Global Prevalence of ATTR-CM in Participants With HFpEF

NCT ID: NCT04424914

Last Updated: 2024-07-19

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

NA

Total Enrollment

347 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-12-30

Study Completion Date

2023-06-02

Brief Summary

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This study is a global, multi-center study designed to estimate the global prevalence of transthyretin amyloid cardiomyopathy (ATTR-CM) within a clinically at risk population \[participants with heart failure with preserved ejection fraction (HFpEF)\].

Detailed Description

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Conditions

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Transthyretin Amyloid Cardiomyopathy Heart Failure With Preserved Ejection Fraction

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

To determine global prevalence of transthyretin amyloid cardiomyopathy in participants diagnosed with heart failure with preserved ejection fraction. No study treatment will be dispensed however, participants will undergo scintigraphy.
Primary Study Purpose

SCREENING

Blinding Strategy

NONE

Study Groups

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ATTR-CM positive

Participants diagnosed with ATTR-CM by scintigraphy

Group Type OTHER

Scintigraphy

Intervention Type DIAGNOSTIC_TEST

scintigraphy

ATTR-CM negative

Participants who are scintigraphy negative for ATTR-CM

Group Type OTHER

Scintigraphy

Intervention Type DIAGNOSTIC_TEST

scintigraphy

Interventions

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Scintigraphy

scintigraphy

Intervention Type DIAGNOSTIC_TEST

Eligibility Criteria

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Inclusion Criteria

1. Medical history of heart failure (HF) with:

1. At least 1 episode with clinical evidence of HF (without hospitalization) by signs or symptoms of volume overload or elevated intracardiac pressures that required/requires treatment with a diuretic for improvement; OR
2. 1 prior hospitalization for HF.
2. Left ventricular ejection fraction (LVEF) \>40%.
3. End-diastolic interventricular septal wall thickness (IVST) ≥12 mm.
4. Willing and able to undergo scintigraphy.

Exclusion Criteria

1. Diagnosis of heart failure with reduced ejection fraction (HFrEF) (EF ≤40%).
2. Prior clinical history of myocardial infarction, CABG or multi-vessel obstructive coronary disease (\>50% stenosis of ≥2 epicardial coronary arteries).
3. Presence or history of any severe valvular heart disease (obstructive or regurgitant).
4. A confirmed diagnosis of a non-amyloid infiltrative cardiomyopathy (ie, cardiac sarcoidosis, hemochromatosis), muscular dystrophies, cardiomyopathy with reversible causes, hypertrophic obstructive cardiomyopathy with known genetic etiology, or known pericardial constriction.
5. Any type of diagnosed amyloidosis (eg, amyloid A amyloidosis, primary \[light chain\] amyloidosis) or prior diagnosis of ATTR-CM.

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Minimum Eligible Age

60 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Eastern shore Research Institute LLC

Fairhope, Alabama, United States

Site Status

Heart Center Research, LLC

Huntsville, Alabama, United States

Site Status

Advance Medical Research Center

Miami, Florida, United States

Site Status

Bioclinical Research Alliance Inc.

Miami, Florida, United States

Site Status

Biogenix Molecular

Miami, Florida, United States

Site Status

CIRA (Nuclear Imaging Facility)

