Phase 3 Study to Evaluate Two Regimens of Ianalumab on Top of Standard-of-care Therapy in Patients With Systemic Lupus Erythematosus (SIRIUS-SLE 1)

NCT ID: NCT05639114

Last Updated: 2026-02-04

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

436 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-03-02

Study Completion Date

2029-04-20

Brief Summary

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The trial will evaluate efficacy, safety and tolerability of two regimens of ianalumab compared to placebo, given as monthly or quarterly subcutaneous (s.c.) injection on top of standard-of-care (SoC) treatment in participants with active systemic lupus erythematosus (SLE).

Detailed Description

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A randomized, double-blind, parallel group, placebo-controlled multicenter phase 3 study to evaluate efficacy, safety and tolerability of two regimens of ianalumab on top of standard-of-care therapy in patients with systemic lupus erythematosus (SIRIUS-SLE 1)

Conditions

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Systemic Lupus Erythematosus

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

The trial is designed to evaluate efficacy, safety and tolerability of two regimens of ianalumab compared to placebo, given as monthly or quarterly subcutaneous (s.c.) injection on top of standard-of-care (SoC) treatment in participants with active systemic lupus erythematosus (SLE).
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Ianalumab s.c. monthly

Ianalumab s.c. monthly

Group Type EXPERIMENTAL

Ianalumab

Intervention Type DRUG

ianalumab s.c. monthly or quarterly

Ianalumab s.c. quarterly

Ianalumab s.c. quarterly

Group Type EXPERIMENTAL

Ianalumab

Intervention Type DRUG

ianalumab s.c. monthly or quarterly

Placebo s.c. monthly

placebo s.c. monthly

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

placebo s.c. monthly

Interventions

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Ianalumab

ianalumab s.c. monthly or quarterly

Intervention Type DRUG

Placebo

placebo s.c. monthly

Intervention Type DRUG

Other Intervention Names

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VAY736

Eligibility Criteria

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Inclusion Criteria

* Male and female participants aged 12 years or older at the time of screening, or limited to 18 years or older in European Economic Area countries and other countries where inclusion of participants below 18 years is not allowed.
* Diagnosis of systemic lupus erythematosus meeting the 2019 European League Against Rheumatism/American College of Rheumatology (EULAR/ACR) SLE classification criteria at least 6 months prior to screening.
* Elevated serum titers at screening of anti-nuclear antibodies ≥ 1:80 as determined by a central laboratory with a SLE-typical fluorescence pattern.
* Currently receiving CS and/or anti-malarial treatment and/or another disease-modifying antirheumatic drug (DMARD) as specified in the protocol.
* SLEDAI-2K criteria at screening: SLEDAI-2K score ≥ 6 points, excluding points attributed to "fever", "lupus headache", "alopecia", and "organic brain syndrome"
* BILAG-2004 disease activity level at screening of at least 1 of the following:

* BILAG-2004 level 'A' disease in ≥ 1 organ system, Or
* BILAG-2004 level 'B' disease in ≥ 2 organ systems
* Weigh at least 35 kg at screening

* Active viral, bacterial or other infections requiring intravenous or intramuscular treatment for clinically significant infection
* Chronic infection with hepatitis B virus (HBV) or hepatitis C virus (HCV)
* Evidence of active tuberculosis infection
* History of primary or secondary immunodeficiency, including a positive human immunodeficiency virus (HIV) test result at screening
* Any one of the following abnormal laboratory values prior to randomization

