Subcutaneous Treatment In Randomized Subjects To Evaluate Safety And Efficacy In Generalized Lupus Erythematosus

NCT ID: NCT01405196

Last Updated: 2017-12-19

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

183 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-12-31

Study Completion Date

2014-03-31

Brief Summary

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The objective of this study is to evaluate and compare efficacy of 3 dose levels of PF-04236921 to placebo in subjects with generalized lupus using a measure called the Systemic Lupus Erythematosus (SLE) Responder Index. The study will evaluate secondary and exploratory measures as well.

Detailed Description

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Conditions

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Lupus Erythematosus, Systemic

Keywords

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double-blind placebo-controlled multicenter dose-ranging efficacy safety lupus.

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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10 mg of PF-04236921

Group Type OTHER

PF-04236921

Intervention Type BIOLOGICAL

subcutaneous injection; administered at day 1, weeks 8, 16.

50 mg of PF-04236921

Group Type OTHER

PF-04236921

Intervention Type BIOLOGICAL

subcutaneous injection; administered at day 1, weeks 8, 16.

200 mg of PF-04236921

Group Type OTHER

PF-04236921

Intervention Type BIOLOGICAL

subcutaneous injection; administered at day 1, weeks 8, 16.

Placebo

Group Type OTHER

PF-04236921

Intervention Type BIOLOGICAL

subcutaneous injection; administered at day 1, weeks 8, 16

Interventions

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PF-04236921

subcutaneous injection; administered at day 1, weeks 8, 16.

Intervention Type BIOLOGICAL

PF-04236921

subcutaneous injection; administered at day 1, weeks 8, 16.

Intervention Type BIOLOGICAL

PF-04236921

subcutaneous injection; administered at day 1, weeks 8, 16.

Intervention Type BIOLOGICAL

PF-04236921

subcutaneous injection; administered at day 1, weeks 8, 16

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

* Male or female subjects between ages of 18 and 75 years old at time of signing consent.
* Have a clinical diagnosis of SLE according to 1997 update on the revised 1982 American College of Rheumatology (ACR) criteria.
* Have a unequivocally positive anti-nuclear antibody (ANA) test result.
* Active disease at screening defined by both: SLEDAI-2K score greater than or equal to 6 and BILAG Level A disease in more than or equal to 1 organ system (except renal or central nervous system) or BILAG B disease in more than or equal to 2 organ systems if no level A disease in present.

Exclusion Criteria

* Any prior history of treatment with PF-04236921, or anti-IL-6 agent;
* Have received any of the following within 364 days of day 1: a biologic investigational agent other than B cell targeted therapy; required 3 or more courses of systemic corticosteroids for concomitant conditions; history of previously untreated or current evidence of active or untreated latent infection with Tuberculosis (TB), evidence of prior untreated or currently active TB by chest radiography, residing with or frequent close contact with an individual with active TB.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Anniston Medical Clinic, PC

Anniston, Alabama, United States

Site Status

Pinnacle Research Group, LLC

Anniston, Alabama, United States

Site Status

Achieve Clinical Research, LLC

Birmingham, Alabama, United States

Site Status

Med Investigations, Inc.

Fair Oaks, California, United States

Site Status

Premier Clinical Research, LLC

Lakewood, California, United States

Site Status

Novo Research

Long Beach, California, United States

Site Status

St Mary Medical Center

Long Beach, California, United States

Site Status

Cedars-Sinai Medical Center

Los Angeles, California, United States

Site Status

Wallace Rheumatic Study Center

Los Angeles, California, United States

Site Status

UCLA Division of Rheumatology

Los Angeles, California, United States

Site Status

UCLA Rheumatology Clinical Research Center

Los Angeles, California, United States

Site Status

Ronald Reagan UCLA Medical Center

Los Angeles, California, United States

Site Status

UCLA Medical Center

Los Angeles, California, United States

Site Status

Inland Rheumatology and Osteoporosis Medical Group

Upland, California, United States

Site Status

Inland Rheumatology Clinical Trials, Inc.

Upland, California, United States

Site Status

Asthma, Allergy, Arthritis and Lung Center

Daytona Beach, Florida, United States

Site Status

Southeastern Arthritis Center

Gainesville, Florida, United States

Site Status

Southeastern Community Pharmacy

Gainesville, Florida, United States

Site Status

Southeastern Integrated Medical, PL, d/b/a Florida Medical Research Institute

Gainesville, Florida, United States

Site Status

Southeastern lmaging & Diagnostics

Gainesville, Florida, United States

Site Status

New Horizon Research Center

Miami, Florida, United States

Site Status

Arthritis Associates

Orlando, Florida, United States

Site Status

Millennium Research

Ormond Beach, Florida, United States

Site Status

The Arthritis Center

Palm Harbor, Florida, United States

Site Status

Advent Clinical Research Centers, Inc.

