Study of Efficacy and Safety of LNP023 in Participants With Active Lupus Nephritis Class III-IV, +/- V

NCT ID: NCT05268289

Last Updated: 2025-12-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

240 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-08-10

Study Completion Date

2028-09-28

Brief Summary

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The overall purpose of this two-part study is to evaluate the efficacy, safety and tolerability of iptacopan (LNP023) in addition to standard of care treatment.

Detailed Description

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The overall purpose of this two-part study is to evaluate the efficacy, safety and tolerability of iptacopan (LNP023) in addition to standard of care treatment.

Conditions

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Lupus Nephritis

Keywords

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LNP023 Iptacopan Lupus Nephritis proteinuria Urine Protein-to-Creatinine Ratio complete renal response estimated glomerular filtration rate renal flares Systemic Lupus Erythematosus

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Iptacopan + standard of care (part 1)

Iptacopan + standard of care

Group Type ACTIVE_COMPARATOR

Iptacopan (part 1)

Intervention Type DRUG

Taken for 52 Weeks

Placebo matching iptacopan + standard of care (part 1)

Placebo matching iptacopan standard of care

Group Type PLACEBO_COMPARATOR

Placebo + standard of care

Intervention Type DRUG

Taken for 52 Weeks

Iptacopan + standard of care (part 2)

Iptacopan + standard of care

Group Type ACTIVE_COMPARATOR

Iptacopan (part 2)

Intervention Type DRUG

Taken for 52 Weeks

Iptacopan + placebo (part 2)

Iptacopan + placebo standard of care

Group Type ACTIVE_COMPARATOR

Iptacopan + placebo

Intervention Type DRUG

Taken for 52 Weeks

Placebo matching iptacopan + standard of care (part 2)

Placebo matching iptacopan + standard of care

Group Type ACTIVE_COMPARATOR

Placebo + standard of care

Intervention Type DRUG

Taken for 52 Weeks

Interventions

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Iptacopan (part 1)

Taken for 52 Weeks

Intervention Type DRUG

Iptacopan (part 2)

Taken for 52 Weeks

Intervention Type DRUG

Placebo + standard of care

Taken for 52 Weeks

Intervention Type DRUG

Iptacopan + placebo

Taken for 52 Weeks

Intervention Type DRUG

Other Intervention Names

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LNP023 LNP023 LNP023 and placebo

Eligibility Criteria

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Inclusion Criteria

Unequivocally positive ANA test result and/or a positive anti dsDNA at screening Active biopsy-proven lupus nephritis within 3 months of screening demonstrating Class III or IV lupus nephritis with or without co-existing features of Class V lupus nephritis.

Documentation of active renal disease at the time of screening necessitating the commencement of therapy with corticosteroids in combination with MMF/MPS.

eGFR ≥ 30 ml/min/1.73 m2 Vaccination against Neisseria meningitidis and Streptococcus pneumoniae infections Vaccination against Haemophilus influenzae infection Supportive care including stable dose regimen of anti-malarials (e.g. hydroxychloroquine) unless contraindicated, ACEi or ARB at either locally approved maximal daily dose or the maximally tolerated dose (per investigators' judgement) at screening, as per the local clinical practice. Doses should remain stable throughout the study.

First presentation or flare of lupus nephritis.

Exclusion Criteria

Induction treatment with cyclophosphamide within 3 months of planned treatment for this study; treatment with calcineurin inhibitors within the previous 3 months prior to randomization.

Presence of rapidly progressive glomerulonephritis (RPGN) as defined by 50% decline in eGFR within 3 months prior to screening.

Renal biopsy presenting with interstitial fibrosis/tubular atrophy (IF/TA) or glomerulosclerosis of more than 50%, or which in the opinion of the investigator is such that it precludes likely response to immunosuppressive therapy.

Participants being treated with systemic corticosteroids (\>5 mg/day prednisone or equivalent) for indications other than SLE or LN e.g. acute asthma, inflammatory bowel disease.

Participants being treated with systemic corticosteroids for SLE or LN will be excluded if they have taken more than an average of 15 mg/day prednisone (or equivalent) in the previous 4 weeks and more than an average of 30 mg/day in the previous 1 week Receipt of more than a total dose of 1000 mg equivalent i.v. pulse methylprednisolone (cumulative dose) within 2 weeks prior to enrollment (and at enrollment)
Minimum Eligible Age

18 Years

Maximum Eligible Age

100 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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AKDHC Medical Research ServicesLLC