* Platelets \< 25000/mm\^3 (\< 25 x 10\^3/μL)
* Hemoglobin (Hgb) \< 8.0 g/dL (\< 5 mmol/L), or \< 7.0 g/dL (\< 4.3 mmol/L) if related to participant's SLE such as in active hemolytic anaemia
* Absolute neutrophil count (ANC) (\< 0.8 x 10\^3/ μL)
* Severe organ dysfunction or life-threatening disease at screening
* Presence of severe lupus kidney disease as defined by proteinuria above 2 g/day or equivalent using spot urine protein creatinine ratio, or serum creatinine greater than 2.0 mg/dL (176.84 µmol/L), or requiring immune-suppressive induction or maintenance treatment at screening
* Receipt of live/attenuated vaccine within a 4-week period before first dosing
* Any uncontrolled, co-existing serious disease, which in the opinion of the investigator will place the participant at risk for participation or interfere with evaluation for SLE-related symptoms
* Non-lupus conditions such as asthma, gout or urticaria, requiring intermittent or chronic treatment with systemic CS
* History of malignancy of any organ system other than localized basal cell carcinoma of the skin or in situ cervical cancer
* Pregnant or nursing (lactating) women.
* Women of child-bearing potential (WOCBP), defined as all women physiologically capable of becoming pregnant, unless they are using highly effective methods of contraception while on study treatment and for 6 months after stopping of investigational drug.
* Any surgical, medical, psychiatric or additional physical condition that may jeopardize participation in this study

Exclusion Criteria

* Prior treatment with ianalumab
Minimum Eligible Age

12 Years

Maximum Eligible Age

100 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Pinnacle Research Group Llc

Anniston, Alabama, United States

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Providence Medical Center

Burbank, California, United States

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University of California San Diego

La Jolla, California, United States

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Keck School of Medicine

Los Angeles, California, United States

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Millennium Clinical Trials

Westlake Village, California, United States

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University of Colorado

Aurora, Colorado, United States

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Yale University School Of Medicine

New Haven, Connecticut, United States

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Clinical Res Of W Florida

Clearwater, Florida, United States

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GNP Research

Cooper City, Florida, United States

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University Of Miami

Miami, Florida, United States

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Clinical Research of West Florida Inc

Tampa, Florida, United States

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Parris and Associates Rheumatology

Lawrenceville, Georgia, United States

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Chicago Clinical Research Inst

Chicago, Illinois, United States

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Robert A Hozman MD SC

Skokie, Illinois, United States

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Lake Cumberland Rheumatology and In

New Albany, Indiana, United States

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Ochsner Clinic Foundation

Baton Rouge, Louisiana, United States

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Henry Ford Health

Detroit, Michigan, United States

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Univ of Nevada School of Med

Las Vegas, Nevada, United States

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Sahni Rheumatology and Therapy

West Long Branch, New Jersey, United States

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NYU Langone Health

Brooklyn, New York, United States

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Paramount Med Rsrch and Consult LLC

Middleburg Heights, Ohio, United States

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University Of Pittsburgh

Pittsburgh, Pennsylvania, United States

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Prisma Health

Columbia, South Carolina, United States

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Shelby Research LLC

Memphis, Tennessee, United States

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Accurate Clinical Research Research

Baytown, Texas, United States

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Novel Research LLC

Bellaire, Texas, United States

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Texas Arthritis Center

El Paso, Texas, United States

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Accurate Clinical Research

League City, Texas, United States

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Epic Medical Research

Red Oak, Texas, United States

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Novartis Investigative Site

San Miguel, Tucumán Province, Argentina

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San Miguel de Tucumán, , Argentina

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Fortaleza, Ceará, Brazil

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Vitória, Espírito Santo, Brazil

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Salvador, Estado de Bahia, Brazil

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Salvador, Estado de Bahia, Brazil

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Belo Horizonte, Minas Gerais, Brazil

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Curitiba, Paraná, Brazil

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Recife, Pernambuco, Brazil

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Niterói, Rio de Janeiro, Brazil

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Rio de Janeiro, Rio de Janeiro, Brazil

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Barretos, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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Salvador, , Brazil

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Plovdiv, , Bulgaria

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Rousse, , Bulgaria

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Sofia, , Bulgaria

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Calgary, Alberta, Canada

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Vancouver, British Columbia, Canada