Miami, Florida, United States

Site Status

Nucleotron/ Doral Imaging Institute, CIRA DBA

Miami, Florida, United States

Site Status

Innova Pharma Research

Miami, Florida, United States

Site Status

Ocala Cardiovascular Research

Ocala, Florida, United States

Site Status

Chicago Medical Research, LLC

Hazel Crest, Illinois, United States

Site Status

Advocate Christ Medical Center

Oak Lawn, Illinois, United States

Site Status

Stormont Vail Health

Topeka, Kansas, United States

Site Status

Cotton O'Neil Heart Center

Topeka, Kansas, United States

Site Status

Ochsner Medical Center

New Orleans, Louisiana, United States

Site Status

Corewell Health

Grand Rapids, Michigan, United States

Site Status

Spectrum Health Medical Group Cardiovascular Medicine

Grand Rapids, Michigan, United States

Site Status

Cardiology Associates of North Mississippi, LLC

Tupelo, Mississippi, United States

Site Status

Cardiology Associates Research, LLC

Tupelo, Mississippi, United States

Site Status

NYU Langone Health

New York, New York, United States

Site Status

WakeMed Health and Hospital

Raleigh, North Carolina, United States

Site Status

The Jackson Clinic

Jackson, Tennessee, United States

Site Status

Providence Sacred Heart Medical Center and Children's Hospital

Spokane, Washington, United States

Site Status

University of Ottawa Heart Institute

Ottawa, Ontario, Canada

Site Status

CardioVasc HR Inc

Saint-Jean-sur-Richelieu, Quebec, Canada

Site Status

Diex Recherche Trois-Rivieres

Trois-Rivières, Quebec, Canada

Site Status

Hôpital Louis Pradel

Bron, , France

Site Status

Centre Hospitalier Saint-Joseph Saint-Luc

Lyon, , France

Site Status

CHU Nimes - Hospital Caremeau

Nîmes, , France

Site Status

CHU de Toulouse - Hôpital de Rangueil

Toulouse, , France

Site Status

Médecine Nucléaire de la Doua

Villeurbanne, , France

Site Status

IRCCS Azienda Ospedaliero-Universitaria di Bologna, Policlinico di Sant'Orsola

Bologna, BO, Italy

Site Status

U.O. Clinica delle Malattie dell'Apparato Cardiovascolare - Ospedale Policlinico San Martino IRCCS

Genova, Genoa, Italy

Site Status

U.O. Clinica delle Malattie dell'Apparato Cardiovascolare - Ospedale Policlinico San Martino IRCCS

Genova, , Italy

Site Status

Fondazione IRCCS Policlinico San Matteo - Centro per lo Studio e la Cura delle Amiloidosi Sistemiche

Pavia, , Italy

Site Status

Fondazione Toscana Gabriele Monasterio-UOC Cardiologia e Medicina Cardiovascolare

Pisa, , Italy

Site Status

Nagoya Tokushukai General Hospital

Kasugai, Aichi-ken, Japan

Site Status

Fukuoka Tokushukai Hospital

Kasuga, Fukuoka, Japan

Site Status

Keio University Hospital

Shinjuku-ku, Tokyo, Japan

Site Status

Okayama University Hospital

Okayama, , Japan

Site Status

Krakowski Szpital Specjalistyczny im. Jana Pawła II

Krakow, Lesser Poland Voivodeship, Poland

Site Status

Uniwersytecki Szpital Kliniczny im. Jana Mikulicza-Radeckiego we Wrocławiu

Wroclaw, Lower Silesian Voivodeship, Poland

Site Status

Uniwersytecki Szpital Kliniczny w Białymstoku

Bialystok, Podlaskie Voivodeship, Poland

Site Status

SPZOZ Uniwersytecki Szpital Kliniczny Im. Wojskowej Akademii Medycznej UM W Łodzi Centralny Szpital

Lodz, Łódź Voivodeship, Poland

Site Status

Hospital Universitario Puerta de Hierro Majadahonda

Majadahonda, Madrid, Spain

Site Status

Hospital Universitari Vall d´Hebron

Barcelona, , Spain

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

Hospital Universitari De Bellvitge

Barcelona, , Spain

Site Status

Hospital Universitario Ramón y Cajal

Madrid, , Spain

Site Status

Hospital Universitario de Salamanca - Complejo Asistencial Universitario de Salamanca

Salamanca, , Spain

Site Status

Hospital Universitari i Politècnic La Fe

Valencia, , Spain

Site Status

St George's Hospital, St George's University Hospitals NHS Foundation Trust

London, , United Kingdom

Site Status

Countries

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United States Canada France Italy Japan Poland Spain United Kingdom

References

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Yun S, Palladini G, Anderson LJ, Cariou E, Wang R, Angeli FS, Ebede B, Garcia-Pavia P. International prevalence of transthyretin amyloid cardiomyopathy in high-risk patients with heart failure and preserved or mildly reduced ejection fraction. Amyloid. 2024 Dec;31(4):291-301. doi: 10.1080/13506129.2024.2398446. Epub 2024 Sep 8.

Reference Type DERIVED
PMID: 39245873 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://pmiform.com/clinical-trial-info-request?StudyID=B3461087

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Other Identifiers

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HFpEF ATTR-CM prevalence study

Identifier Type: OTHER

Identifier Source: secondary_id

2020-002378-29

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

ATTR-POP

Identifier Type: OTHER

Identifier Source: secondary_id

B3461087

Identifier Type: -

Identifier Source: org_study_id

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