A Study to Learn About the Safety of Litifilimab (BIIB059) Injections and Whether They Can Improve Symptoms of Adult Participants Who Have Systemic Lupus Erythematosus

NCT ID: NCT04961567

Last Updated: 2026-01-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

562 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-07-16

Study Completion Date

2027-03-16

Brief Summary

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In this study, researchers will learn more about a study drug called litifilimab (BIIB059) in participants with systemic lupus erythematosus (SLE). The study will focus on participants who have active disease and are already taking standard of care medications. These may include antimalarials, steroids, and immunosuppressants.

The main objective of the study is to learn about the effect litifilimab has on lowering the activity of the disease. The main question researchers want to answer is:

\- How many participants have an improvement in their symptoms after 52 weeks of treatment? Researchers will answer this and other questions by measuring the symptoms of SLE over time using a variety of scoring tools. These include the SLE Responder Index (SRI), the Systemic Lupus Erythematosus Disease Activity Index-2000 (SLEDAI-2K), the British Isles Lupus Activity Group-2004 index (BILAG-2004), and the BILAG-BASED Combined Lupus Assessment (BICLA), among others.

Researchers will also learn more about the safety of litifilimab. They will study how participants' immune systems respond to litifilimab. Additionally, they will measure the effect litifilimab and SLE have on the quality of life of participants using a group of questionnaires.

The study will be done as follows:

* After screening, participants will be randomized to receive either a high or low dose of litifilimab, or placebo. A placebo looks like the study drug but contains no real medicine.
* All participants will receive either litifilimab or placebo as injections under the skin once every 4 weeks. The treatment period will last 52 weeks. Participants will continue to take their standard of care medications.
* Neither the researchers nor the participants will know if the participants are receiving litifilimab or placebo.
* There will be a follow-up safety period that lasts up to 24 weeks.
* In total, participants will have up to 22 study visits. The total study duration for participants will be up to 80 weeks.

Detailed Description

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The primary objective of the study is to demonstrate efficacy of litifilimab compared with placebo in participants with active SLE, who are receiving background lupus standard of care (SOC) therapy in reducing disease activity.

The secondary objectives of this study are to demonstrate efficacy of litifilimab compared with placebo in participants with active SLE, who are receiving background lupus SOC therapy in reducing disease activity and occurrence of flare up to Week 52; to demonstrate organ-specific efficacy of litifilimab compared with placebo in participants with active SLE, who are receiving background lupus SOC therapy in reducing joint disease activity and skin disease activity; to demonstrate and evaluate effect of litifilimab compared with placebo in reducing oral corticosteroid(s) (OCS) use; to evaluate additional efficacy of litifilimab compared with placebo in reducing disease activity with additional disease activity measures; assess the difference between litifilimab and placebo on participant reported health-related quality of life (HRQoL), symptoms, and impacts of SLE; to evaluate the safety, tolerability and immunogeneicty of litifilimab in participants with active SLE.

Conditions

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Lupus Erythematosus, Systemic

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Litifilimab High Dose

Participants who are receiving background nonbiologic lupus SOC therapy will receive high dose of litifilimab, subcutaneously (SC), every 4 weeks (Q4W), up to Week 48 with an additional dose at Week 2.

Group Type EXPERIMENTAL

Litifilimab

Intervention Type DRUG

Administered as specified in the treatment arm.

Litifilimab Low Dose

Participants who are receiving background nonbiologic lupus SOC therapy will receive low dose of litifilimab, SC Q4W, up to Week 48 with an additional dose at Week 2.

Group Type EXPERIMENTAL

Litifilimab

Intervention Type DRUG

Administered as specified in the treatment arm.

Placebo

Participants who are receiving background nonbiologic lupus SOC therapy will receive litifilimab-matching placebo, SC Q4W, up to Week 48 with an additional dose at Week 2.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Administered as specified in the treatment arm.