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Hamilton, Ontario, Canada

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Toronto, Ontario, Canada

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Rimouski, Quebec, Canada

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Guangzhou, Guangdong, China

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Guangzhou, Guangdong, China

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Shantou, Guangdong, China

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Haikou, Hainan, China

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Zhuzhou, Hunan, China

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Nanjing, Jiangsu, China

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Suzhou, Jiangsu, China

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Nanchang, Jiangxi, China

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Pingxiang, Jiangxi, China

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Changchun, Jilin, China

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Linyi, Shandong, China

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Chengdu, Sichuan, China

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Ürümqi, Xinjiang, China

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Ningbo, Zhejiang, China

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Wenzhou, Zhejiang, China

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Beijing, , China

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Beijing, , China

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Shanghai, , China

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Xinxiang, , China

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Barranquilla, Atlántico, Colombia

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Bucaramanga, Santander Department, Colombia

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Cali, Valle del Cauca Department, Colombia

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Brno, , Czechia

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Prague, , Czechia

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Uherské Hradiště, , Czechia

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Guatemala City, , Guatemala

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Guatemala City, , Guatemala

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Székesfehérvár, Fejér, Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Gyula, , Hungary

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Zalaegerszeg, , Hungary

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Haifa, , Israel

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Ramat Gan, , Israel

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Nagoya, Aichi-ken, Japan

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Nagoya, Aichi-ken, Japan

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Sapporo, Hokkaido, Japan

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Yokohama, Kanagawa, Japan

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Yokohama, Kanagawa-ku, Japan

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Sendai, Miyagi, Japan

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Bunkyo Ku, Tokyo, Japan

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Bunkyo Ku, Tokyo, Japan

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Bunkyo-ku, Tokyo, Japan

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Chuo Ku, Tokyo, Japan

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Fuchū, Tokyo, Japan

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Itabashi-ku, Tokyo, Japan

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Meguro City, Tokyo, Japan

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Shinjuku-ku, Tokyo, Japan

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Fukuoka, , Japan

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Miyazaki, , Japan

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Osaka, , Japan

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Wroclaw, Lower Silesian Voivodeship, Poland

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Bydgoszcz, , Poland

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Bydgoszcz, , Poland

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Bytom, , Poland

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Lodz, , Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Braga, , Portugal

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Lisbon, , Portugal

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Lisbon, , Portugal

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Lisbon, , Portugal

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Vila Nova de Gaia, , Portugal

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Bratislava, , Slovakia

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Košice, , Slovakia

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Košice, , Slovakia

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Pretoria, Gauteng, South Africa

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Cape Town, Western Cape, South Africa

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Cape Town, Western Cape, South Africa

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Stellenbosch, Western Cape, South Africa

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Umhlanga, , South Africa

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Santiago Compostela, A Coruna, Spain

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Elche, Alicante, Spain

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Badalona, Barcelona, Spain

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Santander, Cantabria, Spain

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Barcelona, Catalonia, Spain

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San Sebastian Reyes, Madrid, Spain

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Pamplona, Navarre, Spain

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Vigo, Pontevedra, Spain

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San Cristóbal de La Laguna, Santa Cruz De Tenerife, Spain

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Barcelona, , Spain

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Madrid, , Spain

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Valencia, , Spain

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Valladolid, , Spain

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Songkhla, Hat Yai, Thailand

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Muang, Thailand, Thailand

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Bangkok, , Thailand

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Bangkok, , Thailand

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Ankara, Bilkent Cankaya, Turkey (Türkiye)

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Ankara, Etlik, Turkey (Türkiye)

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Istanbul, Fatih, Turkey (Türkiye)

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Istanbul, Umraniye, Turkey (Türkiye)

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Countries

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United States Argentina Brazil Bulgaria Canada China Colombia Czechia Guatemala Hungary Israel Japan Poland Portugal Slovakia South Africa Spain Thailand Turkey (Türkiye)

Other Identifiers

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2022-002691-36

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2023-508498-97-00

Identifier Type: OTHER

Identifier Source: secondary_id

CVAY736F12301

Identifier Type: -

Identifier Source: org_study_id

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