V, Kalunian KC, Lee KW, Seo C, Abreu G, Tummala R, Al-Mossawi H, Duncan EA, Lindholm C. Long-term effect of anifrolumab on patient-reported outcomes in systemic lupus erythematosus (TULIP-LTE): a randomised, placebo-controlled, phase 3 long-term extension trial. Lancet Rheumatol. 2025 Jul;7(7):e485-e494. doi: 10.1016/S2665-9913(25)00022-0. Epub 2025 May 2.

Reference Type DERIVED
PMID: 40324450 (View on PubMed)

Tanaka Y, Atsumi T, Okada M, Miyamura T, Ishii T, Nishiyama S, Matsumura R, Kawakami A, Hayashi N, Abreu G, Yavuz S, Lindholm C, Al-Mossawi H, Takeuchi T. The long-term safety and tolerability of anifrolumab for patients with systemic lupus erythematosus in Japan: TULIP-LTE subgroup analysis. Mod Rheumatol. 2024 Jul 6;34(4):720-731. doi: 10.1093/mr/road092.

Reference Type DERIVED
PMID: 37706527 (View on PubMed)

Kalunian KC, Furie R, Morand EF, Bruce IN, Manzi S, Tanaka Y, Winthrop K, Hupka I, Zhang LJ, Werther S, Abreu G, Hultquist M, Tummala R, Lindholm C, Al-Mossawi H. A Randomized, Placebo-Controlled Phase III Extension Trial of the Long-Term Safety and Tolerability of Anifrolumab in Active Systemic Lupus Erythematosus. Arthritis Rheumatol. 2023 Feb;75(2):253-265. doi: 10.1002/art.42392. Epub 2022 Nov 11.

Reference Type DERIVED
PMID: 36369793 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

D3461C00009

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.