Interventions

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Litifilimab

Administered as specified in the treatment arm.

Intervention Type DRUG

Placebo

Administered as specified in the treatment arm.

Intervention Type DRUG

Other Intervention Names

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BIIB059

Eligibility Criteria

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Inclusion Criteria

* Participant must be diagnosed with SLE at least 24 weeks prior to screening and must meet the 2019 European League Against Rheumatism (EULAR)/American College of Rheumatology (ACR) classification criteria for SLE, at screening by a qualified physician.
* Participant has a modified Systemic Lupus Erythematosus Disease Activity Index-200 (SLEDAI-2K) score ≥6 (excluding alopecia, fever, lupus-related headache, and organic brain syndrome) at screening (adjudicated).
* Participant has a modified clinical SLEDAI-2K score ≥4 (excluding anti-dsDNA, low complement component 3 \[C3\] and/or complement component 4 \[C4\], alopecia, fever, lupus-related headache, and organic brain syndrome) at screening (adjudicated) and randomization.
* Participant has BILAG-2004 grade A in ≥1 organ system or BILAG-2004 grade B in ≥2 organ systems at screening (adjudicated) and randomization.
* Participants must be treated with one of the following background nonbiologic lupus SOC therapies, initiated ≥12 weeks prior to screening and at stable dose ≥4 weeks prior to randomization:

1. Antimalarials as stand-alone treatment
2. Antimalarial treatment in combination with OCS and/or a single immunosuppressant
3. Treatment with OCS and/or a single immunosuppressant.

Exclusion Criteria

* History of or positive test result for human immunodeficiency virus (HIV).
* Current hepatitis C infection (defined as positive hepatitis C virus \[HCV\] antibody and detectable HCV ribonucleic acid \[RNA\]).
* Current hepatitis B infection (defined as positive for antibody to hepatitis B surface antigen \[HBsAg\] and/or positive for total antibody to hepatitis B core antigen \[anti-HBc\] with positive reflex HBV DNA).
* History of severe herpes infection.
* Presence of uncontrolled or New York Heart Association class III or IV congestive heart failure.
* Active severe lupus nephritis where, in the opinion of the investigator, protocol-specified SOC is insufficient and use of a more aggressive therapeutic approach, such as adding intravenous (IV) cyclophosphamide and/or high-dose IV pulse corticosteroid therapy or other treatments not permitted in the protocol, is indicated; or urine protein-creatinine ratio \>2.0 or severe chronic kidney disease (estimated glomerular filtration rate \<30 milliliters per minute per 1.73 meter square \[mL/min/1.73 m\^2\]) calculated using the abbreviated Modification of Diet in Renal Disease equation.
* Any active skin conditions other than cutaneous lupus erythematosus (CLE) that may interfere with the study assessment of CLE such as but not limited to psoriasis, dermatomyositis, systemic sclerosis, non-LE skin lupus manifestation or drug-induced lupus.
* History or current diagnosis of a clinically significant non-SLE-related vasculitis syndrome.
* Active neuropsychiatric SLE.
* Use of oral prednisone (or equivalent) above 20 mg/day.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Biogen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Biogen

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Arizona Arthritis & Rheumatology Associates, P.C.

Glendale, Arizona, United States

Site Status

Care Access Research - Huntington BeachCare Access Research - Huntington Beach

Huntington Beach, California, United States

Site Status

Valerius Medical Group

Los Alamitos, California, United States

Site Status

The Practice of Medicine

Los Angeles, California, United States

Site Status

R. Srinivasan, M.D., Inc. dba Monterey Park Medical Center

Monterey Park, California, United States

Site Status

Neurovations

Napa, California, United States

Site Status

Joo-Hyung Lee MD

Orange, California, United States

Site Status

Medvin Clinical Research

Whittier, California, United States

Site Status

RASF - Clinical Research Center

Boca Raton, Florida, United States

Site Status

University of Florida

Gainesville, Florida, United States

Site Status

Vida Clinical Research

Kissimmee, Florida, United States

Site Status

University of Miami Miller School of Medicine

Miami, Florida, United States

Site Status

HMD Research, LLC

Orlando, Florida, United States

Site Status

Clinical Research of West Florida, Inc.