Phoenix, Arizona, United States

Site Status WITHDRAWN

Kaiser Permanente Fontana

Fontana, California, United States

Site Status WITHDRAWN

Univ Calif Irvine

Irvine, California, United States

Site Status ACTIVE_NOT_RECRUITING

Ronald Reagan UCLA Medical Center

Los Angeles, California, United States

Site Status RECRUITING

Loma Linda University

San Bernardino, California, United States

Site Status RECRUITING

Olive View UCLA Medical Center

Sylmar, California, United States

Site Status ACTIVE_NOT_RECRUITING

University of Colorado Denver

Aurora, Colorado, United States

Site Status RECRUITING

Royal Research Corp

Hollywood, Florida, United States

Site Status RECRUITING

Mayo Clinic Jacksonville

Jacksonville, Florida, United States

Site Status RECRUITING

Nephrology Associates Of Central FL

Orlando, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Florida Kidney Physicians

Riverview, Florida, United States

Site Status RECRUITING

Florida Kidney Physicians

Riverview, Florida, United States

Site Status RECRUITING

Nep Assoc of Northern Illinois

Hinsdale, Illinois, United States

Site Status ACTIVE_NOT_RECRUITING

Wichita Community Clcl Onco Program

Wichita, Kansas, United States

Site Status RECRUITING

Ochsner Health System

New Orleans, Louisiana, United States

Site Status RECRUITING

Johns Hopkins Hospital

Baltimore, Maryland, United States

Site Status ACTIVE_NOT_RECRUITING

Brigham and Womens Hosp Harvard Med School

Boston, Massachusetts, United States

Site Status RECRUITING

Mayo Clinic Rochester

Rochester, Minnesota, United States

Site Status WITHDRAWN

University of Nebraska Medical Center

Omaha, Nebraska, United States

Site Status ACTIVE_NOT_RECRUITING

Stony Brook Internists PC

East Setauket, New York, United States

Site Status RECRUITING

Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status RECRUITING

Temple University

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Allegheny Health Network

Pittsburgh, Pennsylvania, United States

Site Status ACTIVE_NOT_RECRUITING

Dallas Nephrology Associates

Dallas, Texas, United States

Site Status ACTIVE_NOT_RECRUITING

Prolato Clinical Research Center

Houston, Texas, United States

Site Status RECRUITING

Virginia Commonwealth University

Richmond, Virginia, United States

Site Status RECRUITING

Novartis Investigative Site

Rosario, Santa Fe Province, Argentina

Site Status WITHDRAWN

Novartis Investigative Site

San Luis, , Argentina

Site Status WITHDRAWN

Novartis Investigative Site

Santa Fe, , Argentina

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Salvador, Estado de Bahia, Brazil

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Belo Horizonte, Minas Gerais, Brazil

Site Status COMPLETED

Novartis Investigative Site

Juiz de Fora, Minas Gerais, Brazil

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Barretos, São Paulo, Brazil

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

São Paulo, São Paulo, Brazil

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

São Paulo, São Paulo, Brazil

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

São Paulo, São Paulo, Brazil

Site Status COMPLETED

Novartis Investigative Site

Salvador, , Brazil

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Nanning, Guangxi, China

Site Status RECRUITING

Novartis Investigative Site

Wuhan, Hubei, China

Site Status RECRUITING

Novartis Investigative Site

Shenyang, Liaoning, China

Site Status RECRUITING

Novartis Investigative Site

Yinchuan, Ningxia, China

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Beijing, , China

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Shenzhen, , China

Site Status RECRUITING

Novartis Investigative Site

Barranquilla, Atlántico, Colombia

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Bogota, Cundinamarca, Colombia

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Bucaramanga, Santander Department, Colombia

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Montería, , Colombia

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Marseille, , France

Site Status COMPLETED

Novartis Investigative Site

Nantes, , France

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Paris, , France

Site Status WITHDRAWN

Novartis Investigative Site

Strasbourg, , France

Site Status WITHDRAWN

Novartis Investigative Site

Munich, Bavaria, Germany

Site Status WITHDRAWN

Novartis Investigative Site

Ludwigshafen, Germany, Germany

Site Status WITHDRAWN

Novartis Investigative Site

Frankfurt am Main, Hesse, Germany

Site Status WITHDRAWN

Novartis Investigative Site

Braunschweig, Lower Saxony, Germany

Site Status COMPLETED

Novartis Investigative Site

Cologne, North Rhine-Westphalia, Germany

Site Status RECRUITING

Novartis Investigative Site

Berlin, , Germany

Site Status WITHDRAWN

Novartis Investigative Site

Mainz, , Germany

Site Status RECRUITING

Novartis Investigative Site

Hong Kong, Hong Kong, Hong Kong

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Debrecen, Hajdu Bihar Megye, Hungary