Pinellas Park, Florida, United States

Site Status

Burnette & Silverfield, MDS PLC

Tampa, Florida, United States

Site Status

Emory University

Atlanta, Georgia, United States

Site Status

Grady Health Systems

Atlanta, Georgia, United States

Site Status

Idaho Arthritis Center

Meridian, Idaho, United States

Site Status

University of Chicago Medical Center

Chicago, Illinois, United States

Site Status

Beacon Medical Group Rheumatology

Granger, Indiana, United States

Site Status

Indiana CTSI Clinical Research Center

Indianapolis, Indiana, United States

Site Status

Investigational Drug Services

Indianapolis, Indiana, United States

Site Status

Johns Hopkins University School of Medicine

Baltimore, Maryland, United States

Site Status

Johns Hopkins Outpatient Center

Baltimore, Maryland, United States

Site Status

Johns Hopkins Outpatient Express Testing Center

Baltimore, Maryland, United States

Site Status

Tufts Medical Center/ Center for Arthritis and Rheumatic Diseases

Boston, Massachusetts, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

University of Michigan Health System

Ann Arbor, Michigan, United States

Site Status

University of Michigan Health System,

Ann Arbor, Michigan, United States

Site Status

Henry Ford Health System (Henry Ford Medical Center)

Detroit, Michigan, United States

Site Status

Shores Rheumatology P.C

Saint Clair Shores, Michigan, United States

Site Status

University of Nevada School of Medicine

Las Vegas, Nevada, United States

Site Status

Albuquerque Clinical Trials

Albuquerque, New Mexico, United States

Site Status

Arthritis and Osteoporosis Medical Associates, PLLC

Brooklyn, New York, United States

Site Status

Feinstein Institute for Medical Research

Manhasset, New York, United States

Site Status

NYU Center for Musculoskeletal Care

New York, New York, United States

Site Status

Allergy/Immunology and Rheumatology

Rochester, New York, United States

Site Status

The University of North Carolina Clinical and Translational Research Center

Chapel Hill, North Carolina, United States

Site Status

The University of North Carolina Hospitals Investigational Drug Services

Chapel Hill, North Carolina, United States

Site Status

The University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Site Status

Joint and Muscle Medical Care

Charlotte, North Carolina, United States

Site Status

Box Arthritis & Rheumatology of the Carolinas, PLLC

Charlotte, North Carolina, United States

Site Status

Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

Paramount Medical Research and Consulting, LLC

Middleburg Heights, Ohio, United States

Site Status

Oklahoma Medical Research Foundation

Oklahoma City, Oklahoma, United States

Site Status

Clinical Research Center of Reading, LLP

Wyomissing, Pennsylvania, United States

Site Status

Low Country Rheumatology, PA/Low Country Research

Charleston, South Carolina, United States

Site Status

Arthritis Clinic

Jackson, Tennessee, United States

Site Status

West Tennessee Research Institute

Jackson, Tennessee, United States

Site Status

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status

Rheumatic Disease Clinical Research Center, LLC

Houston, Texas, United States

Site Status

Accurate Clinical Research, Inc.

Houston, Texas, United States

Site Status

Southwest Rheumatology Research, LLC

Mesquite, Texas, United States

Site Status

The Seattle Arthritis Clinic

Seattle, Washington, United States

Site Status

Tacoma Center for Arthritis Research, PS

Tacoma, Washington, United States

Site Status

Mountain State Clinical Research

Clarksburg, West Virginia, United States

Site Status

Framingham Centro Medico

La Plata, Buenos Aires, Argentina

Site Status

Instituto CAICI S.R.L.

Rosario, Santa Fe Province, Argentina

Site Status

Centro Medico Privado de Reumatologia

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status

Centro de Educación Medica e Investigaciones Clinicas "Norberto Quirno" CEMIC

C.a.b.a, , Argentina

Site Status

Centro Polivalente de Asistencia e Investigación Clínica - CER- San Juan

San Juan, , Argentina

Site Status

Centro de Estudios Reumatologicos

Santiago, RM, Chile

Site Status

Centro Medico Prosalud

Santiago, RM, Chile

Site Status

Sociedad Medica del Aparato Locomotor S.A. (SOMEAL)

Santiago, Santiago Metropolitan, Chile

Site Status

Centro Integral de Reumatologia REUMALAB S.A.S.

Envigado, Antioquia, Colombia

Site Status

Hospital Pablo Tobon Uribe

Medellín, Antioquia, Colombia

Site Status

Mix Supplier S.A.

Envigado, Antioquia, Colombia, Colombia

Site Status

Centro Integral de Reumatología del Caribe CIRCARIBE SAS

Barranquilla, Atlántico, Colombia

Site Status

Congregacion de Hermanas Franciscanas Misioneras de Maria Auxiliadora- Clinica Asunción

Barranquilla, Atlántico, Colombia

Site Status

Organizacion Clinica General del Norte S.A.