Tampa, Florida, United States

Site Status

The Emory Clinic Emory University

Atlanta, Georgia, United States

Site Status

Jefrey Lieberman, M.D., P.C.

Decatur, Georgia, United States

Site Status

Southeastern Rheumatology Alliance dba Arthritis Center of North Georgia

Gainesville, Georgia, United States

Site Status

RNA America Health Sciences

Gainesville, Georgia, United States

Site Status

EBGS Clinical Trials

Snellville, Georgia, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

Boston University School of Medicine

Boston, Massachusetts, United States

Site Status

DM Clinical Research - Boston

Brookline, Massachusetts, United States

Site Status

University of Massachusetts

Worcester, Massachusetts, United States

Site Status

Saint Louis Rheumatology

St Louis, Missouri, United States

Site Status

Arthritis & Osteoporosis Associates, PA

Freehold, New Jersey, United States

Site Status

Arthritis and Osteoporosis Associates of New Mexico

Las Cruces, New Mexico, United States

Site Status

DJL Clinical Research, PLLC

Charlotte, North Carolina, United States

Site Status

Carolina Arthritis Associates

Wilmington, North Carolina, United States

Site Status

University of Cincinnati

Cincinnati, Ohio, United States

Site Status

STAT Research

Dayton, Ohio, United States

Site Status

Piedmont Arthritis Clinic, P.A.

Greenville, South Carolina, United States

Site Status

Low Country Rheumatology, PA

Summerville, South Carolina, United States

Site Status

West Tennessee Research Institute

Jackson, Tennessee, United States

Site Status

Arthritis & Rheumatology Institute

Allen, Texas, United States

Site Status

Office of John P. Lavery M.D., PA

Allen, Texas, United States

Site Status

Tekton Research

Austin, Texas, United States

Site Status

Precision Comprehensive Clinical Research Solutions

Colleyville, Texas, United States

Site Status

R and H Clinical Research

Katy, Texas, United States

Site Status

Prime Clinical Research

Mansfield, Texas, United States

Site Status

SouthWest Rheumatology Research, LLC

Mesquite, Texas, United States

Site Status

Sun Research Institute, LLC

San Antonio, Texas, United States

Site Status

The University of Texas Health Science Center at San Antonio

San Antonio, Texas, United States

Site Status

Swedish Medical Center

Seattle, Washington, United States

Site Status

Instituto de Investigaciones Clinicas Quilmes

Buenos Aires, Buenos Aires, Argentina

Site Status

Hospital Italiano de La Plata

Buenos Aires, Buenos Aires, Argentina

Site Status

Hospital General de Agudos Dr. J. M. Ramos Mejia

Ciudad Autonoma Buenos Aires, Buenos Aires, Argentina

Site Status

Centro de Investigaciones Medicas Mar del Plata

Mar del Plata, Buenos Aires, Argentina

Site Status

Policlìnica Red Omip S.A - Ensayos Clinicos GC

Mar del Plata, Buenos Aires, Argentina

Site Status

Centro Dermatologico Schejtman

San Miguel, Buenos Aires, Argentina

Site Status

APRILLUS Asistencia e Investigacion

Buenos Aires, Ciudad Autonoma Buenos Aires, Argentina

Site Status

Instituto CAICI

Rosario, Santa Fe Province, Argentina

Site Status

Clinica Mayo de Urgencias Medicas Cruz Blanca SRL

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status

Centro de Investigaciones Medicas Tucuman

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status

Investigaciones Clinicas Tucuman

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status

Centro Medico Barrio Parque

Buenos Aires, , Argentina

Site Status

Centro Medico Dra Laura Maffei Investigacion Clinica Aplicada

Ciudad Autonoma Buenos Aires, , Argentina

Site Status

STAT Research S.A.