Site Status WITHDRAWN

Novartis Investigative Site

Budapest, , Hungary

Site Status WITHDRAWN

Novartis Investigative Site

Szeged, , Hungary

Site Status WITHDRAWN

Novartis Investigative Site

Ahmedabad, Gujarat, India

Site Status WITHDRAWN

Novartis Investigative Site

Kozhikode, Kerala, India

Site Status COMPLETED

Novartis Investigative Site

New Delhi, National Capital Territory of Delhi, India

Site Status COMPLETED

Novartis Investigative Site

Vellore, Tamil Nadu, India

Site Status WITHDRAWN

Novartis Investigative Site

Hyderabad, Telangana, India

Site Status COMPLETED

Novartis Investigative Site

Lucknow, Uttar Pradesh, India

Site Status WITHDRAWN

Novartis Investigative Site

Puducherry, , India

Site Status WITHDRAWN

Novartis Investigative Site

Ashkelon, , Israel

Site Status WITHDRAWN

Novartis Investigative Site

Jerusalem, , Israel

Site Status WITHDRAWN

Novartis Investigative Site

Ramat Gan, , Israel

Site Status WITHDRAWN

Novartis Investigative Site

Kuantan, Pahang, Malaysia

Site Status COMPLETED

Novartis Investigative Site

Taiping, Perak, Malaysia

Site Status COMPLETED

Novartis Investigative Site

Selangor Darul Ehsan, , Malaysia

Site Status COMPLETED

Novartis Investigative Site

Tampico, Tamaulipas, Mexico

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Mérida, Yucatán, Mexico

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Aguascalientes, , Mexico

Site Status COMPLETED

Novartis Investigative Site

Veracruz, , Mexico

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Makati City, National Capital Region, Philippines

Site Status COMPLETED

Novartis Investigative Site

Iloilo City, , Philippines

Site Status WITHDRAWN

Novartis Investigative Site

Quezon, , Philippines

Site Status COMPLETED

Novartis Investigative Site

Carnaxide, , Portugal

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Coimbra, , Portugal

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Lisbon, , Portugal

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Porto, , Portugal

Site Status WITHDRAWN

Novartis Investigative Site

Vila Nova de Gaia, , Portugal

Site Status RECRUITING

FDI Clinical Research

San Juan, , Puerto Rico

Site Status RECRUITING

Novartis Investigative Site

Singapore, Singapore, Singapore

Site Status WITHDRAWN

Novartis Investigative Site

Port de Sagunt, Valencia, Spain

Site Status WITHDRAWN

Novartis Investigative Site

Barcelona, , Spain

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Ciudad Real, , Spain

Site Status RECRUITING

Novartis Investigative Site

Madrid, , Spain

Site Status RECRUITING

Novartis Investigative Site

Madrid, , Spain

Site Status RECRUITING

Novartis Investigative Site

Seville, , Spain

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Ankara, Bilkent-Cankaya, Turkey (Türkiye)

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Istanbul, Fatih, Turkey (Türkiye)

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Kayseri, Melikgazi, Turkey (Türkiye)

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Bursa, Nilufer, Turkey (Türkiye)

Site Status RECRUITING

Novartis Investigative Site

Ankara, Yenimahalle, Turkey (Türkiye)

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Mersin, Yenisehir, Turkey (Türkiye)

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Cambridge, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Leicester, , United Kingdom

Site Status WITHDRAWN

Countries

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United States Argentina Brazil China Colombia France Germany Hong Kong Hungary India Israel Malaysia Mexico Philippines Portugal Puerto Rico Singapore Spain Turkey (Türkiye) United Kingdom

Central Contacts

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Novartis Pharmaceuticals

Role: CONTACT

Phone: 1-888-669-6682

Email: [email protected]

Novartis Pharmaceuticals

Role: CONTACT

Phone: +41613241111

Facility Contacts

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Rana Nikbakht Malvajerdi

Role: primary

Gema Castaneda Duenas

Role: primary

Elizabeth Wagner

Role: primary

Yalily Perez

Role: primary

Cameron King

Role: primary

Jamie Coney

Role: primary

Yvette Martinez

Role: primary

Barb Johnson

Role: primary

Gavin Skipper

Role: primary

Valentina Castro

Role: primary

Melissa Espinoza

Role: primary

Sarah Cleveland

Role: primary

Julia Aruta

Role: primary

Dilshad Begum

Role: primary

Keila Najera

Role: primary

Digmarie Rivera Franceschini

Role: primary

References

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Avasare R, Drexler Y, Caster DJ, Mitrofanova A, Jefferson JA. Management of Lupus Nephritis: New Treatments and Updated Guidelines. Kidney360. 2023 Oct 1;4(10):1503-1511. doi: 10.34067/KID.0000000000000230.

Reference Type DERIVED
PMID: 37528520 (View on PubMed)

Other Identifiers

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2021-002046-33

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CLNP023K12201

Identifier Type: -

Identifier Source: org_study_id