Barranquilla, Atlántico, Colombia

Site Status

Farmamix Ltda.

Bogota, Distrito Capital, Cundimarca, Colombia

Site Status

Centro Integral de Reumatologia e Inmunologia S.A.S.- CIREI S.A.S.

Bogota, Cundinamarca, Colombia

Site Status

Riesgo De Fractura S.A

Bogota, Cundinamarca, Colombia

Site Status

Servimed E.U

Bucaramanga, Santander Department, Colombia

Site Status

Farmamix Ltda.

Bogotá, , Colombia

Site Status

Charité - Universitaetsmedizin Berlin

Berlin, , Germany

Site Status

Charité University Medicine Berlin. Schlosspark-Klinik

Berlin, , Germany

Site Status

Universitaetsklinikum Koeln

Cologne, , Germany

Site Status

Universitaetsklinikum Erlangen

Erlangen, , Germany

Site Status

CIRI am Klinikum der Goethe-Universitaet

Frankfurt am Main, , Germany

Site Status

Universitaetsklinikum Leipzig AoeR, Department fuer Innere Medizin

Leipzig, , Germany

Site Status

Qualiclinic Kft.

Budapest, , Hungary

Site Status

Debreceni Egyetem Orvos és Egeszsegtudomanyi Centrum

Debrecen, , Hungary

Site Status

Bekes Megyei Kepviselo-testulet Pandy Kalman Korhaz Infektologia, Hepatologia es Immunologia

Gyula, , Hungary

Site Status

Spitalul Clinic Republican

Chisinau, Md-2025, Moldova

Site Status

Centro de Investigacion REUMED, Clinica Anglo Americana

San Isidro, Lima region, Peru

Site Status

Investigaciones Clínicas SAC

Santiago de Surco, Lima region, Peru

Site Status

Investigaciones Clinicas SAC

Surco, Lima region, Peru

Site Status

Unidad de Investigación en Medicina Interna y Enfermedades Críticas

Arequipa, , Peru

Site Status

NZOZ Centrum Reumatologiczne Indywidualna Specjalistyczna Praktyka Lekarska lek.med. Barbara Bazela

Elblag, , Poland

Site Status

Medyczne Centrum Hetmanska - Indywidualna Specjalistyczna Praktyka Lekarska -

Poznan, , Poland

Site Status

Prywatna Praktyka Lekarska Prof. UM Dr hab. med. Pawel Hrycaj

Poznan, , Poland

Site Status

Centralny Szpital Kliniczny Ministerstwa Spraw Wewnetrznych

Warsaw, , Poland

Site Status

University of Puerto Rico

Rio Piedras, , Puerto Rico

Site Status

Division of Rheumatology, Allergy and Immunology

San Juan, , Puerto Rico

Site Status

Spitalul Clinic Sf. Maria

Bucharest, , Romania

Site Status

Spitalul Clinic Colentina

Bucharest, , Romania

Site Status

Spitalul Clinic Jedetean de urgenta Cluj, Reumatologie

Cluj-Napoca, , Romania

Site Status

Spitalul Clinic Judetean de Urgenta "Sf. Apostol Andrei"

Galati, , Romania

Site Status

Dong-A University Medical Center 1

Busan, , South Korea

Site Status

National Taiwan University Hospital

Taipei TOC, , Taiwan

Site Status

Countries

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Mexico United States Argentina Chile Colombia Germany Hungary Moldova Peru Poland Puerto Rico Romania South Korea Taiwan

References

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Li C, Shoji S, Beebe J. Pharmacokinetics and C-reactive protein modelling of anti-interleukin-6 antibody (PF-04236921) in healthy volunteers and patients with autoimmune disease. Br J Clin Pharmacol. 2018 Sep;84(9):2059-2074. doi: 10.1111/bcp.13641. Epub 2018 Jun 25.

Reference Type DERIVED
PMID: 29776017 (View on PubMed)

Wallace DJ, Strand V, Merrill JT, Popa S, Spindler AJ, Eimon A, Petri M, Smolen JS, Wajdula J, Christensen J, Li C, Diehl A, Vincent MS, Beebe J, Healey P, Sridharan S. Efficacy and safety of an interleukin 6 monoclonal antibody for the treatment of systemic lupus erythematosus: a phase II dose-ranging randomised controlled trial. Ann Rheum Dis. 2017 Mar;76(3):534-542. doi: 10.1136/annrheumdis-2016-209668. Epub 2016 Sep 26.

Reference Type DERIVED
PMID: 27672124 (View on PubMed)

Related Links

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Other Identifiers

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2011-000420-15

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

BUTTERFLY

Identifier Type: OTHER

Identifier Source: secondary_id

B0151006

Identifier Type: -

Identifier Source: org_study_id