Ciudad Autonoma Buenos Aires, , Argentina

Site Status

Organizacion Medica de Investigacion (OMI)

Ciudad Autonoma Buenos Aires, , Argentina

Site Status

Hospital Britanico de Buenos Aires

Ciudad Autonoma Buenos Aires, , Argentina

Site Status

Centro Privado de Medicina Familiar - Mind Out Research

Ciudad Autonoma Buenos Aires, , Argentina

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Sanatorio Allende

Córdoba, , Argentina

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Instituto de Reumatologia

Mendoza, , Argentina

Site Status

CER San Juan Centro Polivalente de Asistencia e Inv. Clinica

San Juan, , Argentina

Site Status

UZ Leuven

Leuven, , Belgium

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Centre Hospitalier Universitaire de Liege

Liège, , Belgium

Site Status

The Waterside Clinic

Barrie, Ontario, Canada

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Hamilton Health Sciences Corporation

Hamilton, Ontario, Canada

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The Ottawa Hospital - General Campus

Ottawa, Ontario, Canada

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Peking Union Medical College Hospital

Beijing, Beijing Municipality, China

Site Status

Dongguan People's Hospital

Dongguan, Guangdong, China

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Guangdong Second Provincial General Hospital

Guangzhou, Guangdong, China

Site Status

Nanfang Hospital of Southern Medical University

Guangzhou, Guangdong, China

Site Status

Shenzhen People's Hospital

Shenzhen, Guangdong, China

Site Status

Hainan General Hospital

Haikou, Hainan, China

Site Status

The second Xiangya Hospital of Central South University

Changsha, Hu'nan, China

Site Status

ZhuZhou Central Hospital

Zhuzhou, Hu'nan, China

Site Status

EC of Union Hospital Tongji Medical College Huazhong University of Science and Technology

Wuhan, Hubei, China

Site Status

The Second Affiliated Hospital of Nanchang University

Nanchang, Jiangxi, China

Site Status

Jiangxi Pingxiang People's Hospital

Pingxiang, Jiangxi, China

Site Status

Jilin Province People's Hospital

Changchun, Jilin, China

Site Status

Yanbian University Hospital (Yanbian Hospital)

Yanji, Jilin, China

Site Status

Jiujiang No.1 People's Hospital

Jiujiang, Jiujiang, China

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Binzhou Medical University Hospital

Binzhou, Shandong, China

Site Status

Renji Hospital Shanghai Jiaotong University School of Medicine - West Branch

Shanghai, Shanghai Municipality, China

Site Status

Ruijin Hospital of Shanghai Jiaotong University School of Medicine

Shanghai, Shanghai Municipality, China

Site Status

The First Affiliated Hospital of Chengdu Medical College

Chengdu, Sichuan, China

Site Status

Tianjin Medical University General Hospital

Tianjin, Tianjin Municipality, China

Site Status

The First Affiliated Hospital of Ningbo University

Ningbo, Zhejiang, China

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Wenzhou People's Hospital

Wenzhou, Zhejiang, China

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Beijing Chaoyang Hospital, Capital Medical University

Beijing, , China

Site Status

Xuanwu Hospital Capital Medical University

Beijing, , China

Site Status

The First Hospital of Jilin University

Changchun, , China

Site Status

Xiangya Hospital, Central South University

Changsha, , China

Site Status

Centro de Investigacion Medico Asistencial S.A.S

Barranquilla, , Colombia

Site Status

Clínica de la Costa Ltda.

Barranquilla, , Colombia

Site Status

Centro de Investigacion en Reumatologia y Especialidades Medicas CIREEM S.A.S.

Bogotá, , Colombia

Site Status

Servimed S.A.S.

Bucaramanga, , Colombia

Site Status

IPS Centro Medico Julián Coronel S.A.

Cali, , Colombia

Site Status

Preventive Care Ltda

Chía, , Colombia

Site Status

Healthy Medical Center

Zipaquirá, , Colombia

Site Status

Revmatologie s.r.o.

Brno, , Czechia

Site Status

Fakultni nemocnice Olomouc

Olomouc, , Czechia

Site Status

Universitaetsmedizin Goettingen

Göttingen, Lower Saxony, Germany

Site Status

Medizinische Hochschule Hannover

Hanover, Lower Saxony, Germany

Site Status

Universitaetsklinikum Koeln

Cologne, North Rhine-Westphalia, Germany

Site Status

Universitaetsklinikum Muenster

Münster, North Rhine-Westphalia, Germany

Site Status

Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz

Mainz, Rhineland-Palatinate, Germany

Site Status

Obudai Egeszsegugyi Centrum Kft.

Budapest, , Hungary

Site Status

Del-pesti Centrumkorhaz - Orszagos Hematologiai es Infektologiai Intezet

Budapest, , Hungary

Site Status

Bekes Varmegyei Kozponti Korhaz

Gyula, , Hungary

Site Status

Vita Verum Medical Egeszsegugyi Szolgaltato Bt.

Székesfehérvár, , Hungary

Site Status

Vital Medical Center

Veszprém, , Hungary

Site Status

Rambam Health Care Center

Haifa, , Israel

Site Status

Meir Medical Center

Kfar Saba, , Israel

Site Status

Rabin Medical Center-Beilinson Campus

Petah Tikva, , Israel

Site Status

Chaim Sheba Medical Center

Ramat Gan, , Israel

Site Status

Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status

Istituto Clinico Humanitas

Rozzano, Milano, Italy

Site Status

Ospedale M. Scarlato

Scafati, Salerno, Italy

Site Status

Azienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia (Presidio Spedali Civili)

Brescia, , Italy

Site Status

Azienda Ospedale-Università di Padova

Padua, , Italy

Site Status

Azienda Ospedaliero Universitaria Pisana

Pisa, , Italy

Site Status

Azienda Ospedaliera San Camillo Forlanini

Roma, , Italy

Site Status

Università Campus Bio-Medico di Roma

Roma, , Italy

Site Status

Azienda Ospedaliera Universitaria Policlinico Umberto I - Università di Roma La Sapienza

Roma, , Italy

Site Status

JCHO Chukyo Hospital

Nagoya, Aichi-ken, Japan

Site Status

Fujita Health University Hospital

Toyoake-shi, Aichi-ken, Japan

Site Status

Chiba University Hospital

Chiba, Chiba, Japan

Site Status

NHO Chibahigashi National Hospital

Chiba, Chiba, Japan

Site Status

Chibaken Saiseikai Narashino Hospital

Narashino-shi, Chiba, Japan

Site Status

KKR Hamanomachi Hospital

Fukuoka, Fukuoka, Japan

Site Status

NHO Kyushu Medical Center

Fukuoka, Fukuoka, Japan

Site Status

Hospital of the University of Occupational and Environmental Health, Japan

Kitakyushu-shi, Fukuoka, Japan

Site Status

Hiroshima University Hospital

Hiroshima, Hiroshima, Japan

Site Status

Tonan Hospital

Sapporo, Hokkaido, Japan

Site Status

Japanese Red Cross Society Himeji Hospital

Himeji-shi, Hyōgo, Japan

Site Status

Kobe University Hospital

Kobe, Hyōgo, Japan

Site Status

Kobe City Hospital Organization Kobe City Medical Center General Hospital

Kobe, Hyōgo, Japan

Site Status

Kagawa University Hospital

Kita-gun, Kagawa-ken, Japan

Site Status

St. Marianna University Hospital

Kawasaki-shi, Kanagawa, Japan

Site Status

Kitasato University Hospital

Sagamihara-shi, Kanagawa, Japan

Site Status

Yokohama City University Medical Center

Yokohama, Kanagawa, Japan

Site Status

NHO Yokohama Medical Center

Yokohama, Kanagawa, Japan

Site Status

Japanese Red Cross Kumamoto Hospital

Kumamoto, Kumamoto, Japan

Site Status

Tohoku University Hospital

Sendai, Miyagi, Japan

Site Status

Nagasaki University Hospital

Nagasaki, Nagasaki, Japan

Site Status

NHO Osaka Minami Medical Center

Kawachinagano-shi, Osaka, Japan

Site Status

Tazuke-kofukai Medical Research Institute Kitano Hospital

Osaka, Osaka, Japan

Site Status

Kindai University Hospital

Osakasayama-shi, Osaka, Japan

Site Status

Osaka Medical and Pharmaceutical University Hospital

Takatsuki-shi, Osaka, Japan

Site Status

Saitama Medical University Hospital

Iruma-gun, Saitama, Japan

Site Status

Tokyo Medical and Dental University Hospital

Bunkyō City, Tokyo-To, Japan

Site Status

St. Luke's International Hospital

Chūōku, Tokyo-To, Japan

Site Status

Nihon University Itabashi Hospital

Itabashi-ku, Tokyo-To, Japan

Site Status

Toho University Ohashi Medical Center

Meguro-ku, Tokyo-To, Japan

Site Status

Toho University Omori Medical Center

Ōta-ku, Tokyo-To, Japan

Site Status

Keio University Hospital

Shinjuku-ku, Tokyo-To, Japan

Site Status

Center Hospital of the National Center for Global Health and Medicine

Shinjuku-ku, Tokyo-To, Japan

Site Status

Amsterdam UMC, Locatie VUMC

Amsterdam, , Netherlands

Site Status

Universitair Medisch Centrum Groningen

Groningen, , Netherlands

Site Status

UMC Utrecht

Utrecht, , Netherlands

Site Status

Centro Reumatologico

Caguas, , Puerto Rico

Site Status

S.C Centrul Medical de Diagnostic si Tratament Ambulator Neomed S.R.L

Brasov, , Romania

Site Status

S C Delta Health Care SRL

Bucharest, , Romania

Site Status

Spitalul Clinic Judetean de Urgenta Cluj Napoca

Cluj-Napoca, , Romania

Site Status

S.C.Centrul Medical Unirea SRL

Iași, , Romania

Site Status

Spitalul Judetean de Urgenta 'Sf. Ioan cel Nou' Suceava

Suceava, , Romania

Site Status

S.C Centrul Medical Unirea SRL

Târgu Mureş, , Romania

Site Status

Institute of Rheumatology

Belgrade, , Serbia

Site Status

University Clinical Center of Serbia

Belgrade, , Serbia

Site Status

Clinical Hospital Center Bezanijska kosa

Belgrade, , Serbia

Site Status

Institute of Treatment and Rehabilitation 'Niska Banja'

Niška Banja, , Serbia

Site Status

Whipps Cross University Hospital

London, Greater London, United Kingdom

Site Status

Guy's Hospital

London, Greater London, United Kingdom

Site Status

Doncaster Royal Infirmary

Doncaster, South Yorkshire, United Kingdom

Site Status

Cannock Chase Hospital

Cannock, Staffordshire, United Kingdom

Site Status

Countries

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United States Argentina Belgium Canada China Colombia Czechia Germany Hungary Israel Italy Japan Netherlands Puerto Rico Romania Serbia United Kingdom

Related Links

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https://www.topazlupusstudy.com/

Click here to learn more about this trial, visit our study website.

Other Identifiers

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2023-505696-74

Identifier Type: OTHER

Identifier Source: secondary_id

230LE304

Identifier Type: -

Identifier Source: org_study_id

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